Raras
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Nanoftalmia
ORPHA:35612CID-10 · Q11.2CID-11 · LA10.0DOENÇA RARA

A nanoftalmia é uma condição ocular grave onde o olho é muito pequeno. Ela se caracteriza por um olho com comprimento axial (o tamanho da frente para trás) mais curto do que o normal, uma dificuldade grande para enxergar de perto (hipermetropia severa), e o cristalino (a lente natural do olho) é desproporcionalmente grande em relação ao tamanho total do olho. Além disso, pessoas com nanoftalmia têm uma alta probabilidade de desenvolver glaucoma de ângulo fechado, uma doença que eleva a pressão dentro do olho e pode afetar a visão.

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Introdução

O que você precisa saber de cara

📋

A nanoftalmia é uma condição ocular grave onde o olho é muito pequeno. Ela se caracteriza por um olho com comprimento axial (o tamanho da frente para trás) mais curto do que o normal, uma dificuldade grande para enxergar de perto (hipermetropia severa), e o cristalino (a lente natural do olho) é desproporcionalmente grande em relação ao tamanho total do olho. Além disso, pessoas com nanoftalmia têm uma alta probabilidade de desenvolver glaucoma de ângulo fechado, uma doença que eleva a pressão dentro do olho e pode afetar a visão.

Publicações científicas
327 artigos
Último publicado: 2026

Escala de raridade

CLASSIFICAÇÃO ORPHANET · BRASIL 2024
Unknown
Ultra-rara
<1/50k
Muito rara
1/20k
Rara
1/10k
Pouco freq.
1/5k
Incomum
1/2k
Prevalência
0.0
Worldwide
Início
Infancy
+ neonatal
🏥
SUS: Cobertura mínimaScore: 15%
CID-10: Q11.2
🇧🇷Dados SUS / DATASUS
PROCEDIMENTOS SIGTAP (5)
0202010503
Cariótipo — bandas G, Q ou Rgenetic_test
0202010600
Pesquisa de microdeleções/microduplicações por FISHlab_test
0202010694
Sequenciamento completo do exoma (WES)rehabilitation
0202010260
Dosagem de alfa-fetoproteína
0301070040
Atendimento em reabilitação — doenças raras
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Sinais e sintomas

O que aparece no corpo e com que frequência cada sintoma acontece

Características mais comuns

90%prev.
Hipermetropia alta
Muito frequente (99-80%)
90%prev.
Morfologia anormal da coroide
Muito frequente (99-80%)
90%prev.
Microftalmia
Muito frequente (99-80%)
90%prev.
Estrabismo
Muito frequente (99-80%)
90%prev.
Glaucoma
Muito frequente (99-80%)
17%prev.
Anormalidade da pigmentação retiniana
Ocasional (29-5%)
13sintomas
Muito frequente (5)
Ocasional (1)
Sem dados (7)

Os sintomas variam de pessoa para pessoa. Abaixo estão as 13 características clínicas mais associadas, ordenadas por frequência.

Hipermetropia altaHigh hypermetropia
Muito frequente (99-80%)90%
Morfologia anormal da coroideAbnormal choroid morphology
Muito frequente (99-80%)90%
MicroftalmiaMicrophthalmia
Muito frequente (99-80%)90%
EstrabismoStrabismus
Muito frequente (99-80%)90%
Glaucoma
Muito frequente (99-80%)90%

Linha do tempo da pesquisa

Publicações por ano — veja quando o interesse científico cresceu
Anos de pesquisa1desde 2026
Total histórico327PubMed
Últimos 10 anos171publicações
Pico202227 papers
Linha do tempo
2026Hoje · 2026🧪 2001Primeiro ensaio clínico📈 2022Ano de pico
Publicações por ano (últimos 10 anos)

Encontrou um erro ou informação desatualizada? Sugira uma correção →

Genética e causas

O que está alterado no DNA e como passa nas famílias

Genes associados

11 genes identificados com associação a esta condição. Padrão de herança: Autosomal dominant, Autosomal recessive, Not applicable.

SOX2Transcription factor SOX-2Disease-causing germline mutation(s) inAltamente restrito
FUNÇÃO

Transcription factor that forms a trimeric complex with OCT4 on DNA and controls the expression of a number of genes involved in embryonic development such as YES1, FGF4, UTF1 and ZFP206 (By similarity). Binds to the proximal enhancer region of NANOG (By similarity). Critical for early embryogenesis and for embryonic stem cell pluripotency (PubMed:18035408). Downstream SRRT target that mediates the promotion of neural stem cell self-renewal (By similarity). Keeps neural cells undifferentiated by

LOCALIZAÇÃO

Nucleus speckleCytoplasmNucleus

VIAS BIOLÓGICAS (10)
Formation of the posterior neural plateDeactivation of the beta-catenin transactivating complexInterleukin-4 and Interleukin-13 signalingGerm layer formation at gastrulationTranscriptional regulation of pluripotent stem cells
MECANISMO DE DOENÇA

Microphthalmia, syndromic, 3

A disease characterized by the rare association of malformations including uni- or bilateral anophthalmia or microphthalmia, and esophageal atresia with trachoesophageal fistula. Microphthalmia is a disorder of eye formation, ranging from small size of a single eye to complete bilateral absence of ocular tissues (anophthalmia). In many cases, microphthalmia/anophthalmia occurs in association with syndromes that include non-ocular abnormalities.

EXPRESSÃO TECIDUAL(Ubíquo)
Cérebro - Amígdala
69.8 TPM
Brain Caudate basal ganglia
68.0 TPM
Brain Nucleus accumbens basal ganglia
67.1 TPM
Brain Anterior cingulate cortex BA24
66.8 TPM
Brain Frontal Cortex BA9
57.5 TPM
OUTRAS DOENÇAS (4)
anophthalmia/microphthalmia-esophageal atresia syndromemicrophthalmia, isolated, with colobomananophthalmiaseptooptic dysplasia
HGNC:11195UniProt:P48431
OTX2Homeobox protein OTX2Disease-causing germline mutation(s) inAltamente restrito
FUNÇÃO

Transcription factor probably involved in the development of the brain and the sense organs. Can bind to the bicoid/BCD target sequence (BTS): 5'-TCTAATCCC-3'

LOCALIZAÇÃO

Nucleus

VIAS BIOLÓGICAS (2)
Formation of the posterior neural plateFormation of the anterior neural plate
MECANISMO DE DOENÇA

Microphthalmia, syndromic, 5

Patients manifest unilateral or bilateral microphthalmia/clinical anophthalmia and variable additional features including pituitary dysfunction, coloboma, microcornea, cataract, retinal dystrophy, hypoplasia or agenesis of the optic nerve, agenesis of the corpus callosum, developmental delay, joint laxity, hypotonia, and seizures. Microphthalmia is a disorder of eye formation, ranging from small size of a single eye to complete bilateral absence of ocular tissues (anophthalmia). In many cases, microphthalmia/anophthalmia occurs in association with syndromes that include non-ocular abnormalities.

EXPRESSÃO TECIDUAL(Tecido-específico)
Cérebro - Hemisfério cerebelar
24.4 TPM
Cerebelo
23.8 TPM
Substância negra
2.9 TPM
Hipotálamo
1.0 TPM
Testículo
0.7 TPM
OUTRAS DOENÇAS (8)
pituitary hormone deficiency, combined, 6syndromic microphthalmia type 5septooptic dysplasiacombined pituitary hormone deficiencies, genetic form
HGNC:8522UniProt:P32243
MFRPMembrane frizzled-related proteinDisease-causing germline mutation(s) inTolerante
FUNÇÃO

May play a role in eye development

LOCALIZAÇÃO

Apical cell membrane

MECANISMO DE DOENÇA

Nanophthalmos 2

A form of nanophthalmos, a disorder of eye development characterized by extreme hyperopia and small functional eyes. The cornea and lens are normal in size and shape. Hyperopia occurs because insufficient growth along the visual axis places these lensing components too close to the retina. Nanophthalmic eyes show considerable thickening of both the choroidal vascular bed and scleral coat, which provide nutritive and structural support for the retina. NNO2 inheritance is autosomal recessive.

EXPRESSÃO TECIDUAL(Não detectado)
Hipocampo
0.1 TPM
Brain Spinal cord cervical c-1
0.1 TPM
Substância negra
0.1 TPM
Pulmão
0.1 TPM
Baço
0.1 TPM
OUTRAS DOENÇAS (3)
nanophthalmos 2isolated microphthalmia 5nanophthalmia
HGNC:18121UniProt:Q9BY79
SIX6Homeobox protein SIX6Candidate gene tested inTolerante
FUNÇÃO

May be involved in eye development

LOCALIZAÇÃO

Nucleus

MECANISMO DE DOENÇA

Optic disk anomalies with retinal and/or macular dystrophy

An ocular disorder characterized by optic nerve dysplasia, optic disk anomalies, chorioretinal dystrophy and macular atrophy. Some patients have microphthalmia.

EXPRESSÃO TECIDUAL(Tecido-específico)
Pituitária
55.2 TPM
Hipotálamo
1.1 TPM
Testículo
0.4 TPM
Músculo esquelético
0.2 TPM
Próstata
0.1 TPM
OUTRAS DOENÇAS (3)
colobomatous optic disc-macular atrophy-chorioretinopathy syndromenanophthalmiamicrophthalmia, isolated, with coloboma
HGNC:10892UniProt:O95475
PRSS56Serine protease 56Disease-causing germline mutation(s) inTolerante
FUNÇÃO

Serine protease required during eye development

LOCALIZAÇÃO

MECANISMO DE DOENÇA

Microphthalmia, isolated, 6

A developmental ocular disorder characterized by small malformed eyes. Clinical features are extreme hyperopia due to short axial length with essentially normal anterior segment, steep corneal curvatures, shallow anterior chamber, thick lenses, and thickened scleral wall. Palpebral fissures appear narrow because of relatively deep-set eyes, visual acuity is mildly to moderately reduced, and anisometropic or strabismic amblyopia is common. The fundus of the eye shows crowded optical disks, tortuous vessels, and an abnormal foveal avascular zone.

EXPRESSÃO TECIDUAL(Tecido-específico)
Testículo
5.2 TPM
Músculo esquelético
3.4 TPM
Hipotálamo
2.9 TPM
Brain Frontal Cortex BA9
1.1 TPM
Brain Putamen basal ganglia
0.9 TPM
INTERAÇÕES PROTEICAS (2)
OUTRAS DOENÇAS (2)
isolated microphthalmia 6nanophthalmia
HGNC:39433UniProt:P0CW18
ALDH1A3Retinaldehyde dehydrogenase 3Disease-causing germline mutation(s) inTolerante
FUNÇÃO

Catalyzes the NAD-dependent oxidation of aldehyde substrates, such as all-trans-retinal and all-trans-13,14-dihydroretinal, to their corresponding carboxylic acids, all-trans-retinoate and all-trans-13,14-dihydroretinoate, respectively (By similarity) (PubMed:27759097). High specificity for all-trans-retinal as substrate, can also accept acetaldehyde as substrate in vitro but with lower affinity (PubMed:27759097). Required for the biosynthesis of normal levels of retinoate in the embryonic ocula

LOCALIZAÇÃO

Cytoplasm

VIAS BIOLÓGICAS (5)
RA biosynthesis pathwayDevelopmental Lineage of Mammary Gland Luminal Epithelial CellsDevelopmental Lineage of Mammary Gland Alveolar CellsDevelopmental Lineage of Mammary Stem CellsDevelopmental Lineage of Mammary Gland Myoepithelial Cells
MECANISMO DE DOENÇA

Microphthalmia, isolated, 8

A disorder of eye formation, ranging from small size of a single eye to complete bilateral absence of ocular tissues. Ocular abnormalities like opacities of the cornea and lens, scaring of the retina and choroid, and other abnormalities may also be present.

OUTRAS DOENÇAS (3)
isolated microphthalmia 8nanophthalmiamicrophthalmia, isolated, with coloboma
HGNC:409UniProt:P47895
CRB1Protein crumbs homolog 1Disease-causing germline mutation(s) inTolerante
FUNÇÃO

Plays a role in photoreceptor morphogenesis in the retina (By similarity). May maintain cell polarization and adhesion (By similarity)

LOCALIZAÇÃO

Apical cell membraneSecretedCell projection, cilium, photoreceptor outer segmentPhotoreceptor inner segment

INTERAÇÕES PROTEICAS (4)
OUTRAS DOENÇAS (6)
pigmented paravenous retinochoroidal atrophyLeber congenital amaurosis 8retinitis pigmentosa 12retinitis pigmentosa
HGNC:2343UniProt:P82279
RAXInterferon-inducible double-stranded RNA-dependent protein kinase activator ADisease-causing germline mutation(s) inTolerante
FUNÇÃO

Activates EIF2AK2/PKR in the absence of double-stranded RNA (dsRNA), leading to phosphorylation of EIF2S1/EFI2-alpha and inhibition of translation and induction of apoptosis. Required for siRNA production by DICER1 and for subsequent siRNA-mediated post-transcriptional gene silencing. Does not seem to be required for processing of pre-miRNA to miRNA by DICER1. Promotes UBC9-p53/TP53 association and sumoylation and phosphorylation of p53/TP53 at 'Lys-386' at 'Ser-392' respectively and enhances it

LOCALIZAÇÃO

Cytoplasm, perinuclear regionCytoplasm

VIAS BIOLÓGICAS (2)
MicroRNA (miRNA) biogenesisSmall interfering RNA (siRNA) biogenesis
MECANISMO DE DOENÇA

Dystonia 16

An early-onset dystonia-parkinsonism disorder. Dystonia is defined by the presence of sustained involuntary muscle contraction, often leading to abnormal postures. DYT16 patients have progressive, generalized dystonia with axial muscle involvement, oro-mandibular (sardonic smile) and laryngeal dystonia and, in some cases, parkinsonian features.

EXPRESSÃO TECIDUAL(Não detectado)
Pituitária
0.3 TPM
Testículo
0.2 TPM
Skin Not Sun Exposed Suprapubic
0.2 TPM
Skin Sun Exposed Lower leg
0.2 TPM
Brain Nucleus accumbens basal ganglia
0.1 TPM
OUTRAS DOENÇAS (3)
isolated microphthalmia 3nanophthalmiamicrophthalmia, isolated, with coloboma
HGNC:18662UniProt:O75569
TMEM98Transmembrane protein 98Disease-causing germline mutation(s) inTolerante
FUNÇÃO

Functions as a negative regulator of MYRF in oligodendrocyte differentiation and myelination. Interacts with the C-terminal of MYRF inhibiting MYRF self-cleavage and N-fragment nuclear translocation. The secreted form promotes differentiation of T helper 1 cells (Th1)

LOCALIZAÇÃO

Cell membraneSecretedSecreted, extracellular exosomeEndoplasmic reticulum membrane

MECANISMO DE DOENÇA

Nanophthalmos 4

A form of nanophthalmos, a disorder of eye development characterized by extreme hyperopia and small functional eyes. The cornea and lens are normal in size and shape. Hyperopia occurs because insufficient growth along the visual axis places these lensing components too close to the retina. Nanophthalmic eyes show considerable thickening of both the choroidal vascular bed and scleral coat, which provide nutritive and structural support for the retina. NNO4 inheritance is autosomal dominant.

EXPRESSÃO TECIDUAL(Ubíquo)
Ovário
111.0 TPM
Nervo tibial
62.6 TPM
Útero
62.1 TPM
Cervix Ectocervix
57.1 TPM
Fallopian Tube
51.5 TPM
INTERAÇÕES PROTEICAS (4)
OUTRAS DOENÇAS (2)
nanophthalmos 4nanophthalmia
HGNC:24529UniProt:Q9Y2Y6
BEST1Bestrophin-1Disease-causing germline mutation(s) inTolerante
FUNÇÃO

Ligand-gated anion channel that allows the movement of anions across cell membranes when activated by calcium (Ca2+) (PubMed:11904445, PubMed:12907679, PubMed:18179881, PubMed:18400985, PubMed:19853238, PubMed:21330666, PubMed:26200502, PubMed:26720466, PubMed:35789156). Allows the movement of chloride and hydrogencarbonate (PubMed:11904445, PubMed:12907679, PubMed:18179881, PubMed:18400985, PubMed:19853238, PubMed:21330666, PubMed:26200502, PubMed:26720466, PubMed:35789156). Found in a partiall

LOCALIZAÇÃO

Cell membraneBasolateral cell membrane

VIAS BIOLÓGICAS (1)
Stimuli-sensing channels
MECANISMO DE DOENÇA

Macular dystrophy, vitelliform, 2

An autosomal dominant form of macular degeneration that usually begins in childhood or adolescence. VMD2 is characterized by typical 'egg-yolk' macular lesions due to abnormal accumulation of lipofuscin within and beneath the retinal pigment epithelium cells. Progression of the disease leads to destruction of the retinal pigment epithelium and vision loss.

VIAS REACTOME (1)
OUTRAS DOENÇAS (8)
vitelliform macular dystrophy 2retinitis pigmentosa 50autosomal dominant vitreoretinochoroidopathyautosomal recessive bestrophinopathy
HGNC:12703UniProt:O76090
MYRFMyelin regulatory factorDisease-causing germline mutation(s) inAltamente restrito
FUNÇÃO

Constitutes a precursor of the transcription factor. Mediates the autocatalytic cleavage that releases the Myelin regulatory factor, N-terminal component that specifically activates transcription of central nervous system (CNS) myelin genes (PubMed:23966832) Membrane-bound part that has no transcription factor activity and remains attached to the endoplasmic reticulum membrane following cleavage Transcription factor that specifically activates expression of myelin genes such as MBP, MOG, MAG, DU

LOCALIZAÇÃO

Endoplasmic reticulum membraneNucleusCytoplasm

MECANISMO DE DOENÇA

Encephalitis/encephalopathy, mild, with reversible myelin vacuolization

An autosomal dominant disease characterized by episodes of acute encephalitis associated with impaired consciousness, delirious behavior, seizures, and reversible splenial lesions observed on diffusion magnetic resonance imaging. Most patients completely recover and there are no neurologic sequelae. MMERV occurs in children and is frequently associated with a trigger, such as a febrile illness.

EXPRESSÃO TECIDUAL(Ubíquo)
Brain Spinal cord cervical c-1
204.5 TPM
Estômago
124.4 TPM
Hipocampo
63.4 TPM
Substância negra
62.3 TPM
Brain Putamen basal ganglia
53.4 TPM
OUTRAS DOENÇAS (3)
encephalitis/encephalopathy, mild, with reversible myelin vacuolizationcardiac-urogenital syndromenanophthalmos 1
HGNC:1181UniProt:Q9Y2G1

Variantes genéticas (ClinVar)

583 variantes patogênicas registradas no ClinVar.

🧬 MYRF: NM_001127392.3(MYRF):c.1728T>A (p.Asn576Lys) ()
🧬 MYRF: NM_001127392.3(MYRF):c.2869C>A (p.Pro957Thr) ()
🧬 MYRF: NM_001127392.3(MYRF):c.1048del (p.Ser350fs) ()
🧬 MYRF: NM_001127392.3(MYRF):c.1134_1135del (p.Val379fs) ()
🧬 MYRF: NM_001127392.3(MYRF):c.278del (p.Pro93fs) ()
Ver todas no ClinVar

Classificação de variantes (ClinVar)

Distribuição de 29 variantes classificadas pelo ClinVar.

26
3
Patogênica (89.7%)
VUS (10.3%)
VARIANTES MAIS SIGNIFICATIVAS
MYRF: NM_001127392.3(MYRF):c.1048del (p.Ser350fs) [Likely pathogenic]
FUS: NM_004960.4(FUS):c.1483dup (p.Arg495fs) [Likely pathogenic]
MYRF: MYRF, ARG986TER [Pathogenic]
MYRF: MYRF, ARG478PRO [Pathogenic]
MYRF: MYRF, 1-BP DUP, 789C (rs769274302) [Pathogenic]

Diagnóstico

Os sinais que médicos procuram e os exames que confirmam

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Tratamento e manejo

Remédios, cuidados de apoio e o que precisa acompanhar

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Medicamentos catalogadosEnsaios clínicos· 0 medicamentos · 2 ensaios
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Onde tratar no SUS

Hospitais de referência no Brasil e o protocolo oficial do SUS (PCDT)

🇧🇷 Atendimento SUS — Nanoftalmia

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Pesquisa ativa

Ensaios clínicos abertos e novidades científicas recentes

Pesquisa e ensaios clínicos

17 ensaios clínicos encontrados.

Distribuição por fase
Ver todos no ClinicalTrials.gov
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Publicações mais relevantes

Timeline de publicações
174 papers (10 anos)
#1

Splicing variants in MYRF cause partial loss of function in the retinal pigment epithelium leading to nanophthalmos.

JCI insight2026 Mar 23

Improper light focus on the retina, refractive error, is primarily caused by eye size differences and is the leading cause of vision loss worldwide. C-terminal variants in the Myelin regulatory factor (MYRF) gene, a retinal pigment epithelium-derived (RPE-derived) transcription factor, lead to isolated nanophthalmos characterized by a small, though structurally sound eye. However, other MYRF loss-of-function variants cause syndromic disease. To address this discrepancy, in vitro and animal studies were performed on a pathogenic C-terminal variant dG-MYRF (p.Gly1126fs30*, c.3376-1G>A). Human RPE cells or primary RPE transduced with dG-MYRF showed reduced target gene expression, with decreased steady-state levels of the C-terminal cleavage product, but normal cleavage and localization. A homozygous humanized MYRF C-terminal mouse model (MyrfhumdG/humdG) was embryonic lethal by E18.5, while WT (MyrfhumWT/humWT) mice were viable. Single-cell RNA-seq from E17.5 MyrfhumdG/humdG and KO RxCre;Myrffl/fl (E15.5 and P0) mice revealed shared differentially expressed genes, with decreased effect size in the MyrfhumdG/humdG eyes. These findings support dG-MYRF as a hypomorphic allele. Additionally, 2 MYRF splicing variants creating nonfunctional isoforms were found in families with isolated nanophthalmos. Overall, hypomorphic MYRF alleles underlie isolated nanophthalmos, supporting a tissue-specific threshold effect and highlighting unique roles for the MYRF C-terminus in the RPE.

#2

Corrigendum to "Medical management of post-phacoemulsification uveal effusion in nanophthalmos: A case report [Am. J. Ophthalmol. Case Rep. (41), March 2026, 102507].

American journal of ophthalmology case reports2026 Mar

[This corrects the article DOI: 10.1016/j.ajoc.2025.102507.].

#3

Medical management of post-phacoemulsification uveal effusion in nanophthalmos: A case report.

American journal of ophthalmology case reports2026 Mar

Nanophthalmos presents a unique surgical challenge due to anatomical constraints and increased risk for postoperative complications. In presenting this case, our aim is to raise awareness of nanophthalmic uveal effusion syndrome (UES) and exudative retinal detachment (RD), emphasize the importance of accurate postoperative diagnosis in such cases, and challenge the prevailing notion that surgical intervention is required in such scenarios. We report a case of successful non-surgical management of UES with exudative RD following uncomplicated cataract surgery in a nanophthalmic eye. A 65-year-old monocular female with nanophthalmos (axial length 15.25mm) underwent phacoemulsification with intraocular lens implantation. Postoperatively, the patient developed cystoid macular edema, and subretinal fluid. Prominent choroidal folds and the absence of retinal breaks aided the diagnosis of UES with exudative RD. Given the complexity of this case, and the patient's monocular status, we opted for a conservative approach. A regimen of topical dexamethasone and oral acetazolamide was initiated. Clinical improvement was observed within days, with complete resolution of subretinal fluid and reattachment of the retina over the following month. Six months postoperatively, best-corrected visual acuity improved to 6/12, with maintained anatomical and functional stability at one year. This case highlights the importance of accurate postoperative assessment in nanophthalmic patients, particularly distinguishing exudative from rhegmatogenous RD. Furthermore, it underscores the potential for conservative therapy in managing UES, challenging the prevailing reliance on surgical intervention. Further research is needed to delineate criteria for medical management candidacy and optimize treatment regimens.

#4

Multimodal imaging in nanophthalmos.

Eye (London, England)2026 Mar 02
#5

MYRF gene mutation leading to coronary artery anomaly combined with 46,XY sex development disorder, a case report and literature review.

BMC pediatrics2025 Aug 16

MYRF gene mutations can lead to the development of Cardio-Urogenital Syndrome (CUGS), characterized by congenital heart disease, abnormalities in the internal and external reproductive organs, and ocular anomalies. CUGS can manifest with various types of congenital heart diseases, such as Tetralogy of Fallot, Scimitar syndrome, Hypoplastic Left Heart Syndrome, Atrial Septal Defect, Ventricular Septal Defect, Dextrocardia, Aortic Arch Anomalies, and Pulmonary Vein Anomalies et al. Male patients (46,XY) may present with unilateral cryptorchidism, ambiguous genitalia, or even typical female genitalia. The most common ocular issues consistent with high myopia and nanophthalmos. To date, there have been reports of over 30 cases of MYRF gene mutations worldwide. A 5-month-old female infant was admitted to Beijing Children's Hospital affiliated with Capital Medical University due to "rapid breathing since birth." No targeted therapy was administered prior to admission despite persistent tachypnea. Four months before admission, the infant was seen at a local hospital due to abnormalities in the external reproductive organs. Chromosomal analysis revealed 46, XY, and whole exome gene testing showed a MYRF gene mutation, identified heterozygosity for de novo mutations in the MYRF gene, splice site variant, respectively, that was not found in the gnomAD database, clinically presenting as Cardio-Urogenital Syndrome (GUGS; OMIM: 618280), inherited in an autosomal dominant (AD) manner. Family history was negative. The infant's showed severely breathing progressively, leading to admission to our hospital. Electrocardiography showed pathological Q waves in leads I, avL, and V4-V6. Echocardiography revealed congenital heart disease of anomalous origin of the left coronary artery from the pulmonary artery, severe left ventricular enlargement (left ventricular end-diastolic diameter 35.2 mm), mild-to-moderate mitral regurgitation, and slightly reduced left ventricular systolic function (EF: 54%, which is just below the normal threshold 55%). Subsequent coronary angiography indicated the left coronary artery originating from the main pulmonary artery. The infant underwent further surgical treatment which confirmed the prior diagnosis and had a good postoperative recovery. This case represents an exceptionally rare instance of MYRF-CUGS combined with coronary artery anomaly. This case report enriches the clinical phenotype spectrum of CUGS caused by MYRF gene mutations and improves recognition among clinicians.

Publicações recentes

Ver todas no PubMed

📚 EuropePMC203 artigos no totalmostrando 166

2026

Multimodal imaging in nanophthalmos.

Eye (London, England)
2026

Splicing variants in MYRF cause partial loss of function in the retinal pigment epithelium leading to nanophthalmos.

JCI insight
2026

Corrigendum to "Medical management of post-phacoemulsification uveal effusion in nanophthalmos: A case report [Am. J. Ophthalmol. Case Rep. (41), March 2026, 102507].

American journal of ophthalmology case reports
2026

Medical management of post-phacoemulsification uveal effusion in nanophthalmos: A case report.

American journal of ophthalmology case reports
2025

Refractive Results and Complications of Lensectomy in Simple Extreme Microphthalmos Cases.

Turkish journal of ophthalmology
2025

[Progress in clinical research on nanophthalmos secondary angle-closure glaucoma].

[Zhonghua yan ke za zhi] Chinese journal of ophthalmology
2025

Risk factors for glaucoma in nanophthalmos - a systematic review and meta-analysis.

BMC ophthalmology
2025

Membrane frizzled-related protein: a comprehensive analysis of genetic characteristics, phenotypic manifestations and impact on retinal microvasculature.

Ophthalmic genetics
2025

Suprachoroidal Proliferative Membrane in Uveal Effusion Syndrome with Nanophthalmos: Incidental Finding During Sclerectomy.

Ocular immunology and inflammation
2025

Comprehensive genetic landscapes and clinical heterogeneity in nanophthalmos: new insights from a large Chinese cohort.

Journal of medical genetics
2025

Peripheral vitreoretinal abnormality and its correlation with malignant glaucoma in nanophthalmos with secondary angle closure glaucoma.

Eye (London, England)
2025

MYRF gene mutation leading to coronary artery anomaly combined with 46,XY sex development disorder, a case report and literature review.

BMC pediatrics
2025

Retinal detachment associated to macular hole in nanophthalmos and high hyperopia.

Archivos de la Sociedad Espanola de Oftalmologia
2025

Sclerectomies in nanophthalmos and idiopathic uveal effusion syndrome: a systematic review.

Graefe's archive for clinical and experimental ophthalmology = Albrecht von Graefes Archiv fur klinische und experimentelle Ophthalmologie
2025

Hashimoto's thyroiditis and nanophthalmos in Gabriele-de Vries syndrome: a case report.

Frontiers in endocrinology
2025

Genetic Spectrum and Genotype-Phenotype Correlations in a Chinese Cohort With Nanophthalmos With Secondary Angle-Closure Glaucoma.

Investigative ophthalmology &amp; visual science
2025

Splicing variants in MYRF cause partial loss of function in the retinal pigment epithelium.

bioRxiv : the preprint server for biology
2025

[Recent advances in congenital nanophthalmos: a comprehensive literature review].

[Zhonghua yan ke za zhi] Chinese journal of ophthalmology
2025

MFRP is a molecular hub that organizes the apical membrane of RPE cells by engaging in interactions with specific proteins and lipids.

Proceedings of the National Academy of Sciences of the United States of America
2025

Myelin regulatory factor (MYRF) is a critical early regulator of retinal pigment epithelial development.

PLoS genetics
2025

A biometric survey of known and prospective murine models of posterior microphthalmia-nanophthalmia.

Experimental eye research
2025

Cataract Surgery in the Small Adult Eye: A Review.

Clinical &amp; experimental ophthalmology
2025

Cataract surgery in the extremely small eye: morphology, comorbidities and outcomes in 300 eyes.

The British journal of ophthalmology
2025

Phacoemulsification combined glaucoma surgeries in the treatment of nanophthalmos patients with secondary angle closure glaucoma.

Graefe's archive for clinical and experimental ophthalmology = Albrecht von Graefes Archiv fur klinische und experimentelle Ophthalmologie
2025

Prime Editing Strategy to Install the Mfrp Retinal Degeneration 6 Mutation.

Advances in experimental medicine and biology
2024

Kenny-Caffey Syndrome Type 2 (KCS2): A New Case Report and Patient Follow-Up Optimization.

Journal of clinical medicine
2025

MFRP, PRSS56, and MYRF account for 60.5% of a Chinese cohort with nanophthalmos.

Clinical &amp; experimental ophthalmology
2024

Management of persistent exudative retinal detachment: exploring etiology and surgical outcomes.

BMC ophthalmology
2025

Ultrawidefield Imaging of Nanophthalmos with Choroidal Congestion.

Ophthalmology
2024

Clinical and Genetic Characteristics of Patients with Peripheral Retinal Flecks in Koreans.

Korean journal of ophthalmology : KJO
2024

Nanophthalmos with Foveal Hypoplasia and Wrinkling of Macular Mound Caused by Novel Biallelic PRSS56 Variants: A Case Report.

Korean journal of ophthalmology : KJO
2024

Phacoemulsification in Nanophthalmic Eye, a Way to Manage Glaucoma: Case Report.

Case reports in ophthalmological medicine
2024

Bilateral Chandler Syndrome, Nanophthalmos, and Angle Closure Glaucoma: A Complex Presentation, Challenging Diagnosis, and Pathological Insight-A Case Report.

Journal of current glaucoma practice
2024

Surgery for Esotropia in a Case of Nanophthalmos.

Cureus
2024

MFRP variations cause nanophthalmos in five Chinese families with distinct phenotypic diversity.

Frontiers in genetics
2024

Micropulse transscleral laser therapy for secondary angle-closure glaucoma in nanophthalmos: a case report.

International journal of ophthalmology
2024

Nanophthalmos-Associated MYRF gene mutation facilitates intraocular inflammation in mice.

International immunopharmacology
2024

Clinical features of patients with mutations in genes for nanophthalmos.

The British journal of ophthalmology
2024

Myelin regulatory factor ( Myrf ) is a critical early regulator of retinal pigment epithelial development.

bioRxiv : the preprint server for biology
2024

Sclerectomy Reverses Nanophthalmic Optic Neuropathy.

Case reports in ophthalmology
2024

Surgical Approaches to Serous Retinal Detachment With Retina-Lens Touch in Eyes With Nanophthalmos.

Journal of vitreoretinal diseases
2024

Insight into small eyes: a practical description from phenotypes presentations to the management.

International journal of ophthalmology
2024

Femtosecond LASER-Assisted Double Intraocular Lens Exchange in Nanophthalmic Eyes.

Case reports in ophthalmology
2024

Generation of the induced pluripotent stem cell line IOCVi001-A from a patient with the MFRP-related retinitis pigmentosa-nanophthalmos syndrome.

Stem cell research
2023

Topical brimonidine induced acute uveal effusion in a patient with nanophthalmos: a case report.

BMC ophthalmology
2023

Clinical update in nanophthalmos: Features, diseases and complications associated.

Archivos de la Sociedad Espanola de Oftalmologia
2023

A unique case of bilateral nanophthalmos and pigmentary retinal abnormality with unilateral angle closure glaucoma and optic disc pit.

BMC ophthalmology
2023

Anterior Scleral Thickness and Other Dimensions in Nanophthalmos by Swept-Source Optical Coherence Tomography: A Comparative Study.

Journal of clinical medicine
2024

Primary Transscleral Diode Laser Cyclophotocoagulation for Management of Glaucoma in Nanophthalmic Eyes.

Journal of glaucoma
2023

Pathogenic variants of MFRP and PRSS56 genes are major causes of nanophthalmos in Japanese patients.

Ophthalmic genetics
2023

Phenotypic consequences of a nanophthalmos-associated TMEM98 variant in human and mouse.

Scientific reports
2022

Posterior Microphthalmos Pigmentary Retinopathy Syndrome with Angle-Closure Glaucoma: A Case Report.

Journal of current ophthalmology
2023

Topiramate-Induced Aqueous Misdirection in a Nanophthalmic Eye.

Cureus
2023

Retinitis pigmentosa and nanophthalmos in a patient with attenuated Hunter's syndrome.

Documenta ophthalmologica. Advances in ophthalmology
2022

MFRP-Associated Retinopathy and Nanophthalmos in Two Irish Probands: A Case Report.

Case reports in ophthalmology
2022

Clinical Outcomes of Piggybacking a One-Piece IOL With a Three-Piece IOL in Eyes With Nanophthalmos.

Journal of refractive surgery (Thorofare, N.J. : 1995)
2022

Case Report: De novo variant in myelin regulatory factor in a Chinese child with 46,XY disorder/difference of sex development, cardiac and urogenital anomalies, and short stature.

Frontiers in pediatrics
2022

Clinical presentation and treatment outcomes of an algorithmic approach to uveal effusion syndrome.

Indian journal of ophthalmology
2022

[A family with nanophthalmos caused by a TMEM98 gene variant].

[Zhonghua yan ke za zhi] Chinese journal of ophthalmology
2022

Tunnel-floor entry continuous curvilinear capsulorhexis technique: Rhexis in a controlled and stable anterior chamber always.

Indian journal of ophthalmology
2022

Effect of Combined Surgery in Patients with Complex Nanophthalmos.

Journal of clinical medicine
2023

A Comparative Study on the Accuracy of IOL Calculation Formulas in Nanophthalmos and Relative Anterior Microphthalmos.

American journal of ophthalmology
2022

MYRF: A New Regulator of Cardiac and Early Gonadal Development-Insights from Single Cell RNA Sequencing Analysis.

Journal of clinical medicine
2022

Clinical and Genetic Analysis of Retinitis Pigmentosa with Primary Angle Closure Glaucoma in the Chinese Population.

Current eye research
2023

MFRP variant results in nanophthalmos, retinitis pigmentosa, variability in foveal avascular zone.

Ophthalmic genetics
2022

Treatment of Nanophthalmos Cataracts: Surgery and Complications.

Seminars in ophthalmology
2022

A report on a series of nanophthalmos with histopathology and immunohistochemistry analyses using light microscopy.

Indian journal of ophthalmology
2022

Commentary: Clinical and biometric characteristics of pediatric eyes with nanophthalmos.

Indian journal of ophthalmology
2022

Commentary: Short eyes and bigger challenges - Growing evidence in the management of pediatric nanophthalmos.

Indian journal of ophthalmology
2022

Comparison of clinical and biometric characteristics between nanophthalmic children and age-matched controls.

Indian journal of ophthalmology
2023

Outcomes of combined phacoemulsification, anterior vitrectomy, and sclerectomy in nanophthalmic eyes with glaucoma.

Eye (London, England)
2023

Heterozygous variants c.781G>A and c.1066dup of serine protease 56 cause familial nanophthalmos by impairing serine-type endopeptidase activity.

The British journal of ophthalmology
2022

Diverse clinical manifestations and intrafamilial variability due to an inherited recurrent MYRF variant.

American journal of medical genetics. Part A
2022

Extensive serous ciliochoroidal detachments and macular subretinal and intraretinal fluid following laser peripheral iridotomy.

American journal of ophthalmology case reports
2022

Treatment of Nanophthalmos-Related Uveal Effusion with Two- vs. Four-Quadrant Partial-Thickness Sclerectomy and Sclerotomy Surgery.

Turkish journal of ophthalmology
2022

Femtosecond laser-assisted refractive lens exchange and piggyback intraocular lens implantation in nanophthalmos: A case report.

Asian journal of surgery
2022

Prevalence of complications in eyes with nanophthalmos or microphthalmos: protocol for a systematic review and meta-analysis.

Systematic reviews
2021

Evaluation of MYRF as a candidate gene for primary angle closure glaucoma.

Molecular vision
2022

Phacoemulsification with double-in-bag intraocular lens implantation in nanophthalmic eyes with angle-closure glaucoma.

International ophthalmology
2022

Clinical spectrum of blunted foveal contour.

Therapeutic advances in ophthalmology
2022

[Clinical features of young inpatients with angle-closure glaucoma].

[Zhonghua yan ke za zhi] Chinese journal of ophthalmology
2021

Cataract Surgery in Short Eyes, Including Nanophthalmos: Visual Outcomes, Complications and Refractive Results.

Clinical ophthalmology (Auckland, N.Z.)
2021

Rapid resolution of severe exudation in uveal effusion syndrome with anti-vascular endothelial growth factor alone in a case of bilateral nanophthalmos: a case report.

Journal of medical case reports
2021

Glaucoma Syndromes: Insights into Glaucoma Genetics and Pathogenesis from Monogenic Syndromic Disorders.

Genes
2022

[Cataract surgery and the small eye: relative anterior microphthalmos, high hyperopia and nanophthalmos].

Der Ophthalmologe : Zeitschrift der Deutschen Ophthalmologischen Gesellschaft
2022

Foveal structure and visual function in nanophthalmos and posterior microphthalmos.

The British journal of ophthalmology
2023

NOVEL MFRP MUTATION WITH NANOPHTHALMOS, OPTIC DISK DRUSEN, AND PERIPHERAL RETINOSCHISIS IMAGED WITH ULTRA-WIDEFIELD OPTICAL COHERENCE TOMOGRAPHY.

Retinal cases &amp; brief reports
2021

Myelin regulatory factor deficiency is associated with the retinal photoreceptor defects in mice.

Visual neuroscience
2021

Etiologies and clinical characteristics of young patients with angle-closure glaucoma: a 15-year single-center retrospective study.

Graefe's archive for clinical and experimental ophthalmology = Albrecht von Graefes Archiv fur klinische und experimentelle Ophthalmologie
2021

Nanophthalmos: An Update on the Biological Parameters and Fundus Abnormalities.

Journal of ophthalmology
2021

Identification of MFRP and the secreted serine proteases PRSS56 and ADAMTS19 as part of a molecular network involved in ocular growth regulation.

PLoS genetics
2021

Nanophthalmos-Associated MYRF Gene Mutation Causes Ciliary Zonule Defects in Mice.

Investigative ophthalmology &amp; visual science
2021

MFRP-Related Nanophthalmos-Retinitis Pigmentosa-Foveoschisis-Optic Disc Drusen Syndrome.

Ophthalmic surgery, lasers &amp; imaging retina
2021

A novel proline substitution (Arg201Pro) in alpha helix 8 of TMEM98 causes autosomal dominant nanophthalmos-4, closed angle glaucoma and attenuated visual acuity.

Experimental eye research
2021

Comparing the Results of Vitrectomy and Sclerectomy in a Patient with Nanophthalmic Uveal Effusion Syndrome.

Medicina (Kaunas, Lithuania)
2021

Defining inclusion criteria and endpoints for clinical trials: a prospective cross-sectional study in CRB1-associated retinal dystrophies.

Acta ophthalmologica
2021

A comparative study on endothelial cell loss in nanophthalmic eyes undergoing cataract surgery by phacoemulsification.

Indian journal of ophthalmology
2020

Novel TMEM98, MFRP, PRSS56 variants in a large United States high hyperopia and nanophthalmos cohort.

Scientific reports
2021

Foveal structure in nanophthalmos and visual acuity.

International ophthalmology
2022

Goniosynechialysis combined with multiple surgeries for secondary glaucoma in nanophthalmos: A case report.

European journal of ophthalmology
2020

Bilateral implantation of +56 and +58 diopter custom-made intraocular lenses in patient with extreme nanophthalmos.

American journal of ophthalmology case reports
2020

Nanophthalmos patient with a THR518MET mutation in MYRF, a case report.

BMC ophthalmology
2021

Genotype-phenotype spectrum in isolated and syndromic nanophthalmos.

Acta ophthalmologica
2020

Morphological features of anterior segment: factors influencing intraocular pressure after cataract surgery in nanophthalmos.

Eye and vision (London, England)
2020

Posterior segment abnormalities in posterior microphthalmos.

American journal of ophthalmology case reports
2020

The Pathogenesis and Treatment of Complications in Nanophthalmos.

Journal of ophthalmology
2020

Nanophthalmos in children: morphometric and clinical characterization.

Journal of AAPOS : the official publication of the American Association for Pediatric Ophthalmology and Strabismus
2020

Unusual non-nanophthalmic uveal effusion syndrome with histologically normal scleral architecture: a case report.

BMC ophthalmology
2021

Clinical spectrum and treatment outcomes of patients with nanophthalmos.

Eye (London, England)
2020

Pseudodominant Nanophthalmos in a Roma Family Caused by a Novel PRSS56 Variant.

Journal of ophthalmology
2020

Choroidal vascularity index as an indicator of vascular status of choroid, in eyes with nanophthalmos.

Eye (London, England)
2020

The nanophthalmos protein TMEM98 inhibits MYRF self-cleavage and is required for eye size specification.

PLoS genetics
2020

Novel mutations in MFRP and PRSS56 are associated with posterior microphthalmos.

Ophthalmic genetics
2020

The genetic and clinical landscape of nanophthalmos and posterior microphthalmos in an Australian cohort.

Clinical genetics
2020

The majority of autosomal recessive nanophthalmos and posterior microphthalmia can be attributed to biallelic sequence and structural variants in MFRP and PRSS56.

Scientific reports
2019

Spontaneous malignant glaucoma: Case report and review of the literature.

Saudi journal of ophthalmology : official journal of the Saudi Ophthalmological Society
2019

Transscleral cyclophotocoagulation as primary management in a nanophthalmic eye with anterior uveitis and secondary mixed mechanism glaucoma.

BMJ case reports
2020

Efficacy of toric intraocular lens implantation with high corneal astigmatism within the United Kingdom's National Health Service.

Eye (London, England)
2019

Autosomal dominant nanophthalmos and high hyperopia associated with a C-terminal frameshift variant in MYRF.

Molecular vision
2019

Quadrantic vortex vein decompression with subretinal fluid drainage for manangement of Nanophthalmic choroidal effusions- a review of literature and case series.

BMC ophthalmology
2019

Serous macular detachment in nanophthalmos: A manifestation of pachychoroid spectrum.

American journal of ophthalmology case reports
2019

Detection of Clinically Relevant Genetic Variants in Chinese Patients With Nanophthalmos by Trio-Based Whole-Genome Sequencing Study.

Investigative ophthalmology &amp; visual science
2019

Missense Mutations in the Human Nanophthalmos Gene TMEM98 Cause Retinal Defects in the Mouse.

Investigative ophthalmology &amp; visual science
2019

Anterior Segment Features in Nanophthalmos With Secondary Chronic Angle Closure Glaucoma: An Ultrasound Biomicroscopy Study.

Investigative ophthalmology &amp; visual science
2020

Unusual rapid resolution of postsclerectomy exudative retinal detachment with topical NSAIDs therapy in a case of nanophthalmos.

The Journal of international medical research
2019

Variants in myelin regulatory factor (MYRF) cause autosomal dominant and syndromic nanophthalmos in humans and retinal degeneration in mice.

PLoS genetics
2018

Nanophthalmos-Retinitis Pigmentosa-Foveoschisis-Optic Disc Drusen Syndrome (MFRP).

Ophthalmology. Retina
2019

Extensive circumferential partial-thickness sclerectomy in eyes with extreme nanophthalmos and spontaneous uveal effusion.

The British journal of ophthalmology
2019

Consultation Section: Refractive. Unhappy patient after uneventful refractive lens exchange in nanophthalmos: March consultation #1.

Journal of cataract and refractive surgery
2019

A new rhodopsin R135W mutation induces endoplasmic reticulum stress and apoptosis in retinal pigment epithelial cells.

Journal of cellular physiology
2020

Familial Nanophthalmos Presenting with Spontaneous Uveal Effusion Syndrome.

Ocular immunology and inflammation
2019

[Glaucoma and nanophthalmos].

Der Ophthalmologe : Zeitschrift der Deutschen Ophthalmologischen Gesellschaft
2019

Absence of the foveal avascular zone in a nanophthalmic child revealed by optical coherence tomography angiography.

American journal of ophthalmology case reports
2018

Clinical features of posterior microphthalmic and nanophthalmic eyes.

International journal of ophthalmology
2018

Association of Genes implicated in primary angle-closure Glaucoma and the ocular biometric parameters of anterior chamber depth and axial length in a northern Chinese population.

BMC ophthalmology
2019

The role of corneo-scleral junction in soft contact lens fitting: Case report on nanophthalmos.

Contact lens &amp; anterior eye : the journal of the British Contact Lens Association
2019

Unmeasurable small size superficial and deep foveal avascular zone in nanophthalmos: the Collaborative Nanophthalmos OCTA Study.

The British journal of ophthalmology
2019

Foveal avascular zone area measurements with optical coherence tomography angiography in patients with nanophthalmos.

Eye (London, England)
2018

Prophylactic anterior vitrectomy during cataract surgery in eyes at increased risk for aqueous misdirection.

American journal of ophthalmology case reports
2018

Nanophthalmos: A Review of the Clinical Spectrum and Genetics.

Journal of ophthalmology
2018

Research progress on human genes involved in the pathogenesis of glaucoma (Review).

Molecular medicine reports
2018

The treatment of malignant glaucoma in nanophthalmos: a case report.

BMC ophthalmology
2018

Genetic investigation of 93 families with microphthalmia or posterior microphthalmos.

Clinical genetics
2019

Successful recovery from misdirection syndrome in nanophthalmic eyes by performing an anterior vitrectomy through the anterior chamber.

International ophthalmology
2017

Medical therapy for bilateral uveal effusion syndrome in nanophthalmos.

Canadian journal of ophthalmology. Journal canadien d'ophtalmologie
2017

Gene Therapy Restores Mfrp and Corrects Axial Eye Length.

Scientific reports
2017

Refractive lens exchange and piggyback intraocular lens implantation in nanophthalmos: Visual and structural outcomes.

Journal of cataract and refractive surgery
2017

A Randomized Controlled Trial Comparing Outcomes of Cataract Surgery in Nanophthalmos With and Without Prophylactic Sclerostomy.

American journal of ophthalmology
2018

Combined 23-G Pars Plana Vitrectomy and Lensectomy in the Management of Glaucoma Associated with Nanophthalmos.

Ophthalmic research
2017

Vascularisation of the anterior lens capsule in an eye with excellent visual acuity.

BMJ case reports
2016

Contact lenses for visual rehabilitation in Bilateral Nanophthalmos with Retinal Dystrophy- A case report.

Nepalese journal of ophthalmology : a biannual peer-reviewed academic journal of the Nepal Ophthalmic Society : NEPJOPH
2017

Choroidal thickness findings in two siblings with nanophthalmos by swept source-OCT: a case report.

BMC research notes
2016

Spectrum of Angle Closure, Uveal Effusion Syndrome, and Nanophthalmos.

Journal of current glaucoma practice
2016

Scleral resection in chronic central serous chorioretinopathy complicated by exudative retinal detachment.

Eye and vision (London, England)
2016

Surgical outcomes of congenital and developmental cataracts in Japan.

Japanese journal of ophthalmology
2015

Outcomes of Coaxial Micro-incision Phacoemulsification in Nanophthalmic Eyes: Report of Retrospective Case Series.

Eye science
2016

A Patient with Keratoconus, Nanophthalmos, Lipodermoids, and Pigmentary Retinopathy.

Ophthalmic genetics
2016

[Uveal effusion syndrome – a case study].

Klinika oczna
2016

BESTROPHINOPATHY: A Spectrum of Ocular Abnormalities Caused by the c.614T>C Mutation in the BEST1 Gene.

Retina (Philadelphia, Pa.)
2016

Identification of MFRP Mutations in Chinese Families with High Hyperopia.

Optometry and vision science : official publication of the American Academy of Optometry
2015

Contribution of Electronic Medical Records to the Management of Rare Diseases.

BioMed research international
2016

High-hyperopia database, part I: clinical characterisation including morphometric (biometric) differentiation of posterior microphthalmos from nanophthalmos.

Eye (London, England)
2015

Novel TMEM98 mutations in pedigrees with autosomal dominant nanophthalmos.

Molecular vision
2016

Cataract surgery in patients with nanophthalmos: results and complications.

European journal of ophthalmology
2015

RETINAL AND CHOROIDAL CHANGES OF NANOPHTHALMIC EYES WITH AND WITHOUT SECONDARY GLAUCOMA.

Retina (Philadelphia, Pa.)
2015

Nanophthalmos and hemiretinal vein occlusion: A case report.

Saudi journal of ophthalmology : official journal of the Saudi Ophthalmological Society
Ver todos os 203 no EuropePMC

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Doenças relacionadas

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Referências e fontes

Bases de dados externas citadas neste artigo

Publicações científicas

Artigos indexados no PubMed ligados a esta doença no grafo RarasNet — título, periódico e PMID direto da fonte, sem intermediação de IA.

  1. Splicing variants in MYRF cause partial loss of function in the retinal pigment epithelium leading to nanophthalmos.
    JCI insight· 2026· PMID 41746734mais citado
  2. Corrigendum to "Medical management of post-phacoemulsification uveal effusion in nanophthalmos: A case report [Am. J. Ophthalmol. Case Rep. (41), March 2026, 102507].
    American journal of ophthalmology case reports· 2026· PMID 41695085mais citado
  3. Medical management of post-phacoemulsification uveal effusion in nanophthalmos: A case report.
    American journal of ophthalmology case reports· 2026· PMID 41561664mais citado
  4. Multimodal imaging in nanophthalmos.
    Eye (London, England)· 2026· PMID 41772073mais citado
  5. MYRF gene mutation leading to coronary artery anomaly combined with 46,XY sex development disorder, a case report and literature review.
    BMC pediatrics· 2025· PMID 40819034mais citado
  6. Modular surgical approach for angle-closure glaucoma secondary to nanophthalmos.
    Int J Ophthalmol· 2026· PMID 41924377recente

Bases de dados e fontes oficiais

Identificadores e referências canônicas usadas para montar este verbete.

  1. ORPHA:35612(Orphanet)
  2. MONDO:0005514(MONDO)
  3. GARD:16637(GARD (NIH))
  4. Variantes catalogadas(ClinVar)
  5. Busca completa no PubMed(PubMed)
  6. Q1557239(Wikidata)

Dados compilados pelo RarasNet a partir de fontes abertas (Orphanet, OMIM, MONDO, PubMed/EuropePMC, ClinicalTrials.gov, DATASUS, PCDT/MS). Este conteúdo é informativo e não substitui avaliação médica.

Conteúdo mantido por Agente Raras · Médicos e pesquisadores podem colaborar

Compêndio · Raras BR

Nanoftalmia

ORPHA:35612 · MONDO:0005514
Prevalência
Unknown
Herança
Autosomal dominant, Autosomal recessive, Not applicable
CID-10
Q11.2 · Microftalmia
CID-11
Início
Infancy, Neonatal
Prevalência
0.0 (Worldwide)
MedGen
UMLS
C0026010
EuropePMC
Wikidata
Papers 10a
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