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Antisense oligonucleotides targeting valosin-containing protein ameliorate muscle pathology and molecular defects in cell and mouse models of multisystem proteinopathy.
VCP p.Arg191Gln mutation in a patient with semantic dementia: a case report.
Utilization of CoRDS registry to monitor quality of life in patients with VCP multisystem proteinopathy.
2024 VCP International Conference: Exploring multi-disciplinary approaches from basic science of valosin containing protein, an AAA+ ATPase protein, to the therapeutic advancement for VCP-associated multisystem proteinopathy.
Valosin-Containing Protein (VCP)/p97 Oligomerization.