Raras
Buscar doenças, sintomas, genes...
Lipomatose simétrica múltipla
ORPHA:2398CID-10 · E88.8CID-11 · EF02.1OMIM 151800DOENÇA RARA

Uma doença rara do tecido embaixo da pele, caracterizada pelo crescimento de massas de gordura simétricas e sem uma cápsula definida, principalmente no rosto e pescoço. Isso pode causar diferentes problemas de saúde, como dificuldade para mover o pescoço ou compressão (apertamento) das vias respiratórias.

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Introdução

O que você precisa saber de cara

📋

Uma doença rara do tecido embaixo da pele, caracterizada pelo crescimento de massas de gordura simétricas e sem uma cápsula definida, principalmente no rosto e pescoço. Isso pode causar diferentes problemas de saúde, como dificuldade para mover o pescoço ou compressão (apertamento) das vias respiratórias.

Pesquisas ativas
1 ensaio
34 total registrados no ClinicalTrials.gov
Publicações científicas
198 artigos
Último publicado: 2026 Mar 30

Escala de raridade

CLASSIFICAÇÃO ORPHANET · BRASIL 2024
Unknown
Ultra-rara
<1/50k
Muito rara
1/20k
Rara
1/10k
Pouco freq.
1/5k
Incomum
1/2k
Prevalência
0.0
Worldwide
Início
Adolescent
+ adult, childhood, elderly
🏥
SUS: Sem cobertura SUSScore: 0%
CID-10: E88.8
Você se identifica com essa condição?
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Entender a doença

Do básico ao detalhe, leia no seu ritmo

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Sinais e sintomas

O que aparece no corpo e com que frequência cada sintoma acontece

Partes do corpo afetadas

💪
Músculos
4 sintomas
🧠
Neurológico
2 sintomas
😀
Face
2 sintomas
🦴
Ossos e articulações
2 sintomas
📏
Crescimento
1 sintomas
🫃
Digestivo
1 sintomas

+ 12 sintomas em outras categorias

Características mais comuns

100%prev.
Neuropatia periférica
Frequente (79-30%)
100%prev.
Lipomas múltiplos
Muito frequente (99-80%)
100%prev.
Neuropatia axonal periférica
Obrigatório (100%)
100%prev.
Cifose
Obrigatório (100%)
100%prev.
Fraqueza muscular progressiva
Obrigatório (100%)
100%prev.
Atrofia do músculo esquelético
Obrigatório (100%)
25sintomas
Muito frequente (17)
Frequente (7)
Sem dados (1)

Os sintomas variam de pessoa para pessoa. Abaixo estão as 25 características clínicas mais associadas, ordenadas por frequência.

Neuropatia periféricaPeripheral neuropathy
Frequente (79-30%)100%
Lipomas múltiplosMultiple lipomas
Muito frequente (99-80%)100%
Neuropatia axonal periféricaPeripheral axonal neuropathy
Obrigatório (100%)100%
CifoseKyphosis
Obrigatório (100%)100%
Fraqueza muscular progressivaProgressive muscle weakness
Obrigatório (100%)100%

Linha do tempo da pesquisa

Publicações por ano — veja quando o interesse científico cresceu
Anos de pesquisa1desde 2026
Total histórico198PubMed
Últimos 10 anos71publicações
Pico202011 papers
Linha do tempo
2026Hoje · 2026🧪 1994Primeiro ensaio clínico📈 2020Ano de pico
Publicações por ano (últimos 10 anos)

Encontrou um erro ou informação desatualizada? Sugira uma correção →

Genética e causas

O que está alterado no DNA e como passa nas famílias

Genes associados

1 gene identificado com associação a esta condição. Padrão de herança: Autosomal dominant, Autosomal recessive, Mitochondrial inheritance, Not applicable.

MFN2Mitofusin-2Disease-causing germline mutation(s) (loss of function) inTolerante
FUNÇÃO

Mitochondrial outer membrane GTPase that mediates mitochondrial clustering and fusion (PubMed:11181170, PubMed:11950885, PubMed:19889647, PubMed:26214738, PubMed:28114303). Mitochondria are highly dynamic organelles, and their morphology is determined by the equilibrium between mitochondrial fusion and fission events (PubMed:28114303). Overexpression induces the formation of mitochondrial networks (PubMed:28114303). Membrane clustering requires GTPase activity and may involve a major rearrangeme

LOCALIZAÇÃO

Mitochondrion outer membrane

VIAS BIOLÓGICAS (2)
Factors involved in megakaryocyte development and platelet productionRHOT2 GTPase cycle
MECANISMO DE DOENÇA

Charcot-Marie-Tooth disease, axonal, type 2A2B

An axonal form of Charcot-Marie-Tooth disease, a disorder of the peripheral nervous system, characterized by progressive weakness and atrophy, initially of the peroneal muscles and later of the distal muscles of the arms. Charcot-Marie-Tooth disease is classified in two main groups on the basis of electrophysiologic properties and histopathology: primary peripheral demyelinating neuropathies (designated CMT1 when they are dominantly inherited) and primary peripheral axonal neuropathies (CMT2). Neuropathies of the CMT2 group are characterized by signs of axonal degeneration in the absence of obvious myelin alterations, normal or slightly reduced nerve conduction velocities, and progressive distal muscle weakness and atrophy. CMT2A2B is a severe form with autosomal recessive inheritance.

EXPRESSÃO TECIDUAL(Ubíquo)
Coração - Ventrículo esquerdo
173.4 TPM
Músculo esquelético
158.4 TPM
Esôfago - Muscular
143.1 TPM
Coração - Átrio
137.5 TPM
Esôfago - Junção
119.7 TPM
OUTRAS DOENÇAS (7)
multiple symmetric lipomatosisCharcot-Marie-Tooth disease type 2A2Charcot-Marie-Tooth disease, axonal, autosomal recessive, type 2a2b;neuropathy, hereditary motor and sensory, type 6A
HGNC:16877UniProt:O95140

Variantes genéticas (ClinVar)

408 variantes patogênicas registradas no ClinVar.

🧬 MFN2: NM_014874.4(MFN2):c.1355del (p.Phe452fs) ()
🧬 MFN2: NM_014874.4(MFN2):c.2148del (p.Ala716_Met717insTer) ()
🧬 MFN2: NM_014874.4(MFN2):c.2182C>T (p.Gln728Ter) ()
🧬 MFN2: NM_014874.4(MFN2):c.175+1G>A ()
🧬 MFN2: NM_014874.4(MFN2):c.1717-30_1771del ()
Ver todas no ClinVar

Classificação de variantes (ClinVar)

Distribuição de 4 variantes classificadas pelo ClinVar.

3
1
Patogênica (75.0%)
VUS (25.0%)
VARIANTES MAIS SIGNIFICATIVAS
MFN2: NM_014874.4(MFN2):c.2230G>A (p.Glu744Lys) [Conflicting classifications of pathogenicity]
MFN2: NM_014874.4(MFN2):c.749G>A (p.Arg250Gln) [Conflicting classifications of pathogenicity]
MFN2: NM_014874.4(MFN2):c.2119C>T (p.Arg707Trp) [Pathogenic/Likely pathogenic]
MFN2: NM_014874.4(MFN2):c.1555C>T (p.Arg519Cys) [Uncertain significance]

Vias biológicas (Reactome)

3 vias biológicas associadas aos genes desta condição.

Diagnóstico

Os sinais que médicos procuram e os exames que confirmam

Carregando...

Tratamento e manejo

Remédios, cuidados de apoio e o que precisa acompanhar

Pipeline de tratamentos
Pipeline regulatório — de medicamentos já aprovados a drogas em pesquisa exploratória.
3Fase 31
2Fase 21
·Pré-clínico2
Medicamentos catalogadosEnsaios clínicos· 0 medicamentos · 4 ensaios
Carregando informações de tratamento...

Onde tratar no SUS

Hospitais de referência no Brasil e o protocolo oficial do SUS (PCDT)

🇧🇷 Atendimento SUS — Lipomatose simétrica múltipla

🗺️

Selecione um estado ou use sua localização para ver resultados.

Dados de DATASUS/CNES, SBGM, ABNeuro e Ministério da Saúde. Sempre confirme a disponibilidade diretamente com o estabelecimento.

Pesquisa ativa

Ensaios clínicos abertos e novidades científicas recentes

Pesquisa e ensaios clínicos

34 ensaios clínicos encontrados, 1 ativos.

Distribuição por fase
Ver todos no ClinicalTrials.gov
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Publicações mais relevantes

Timeline de publicações
74 papers (10 anos)
#1

Madelung's disease involving the scrotum: a case report and diagnostic pitfalls with liposarcoma.

Frontiers in oncology2026

Madelung's disease is a rare metabolic disorder characterized by diffuse, symmetrical adipose tissue proliferation, strongly associated with chronic alcohol consumption. Scrotal involvement is exceedingly rare and can mimic malignancy. We report a 59-year-old man with a history of chronic alcohol intake who presented with progressive bilateral scrotal enlargement. Unlike previously reported cases of scrotal Madelung's disease, which typically demonstrate homogeneous and unencapsulated fat proliferation, MRI in this patient revealed atypical imaging features, including multiple internal fibrous septa and distinct nodular-like foci within fat-containing scrotal masses, raising suspicion of liposarcoma. Complete surgical excision was performed. Histopathology confirmed benign lipomatosis with CDK4(+), MDM2(+), Ki-67 (+,2%), and negative MDM2 amplification on fluorescence in situ hybridization (FISH), arguing against well-differentiated liposarcoma. The patient remained recurrence-free at 12-month follow-up. This case emphasizes the critical role of multimodal medical imaging, rigorous histopathological evaluation, and molecular testing in establishing an accurate diagnosis and guiding appropriate management, while highlighting that Madelung's disease may occasionally present with atypical imaging features, such as nodules and septa which closely mimic a malignant lesion.

#2

Madelung Disease of the Scrotal Region: A Case Report.

IJU case reports2026 Jan

Madelung disease is a rare disorder characterized by symmetrical fat accumulation, typically around the neck, shoulders, and trunk. A 56-year-old man presented for 10-month history of dysuria and painless swelling of the lower abdomen and scrotum. A large scrotal mass completely buried the penis, and cranially displaced both testes. Contrast-enhanced magnetic resonance imaging suggested a well differentiated liposarcoma but whole-body computed tomography revealed symmetrical fat accumulation in the upper body trunk, raising suspicion of Madelung disease. Biopsy of the mass confirmed a benign lipoma. Excision of a 664 g lipoma improved the patient's penile configuration, enabling him to urinate in a standing position. Madelung disease in the scrotal region is rare, only nine cases reported to date. However, it should be considered when bilateral symmetrical fat accumulation is present because a correct diagnosis has a decisive impact on treatment strategy.

#3

Teaching NeuroImage: Multiple Symmetric Lipomatosis as a Manifestation of Mitochondrial Cytopathy.

Neurology2025 Nov 11
#4

Multiple symmetric lipomatosis as a marker of mitochondrial disease. Case report and review of the literature.

Neurological sciences : official journal of the Italian Neurological Society and of the Italian Society of Clinical Neurophysiology2025 Jan
#5

Correction: Madelung's disease -a case series from a single-center experience.

Frontiers in surgery2025

[This corrects the article DOI: 10.3389/fsurg.2025.1636822.].

Publicações recentes

Ver todas no PubMed

📚 EuropePMC132 artigos no totalmostrando 69

2026

Madelung's disease involving the scrotum: a case report and diagnostic pitfalls with liposarcoma.

Frontiers in oncology
2026

Madelung Disease of the Scrotal Region: A Case Report.

IJU case reports
2025

Madelung's disease -a case series from a single-center experience.

Frontiers in surgery
2025

Teaching NeuroImage: Multiple Symmetric Lipomatosis as a Manifestation of Mitochondrial Cytopathy.

Neurology
2025

A real-world pharmacovigilance assessment and literature review of lymphoma development in lipodystrophy.

Frontiers in endocrinology
2025

Benign Symmetric Lipomatosis of the Tongue With Dysgeusia: A Case Report and Literature Review.

Cureus
2024

Loss of Mfn1 but not Mfn2 enhances adipogenesis.

PloS one
2024

Research progress on the pathogenesis of multiple symmetrical lipomatosis.

Adipocyte
2024

Could Madelung disease be a cause of stroke? A rare case report.

Folia medica
2024

A case report on Madelung's disease and comprehensive review of the literature.

Orphanet journal of rare diseases
2025

Multiple symmetric lipomatosis as a marker of mitochondrial disease. Case report and review of the literature.

Neurological sciences : official journal of the Italian Neurological Society and of the Italian Society of Clinical Neurophysiology
2024

Madelung's Disease Evolving to Liposarcoma: An Uncommon Encounter.

Life (Basel, Switzerland)
2023

Multiple symmetrical lipomatosis: A literature review and case report of a patient with Madelung's disease.

Polski przeglad chirurgiczny
2023

Shedding Light on Multiple Symmetric Lipomatosis: An Overlooked Syndrome in the Evaluation of Obesity.

The American journal of case reports
2023

Multiple symmetric lipomatosis with chronic kidney disease and tophi.

Oxford medical case reports
2022

Multiple Symmetric Lipomatosis: Lipectomy for Madelung Collar.

Plastic and aesthetic nursing
2022

Is There any Link between Madelung Disease and Ischemic Stroke? A Case Report.

Neurology India
2022

Madelung's Disease: Analysis of Clinical Characteristics, Fatty Mass Distribution, Comorbidities and Treatment of 54 Patients in China.

Diabetes, metabolic syndrome and obesity : targets and therapy
2022

Diagnostic and surgical challenges of progressive neck and upper back painless masses in Madelung's disease: A case report and review of literature.

World journal of clinical cases
2022

Ketogenic diet for mitochondrial disease: potential role in treating the Multiple Symmetric Lipomatosis phenotype associated with the common MT-TK genetic mutation.

Orphanet journal of rare diseases
2021

Transcutaneous electrical stimulation therapy and genetic analysis in Dercum's disease: A pilot study.

Medicine
2022

Invited Response on: Adipose Tissue in Multiple Symmetric Lipomatosis Shows Features of Brown/Beige Fat.

Aesthetic plastic surgery
2021

Multiple symmetric and multiple familial lipomatosis.

Presse medicale (Paris, France : 1983)
2021

Madelung's disease with alcoholic liver disease and acute kidney injury: A case report.

World journal of clinical cases
2022

Adipose Tissue in Multiple Symmetric Lipomatosis Shows Features of Brown: Beige Fat.

Aesthetic plastic surgery
2021

Multiple symmetric lipomatosis (Madelung's disease) with symptoms and signs of hypertension, lipodystrophy, and dyspnea: A case report and literature review.

Clinical case reports
2021

Madelung's disease. Two case reports with pseudoathletic appearance.

La Clinica terapeutica
2021

A non-alcohol-related case of Madelung's disease: Challenging patient with progressive jugular vein distension.

Radiology case reports
2021

Madelung Disease Epidemiology and Clinical Characteristics: a Systemic Review.

Aesthetic plastic surgery
2020

Loss of FZO1 gene results in changes of cell dynamics in fission yeast.

International journal of molecular medicine
2020

Cbl Proto-Oncogene B (CBLB) c.197A>T Mutation Induces Mild Metabolic Dysfunction in Partial Type I Multiple Symmetric Lipomatosis (MSL).

Diabetes, metabolic syndrome and obesity : targets and therapy
2020

White Adipose Tissue Expansion in Multiple Symmetric Lipomatosis Is Associated with Upregulation of CK2, AKT and ERK1/2.

International journal of molecular sciences
2021

LIPE-related lipodystrophic syndrome: clinical features and disease modeling using adipose stem cells.

European journal of endocrinology
2020

A case report of Multiple Symmetric Lipomatosis (MSL) in an East Asian Female.

BMC women's health
2020

Establishment of a human induced pluripotent stem cell line, JUCTCi012-A, from multiple symmetric lipomatosis (MSL) patient carrying a homozygous Arg707Trp (c.2119C > T) mutation in the MFN2 gene.

Stem cell research
2020

Multiple symmetric lipomatosis with secondary laryngeal obstruction: A case report.

Medicine
2020

Multiple symmetric lipomatosis of the male breast: An unusual mimic of gynecomastia.

Nigerian journal of clinical practice
2020

Self-initiated lifestyle interventions lead to potential insight into an effective, alternative, non-surgical therapy for mitochondrial disease associated multiple symmetric lipomatosis.

Mitochondrion
2020

Adipose Tissue in Multiple Symmetric Lipomatosis Shows Features of Brown/Beige Fat.

Aesthetic plastic surgery
2020

Imaging spectrum of abnormal subcutaneous and visceral fat distribution.

Insights into imaging
2020

Mitochondrial DNA pathogenic mutations in multiple symmetric lipomatosis.

Clinical genetics
2019

Madelung's Disease Leading to Presenile Dementia in a Non-alcoholic Patient.

Medical archives (Sarajevo, Bosnia and Herzegovina)
2019

Genetic syndromes with localized subcutaneous fat tissue accumulation.

Acta bio-medica : Atenei Parmensis
2019

Multiple symmetric lipomatosis: A clinical marker of mitochondrial cytopathy.

Neurology India
2019

Calcyphosine-like (CAPSL) is regulated in Multiple Symmetric Lipomatosis and is involved in Adipogenesis.

Scientific reports
2019

Multiple Symmetric Lipomatosis in a Chronic Male Alcoholic.

Ear, nose, &amp; throat journal
2018

Multiple Symmetric Lipomatosis (Madelung Disease) in a Large Canadian Family With the Mitochondrial MTTK c.8344A>G Variant.

Journal of investigative medicine high impact case reports
2018

MFN2-associated lipomatosis: Clinical spectrum and impact on adipose tissue.

Journal of clinical lipidology
2018

Madelung disease (multiple symmetric lipomatosis).

Autopsy &amp; case reports
2018

Multiple Symmetric Lipomatosis: New Classification System Based on the Largest German Patient Cohort.

Plastic and reconstructive surgery. Global open
2018

Adipose tissue-derived stem cells from affected and unaffected areas in patients with multiple symmetric lipomatosis show differential regulation of mTOR pathway genes.

Clinical hemorheology and microcirculation
2018

Madelung's disease (multiple symmetric lipomatosis) in an alcoholic patient.

Revista de gastroenterologia de Mexico (English)
2017

Profiling of differentially expressed genes in adipose tissues of multiple symmetric lipomatosis.

Molecular medicine reports
2017

Multiple symmetric lipomatosis.

Polish archives of internal medicine
2017

Multiple symmetric lipomatosis and gynecomastia: A case report and relative literature review.

Journal of clinical lipidology
2017

Madelung's Disease: Revision of 59 Surgical Cases.

Aesthetic plastic surgery
2017

Homozygous LIPE mutation in siblings with multiple symmetric lipomatosis, partial lipodystrophy, and myopathy.

American journal of medical genetics. Part A
2016

Central nervous system involvement in multiple symmetric lipomatosis.

Journal of the neurological sciences
2016

A case of symmetrical lipomatosis of the tongue presenting as macroglossia.

Annali italiani di chirurgia
2016

Adipose-Derived Stromal Cells from Lipomas: Isolation, Characterisation and Review of the Literature.

Pathobiology : journal of immunopathology, molecular and cellular biology
2016

Transcription Profile in Sporadic Multiple Symmetric Lipomatosis Reveals Differential Expression at the Level of Adipose Tissue-Derived Stem Cells.

Plastic and reconstructive surgery
2016

Multiple symmetric lipomatosis with spindle cell proliferation.

Pathology international
2015

Multiple Symmetric Lipomatosis Presenting with Bilateral Brachial Plexopathy.

Journal of clinical neurology (Seoul, Korea)
2015

Symmetrical lipomatosis of the tongue: Case report and literature review.

Journal of clinical lipidology
2015

Extracorporeal Acoustic Wave Therapy and Multiple Symmetric Lipomatosis.

Plastic and reconstructive surgery. Global open
2015

miR-125a-3p and miR-483-5p promote adipogenesis via suppressing the RhoA/ROCK1/ERK1/2 pathway in multiple symmetric lipomatosis.

Scientific reports
2015

Homozygous mutations in MFN2 cause multiple symmetric lipomatosis associated with neuropathy.

Human molecular genetics
2014

A middle-aged man with increasing body fat.

Clinical obesity
2015

Multiple symmetric lipomatosis: a rare disease and its possible links to brown adipose tissue.

Nutrition, metabolism, and cardiovascular diseases : NMCD
Ver todos os 132 no EuropePMC

Associações

Organizações que acompanham esta doença — pra ter apoio e orientação

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Comunidades

Grupos ativos de quem convive com esta doença aqui no Raras

Ainda não existe comunidade no Raras para Lipomatose simétrica múltipla

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Doenças relacionadas

Doenças com sintomas parecidos — ajudam quem ainda está buscando diagnóstico

Ordenadas pelo número de sintomas em comum.

Referências e fontes

Bases de dados externas citadas neste artigo

Publicações científicas

Artigos indexados no PubMed ligados a esta doença no grafo RarasNet — título, periódico e PMID direto da fonte, sem intermediação de IA.

  1. Madelung's disease involving the scrotum: a case report and diagnostic pitfalls with liposarcoma.
    Frontiers in oncology· 2026· PMID 41869673mais citado
  2. Madelung Disease of the Scrotal Region: A Case Report.
    IJU case reports· 2026· PMID 41492307mais citado
  3. Teaching NeuroImage: Multiple Symmetric Lipomatosis as a Manifestation of Mitochondrial Cytopathy.
    Neurology· 2025· PMID 41026963mais citado
  4. Multiple symmetric lipomatosis as a marker of mitochondrial disease. Case report and review of the literature.
    Neurological sciences : official journal of the Italian Neurological Society and of the Italian Society of Clinical Neurophysiology· 2025· PMID 39060540mais citado
  5. Correction: Madelung's disease -a case series from a single-center experience.
    Frontiers in surgery· 2025· PMID 41256837mais citado
  6. Novel MFN2 compound heterozygote genotype in a patient with multiple symmetric lipomatosis and metabolic dysfunction.
    J Clin Lipidol· 2026· PMID 41991472recente
  7. Giant Cervicothoracic Madelung Disease Presenting with Airway Compromise: A Case Report from Ethiopia.
    Surg Case Rep· 2026· PMID 41928894recente

Bases de dados e fontes oficiais

Identificadores e referências canônicas usadas para montar este verbete.

  1. ORPHA:2398(Orphanet)
  2. OMIM OMIM:151800(OMIM)
  3. MONDO:0007908(MONDO)
  4. GARD:6957(GARD (NIH))
  5. Variantes catalogadas(ClinVar)
  6. Busca completa no PubMed(PubMed)
  7. Q4887975(Wikidata)

Dados compilados pelo RarasNet a partir de fontes abertas (Orphanet, OMIM, MONDO, PubMed/EuropePMC, ClinicalTrials.gov, DATASUS, PCDT/MS). Este conteúdo é informativo e não substitui avaliação médica.

Conteúdo mantido por Agente Raras · Médicos e pesquisadores podem colaborar

Lipomatose simétrica múltipla
Compêndio · Raras BR

Lipomatose simétrica múltipla

ORPHA:2398 · MONDO:0007908
Prevalência
Unknown
Herança
Autosomal dominant, Autosomal recessive, Mitochondrial inheritance, Not applicable
CID-10
E88.8 · Outros distúrbios especificados do metabolismo
CID-11
Ensaios
1 ativos
Início
Adolescent, Adult, Childhood, Elderly
Prevalência
0.0 (Worldwide)
MedGen
UMLS
C0024445
EuropePMC
Wikidata
Papers 10a
DiscussaoAtiva

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