Raras
Buscar doenças, sintomas, genes...
Hipertensão arterial pulmonar
ORPHA:182090CID-11 · BB01.0PCDT · SUSDOENÇA RARA

A hipertensão arterial pulmonar (HAP) é um grupo de doenças caracterizadas por pressão média da artéria pulmonar >20 mmHg e resistência arterial pulmonar elevada, levando à insuficiência cardíaca direita. A HAP é progressiva e potencialmente fatal. A HAP pode ser idiopática e/ou familiar, ter características evidentes de envolvimento venoso/capilar (doença veno-oclusiva pulmonar, PVOD/hemangiomatose capilar pulmonar, HCP), induzida por medicamento ou toxina (HAP induzida por medicamento ou toxina), ou associada a outras doenças como cardiopatia congênita, doença do tecido conjuntivo, HIV, esquistossomose, hipertensão portal (HAP associada a outras doenças).

Mantido por Agente Raras·Colaborar como especialista →

Introdução

O que você precisa saber de cara

📋

A hipertensão arterial pulmonar (HAP) é um grupo de doenças caracterizadas por pressão média da artéria pulmonar >20 mmHg e resistência arterial pulmonar elevada, levando à insuficiência cardíaca direita. A HAP é progressiva e potencialmente fatal. A HAP pode ser idiopática e/ou familiar, ter características evidentes de envolvimento venoso/capilar (doença veno-oclusiva pulmonar, PVOD/hemangiomatose capilar pulmonar, HCP), induzida por medicamento ou toxina (HAP induzida por medicamento ou toxina), ou associada a outras doenças como cardiopatia congênita, doença do tecido conjuntivo, HIV, esquistossomose, hipertensão portal (HAP associada a outras doenças).

Pesquisas ativas
36 ensaios
834 total registrados no ClinicalTrials.gov
Publicações científicas
18.986 artigos
Último publicado: 2026

Escala de raridade

CLASSIFICAÇÃO ORPHANET · BRASIL 2024
1-9 / 100 000
Ultra-rara
<1/50k
Muito rara
1/20k
Rara
1/10k
Pouco freq.
1/5k
Incomum
1/2k
Prevalência
2.0
Europe
Início
All ages
🏥
SUS: Cobertura parcialScore: 50%
PCDT disponível7 medicamentos CEAF
Você se identifica com essa condição?
O Raras está aqui pra te apoiar — com ou sem diagnóstico

Encontrou um erro ou informação desatualizada? Sugira uma correção →

Entender a doença

Do básico ao detalhe, leia no seu ritmo

Preparando trilha educativa...

Sinais e sintomas

O que aparece no corpo e com que frequência cada sintoma acontece

Partes do corpo afetadas

❤️
Coração
27 sintomas
🫁
Pulmão
13 sintomas
🩸
Sangue
6 sintomas
🫃
Digestivo
4 sintomas
🧠
Neurológico
1 sintomas
🫘
Rins
1 sintomas

+ 41 sintomas em outras categorias

Características mais comuns

Insuficiência cardíaca congestiva
Hipercoagulabilidade
Abscesso cerebral
Acidente vascular cerebral
Defeito do canal atrioventricular
Concentração elevada de proteína C-reativa circulante
95sintomas
Sem dados (95)

Os sintomas variam de pessoa para pessoa. Abaixo estão as 95 características clínicas mais associadas, ordenadas por frequência.

Insuficiência cardíaca congestivaCongestive heart failure
HipercoagulabilidadeHypercoagulability
Abscesso cerebralBrain abscess
Acidente vascular cerebralStroke
Defeito do canal atrioventricularAtrioventricular canal defect

Linha do tempo da pesquisa

Publicações por ano — veja quando o interesse científico cresceu
Anos de pesquisa1desde 2026
Total histórico18.986PubMed
Últimos 10 anos200publicações
Pico2026194 papers
Linha do tempo
2026Hoje · 2026🧪 1965Primeiro ensaio clínico
Publicações por ano (últimos 10 anos)

Encontrou um erro ou informação desatualizada? Sugira uma correção →

Genética e causas

O que está alterado no DNA e como passa nas famílias

Genes associados

12 genes identificados com associação a esta condição. Padrão de herança: Autosomal dominant, Not applicable.

CAV1Caveolin-1Disease-causing germline mutation(s) inTolerante
FUNÇÃO

May act as a scaffolding protein within caveolar membranes (PubMed:11751885). Forms a stable heterooligomeric complex with CAV2 that targets to lipid rafts and drives caveolae formation. Mediates the recruitment of CAVIN proteins (CAVIN1/2/3/4) to the caveolae (PubMed:19262564). Interacts directly with G-protein alpha subunits and can functionally regulate their activity (By similarity). Involved in the costimulatory signal essential for T-cell receptor (TCR)-mediated T-cell activation. Its bind

LOCALIZAÇÃO

Golgi apparatus membraneCell membraneMembrane, caveolaMembrane raftGolgi apparatus, trans-Golgi networkCytoplasm

VIAS BIOLÓGICAS (4)
SARS-CoV-2 targets host intracellular signalling and regulatory pathwaysSARS-CoV-1 targets host intracellular signalling and regulatory pathwaysExtra-nuclear estrogen signalingBasigin interactions
MECANISMO DE DOENÇA

Lipodystrophy, congenital generalized, 3

A form of congenital generalized lipodystrophy, a metabolic disorder characterized by a near complete absence of adipose tissue, extreme insulin resistance, hypertriglyceridemia, hepatic steatosis and diabetes mellitus. CGL3 inheritance is autosomal recessive.

OUTRAS DOENÇAS (6)
pulmonary hypertension, primary, 3partial lipodystrophy, congenital cataracts, and neurodegeneration syndromecongenital generalized lipodystrophy type 3heritable pulmonary arterial hypertension
HGNC:1527UniProt:Q03135
ENGEndoglinCandidate gene tested inAltamente restrito
FUNÇÃO

Vascular endothelium glycoprotein that plays an important role in the regulation of angiogenesis (PubMed:21737454, PubMed:23300529). Required for normal structure and integrity of adult vasculature (PubMed:7894484). Regulates the migration of vascular endothelial cells (PubMed:17540773). Required for normal extraembryonic angiogenesis and for embryonic heart development (By similarity). May regulate endothelial cell shape changes in response to blood flow, which drive vascular remodeling and est

LOCALIZAÇÃO

Cell membrane

VIAS BIOLÓGICAS (1)
N-glycan trimming in the ER and Calnexin/Calreticulin cycle
MECANISMO DE DOENÇA

Telangiectasia, hereditary hemorrhagic, 1

A multisystemic vascular dysplasia leading to dilation of permanent blood vessels and arteriovenous malformations of skin, mucosa, and viscera. The disease is characterized by recurrent epistaxis and gastro-intestinal hemorrhage. Visceral involvement includes arteriovenous malformations of the lung, liver, and brain.

EXPRESSÃO TECIDUAL(Ubíquo)
Aorta
476.7 TPM
Pulmão
392.6 TPM
Ovário
380.3 TPM
Artéria coronária
376.9 TPM
Coração - Átrio
355.2 TPM
OUTRAS DOENÇAS (5)
telangiectasia, hereditary hemorrhagic, type 1generalized juvenile polyposis/juvenile polyposis colihereditary hemorrhagic telangiectasiaintracranial berry aneurysm
HGNC:3349UniProt:P17813
TBX4T-box transcription factor TBX4Candidate gene tested inAltamente restrito
FUNÇÃO

Transcriptional regulator that has an essential role in the organogenesis of lungs, pelvis, and hindlimbs

LOCALIZAÇÃO

Nucleus

MECANISMO DE DOENÇA

Ischiocoxopodopatellar syndrome with or without pulmonary arterial hypertension

An autosomal dominant bone disease characterized by patellar aplasia or hypoplasia and by anomalies of the pelvis and feet, including disrupted ossification of the ischia and inferior pubic rami.

EXPRESSÃO TECIDUAL(Tecido-específico)
Pulmão
54.1 TPM
Bladder
6.1 TPM
Próstata
5.3 TPM
Artéria tibial
4.7 TPM
Testículo
2.7 TPM
OUTRAS DOENÇAS (6)
coxopodopatellar syndromeautosomal recessive ameliafamilial clubfoot due to 17q23.1q23.2 microduplicationchromosome 17q23.1-q23.2 deletion syndrome
HGNC:11603UniProt:P57082
SOX17Transcription factor SOX-17Candidate gene tested inAltamente restrito
FUNÇÃO

Acts as a transcription regulator that binds target promoter DNA (PubMed:33952808). Binds to the sequences 5'-AACAAT-'3 or 5'-AACAAAG-3'. Modulates transcriptional regulation via WNT3A. Inhibits Wnt signaling. Promotes degradation of activated CTNNB1. Plays a key role in the regulation of embryonic development. Required for normal development of the definitive gut endoderm. Required for normal looping of the embryonic heart tube. Plays an important role in embryonic and postnatal vascular develo

LOCALIZAÇÃO

Nucleus

VIAS BIOLÓGICAS (4)
Deactivation of the beta-catenin transactivating complexFormation of definitive endodermDevelopmental Lineage of Multipotent Pancreatic Progenitor CellsSpecification of primordial germ cells
MECANISMO DE DOENÇA

Vesicoureteral reflux 3

A disease belonging to the group of congenital anomalies of the kidney and urinary tract. It is characterized by the reflux of urine from the bladder into the ureters and sometimes into the kidneys, and is a risk factor for urinary tract infections. Primary disease results from a developmental defect of the ureterovesical junction. In combination with intrarenal reflux, the resulting inflammatory reaction may result in renal injury or scarring, also called reflux nephropathy. Extensive renal scarring impairs renal function and may predispose patients to hypertension, proteinuria, renal insufficiency and end-stage renal disease.

EXPRESSÃO TECIDUAL(Ubíquo)
Adipose Visceral Omentum
69.4 TPM
Nervo tibial
51.3 TPM
Mama
47.3 TPM
Fallopian Tube
45.6 TPM
Tecido adiposo
44.5 TPM
OUTRAS DOENÇAS (3)
vesicoureteral reflux 3heritable pulmonary arterial hypertensionfamilial vesicoureteral reflux
HGNC:18122UniProt:Q9H6I2
EIF2AK4eIF-2-alpha kinase GCN2Candidate gene tested inTolerante
FUNÇÃO

Metabolic-stress sensing protein kinase that phosphorylates the alpha subunit of eukaryotic translation initiation factor 2 (EIF2S1/eIF-2-alpha) in response to low amino acid availability (PubMed:25329545, PubMed:32610081). Plays a role as an activator of the integrated stress response (ISR) required for adaptation to amino acid starvation (By similarity). EIF2S1/eIF-2-alpha phosphorylation in response to stress converts EIF2S1/eIF-2-alpha into a global protein synthesis inhibitor, leading to a

LOCALIZAÇÃO

Cytoplasm

VIAS BIOLÓGICAS (1)
Response of EIF2AK4 (GCN2) to amino acid deficiency
MECANISMO DE DOENÇA

Pulmonary venoocclusive disease 2, autosomal recessive

A disease characterized by widespread fibrous obstruction and intimal thickening of septal veins and preseptal venules, a low diffusing capacity for carbon monoxide, occult alveolar hemorrhage, and nodular ground-glass opacities, septal lines and lymph node enlargement showed by high-resolution computed tomography of the chest. It is frequently associated with pulmonary capillary dilatation and proliferation, and is a rare and devastating cause of pulmonary hypertension.

EXPRESSÃO TECIDUAL(Ubíquo)
Fibroblastos
48.7 TPM
Linfócitos
23.7 TPM
Pituitária
21.8 TPM
Nervo tibial
17.1 TPM
Útero
16.6 TPM
OUTRAS DOENÇAS (3)
pulmonary venoocclusive disease 2heritable pulmonary arterial hypertensionpulmonary venoocclusive disease
HGNC:19687UniProt:Q9P2K8
ACVRL1Activin receptor type-1-likeCandidate gene tested inRestrito
FUNÇÃO

Type I receptor for TGF-beta family ligands BMP9/GDF2 and BMP10 and important regulator of normal blood vessel development. On ligand binding, forms a receptor complex consisting of two type II and two type I transmembrane serine/threonine kinases. Type II receptors phosphorylate and activate type I receptors which autophosphorylate, then bind and activate SMAD transcriptional regulators. May bind activin as well

LOCALIZAÇÃO

Cell membrane

VIAS BIOLÓGICAS (1)
Signaling by BMP
MECANISMO DE DOENÇA

Telangiectasia, hereditary hemorrhagic, 2

A multisystemic vascular dysplasia leading to dilation of permanent blood vessels and arteriovenous malformations of skin, mucosa, and viscera. The disease is characterized by recurrent epistaxis and gastro-intestinal hemorrhage. Visceral involvement includes arteriovenous malformations of the lung, liver, and brain.

VIAS REACTOME (1)
OUTRAS DOENÇAS (3)
telangiectasia, hereditary hemorrhagic, type 2hereditary hemorrhagic telangiectasiaheritable pulmonary arterial hypertension
HGNC:175UniProt:P37023
GDF2Growth/differentiation factor 2Candidate gene tested inTolerante
FUNÇÃO

Potent circulating inhibitor of angiogenesis. Signals through the type I activin receptor ACVRL1 but not other Alks. Signaling through SMAD1 in endothelial cells requires TGF-beta coreceptor endoglin/ENG

LOCALIZAÇÃO

Secreted

VIAS BIOLÓGICAS (1)
Signaling by BMP
MECANISMO DE DOENÇA

Telangiectasia, hereditary hemorrhagic, 5

A multisystemic vascular dysplasia leading to dilation of permanent blood vessels and arteriovenous malformations of skin, mucosa, and viscera. The disease is characterized by recurrent epistaxis and gastro-intestinal hemorrhage. Visceral involvement includes arteriovenous malformations of the lung, liver, and brain.

VIAS REACTOME (1)
EXPRESSÃO TECIDUAL(Tecido-específico)
Fígado
8.3 TPM
Testículo
0.1 TPM
Coração - Átrio
0.1 TPM
Brain Nucleus accumbens basal ganglia
0.0 TPM
Hipotálamo
0.0 TPM
OUTRAS DOENÇAS (3)
telangiectasia, hereditary hemorrhagic, type 5hereditary hemorrhagic telangiectasiaheritable pulmonary arterial hypertension
HGNC:4217UniProt:Q9UK05
ATP13A3Polyamine-transporting ATPase 13A3Disease-causing germline mutation(s) inAltamente restrito
FUNÇÃO

ATP-driven pump involved in endocytosis-dependent polyamine transport. Uses ATP as an energy source to transfer polyamine precursor putrescine from the endosomal compartment to the cytosol

LOCALIZAÇÃO

Recycling endosome membraneEarly endosome membraneLate endosome membrane

MECANISMO DE DOENÇA

Pulmonary hypertension, primary, 5

A form of primary pulmonary hypertension, a disease defined by plexiform lesions of proliferating endothelial cells in pulmonary arterioles. The lesions lead to elevated pulmonary arterial pression, right ventricular failure, and death. Primary pulmonary hypertension exhibits incomplete penetrance, sex bias and variable age of onset, both within and between families. PPH5 is an autosomal recessive form characterized by the onset in infancy. Death in early childhood is common.

INTERAÇÕES PROTEICAS (2)
OUTRAS DOENÇAS (2)
pulmonary hypertension, primary, 5heritable pulmonary arterial hypertension
HGNC:24113UniProt:Q9H7F0
KCNK3Potassium channel subfamily K member 3Disease-causing germline mutation(s) inRestrito
FUNÇÃO

K(+) channel that conducts voltage-dependent outward rectifying currents upon membrane depolarization. Voltage sensing is coupled to K(+) electrochemical gradient in an 'ion flux gating' mode where outward but not inward ion flow opens the gate (PubMed:23169818, PubMed:26919430, PubMed:32499642, PubMed:36195757, PubMed:9312005). Changes ion selectivity and becomes permeable to Na(+) ions in response to extracellular acidification. Protonation of the pH sensor His-98 stabilizes C-type inactivatio

LOCALIZAÇÃO

Cell membrane

VIAS BIOLÓGICAS (2)
Phase 4 - resting membrane potentialTWIK-releated acid-sensitive K+ channel (TASK)
MECANISMO DE DOENÇA

Pulmonary hypertension, primary, 4

A rare disorder characterized by plexiform lesions of proliferating endothelial cells in pulmonary arterioles. The lesions lead to elevated pulmonary arterial pression, right ventricular failure, and death. The disease can occur from infancy throughout life and it has a mean age at onset of 36 years. Penetrance is reduced. Although familial pulmonary hypertension is rare, cases secondary to known etiologies are more common and include those associated with the appetite-suppressant drugs.

EXPRESSÃO TECIDUAL(Ubíquo)
Glândula adrenal
248.3 TPM
Pulmão
47.2 TPM
Cérebro - Hemisfério cerebelar
21.2 TPM
Cerebelo
20.3 TPM
Artéria coronária
17.0 TPM
OUTRAS DOENÇAS (2)
pulmonary hypertension, primary, 4heritable pulmonary arterial hypertension
HGNC:6278UniProt:O14649
BMPR2Bone morphogenetic protein receptor type-2Disease-causing germline mutation(s) inAltamente restrito
FUNÇÃO

On ligand binding, forms a receptor complex consisting of two type II and two type I transmembrane serine/threonine kinases. Type II receptors phosphorylate and activate type I receptors which autophosphorylate, then bind and activate SMAD transcriptional regulators. Can also mediate signaling through the activation of the p38MAPK cascade (PubMed:12045205). Binds to BMP7, BMP2 and, less efficiently, BMP4. Binding is weak but enhanced by the presence of type I receptors for BMPs. Mediates inducti

LOCALIZAÇÃO

Cell membrane

VIAS BIOLÓGICAS (1)
Signaling by BMP
MECANISMO DE DOENÇA

Pulmonary hypertension, primary, 1

A rare disorder characterized by plexiform lesions of proliferating endothelial cells in pulmonary arterioles. The lesions lead to elevated pulmonary arterial pression, right ventricular failure, and death. The disease can occur from infancy throughout life and it has a mean age at onset of 36 years. Penetrance is reduced. Although familial pulmonary hypertension is rare, cases secondary to known etiologies are more common and include those associated with the appetite-suppressant drugs.

VIAS REACTOME (1)
OUTRAS DOENÇAS (6)
pulmonary hypertension, primary, 1pulmonary venoocclusive disease 1pulmonary arterial hypertensionpulmonary venoocclusive disease
HGNC:1078UniProt:Q13873
CAPNS1Calpain small subunit 1Disease-causing germline mutation(s) inTolerante
FUNÇÃO

Regulatory subunit of the calcium-regulated non-lysosomal thiol-protease which catalyzes limited proteolysis of substrates involved in cytoskeletal remodeling and signal transduction. Essential for embryonic development (By similarity)

LOCALIZAÇÃO

CytoplasmCell membrane

VIAS BIOLÓGICAS (5)
Turbulent (oscillatory, disturbed) flow shear stress activates signaling by PIEZO1 and integrins in endothelial cellsHigh laminar flow shear stress activates signaling by PIEZO1 and PECAM1:CDH5:KDR in endothelial cellsDeregulated CDK5 triggers multiple neurodegenerative pathways in Alzheimer's disease modelsDegradation of the extracellular matrixFormation of the cornified envelope
MECANISMO DE DOENÇA

Pulmonary hypertension, primary, 6

A form of primary pulmonary hypertension, a disease defined by plexiform lesions of proliferating endothelial cells in pulmonary arterioles. The lesions lead to elevated pulmonary arterial pression, right ventricular failure, and death. Primary pulmonary hypertension exhibits incomplete penetrance, sex bias and variable age of onset, both within and between families. PPH6 is an autosomal recessive form.

OUTRAS DOENÇAS (1)
pulmonary hypertension, primary, 6
HGNC:HGNC:1481UniProt:P04632
SMAD9SMAD family member 9Disease-causing germline mutation(s) inTolerante
FUNÇÃO

Transcriptional modulator activated by BMP (bone morphogenetic proteins) type 1 receptor kinase. SMAD9 is a receptor-regulated SMAD (R-SMAD)

LOCALIZAÇÃO

CytoplasmNucleus

VIAS BIOLÓGICAS (1)
Signaling by BMP
MECANISMO DE DOENÇA

Pulmonary hypertension, primary, 2

A rare disorder characterized by plexiform lesions of proliferating endothelial cells in pulmonary arterioles. The lesions lead to elevated pulmonary arterial pression, right ventricular failure, and death. The disease can occur from infancy throughout life and it has a mean age at onset of 36 years. Penetrance is reduced. Although familial pulmonary hypertension is rare, cases secondary to known etiologies are more common and include those associated with the appetite-suppressant drugs.

VIAS REACTOME (1)
EXPRESSÃO TECIDUAL(Ubíquo)
Tireoide
50.1 TPM
Artéria tibial
41.0 TPM
Aorta
30.6 TPM
Esôfago - Muscular
27.2 TPM
Brain Spinal cord cervical c-1
19.7 TPM
OUTRAS DOENÇAS (2)
pulmonary hypertension, primary, 2heritable pulmonary arterial hypertension
HGNC:6774UniProt:O15198

Medicamentos aprovados (FDA)

3 medicamentos encontrados nos registros da FDA americana.

💊 Sildenafil (SILDENAFIL)
💊 Sildenafil (SILDENAFIL CITRATE)
💊 Tadalafil (TADALAFIL)
Ver no DailyMed/FDA

Variantes genéticas (ClinVar)

982 variantes patogênicas registradas no ClinVar.

🧬 CAV1: NC_000007.13:g.(?_116165117)_(117307162_?)del ()
🧬 CAV1: NM_001753.5(CAV1):c.436del (p.Arg146fs) ()
🧬 CAV1: GRCh38/hg38 7q31.1-31.2(chr7:113604778-117643891) ()
🧬 CAV1: NM_001753.5(CAV1):c.358G>A (p.Ala120Thr) ()
🧬 CAV1: GRCh37/hg19 7q31.1-31.2(chr7:108967155-116850770)x1 ()
Ver todas no ClinVar

Classificação de variantes (ClinVar)

Distribuição de 445 variantes classificadas pelo ClinVar.

200
245
Patogênica (44.9%)
VUS (55.1%)
VARIANTES MAIS SIGNIFICATIVAS
BMPR2: NM_001204.7(BMPR2):c.1259G>T (p.Cys420Phe) [Likely pathogenic]
LOC105378289: GRCh38/hg38 10q11.22-11.23(chr10:45795500-50134000) [Likely pathogenic]
ABCC8: NM_000352.6(ABCC8):c.854G>A (p.Arg285Gln) [Conflicting classifications of pathogenicity]
BMPR2: NM_001204.7(BMPR2):c.2336C>G (p.Ser779Ter) [Likely pathogenic]
EIF2AK4: NM_001013703.4(EIF2AK4):c.1243del (p.Tyr415fs) [Pathogenic]

Vias biológicas (Reactome)

47 vias biológicas associadas aos genes desta condição.

Triglyceride catabolism eNOS activation NOSTRIN mediated eNOS trafficking Thyroxine biosynthesis Basigin interactions Disassembly of the destruction complex and recruitment of AXIN to the membrane VEGFR2 mediated vascular permeability RHOA GTPase cycle Extra-nuclear estrogen signaling RHOB GTPase cycle RHOC GTPase cycle CDC42 GTPase cycle RAC1 GTPase cycle RAC2 GTPase cycle RHOD GTPase cycle RHOQ GTPase cycle RHOH GTPase cycle RHOG GTPase cycle RHOJ GTPase cycle RAC3 GTPase cycle RHOF GTPase cycle FOXO-mediated transcription of cell cycle genes RND3 GTPase cycle RND2 GTPase cycle RND1 GTPase cycle SARS-CoV-1 targets host intracellular signalling and regulatory pathways SARS-CoV-2 targets host intracellular signalling and regulatory pathways Toll Like Receptor 5 (TLR5) Cascade Assembly of the SARS-CoV-2 Replication-Transcription Complex (RTC) SARS-CoV-2 Genome Replication and Transcription Transcription of SARS-CoV-2 sgRNAs Replication of the SARS-CoV-2 genome PI3K/AKT Signaling in Cancer PTEN Loss of Function in Cancer Signaling by BMP Deactivation of the beta-catenin transactivating complex Formation of definitive endoderm Specification of primordial germ cells Developmental Lineage of Multipotent Pancreatic Progenitor Cells Response of EIF2AK4 (GCN2) to amino acid deficiency TWIK-releated acid-sensitive K+ channel (TASK) Phase 4 - resting membrane potential Degradation of the extracellular matrix Formation of the cornified envelope Deregulated CDK5 triggers multiple neurodegenerative pathways in Alzheimer's disease models High laminar flow shear stress activates signaling by PIEZO1 and PECAM1:CDH5:KDR in endothelial cells Turbulent (oscillatory, disturbed) flow shear stress activates signaling by PIEZO1 and integrins in endothelial cells

Diagnóstico

Os sinais que médicos procuram e os exames que confirmam

Carregando...

Tratamento e manejo

Remédios, cuidados de apoio e o que precisa acompanhar

Pipeline de tratamentos
Pipeline regulatório — de medicamentos já aprovados a drogas em pesquisa exploratória.
Aprovado1
3Fase 32
2Fase 28
1Fase 12
·Pré-clínico7
Medicamentos catalogadosEnsaios clínicos· 0 medicamentos · 20 ensaios
Carregando informações de tratamento...

Onde tratar no SUS

Hospitais de referência no Brasil e o protocolo oficial do SUS (PCDT)

🇧🇷 Atendimento SUS — Hipertensão arterial pulmonar

🗺️

Selecione um estado ou use sua localização para ver resultados.

Dados de DATASUS/CNES, SBGM, ABNeuro e Ministério da Saúde. Sempre confirme a disponibilidade diretamente com o estabelecimento.

Pesquisa ativa

Ensaios clínicos abertos e novidades científicas recentes

🟢 Recrutando agora

19 pesquisas recrutando participantes. Converse com seu médico sobre a possibilidade de participar.

NCT07073820 · A Study to Learn About the Study Medicine (Called PF-0786848…Recrutando
PHASE2
NCT07318597 · Phase 2 Study of REGN13335 in Adult Participants With Pulmon…Recrutando
PHASE2
NCT07218029 · A Clinical Study of Sotatercept (MK-7962) in People With Pul…Recrutando
PHASE3
NCT05967299 · Study of Intravenous ZMA001 in Healthy SubjectsRecrutando
PHASE1
NCT05587712 · Study to Evaluate Sotatercept (MK-7962) in Children With Pul…Recrutando
PHASE2
NCT01712620 · Spironolactone for Pulmonary Arterial HypertensionRecrutando
PHASE2
NCT07175038 · A Study of ROC-101 in Patients With Pulmonary Arterial Hyper…Recrutando
PHASE2
NCT01730092 · Natural History Study of Biomarkers in Pulmonary Arterial Hy…Recrutando
NCT05179876 · A Study Providing Treatment Access in Participants With Pulm…Recrutando
PHASE3
NCT07140484 · Sotatercept in Pulmonary Arterial HypertensionRecrutando
PHASE4
NCT04278404 · Pharmacokinetics, Pharmacodynamics, and Safety Profile of Un…Recrutando
NCT03838445 · Reducing Right Ventricular Failure in Pulmonary Arterial Hyp…Recrutando
NA
NCT06549452 · Mobile Health Intervention to Improve Exercise in Pediatric …Recrutando
NA
NCT06554301 · A Study on the Efficacy and Safety of Empagliflozin in the T…Recrutando
PHASE1
NCT07120789 · Validation of a Patient Knowledge Questionnaire for Pulmonar…Recrutando
NA
NCT05584722 · Risk and Resilience in Pulmonary Arterial Hypertension and G…Recrutando
NCT07457762 · AIRDROP: Can we Improve Adherence to Inhaled Treatment for P…Recrutando
NA
NCT06649110 · A Study to Learn About the Treatment LTP001 in Healthy Parti…Recrutando
PHASE1, PHASE2
NCT06846554 · A Trial of "APL-9796'' in Adults With Pulmonary HypertensionRecrutando
PHASE2

Outros ensaios clínicos

834 ensaios clínicos encontrados, 36 ativos.

Distribuição por fase
Ver todos no ClinicalTrials.gov
🧪 Está conduzindo uma pesquisa?
Divulgue para pacientes e familiares que acompanham esta doença.
Divulgar pesquisa →

Publicações mais relevantes

📖Melhor nível de evidência: Revisão
Timeline de publicações
12.293 papers (10 anos)

Mostrando amostra de 200 publicações de um total de 12.293

#1

A Phase 2, Randomized, Clinical Trial of Inhaled Nitric Oxide for Acute Severe Right Heart Failure With Pulmonary Hypertension (PHiNO Study).

Circulation journal : official journal of the Japanese Circulation Society2026 Mar 21

O estudo PHiNO, de Fase 2, demonstrou que o óxido nítrico inalado (iNO) é um tratamento agudo promissor para pacientes com insuficiência cardíaca direita (ICD) grave devido à hipertensão pulmonar. Ele reduziu significativamente a resistência vascular pulmonar (um fator chave na ICD) em apenas 30 minutos, melhorando também marcadores cardíacos importantes ao longo de 7 dias, sem causar eventos adversos graves. Estes resultados sugerem que o iNO pode ser uma opção terapêutica segura e eficaz para essa condição de risco de vida.

🇧🇷 traduzido
#2

When atrioventricular block paves the way to a more severe diagnosis: a case report.

European heart journal. Case reports2026 Mar

Este caso atípico de esclerose sistêmica (ESc) difusa demonstra que um bloqueio atrioventricular (AV) completo pode ser a manifestação inicial, levando à descoberta de hipertensão pulmonar grave e fibrose. É crucial que médicos considerem doenças autoimunes sistêmicas em pacientes com bloqueio AV inexplicado, especialmente com sinais cutâneos, para um diagnóstico precoce. Essa abordagem integrada e multidisciplinar é vital para pacientes, permitindo tratar as múltiplas complicações (cardíacas, pulmonares e gastrointestinais) e estabilizar a condição, melhorando a qualidade de vida.

🇧🇷 traduzido
#3

The emerging role of integrin signaling in pulmonary vascular disease.

American journal of physiology. Lung cellular and molecular physiology2026 Mar 18

A hipertensão arterial pulmonar (HAP) é uma doença grave e incurável, e estudos recentes indicam que as integrinas desempenham um papel promissor em sua patogênese, promovendo a proliferação celular, inflamação e fibrose nos vasos pulmonares. Este artigo de revisão explora a base biológica das integrinas na doença vascular pulmonar e as posiciona como potenciais alvos de tratamento, discutindo caminhos intracelulares e estudos terapêuticos recentes em animais com o objetivo de desenvolver novas terapias.

🇧🇷 traduzido
#4

Endothelial C-type natriuretic peptide/guanylyl cyclase-B signaling prevents pulmonary arterial hypertension.

Nature communications2026 Mar 17

Este estudo revela que a via de sinalização do peptídeo natriurético tipo C (CNP) e GC-B, presente nas células que revestem os vasos sanguíneos (endoteliais), é crucial para prevenir a Hipertensão Arterial Pulmonar (HAP). Em pacientes e modelos da doença, essa via protetora está reduzida. A administração de CNP demonstrou a capacidade de prevenir e tratar a HAP, inclusive com benefícios adicionais quando combinada a terapias existentes. Isso sugere que o CNP possui um potencial terapêutico significativo e promissor para pacientes com HAP.

🇧🇷 traduzido
#5

Iron Deficiency in Pulmonary Hypertension-Prevalence, Impact on Prognosis and Disease Burden in Pulmonary Arterial Hypertension and Pulmonary Hypertension Related to Hypoxia: A Review.

International journal of molecular sciences2026 Mar 02

A hipertensão arterial pulmonar (HAP) é uma condição grave, e embora existam tratamentos avançados, fatores modificáveis também são cruciais para o manejo. A deficiência de ferro (DF) é um déficit nutricional comum que está sendo cada vez mais associado ao prognóstico e à carga da doença na HAP e na HP relacionada à hipóxia. Isso sugere que a DF pode ser um fator importante e potencialmente tratável, influenciando a qualidade de vida e o desfecho dos pacientes, embora mais estudos sejam necessários para definições precisas e manejo ideal.

🇧🇷 traduzido

Publicações recentes

Ver todas no PubMed

📚 EuropePMC10.723 artigos no totalmostrando 197

2026

THBS4 Regulates Pulmonary Hypertension via TGF-β/SMAD2 Signaling.

Hypertension (Dallas, Tex. : 1979)
2026

Reduction in microbiota-derived short-chain fatty acids contributes to the pathogenesis of pulmonary arterial hypertension.

Respiratory research
2026

MnTBAP attenuates pulmonary hypertension-induced right ventricular dysfunction and remodeling by modulating the CaMKIIδ-SERCA2a signaling pathway.

Biochemical pharmacology
2026

Updates in the Treatment of Pediatric Pulmonary Arterial Hypertension.

Cardiology in review
2026

Dilemmas of Self-Management in Patients with Pulmonary Arterial Hypertension: A Descriptive Phenomenological Study.

Patient preference and adherence
2026

Marked clinical and haemodynamic improvement with sotatercept in severe refractory pulmonary arterial hypertension associated with corrected complex congenital heart disease.

Respiratory medicine case reports
2026

Multifaceted mechanisms of plant metabolites in pulmonary arterial hypertension: a critical review beyond vasodilation.

Frontiers in pharmacology
2026

A Phase 2, Randomized, Clinical Trial of Inhaled Nitric Oxide for Acute Severe Right Heart Failure With Pulmonary Hypertension (PHiNO Study).

Circulation journal : official journal of the Japanese Circulation Society
2026

Clinical and hemodynamic evaluation of schistosomiasis-associated pulmonary arterial hypertension from Egyptian pulmonary hypertension centers: epidemiology, risk factors, and survival determinants.

Scientific reports
2026

Sotatercept improves right ventricular function but is associated with new or worsening pericardial effusions: a CMR study in intermediate-high risk PAH.

Journal of cardiovascular magnetic resonance : official journal of the Society for Cardiovascular Magnetic Resonance
2026

Preoperative pulmonary hemodynamics and clinical decision making to determine operability and risk of long-term pulmonary hypertension in infants with open shunt under 1 year.

International journal of cardiology
2026

Cardiac MRI differentiates classical idiopathic pulmonary arterial hypertension from lung phenotype and group 3 pulmonary hypertension.

Respiratory medicine and research
2026

Loss of productivity among commercially insured patients with pulmonary arterial hypertension in the United States.

Journal of medical economics
2026

Nuclear export by COPS5/CSN5/JAB1 mediates vascular smooth muscle cell dedifferentiation in neointimal hyperplasia.

Cardiovascular research
2026

Sphingosine-1-phosphate induces pulmonary artery smooth muscle cell proliferation, migration and pulmonary arterial remodeling by modulating sonic hedgehog signaling effector FoxM1.

Chinese medical journal
2026

[Sleep disorders dynamics in patients with chronic thromboembolic pulmonary hypertension after surgical treatment].

Terapevticheskii arkhiv
2026

Neonatal pulmonary vascular remodeling induced by increased blood flow is associated with an antiviral-like immune signature.

Frontiers in immunology
2026

When atrioventricular block paves the way to a more severe diagnosis: a case report.

European heart journal. Case reports
2026

Insight of traditional Chinese medicine in treating pulmonary hypertension: Achievements from 2021 to 2025.

Journal of ethnopharmacology
2026

S- nitrosylation of Annexin A2 at Cys133 ameliorates pulmonary arterial hypertension by inhibiting the WNT/β-catenin pathway.

Respiratory research
2026

Harnessing metabolomics and proteomics in a clinical trial for pulmonary arterial hypertension: insights from post-hoc analysis of the REHAB-PH trial.

EBioMedicine
2026

The emerging role of integrin signaling in pulmonary vascular disease.

American journal of physiology. Lung cellular and molecular physiology
2026

Hydroxychloroquine withdrawal triggers pregnancy-associated pulmonary arterial hypertension in systemic lupus erythematosus: a case report and exploration of the Complement-EndMT axis.

Frontiers in pharmacology
2026

Myocardial fibrosis and glycolysis: a bibliometric study and visualization analysis (2000-2024).

Journal of translational medicine
2026

Endothelial C-type natriuretic peptide/guanylyl cyclase-B signaling prevents pulmonary arterial hypertension.

Nature communications
2026

Provider networks for pulmonary hypertension in Massachusetts: implications for improving referrals to expert care.

Annals of the American Thoracic Society
2026

Critical Care Management of the Patient with Pulmonary Hypertension.

Journal of intensive care medicine
2026

Targeting autoimmunity: Phosphodiesterase inhibitors as immunomodulators-a review of current insights and future direction.

Autoimmunity reviews
2026

Molecular dynamics simulations refine the pathogenicity of ACVRL1 kinase domain variants by quantifying impacts on ATP binding in pulmonary arterial hypertension.

Journal of structural biology
2026

Enhanced Mitochondrial Mrs2-Mg2+ Signaling Drives Mitochondrial Dysfunction in Pulmonary Arterial Hypertension Rats.

Hypertension (Dallas, Tex. : 1979)
2026

Exercise testing in chronic thromboembolic pulmonary hypertension and chronic thromboembolic pulmonary disease without pulmonary hypertension: a comprehensive systematic review and meta-analysis.

European journal of internal medicine
2026

Right atrial phasic strain in risk stratification of patients with Pulmonary Arterial Hypertension.

Journal of cardiovascular magnetic resonance : official journal of the Society for Cardiovascular Magnetic Resonance
2026

Identification of Key Genes and Pathways Associated With Gender Differences in Pulmonary Arterial Hypertension Based on Bioinformatic Approaches.

BioMed research international
2026

Iron Deficiency in Pulmonary Hypertension-Prevalence, Impact on Prognosis and Disease Burden in Pulmonary Arterial Hypertension and Pulmonary Hypertension Related to Hypoxia: A Review.

International journal of molecular sciences
2026

Stress Echocardiography in the Diagnosis and Evaluation of Pulmonary Hypertension: Practical Recommendations, Haemodynamic Phenotyping, and Application in Adults and Children.

Diagnostics (Basel, Switzerland)
2026

The Role of the Apelin Receptor in the Pathophysiology of Pulmonary Arterial Hypertension.

Cells
2026

Validation Analysis of the Polish-Translated Version of EmPHasis-10 Health-Related Quality of Life Questionnaire in Patients with Pulmonary Arterial Hypertension.

Journal of clinical medicine
2026

Clinically Actionable Explainable AI in Pulmonary Arterial Hypertension: Endpoints, Calibration, and External Validation. Reply to Pagnoni et al. Toward Clinically Actionable Explainable AI in Pulmonary Arterial Hypertension: Endpoints, Calibration, and External Validation. Comment on "Ledziński et al. Personalized Medicine in Pulmonary Arterial Hypertension: Utilizing Artificial Intelligence for Death Prevention. J. Clin. Med. 2025, 14, 8325".

Journal of clinical medicine
2026

Toward Clinically Actionable Explainable AI in Pulmonary Arterial Hypertension: Endpoints, Calibration, and External Validation. Comment on Ledziński et al. Personalized Medicine in Pulmonary Arterial Hypertension: Utilizing Artificial Intelligence for Death Prevention. J. Clin. Med. 2025, 14, 8325.

Journal of clinical medicine
2026

Nailfold capillaroscopy and organ involvement in systemic sclerosis: a systematic review.

Best practice &amp; research. Clinical rheumatology
2026

Long-Term Treatment with Single-Tablet Combination of Macitentan and Tadalafil in Pulmonary Arterial Hypertension: Results from A DUE and Its Open-Label Period.

Advances in therapy
2026

Protocol for an open-label, randomised, controlled trial to evaluate the efficacy and safety of sotatercept add-on therapy compared with pulmonary vasodilator-based standard of care for pulmonary vasodilator-resistant pulmonary arterial hypertension associated with unrepaired congenital shunts (atrial septal defect, ventricular septal defect or patent ductus arteriosus), including Eisenmenger syndrome: the SuMILE trial.

BMJ open
2026

How I do it: How to care for the patient with methamphetamine-associated PAH.

Chest
2026

Long-term efficacy of the treat-to-close strategy for patients with atrial septal defect-pulmonary artery hypertension and characteristics of indicated populations.

Clinics (Sao Paulo, Brazil)
2026

Targeting the Hippo pathway in pulmonary arterial hypertension: emerging pharmacological strategies.

Journal of hypertension
2026

Sotatercept in Patients With Eisenmenger Syndrome.

Pulmonary circulation
2026

Resting Oxygen Consumption Estimates in Scleroderma Can Lead to Underestimation of Cardiac Output.

Pulmonary circulation
2026

Time to Therapy Activation and Initial Combination Therapy (TITANIC) for Patients With Pulmonary Arterial Hypertension.

Pulmonary circulation
2025

[Mechanisms of Qibai Pingfei Capsules in inhibiting pyroptosis of pulmonaryartery adventitial fibroblasts via regulating NLRP3/Caspase-1/ GSDMD pathway to intervene in COPD complicated by pulmonary arterial hypertension].

Zhongguo Zhong yao za zhi = Zhongguo zhongyao zazhi = China journal of Chinese materia medica
2026

Diamond in the Rough or Just the Flavor of the Week?: Transforming Growth Factor 15 as a Biomarker in Pulmonary Arterial Hypertension.

Chest
2026

Pulmonary hypertension associated with nonparenchymal restrictive lung diseases.

European respiratory review : an official journal of the European Respiratory Society
2026

Pulmonary Hypertension Associated With Left Heart Disease: Challenges, Emerging Strategies, and Future Directions.

Journal of the American College of Cardiology
2026

Case Report: Rethinking pulmonary arterial hypertension: immune and metabolic adaptations in a 34-year case of insidious progression.

Frontiers in cardiovascular medicine
2026

Smoking exposure on diagnosis and survival of pulmonary arterial hypertension and chronic thromboembolic pulmonary hypertension: Data from REHAP registry.

Pulmonology
2026

Sotatercept for Decompensated Pulmonary Arterial Hypertension Requiring VA ECMO: First Canadian ICU Experience.

Pulmonary circulation
2026

Industry Payments and Prescribing Patterns of Pulmonary Hypertension Therapies in the United States.

Pulmonary circulation
2026

Ferroptosis of smooth muscle cells in vascular diseases: from basic principles to clinical translation.

Cell death discovery
2026

The Minimal Important Difference in N-Terminal Pro-Brain Natriuretic Peptide in Pulmonary Hypertension.

Chest
2026

Risk stratification for adult patients with pulmonary arterial hypertension associated with congenital heart disease. A scientific statement of the ESC Working Group on Pulmonary Circulation & Right Ventricular Function, the ESC Working Group on Adult Congenital Heart Disease, and the Association of Cardiovascular Nursing & Allied Professions of the ESC.

European journal of heart failure
2026

Pulmonary Artery Denervation for Refractory Sjögren's Syndrome-Associated Pulmonary Arterial Hypertension: A Case Report of Combined Hemodynamic and Renal Recovery.

Catheterization and cardiovascular interventions : official journal of the Society for Cardiac Angiography &amp; Interventions
2026

Alternative Polyadenylation Signatures Distinguish Maladaptive Right Ventricular Remodeling in Pulmonary Hypertension: Implications for RNA-Based Diagnostics and Therapeutics.

British journal of biomedical science
2026

Case Report: A pediatric case of chronic active Epstein-Barr virus infection complicated by pulmonary arterial hypertension.

Frontiers in cardiovascular medicine
2026

A Critical Contribution of Cardiac Myofibroblasts in Right Ventricular Failure and the Role of UCP2 SNPs in the Predisposition to RV Decompensation in Pulmonary Arterial Hypertension.

Circulation
2026

Rectus sheath block a retrospective review of a novel adjunct for treatment of the injection site pain associated with treprostinil subcutaneous infusion in pulmonary hypertension case series.

Pain management
2026

Macitentan vs Standard of Care in Pediatric Pulmonary Arterial Hypertension (TOMORROW): A Randomized Clinical Trial.

The Journal of pediatrics
2026

Therapeutic effects of fingolimod through sphingosine-1-phosphate signaling in pulmonary arterial hypertension.

Journal of pharmacological sciences
2026

BMPR2 Splice-Site Variant in a Patient With Pulmonary Arteriovenous Malformation and Delayed-Onset Pulmonary Arterial Hypertension: A Case Report and Mechanistic Phenocopy Hypothesis.

American journal of medical genetics. Part A
2026

Interpretive considerations on real-world use of selexipag and parenteral prostacyclin in pulmonary arterial hypertension.

Journal of cardiology
2026

Methamphetamine-associated PAH on the rise in the US: geographic trends & disparities in patient demographics and treatment strategies.

The Journal of heart and lung transplantation : the official publication of the International Society for Heart Transplantation
2026

The critical role of HIBCH in pulmonary arterial hypertension.

Toxicology and applied pharmacology
2026

Paradigm shift: from pulmonary vasodilation to cardiopulmonary dual-track therapy-a comprehensive review of pathophysiology and advances in pulmonary hypertension-associated right heart failure.

Respiratory research
2026

LGALS3BP promotes M1 polarization of macrophages and interacts with LGALS3, damaging endothelial function and exacerbating pulmonary arterial hypertension in systemic lupus erythematosus.

Pathology, research and practice
2026

PAH-former: Transfer learning for efficient discovery of pulmonary arterial hypertension-associated genes.

PloS one
2026

Emergency cesarean section in pregnant women with severe pulmonary hypertension: the potential role of extracorporeal life support.

Ulusal travma ve acil cerrahi dergisi = Turkish journal of trauma &amp; emergency surgery : TJTES
2026

Loss of endothelin-2 in pulmonary neuroendocrine cells promotes the development of hypoxia-induced pulmonary hypertension.

Clinical science (London, England : 1979)
2026

A circulating MicroRNA signature for the diagnosis of pulmonary arterial hypertension and functional characterization of candidate miR-3168.

Scientific reports
2026

The clinical phenotype of anti-Th/To+ patients in systemic sclerosis: a case-control study within the European Scleroderma Trials and Research cohort.

Therapeutic advances in musculoskeletal disease
2026

Ferroptosis inhibitors: latest advances and therapeutic potential for pulmonary arterial hypertension.

Drug discovery today
2026

Pulmonary arterial flow alterations in systemic lupus erythematosus on 4D flow CMR: a case-control study.

European radiology experimental
2026

Treatment Paradigm Shifts in Pulmonary Arterial Hypertension: Evidence From Asia on Vasodilators to Antiremodeling Therapies.

JACC. Asia
2026

Real-world use of theophylline in critically ill patients with sinus pauses: a case series.

Frontiers in cardiovascular medicine
2026

Unilateral Pulmonary Artery Agenesis in an Adult: A Case Report and Review of Literature.

Case reports in radiology
2026

Identification of Novel Drug Targets for Pulmonary Arterial Hypertension through Integrated Plasma Proteomics.

Journal of proteome research
2026

Impact of Pulmonary Veno-Occlusive Disease on Posttransplant Survival in Pulmonary Hypertension.

Clinical transplantation
2026

Reduced gastrointestinal iron uptake in pulmonary arterial hypertension: a prospective cross-sectional study.

Respiratory research
2026

The impact of age on six-minute walk distance, functional class, and right ventricular function in pulmonary arterial hypertension.

Respiratory medicine
2026

The Pathophysiology, Mechanism, Diagnosis, and Management of Pulmonary Arterial Hypertension: A Comprehensive Literature Review.

US cardiology
2026

Real-world Persistence on Selexipag for Pulmonary Arterial Hypertension in Canada.

CJC open
2026

Hepatocyte growth factor may contribute to male protection against pulmonary arterial hypertension.

Biology of sex differences
2026

2025 expert consensus on the use of parenteral prostanoids in incident and prevalent PAH patients: The Italian perspective.

Vascular pharmacology
2026

Evaluation of non-invasive techniques for the diagnosis of pulmonary complications in systemic sclerosis and scleroderma-like overlap syndromes: role of lung ultrasound.

Journal of autoimmunity
2026

Impact of ionic imbalances on rat cardiomyocyte function in pulmonary arterial hypertension: insights from energy dispersive X-ray spectroscopy and scanning electron microscopy analysis.

European journal of applied physiology
2026

Feasibility and safety of right heart catheterization via median cubital vein in patients with pulmonary hypertension.

BMC cardiovascular disorders
2026

Circulating fatty acid profiles and risk of pulmonary arterial hypertension: Evidence from a large prospective cohort study.

Medicine
2026

Recurrent Paracentral Acute Middle Maculopathy Secondary to Pulmonary Arterial Hypertension: A Case Report.

Retinal cases &amp; brief reports
2026

New phenotype and outcomes in connective tissue disease-associated pulmonary arterial hypertension: relevance of age-related comorbidities.

Rheumatology (Oxford, England)
2025

Trends and cross-country disparity in the burden of pulmonary arterial hypertension among women of childbearing age from 1990 to 2021.

Frontiers in global women's health
2026

A Case of Antibody-Mediated Recurrent Hypoglycemia in a Patient With Mixed Connective Tissue Disease.

Cureus
2026

Co-Spray-Dried Macitentan-Tadalafil with Leucine Microparticles for Inhalable Delivery in Pulmonary Arterial Hypertension.

Pharmaceutics
2026

Mitochondrial Transplantation from Bone Marrow Mesenchymal Stromal Cells Combined with Sildenafil Attenuated Vascular Remodeling and Improved Right Ventricular Dysfunction in Experimental Pulmonary Arterial Hypertension.

International journal of molecular sciences
2026

Dysregulated Klotho and FGF23 signaling aggravates vascular remodeling in age-related pulmonary hypertension.

Cardiovascular research
2026

A blood biomarker to specifically identify idiopathic pulmonary arterial hypertension.

Nature cardiovascular research
2026

Corrigendum to "Real-world observational study on pulmonary arterial hypertension: Italian cohort treated with macitentan and/or selexipag as a part of a combination treatment (INSPECTIO)" [Vascular Pharmacology 162 (2026) 107585].

Vascular pharmacology
2026

Adventitial Fibrosis and Fibroblast Mechanosensitivity Are Shaped by Sex and Hormonal Status in Pulmonary Arterial Hypertension.

Cells
2026

Pulmonary Arterial Hypertension: Reconfiguring the Vascular Landscape to Reverse Remodeling.

Cells
2026

The prevalence and long-term response to calcium channel blockers in patients with pulmonary arterial hypertension and positive vasoreactivity test - results of multicenter national registry (BNP-PL).

Orphanet journal of rare diseases
2026

Pharmacokinetics, Safety Profile, and Tolerability of MN-08 Tablets after Single and Multiple Ascending Doses in Healthy Chinese Volunteers.

Clinical drug investigation
2026

Risk Averse: Assessing Risk as a Surrogate Measure in Pulmonary Arterial Hypertension.

American journal of respiratory and critical care medicine
2026

Study of Risk Assessment Scores as Surrogate Endpoints in Pulmonary Arterial Hypertension Trials.

American journal of respiratory and critical care medicine
2026

Potts shunt in Pulmonary Arterial Hypertension: Timing and risk assessment.

American journal of respiratory and critical care medicine
2026

Phase 2b trial of inhaled imatinib for treatment of pulmonary arterial hypertension.

American journal of respiratory and critical care medicine
2026

Respiratory complications of systemic autoimmune diseases: the emerging and important role of palliative care.

Current opinion in supportive and palliative care
2026

Neutrophil-mediated delivery of curcumin-loaded manganese-doped zeolitic imidazolate framework-8 nanozymes for pulmonary arterial hypertension.

Journal of nanobiotechnology
2026

Previous resistance exercise training mitigates progression of right ventricle dysfunction and remodeling in male rats with pulmonary arterial hypertension.

Physiological reports
2026

Sotatercept for the treatment of portopulmonary hypertension: a case report.

Communications medicine
2026

Sotatercept Versus Selexipag in Severe Pulmonary Arterial Hypertension: An Indirect Comparison of Efficacy Based on an Artificial-Intelligence Method That Reconstructed Patient-Level Data From Three Randomized Trials.

Cureus
2026

Pulmonary Venous Vasculopathy in Connective Tissue Disease-Associated Pulmonary Arterial Hypertension With Reduced Diffusion Capacity for Carbon Monoxide.

Pulmonary circulation
2026

Plasma GDF-15 and PSP-D Predict the Development of Pulmonary Arterial Hypertension in Systemic Sclerosis.

Pulmonary circulation
2026

Alterations in gut microbiota and plasma metabolites in pulmonary arterial hypertension secondary to congenital left-to-right shunt heart disease: potential mechanisms and biomarkers.

Frontiers in genetics
2026

Transoral videolaryngoscopic surgery for hypopharyngeal anaplastic metastasis from papillary thyroid carcinoma.

JCEM case reports
2026

Pulmonary Arterial Hypertension and Cancer: Unveiling Parallels in Epidemiology, Clinical Pathways, and Therapeutic Strategies.

Journal of market access &amp; health policy
2026

Individualised interventional strategies and clinical outcomes in paediatric patients with pulmonary arterial hypertension.

Cardiology in the young
2026

Bioinformatics-based identification and experimental validation of biomarkers in pulmonary arterial hypertension.

European journal of medical research
2026

The role of pericytes in homeostasis and cardiovascular disease: A comprehensive review.

Journal of advanced research
2026

A Rare Case of Reversible Pulmonary Hypertension Phenotype in a Child with Scurvy: Aetiologies Insights.

Reports (MDPI)
2026

Validity and reliability testing of the Thai version of the emPHasis-10 questionnaire for patients with pulmonary arterial hypertension.

Journal of patient-reported outcomes
2026

Pulmonary hypertension associated with hereditary hemorrhagic telangiectasia: from genetics to clinical management.

The European respiratory journal
2026

Value of right heart haemodynamics for risk stratification of patients with pulmonary arterial hypertension at follow-up.

ESC heart failure
2026

Agreement of thermodilution and direct Fick methods for cardiac output across varying haemodynamic conditions.

ESC heart failure
2026

Evaluation of LCN2 and miR-8078 as diagnostic biomarkers for congenital heart disease-associated pulmonary arterial hypertension.

ESC heart failure
2026

Current State of RV Multimodality Imaging in Pediatric Pulmonary Hypertension: Current Evidence, Knowledge Gaps, and Future Research Directions.

Circulation. Cardiovascular imaging
2026

Performance of Guideline-Recommended Approaches to Echocardiographic Investigation for Pulmonary Hypertension: Analysis of the CIPHER Study.

Pulmonary circulation
2026

Divergent Paths: A Survey of Cardiologist and Obstetrician Decision-Making in High-Risk Pregnancies with Cardiovascular Disease.

International journal of women's health
2026

Sotatercept for pulmonary arterial hypertension.

European journal of internal medicine
2026

Management of pulmonary arterial hypertension in systemic sclerosis: from classical treatments to new horizons.

European respiratory review : an official journal of the European Respiratory Society
2026

The Sigma-1 receptor agonist PRE084 improves cardiopulmonary function and remodelling in an experimental model of pulmonary arterial hypertension.

Biomedicine &amp; pharmacotherapy = Biomedecine &amp; pharmacotherapie
2026

Bulk and single-cell transcriptomics for identification of potential diagnostic biomarkers associated with pulmonary arterial hypertension and integrated stress response and experimental validation.

Clinical and experimental hypertension (New York, N.Y. : 1993)
2026

Improving risk assessment with right ventricular phenotyping in patients with pulmonary arterial hypertension: minimizing future surprises.

European heart journal
2026

Systemic sclerosis-associated pulmonary arterial hypertension and pulmonary fibrosis: exploring biomarker discriminators with advanced omics in a Caucasian cohort.

Frontiers in immunology
2026

An Under-Recognized Manifestation of Systemic Sclerosis: Macrovascular Peripheral Arterial Disease.

Cureus
2026

Modulation of AKT/GSK-3β signaling by ambrisentan alleviates chronic kidney disease.

Pathology, research and practice
2026

GM-CSF exacerbates pulmonary arterial hypertension via CCL2/CCR2-axis-mediated macrophage NLRP3 inflammasome activation.

International immunopharmacology
2026

GLI1 Promotes Hypoxia Induced Pyroptosis of PASMCs and Aggravates Pulmonary Arterial Hypertension in Rats by Upregulating HDAC1 Expression.

Cardiovascular toxicology
2026

Healthcare Resource Utilization and Medical Costs in Pulmonary Arterial Hypertension Management in Japan: A Retrospective Study Using a Claims Database.

Pulmonary therapy
2026

Association of Immunoglobulin E With Right Ventricular Dysfunction in Pulmonary Arterial Hypertension.

Pulmonary circulation
2025

Shunt configuration's role in shaping hemodynamics of reverse Potts shunt in pediatric pulmonary arterial hypertension.

Frontiers in bioengineering and biotechnology
2026

Phase 1 Study Evaluating the Effects of Single-Dose Frespaciguat, an Inhaled Soluble Guanylate Cyclase Stimulator, Co-administered with Multiple-Dose Sildenafil on Systemic Hemodynamics.

Clinical pharmacology in drug development
2026

Genetic Syndromes and Multimorbidity in Adults with Congenital Heart Disease and Heart Failure: Insights from the PATHFINDER-CHD Registry.

Journal of clinical medicine
2026

Cardiac Magnetic Resonance Findings and Their Association with Clinical Outcomes in Pediatric Pulmonary Arterial Hypertension: An Exploratory Study.

Journal of clinical medicine
2026

Comparative analysis of melatonin and sildenafil in a rat model of pulmonary arterial hypertension: Insights into oxidative stress, inflammation, and mitochondrial biogenesis.

Molecular and cellular endocrinology
2026

First longitudinal spatial transcriptomics analysis in pulmonary arterial hypertension.

The Journal of heart and lung transplantation : the official publication of the International Society for Heart Transplantation
2026

Low positive affect as a predictor of mortality in pulmonary arterial hypertension: A Taiwanese cohort study integrating psychological and clinical risk factors.

Heart &amp; lung : the journal of critical care
2026

Transitioning Prostacyclin Pathway Agents to Oral Selexipag in Patients with Pulmonary Arterial Hypertension: A Systematic Literature Review.

Advances in therapy
2026

Sotatercept Reverses SIN3a Deficiency-Driven PAH by Reprogramming BMPR2/TGF-β-HIF-1α Signaling Pathways.

bioRxiv : the preprint server for biology
2026

A Large Animal Model of Heritable Pulmonary Arterial Hypertension Using Gene-edited BMPR2 Sheep.

bioRxiv : the preprint server for biology
2025

Associations between leisure sedentary behaviors, physical activity, and chronic respiratory diseases: a Mendelian randomization study.

Archives of medical science : AMS
2026

Heart-Lung transplantation: Meeting allocation challenges in France.

JHLT open
2026

Development of a Robust, Rapid and Reliable Tandem Mass Spectrometry Method for the Measurement of Sildenafil, Bosentan and their Major Metabolites.

Indian journal of clinical biochemistry : IJCB
2026

Echocardiographic Assessment After Pulmonary Thromboendarterectomy for Chronic Thromboembolic Pulmonary Hypertension: Which Parameters Reflect Improved Right Ventricular Function?

Pulmonary circulation
2026

Second- and Third-Generation BCR-ABL Tyrosine Kinase Inhibitors and the Risk of Pulmonary Arterial Hypertension: A Prevalent New-User Design.

Circulation
2026

Multi-omics integration study of vascular smooth muscle cell phenotypic conversion identified novel biomarkers in idiopathic pulmonary arterial hypertension.

Respiratory research
2026

Efficacy of fasudil in COPD-associated pulmonary arterial hypertension: meta-analysis of randomized controlled trials.

Frontiers in medicine
2026

ANCA-associated vasculitis following sotatercept initiation in a patient with heritable pulmonary arterial hypertension and previously silent eosinophilic granulomatosis with polyangiitis: a case report.

European heart journal. Case reports
2026

Beta arrestin 1 is a key regulator of pulmonary vascular tone.

Proceedings of the National Academy of Sciences of the United States of America
2026

A study on the accessibility and utilisation of targeted drugs for pulmonary arterial hypertension in China.

Frontiers in pharmacology
2026

Rare TRAF5 coding variants in systemic lupus erythematosus patients aggravate pulmonary hypertension via endothelial dysfunction.

Innovation (Cambridge (Mass.))
2026

A Case of IgG4-Related Disease Developing During Long-Term High-Dose Intravenous Epoprostenol Therapy in a Patient With Idiopathic Pulmonary Arterial Hypertension.

Pulmonary circulation
2026

Age and onset timing of Raynaud's phenomenon and first non-Raynaud symptom as prognostic factors in systemic sclerosis: a retrospective analysis from the Italian national multicenter Systemic Sclerosis Progression INvestiGation registry of the Italian Society for Rheumatology (SPRING-SIR).

Therapeutic advances in musculoskeletal disease
2025

Natural terpenoids with therapeutic potential against pulmonary arterial hypertension.

Frontiers in pharmacology
2026

Preselected and preferred immersive virtual reality versus narrative alone to induce post-stress relaxation in patients with pulmonary arterial hypertension: A pilot study on perceived stress and heart rate.

British journal of health psychology
2026

Ambrisentan for Early-Stage Low-Risk Pulmonary Arterial Hypertension: Design of the Randomized, Double-Blind, Placebo-Controlled ALEPH Trial.

JACC. Asia
2026

Exosomal miR-21 mitigates pulmonary hypertension-induced right-heart remodeling by preserves mitochondrial homeostasis.

Journal of translational medicine
2026

Pulmonary arterial hypertension: right ventricular phenotyping to improve risk assessment at follow-up.

European heart journal
2026

A treprostinil inhaler (Yutrepia) for pulmonary hypertension.

The Medical letter on drugs and therapeutics
2026

Nicotinamide phosphoribosyltransferase activates the mitochondrial unfolded protein response to promote pulmonary arterial endothelial cell proliferation.

bioRxiv : the preprint server for biology
2026

Estriol attenuates visceral adiposity and pulmonary artery smooth muscle cell proliferation via ERα-mediated signalling.

European heart journal open
2026

Cleavage and Polyadenylation Specificity Factor Subunit 5 Regulates Pulmonary Artery Smooth Muscle Expansion and Hypoxic Response.

MedComm
2026

Pulmonary Veno-Occlusive Disease: A Clue to Underlying Lymphoma.

Cureus
2026

Perillyl alcohol attenuates hypoxia induced right ventricular dysfunction and remodeling by balancing the renin angiotensin aldosterone system in rats.

Scientific reports
2026

Daily Physical Activity in Pulmonary Arterial Hypertension: Insights from a Multicenter Longitudinal Trial Using Accelerometry.

Chest
2026

Transplantation of Ex Vivo Amplified Mononuclear Cells From Peripheral Blood Improves Rat Pulmonary Hypertension via CD14- and CD163-Positive M2 Macrophages.

Respirology (Carlton, Vic.)
2026

Angioinvasive pulmonary mucormycosis presenting with massive haemoptysis secondary to pulmonary artery pseudoaneurysm.

BMJ case reports
2026

Regional Disparities in Pulmonary Arterial Hypertension Care in Japan - Beyond the Availability of Targeted Therapies.

Circulation journal : official journal of the Japanese Circulation Society
2026

Real-world observational study on pulmonary arterial hypertension: Italian cohort treated with macitentan and/or selexipag as a part of a combination treatment (INSPECTIO).

Vascular pharmacology
2026

Hemoglobin adduction and impaired oxygen transport define the etiology of pyrrolizidine alkaloid-induced pulmonary arterial hypertension.

Phytomedicine : international journal of phytotherapy and phytopharmacology
2026

Paeonol alleviates pulmonary arterial hypertension by activation of BRCC3.

Phytomedicine : international journal of phytotherapy and phytopharmacology
2026

Sine oculis homeobox 1 drives endothelial dysfunction in preclinical pulmonary arterial hypertension.

Science translational medicine
2026

IL-6 and TGF-β1 as biomarkers of schistosomiasis-associated pulmonary hypertension in a murine model.

Brazilian journal of medical and biological research = Revista brasileira de pesquisas medicas e biologicas
2026

Discovery Beyond the "Undiscovered Country": Re-Exploring the Right Ventricle Through Metabolomics and Cardiac Magnetic Resonance.

JACC. Asia
2026

Loss of ROR2 Tyrosine Kinase Receptor Is Associated With Endothelial Dysfunction in PAH via Inappropriate Integrin β1 Activation.

Hypertension (Dallas, Tex. : 1979)
2026

Clinical relevance of the TAPSE/SPAP ratio in pulmonary arterial hypertension: a single-center retrospective study.

BMC cardiovascular disorders
2026

[Research progress on the correlation between Akkermansia muciniphila and cardiovascular diseases].

Nan fang yi ke da xue xue bao = Journal of Southern Medical University
2026

Newly diagnosed pulmonary arterial hypertension following liver transplantation: Insights from a multicenter case series.

Liver transplantation : official publication of the American Association for the Study of Liver Diseases and the International Liver Transplantation Society
2026

Sympatho-Excitation in Pulmonary Hypertension: The Potential Role of Pulmonary Arterial Baroreceptors: An Acute Physiologic Intervention Study.

Respirology (Carlton, Vic.)
2026

[Role of macrophages in pulmonary arterial hypertension and advances in targeted therapeutic interventions].

Zhonghua jie he he hu xi za zhi = Zhonghua jiehe he huxi zazhi = Chinese journal of tuberculosis and respiratory diseases
2026

Efficacy and Safety of Oral Treprostinil in Patients with Pulmonary Arterial Hypertension on Background Monotherapy or Dual Therapy.

Advances in therapy
2025

Case Report: Immune checkpoint inhibitor-associated pulmonary hypertension.

Frontiers in cardiovascular medicine
Ver todos os 10.723 no EuropePMC

Associações

Organizações que acompanham esta doença — pra ter apoio e orientação

Associação brasileira dedicada a Hipertensão arterial pulmonar.

Comunidades

Grupos ativos de quem convive com esta doença aqui no Raras

Ainda não existe comunidade no Raras para Hipertensão arterial pulmonar

Pacientes, familiares e cuidadores se organizam em comunidades pra compartilhar experiências, fazer perguntas e se apoiar. Você pode ser o primeiro.

Tire suas dúvidas

Perguntas, dicas e experiências compartilhadas aqui na página

Participe da discussão

Faça login para postar dúvidas, compartilhar experiências e interagir com especialistas.

Fazer login

Doenças relacionadas

Doenças com sintomas parecidos — ajudam quem ainda está buscando diagnóstico

Referências e fontes

Bases de dados externas citadas neste artigo

Publicações científicas

Artigos indexados no PubMed ligados a esta doença no grafo RarasNet — título, periódico e PMID direto da fonte, sem intermediação de IA.

  1. A Phase 2, Randomized, Clinical Trial of Inhaled Nitric Oxide for Acute Severe Right Heart Failure With Pulmonary Hypertension (PHiNO Study).
    Circulation journal : official journal of the Japanese Circulation Society· 2026· PMID 41866186mais citado
  2. When atrioventricular block paves the way to a more severe diagnosis: a case report.
    European heart journal. Case reports· 2026· PMID 41858696mais citado
  3. The emerging role of integrin signaling in pulmonary vascular disease.
    American journal of physiology. Lung cellular and molecular physiology· 2026· PMID 41849225mais citado
  4. Endothelial C-type natriuretic peptide/guanylyl cyclase-B signaling prevents pulmonary arterial hypertension.
    Nature communications· 2026· PMID 41844596mais citado
  5. Iron Deficiency in Pulmonary Hypertension-Prevalence, Impact on Prognosis and Disease Burden in Pulmonary Arterial Hypertension and Pulmonary Hypertension Related to Hypoxia: A Review.
    International journal of molecular sciences· 2026· PMID 41828555mais citado
  6. The Impact of Fluid Balance on Clinical Outcomes in ICU Patients with Pulmonary Arterial Hypertension: A Retrospective Analysis using MIMIC-IV.
    Open Respir Med J· 2026· PMID 41987839recente
  7. Intermittent fasting and cardiometabolic responses under cardiac stress: a systematic review of preclinical studies.
    Life Sci· 2026· PMID 41985711recente
  8. Identification of RUNX1 as a Biomarker for Right Ventricular Remodeling in Pulmonary Arterial Hypertension Using WGCNA.
    Pulm Circ· 2026· PMID 41982428recente
  9. Biological Sex Differences in the US-CTEPH-R.
    Ann Am Thorac Soc· 2026· PMID 41981721recente
  10. Echocardiographic Assessment of Pulmonary Arterial Hypertension After Complete Atrioventricular Septal Defect Repair.
    Echocardiography· 2026· PMID 41979870recente

Bases de dados e fontes oficiais

Identificadores e referências canônicas usadas para montar este verbete.

  1. ORPHA:182090(Orphanet)
  2. MONDO:0015924(MONDO)
  3. Hipertensao Arterial Pulmonar(PCDT · Ministério da Saúde)
  4. GARD:7501(GARD (NIH))
  5. Variantes catalogadas(ClinVar)
  6. Busca completa no PubMed(PubMed)
  7. Q16070735(Wikidata)

Dados compilados pelo RarasNet a partir de fontes abertas (Orphanet, OMIM, MONDO, PubMed/EuropePMC, ClinicalTrials.gov, DATASUS, PCDT/MS). Este conteúdo é informativo e não substitui avaliação médica.

Conteúdo mantido por Agente Raras · Médicos e pesquisadores podem colaborar

Hipertensão arterial pulmonar
Compêndio · Raras BR

Hipertensão arterial pulmonar

ORPHA:182090 · MONDO:0015924
🇧🇷 Brasil SUS
CEAF
1ABosentana1BAmbrisentanaSildenafilaIloprosta+3 mais
Geral
Prevalência
1-9 / 100 000
Herança
Autosomal dominant, Not applicable
CID-11
Ensaios
36 ativos
Início
All ages
Prevalência
2.0 (Europe)
MedGen
UMLS
C2973725
Repurposing
147 candidatos
acebutololadrenergic receptor antagonist
alaceprilangiotensin converting enzyme inhibitor
aliskiren-hemifumaraterenin inhibitor
+17 outros
Wikidata
Papers 10a
DiscussaoAtiva

Nenhuma novidade ainda. O agente esta monitorando.

0membros
0novidades