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Síndrome Bazex-Dupre-Christol
ORPHA:113CID-10 · L98.8CID-11 · LD27.5OMIM 301845DOENÇA RARA

A síndrome de Bazex-Dupre-Christol é uma doença de pele hereditária rara, com uma maior chance de desenvolver cânceres de pele basocelulares de início precoce.

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Introdução

O que você precisa saber de cara

📋

A síndrome de Bazex-Dupre-Christol é uma doença de pele hereditária rara, com uma maior chance de desenvolver cânceres de pele basocelulares de início precoce.

Publicações científicas
35 artigos
Último publicado: 2025 May-Jun

Escala de raridade

CLASSIFICAÇÃO ORPHANET · BRASIL 2024
<1 / 1 000 000
Ultra-rara
<1/50k
Muito rara
1/20k
Rara
1/10k
Pouco freq.
1/5k
Incomum
1/2k
Prevalência
0.0
Worldwide
Casos conhecidos
143
pacientes catalogados
Início
Infancy
+ neonatal
🏥
SUS: Sem cobertura SUSScore: 0%
CID-10: L98.8
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Entender a doença

Do básico ao detalhe, leia no seu ritmo

Preparando trilha educativa...

Sinais e sintomas

O que aparece no corpo e com que frequência cada sintoma acontece

Partes do corpo afetadas

🧬
Pele e cabelo
15 sintomas
😀
Face
3 sintomas
👁️
Olhos
2 sintomas
🦴
Ossos e articulações
2 sintomas
👂
Ouvidos
1 sintomas
🫁
Pulmão
1 sintomas

+ 19 sintomas em outras categorias

Características mais comuns

90%prev.
Cabelos grosseiros
Muito frequente (99-80%)
55%prev.
Cílios esparsos ou ausentes
Frequente (79-30%)
55%prev.
Milia
Frequente (79-30%)
55%prev.
Sobrancelha esparsa
Frequente (79-30%)
55%prev.
Nódulo subcutâneo
Frequente (79-30%)
55%prev.
Carcinoma basocelular
Frequente (79-30%)
45sintomas
Muito frequente (1)
Frequente (9)
Ocasional (8)
Sem dados (27)

Os sintomas variam de pessoa para pessoa. Abaixo estão as 45 características clínicas mais associadas, ordenadas por frequência.

Cabelos grosseirosCoarse hair
Muito frequente (99-80%)90%
Cílios esparsos ou ausentesSparse or absent eyelashes
Frequente (79-30%)55%
Milia
Frequente (79-30%)55%
Sobrancelha esparsaSparse eyebrow
Frequente (79-30%)55%
Nódulo subcutâneoSubcutaneous nodule
Frequente (79-30%)55%

Linha do tempo da pesquisa

Publicações por ano — veja quando o interesse científico cresceu
Anos de pesquisa1desde 2025
Total histórico35PubMed
Últimos 10 anos47publicações
Pico20177 papers
Linha do tempo
2025Hoje · 2026📈 2017Ano de pico🧪 2019Primeiro ensaio clínico
Publicações por ano (últimos 10 anos)

Encontrou um erro ou informação desatualizada? Sugira uma correção →

Genética e causas

O que está alterado no DNA e como passa nas famílias

🧬

Nenhum gene associado encontrado

Os dados genéticos desta condição ainda estão sendo catalogados.

Diagnóstico

Os sinais que médicos procuram e os exames que confirmam

Carregando...

Tratamento e manejo

Remédios, cuidados de apoio e o que precisa acompanhar

Carregando informações de tratamento...

Onde tratar no SUS

Hospitais de referência no Brasil e o protocolo oficial do SUS (PCDT)

🇧🇷 Atendimento SUS — Síndrome Bazex-Dupre-Christol

🗺️

Selecione um estado ou use sua localização para ver resultados.

Dados de DATASUS/CNES, SBGM, ABNeuro e Ministério da Saúde. Sempre confirme a disponibilidade diretamente com o estabelecimento.

Pesquisa ativa

Ensaios clínicos abertos e novidades científicas recentes

Pesquisa e ensaios clínicos

Nenhum ensaio clínico registrado para esta condição.

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Publicações mais relevantes

Timeline de publicações
14 papers (10 anos)
#1

A 12-Year-Old Female With Facial Bumps, Body Pits, and Coiled Scalp Hair.

Pediatric dermatology2025

A 12-year-old female presented with multiple milia and skin-coloured papules over face and neck, follicular atrophoderma and hypotrichosis. Family history of similar complaints present in mother and maternal aunt. Biopsy from the skin-coloured papule revealed trichoepithelioma. Multiple milia, hypotrichosis and follicular atrophoderma favour the diagnosis of Bazex-Dupre-Christol syndrome (BDCS) which is an X-linked dominant genodermatosis with BCCs developing later in life. Other conditions with multiple BCCs and milia like Gorlin syndrome, Oley syndrome and Rombo syndrome should be differentiated. Follicular atrophoderma and hypotrichosis with X-linked dominant inheritance favour the diagnosis of BDCS. Management should focus on identifying BCCs at the earliest and genetic counselling.

#2

Early onset basal cell carcinoma: Consider Bazex-Dupré-Christol syndrome.

European journal of medical genetics2025 Jun

Bazex-Dupré-Christol syndrome is a rare genetic condition characterised by basal cell carcinomas, follicular atrophoderma and hypotrichosis. Until recently, the molecular basis of the condition was largely unknown. A recent study has identified a section of duplicated DNA on the X chromosome of those with the condition which appears to be the underlying cause of the syndrome. This case study looks at a family with five affected members over three generations. They had been diagnosed with the syndrome in early life and had previously undergone genetic testing with no cause being found. The index patient within this family has now been identified as having the same duplication as those tested in the initial study.

#3

A rare case of acrokeratosis paraneoplastica (Bazex syndrome) and a literature review.

The Journal of international medical research2025 Feb

Acrokeratosis paraneoplastica is a rare and obligate paraneoplastic dermatosis most commonly associated with squamous cell carcinoma of the upper aerodigestive tract and lung. It has also been linked to adenocarcinomas of the lung, colon, and stomach. However, reports of its association with esophageal adenocarcinoma are exceedingly rare, with only one documented case to date. This condition primarily affects middle-aged White men, with limited cases reported in women. Moreover, its occurrence in the Chinese population is uncommon. We herein present a case of acrokeratosis paraneoplastica in a Chinese woman with primary esophageal adenocarcinoma, along with a review of the relevant literature. To our knowledge, this is the first documented instance of paraneoplastic acrokeratosis associated with esophageal adenocarcinoma in a woman.

#4

Whole genome sequencing revealing Xq26.1 intergenic duplications associated with Bazex-Dupré-Christol syndrome in a Chinese family.

Journal of the European Academy of Dermatology and Venereology : JEADV2025 Jan
#5

Acrokeratosis paraneoplastica (Basex syndrome) with trachyonychia preceding the diagnosis of squamous cell carcinoma of the lung.

Dermatology online journal2024 Apr 15

Acrokeratosis paraneoplastica (Basex syndrome) is a rare paraneoplastic condition hallmarked by psoriasiform lesion development on acral surfaces, most often related to an underlying squamous cell carcinoma. Patients may also present with nail plate changes. Successful management of this condition can be accomplished by treating the underlying malignancy.

Publicações recentes

Ver todas no PubMed

📚 EuropePMC25 artigos no totalmostrando 45

2025

A 12-Year-Old Female With Facial Bumps, Body Pits, and Coiled Scalp Hair.

Pediatric dermatology
2025

Early onset basal cell carcinoma: Consider Bazex-Dupré-Christol syndrome.

European journal of medical genetics
2025

A rare case of acrokeratosis paraneoplastica (Bazex syndrome) and a literature review.

The Journal of international medical research
2024

Acrokeratosis paraneoplastica (Basex syndrome) with trachyonychia preceding the diagnosis of squamous cell carcinoma of the lung.

Dermatology online journal
2025

Whole genome sequencing revealing Xq26.1 intergenic duplications associated with Bazex-Dupré-Christol syndrome in a Chinese family.

Journal of the European Academy of Dermatology and Venereology : JEADV
2024

[Bazex syndrome: a rare paraneoplastic disease].

Medicina
2024

[Translated article] Complete Resolution of Bazex Syndrome After Surgical Treatment of Squamous Cell Carcinoma of the Larynx.

Actas dermo-sifiliograficas
2023

Acrokeratosis paraneoplastica in tonsillar carcinoma.

European journal of dermatology : EJD
2023

Bazex Syndrome in Acute Myeloid Leukemia.

Internal medicine (Tokyo, Japan)
2022

A case of Bazex syndrome with type 2 immune response.

European journal of dermatology : EJD
2022

Germline intergenic duplications at Xq26.1 underlie Bazex-Dupré-Christol basal cell carcinoma susceptibility syndrome.

The British journal of dermatology
2022

Advanced basal cell carcinoma: What dermatologists need to know about diagnosis.

Journal of the American Academy of Dermatology
2021

Pili Torti: A Feature of Numerous Congenital and Acquired Conditions.

Journal of clinical medicine
2022

A Case of Bazex Syndrome.

Internal medicine (Tokyo, Japan)
2021

ARP-T1-associated Bazex-Dupré-Christol syndrome is an inherited basal cell cancer with ciliary defects characteristic of ciliopathies.

Communications biology
2020

Acrokeratosis paraneoplastica (Bazex syndrome) as the presenting sign of pancreatic adenocarcinoma.

BMJ case reports
2020

An Unconventional Presentation of Multiple Myeloma: Bazex Syndrome.

Turkish journal of haematology : official journal of Turkish Society of Haematology
2020

[Detecting skin cancer: paraneoplastic skin diseases].

Der Internist
2021

Paraneoplastic acrokeratosis (Bazex syndrome).

Medicina clinica
2020

Paraneoplastic Remitting Seronegative Symmetrical Synovitis with Pitting Edema Syndrome Should Be Treated with Low-dose Prednisolone During Pembrolizumab Therapy.

Internal medicine (Tokyo, Japan)
2020

Acrokeratosis paraneoplastica (Bazex syndrome) with bullous lesions.

Indian journal of dermatology, venereology and leprology
2019

Synchronous Occurrence of Bazex Syndrome and Remitting Seronegative Symmetrical Synovitis with Pitting Edema Syndrome in a Patient with Lung Cancer.

Internal medicine (Tokyo, Japan)
2019

Unilateral Anhidrosis With Ipsilateral Basal Cell Carcinomas.

Dermatologic surgery : official publication for American Society for Dermatologic Surgery [et al.]
2019

Skin Cancer Associated Genodermatoses: A Literature Review.

Acta dermato-venereologica
2018

[What's new in research?].

Annales de dermatologie et de venereologie
2018

Bazex-Dupré-Christol syndrome: First report in an Indian family.

Indian journal of dermatology, venereology and leprology
2018

Bazex syndrome in a patient with head and neck malignancy.

JAAPA : official journal of the American Academy of Physician Assistants
2018

Bazex-Dupré-Christol syndrome: review of clinical and molecular aspects.

International journal of dermatology
2017

Is it just a psoriasiform dermatitis?

Dermatology online journal
2017

Acrokeratosis paraneoplastica (Bazex syndrome).

Ear, nose, &amp; throat journal
2017

Paraneoplastic acrokeratosis (Bazex syndrome): unusual association with in situ follicular lymphoma and response to acitretin.

Cutis
2019

[Hands and feet lesions].

La Revue de medecine interne
2017

Mutations in ACTRT1 and its enhancer RNA elements lead to aberrant activation of Hedgehog signaling in inherited and sporadic basal cell carcinomas.

Nature medicine
2017

Acrokeratosis paraneoplastica (Bazex syndrome) - a systematic review on risk factors, diagnosis, prognosis and management.

Journal of the European Academy of Dermatology and Venereology : JEADV
2017

An unusual cause for a psoriasiform dermatosis.

Clinical and experimental dermatology
2016

The cutaneous manifestations of gastrointestinal malignancy.

Seminars in oncology
2016

Diagnosis and Management of Hereditary Basal Cell Skin Cancer.

Recent results in cancer research. Fortschritte der Krebsforschung. Progres dans les recherches sur le cancer
2016

Acrokeratosis paraneoplastica (Bazex syndrome) associated with metastatic cutaneous squamous cell carcinoma.

Internal medicine journal
2016

Case Report: Bazex Syndrome Associated With Pulmonary Adenocarcinoma.

Medicine
2016

Acitretin amelioration of Acrokeratosis Paraneoplastica (Bazex Syndrome) in cases of incurable squamous cell carcinoma of the hypopharynx.

Dermatology online journal
2015

Psoriasiform dermatitis and hepatocellular carcinoma: a new case of Bazex syndrome.

Giornale italiano di dermatologia e venereologia : organo ufficiale, Societa italiana di dermatologia e sifilografia
2015

[Bazex-Dupré-Christol syndrome: Case series].

Archivos argentinos de pediatria
2015

Borderline cognitive level in a family with Bazex-Dupré-Christol syndrome.

American journal of medical genetics. Part A
2015

Acute Onset of Acrokeratosis Paraneoplastica (Bazex Syndrome).

JAMA dermatology
2015

[Acrokeratosis paraneoplastica Bazex 6 years prior to diagnosis of gastric cancer].

Der Hautarzt; Zeitschrift fur Dermatologie, Venerologie, und verwandte Gebiete

Associações

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Comunidades

Grupos ativos de quem convive com esta doença aqui no Raras

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Doenças relacionadas

Doenças com sintomas parecidos — ajudam quem ainda está buscando diagnóstico

Referências e fontes

Bases de dados externas citadas neste artigo

Publicações científicas

Artigos indexados no PubMed ligados a esta doença no grafo RarasNet — título, periódico e PMID direto da fonte, sem intermediação de IA.

  1. A 12-Year-Old Female With Facial Bumps, Body Pits, and Coiled Scalp Hair.
    Pediatric dermatology· 2025· PMID 40051258mais citado
  2. Early onset basal cell carcinoma: Consider Bazex-Dupr&#xe9;-Christol syndrome.
    European journal of medical genetics· 2025· PMID 40015599mais citado
  3. A rare case of acrokeratosis paraneoplastica (Bazex syndrome) and a literature review.
    The Journal of international medical research· 2025· PMID 40012420mais citado
  4. Whole genome sequencing revealing Xq26.1 intergenic duplications associated with Bazex-Dupr&#xe9;-Christol syndrome in a Chinese family.
    Journal of the European Academy of Dermatology and Venereology : JEADV· 2025· PMID 38713094mais citado
  5. Acrokeratosis paraneoplastica (Basex syndrome) with trachyonychia preceding the diagnosis of squamous cell carcinoma of the lung.
    Dermatology online journal· 2024· PMID 38959920mais citado
  6. Germline intergenic duplications at Xq26.1 underlie Bazex-Dupré-Christol basal cell carcinoma susceptibility syndrome.
    Br J Dermatol· 2022· PMID 35986704recente
  7. Advanced basal cell carcinoma: What dermatologists need to know about diagnosis.
    J Am Acad Dermatol· 2022· PMID 35577405recente

Bases de dados e fontes oficiais

Identificadores e referências canônicas usadas para montar este verbete.

  1. ORPHA:113(Orphanet)
  2. OMIM OMIM:301845(OMIM)
  3. MONDO:0010535(MONDO)
  4. GARD:838(GARD (NIH))
  5. Busca completa no PubMed(PubMed)
  6. Q4875174(Wikidata)

Dados compilados pelo RarasNet a partir de fontes abertas (Orphanet, OMIM, MONDO, PubMed/EuropePMC, ClinicalTrials.gov, DATASUS, PCDT/MS). Este conteúdo é informativo e não substitui avaliação médica.

Conteúdo mantido por Agente Raras · Médicos e pesquisadores podem colaborar

Síndrome Bazex-Dupre-Christol
Compêndio · Raras BR

Síndrome Bazex-Dupre-Christol

ORPHA:113 · MONDO:0010535
Prevalência
<1 / 1 000 000
Casos
143 casos conhecidos
Herança
X-linked dominant
CID-10
L98.8 · Outras afecções especificadas da pele e do tecido subcutâneo
CID-11
Início
Infancy, Neonatal
Prevalência
0.0 (Worldwide)
MedGen
UMLS
C0346104
EuropePMC
Wikidata
Papers 10a
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