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Má absorção de glicose-galactose
ORPHA:35710CID-10 · E74.3CID-11 · 5C61.0OMIM 606824DOENÇA RARA

A má absorção de glicose-galactose (GGM) é uma doença metabólica genética muito rara e que pode ser fatal. Ela é caracterizada pela dificuldade do corpo em absorver a glicose e a galactose, o que causa diarreia aquosa grave e desidratação. Os sintomas aparecem logo após o nascimento.

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Introdução

O que você precisa saber de cara

📋

A má absorção de glicose-galactose (GGM) é uma doença metabólica genética muito rara e que pode ser fatal. Ela é caracterizada pela dificuldade do corpo em absorver a glicose e a galactose, o que causa diarreia aquosa grave e desidratação. Os sintomas aparecem logo após o nascimento.

Publicações científicas
159 artigos
Último publicado: 2026 Jan 15

Escala de raridade

CLASSIFICAÇÃO ORPHANET · BRASIL 2024
Unknown
Ultra-rara
<1/50k
Muito rara
1/20k
Rara
1/10k
Pouco freq.
1/5k
Incomum
1/2k
Prevalência
0.0
Worldwide
Início
Infancy
+ neonatal
🏥
SUS: Cobertura mínimaScore: 15%
CID-10: E74.3
🇧🇷Dados SUS / DATASUS
PROCEDIMENTOS SIGTAP (6)
0202010279
Dosagem de aminoácidos (erros inatos)metabolic_test
0202010295
Dosagem de ácidos orgânicos na urinagenetic_test
0202010490
Teste de triagem para erros inatos do metabolismonewborn_screening
0202010694
Sequenciamento completo do exoma (WES)rehabilitation
0202080013
Teste do pezinho (triagem neonatal)
0301070040
Atendimento em reabilitação — doenças raras
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Entender a doença

Do básico ao detalhe, leia no seu ritmo

Preparando trilha educativa...

Sinais e sintomas

O que aparece no corpo e com que frequência cada sintoma acontece

Partes do corpo afetadas

🫃
Digestivo
6 sintomas
🫘
Rins
3 sintomas
📏
Crescimento
2 sintomas
🧠
Neurológico
1 sintomas

+ 11 sintomas em outras categorias

Características mais comuns

100%prev.
Desidratação hipertônica
Frequência: 2/2
100%prev.
Diarreia crônica
Frequência: 2/2
100%prev.
Início neonatal
Frequência: 2/2
90%prev.
Diarreia
Muito frequente (99-80%)
90%prev.
Diarreia osmótica
Muito frequente (99-80%)
90%prev.
Perda de peso
Muito frequente (99-80%)
23sintomas
Muito frequente (8)
Frequente (3)
Ocasional (5)
Muito raro (2)
Sem dados (5)

Os sintomas variam de pessoa para pessoa. Abaixo estão as 23 características clínicas mais associadas, ordenadas por frequência.

Desidratação hipertônicaHypertonic dehydration
Frequência: 2/2100%
Diarreia crônicaChronic diarrhea
Frequência: 2/2100%
Início neonatalNeonatal onset
Frequência: 2/2100%
DiarreiaDiarrhea
Muito frequente (99-80%)90%
Diarreia osmóticaOsmotic diarrhea
Muito frequente (99-80%)90%

Linha do tempo da pesquisa

Publicações por ano — veja quando o interesse científico cresceu
Anos de pesquisa1desde 2026
Total histórico159PubMed
Últimos 10 anos53publicações
Pico20178 papers
Linha do tempo
2026Hoje · 2026🧪 1999Primeiro ensaio clínico📈 2017Ano de pico
Publicações por ano (últimos 10 anos)

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Genética e causas

O que está alterado no DNA e como passa nas famílias

Genes associados

1 gene identificado com associação a esta condição. Padrão de herança: Autosomal recessive.

SLC5A1Sodium/glucose cotransporter 1Disease-causing germline mutation(s) (loss of function) inTolerante
FUNÇÃO

Electrogenic Na(+)-coupled sugar symporter that actively transports D-glucose or D-galactose at the plasma membrane, with a Na(+) to sugar coupling ratio of 2:1. Transporter activity is driven by a transmembrane Na(+) electrochemical gradient set by the Na(+)/K(+) pump (PubMed:20980548, PubMed:34880492, PubMed:35077764, PubMed:8563765, PubMed:37217492). Has a primary role in the transport of dietary monosaccharides from enterocytes to blood. Responsible for the absorption of D-glucose or D-galac

LOCALIZAÇÃO

Apical cell membrane

VIAS BIOLÓGICAS (2)
Cellular hexose transportIntestinal hexose absorption
MECANISMO DE DOENÇA

Congenital glucose/galactose malabsorption

Intestinal monosaccharide transporter deficiency. It is an autosomal recessive disorder manifesting itself within the first weeks of life. It is characterized by severe diarrhea and dehydration which are usually fatal unless glucose and galactose are eliminated from the diet.

EXPRESSÃO TECIDUAL(Tecido-específico)
Intestino delgado
97.9 TPM
Coração - Ventrículo esquerdo
45.4 TPM
Coração - Átrio
24.0 TPM
Glândula salivar
23.1 TPM
Skin Sun Exposed Lower leg
22.4 TPM
OUTRAS DOENÇAS (1)
glucose-galactose malabsorption
HGNC:11036UniProt:P13866

Variantes genéticas (ClinVar)

79 variantes patogênicas registradas no ClinVar.

🧬 SLC5A1: NM_000343.4(SLC5A1):c.1613_1614insTTTTTTTTTTTTTTTTTTTTNNNNNNNNNNGTCTCGATCTCCTGACCTCGTGATCCGCCCGCCTCGGCCTCCCAAAGTGCTGGGATTACAGGCGTGAGCCACCGCCATTTCTTT (p.Phe538_Ile539insPhePhePhePhePhePheXaaXaaXaaXaaSerArgSerProAspLeuValIleArgProProArgProProLysValLeuGlyLeuGlnAlaTer) ()
🧬 SLC5A1: NM_000343.4(SLC5A1):c.1566del (p.Cys522fs) ()
🧬 SLC5A1: NM_000343.4(SLC5A1):c.1065C>A (p.Cys355Ter) ()
🧬 SLC5A1: NM_000343.4(SLC5A1):c.1495C>T (p.Arg499Cys) ()
🧬 SLC5A1: NM_000343.4(SLC5A1):c.664+1G>A ()
Ver todas no ClinVar

Classificação de variantes (ClinVar)

Distribuição de 490 variantes classificadas pelo ClinVar.

49
49
392
Patogênica (10.0%)
VUS (10.0%)
Benigna (80.0%)
VARIANTES MAIS SIGNIFICATIVAS
SLC5A1: NM_000343.4(SLC5A1):c.1613_1614insTTTTTTTTTTTTTTTTTTTTNNNNNNNNNNGTCTCGATCTCCTGAC... [Pathogenic]
SLC5A1: NM_000343.4(SLC5A1):c.1566del (p.Cys522fs) [Pathogenic]
SLC5A1: NM_000343.4(SLC5A1):c.14C>T (p.Thr5Ile) [Uncertain significance]
SLC5A1: NM_000343.4(SLC5A1):c.1334A>G (p.Gln445Arg) [Uncertain significance]
SLC5A1: NM_000343.4(SLC5A1):c.616T>C (p.Leu206=) [Likely benign]

Diagnóstico

Os sinais que médicos procuram e os exames que confirmam

Carregando...

Tratamento e manejo

Remédios, cuidados de apoio e o que precisa acompanhar

Pipeline de tratamentos
Pipeline regulatório — de medicamentos já aprovados a drogas em pesquisa exploratória.
·Pré-clínico2
Medicamentos catalogadosEnsaios clínicos· 0 medicamentos · 2 ensaios
Carregando informações de tratamento...

Onde tratar no SUS

Hospitais de referência no Brasil e o protocolo oficial do SUS (PCDT)

🇧🇷 Atendimento SUS — Má absorção de glicose-galactose

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Selecione um estado ou use sua localização para ver resultados.

Dados de DATASUS/CNES, SBGM, ABNeuro e Ministério da Saúde. Sempre confirme a disponibilidade diretamente com o estabelecimento.

Pesquisa ativa

Ensaios clínicos abertos e novidades científicas recentes

Pesquisa e ensaios clínicos

15 ensaios clínicos encontrados.

Distribuição por fase
Ver todos no ClinicalTrials.gov
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Publicações mais relevantes

Timeline de publicações
43 papers (10 anos)
#1

Congenital glucose-galactose malabsorption: An unusual cause of chronic diarrhea in infancy.

Revista de gastroenterologia de Mexico (English)2026 Jan 15
#2

Renal glucosuria in children.

World journal of clinical pediatrics2025 Mar 09

The kidneys play a critical role in maintaining glucose homeostasis. Under normal renal tubular function, most of the glucose filtered from the glomeruli is reabsorbed in the proximal tubules, leaving only trace amounts in the urine. Glycosuria can occur as a symptom of generalized proximal tubular dysfunction or when the reabsorption threshold is exceeded or the glucose threshold is reduced, as seen in familial renal glycosuria (FRG). FRG is characterized by persistent glycosuria despite normal blood glucose levels and tubular function and is primarily associated with mutations in the sodium/glucose cotransporter 5A2 gene, which encodes the sodium-glucose cotransporter (SGLT) 2. Inhibiting SGLTs has been proposed as a novel treatment strategy for diabetes, and since FRG is often considered an asymptomatic and benign condition, it has inspired preclinical and clinical studies using SGLT2 inhibitors in type 2 diabetes. However, patients with FRG may exhibit clinical features such as lower body weight or height, altered systemic blood pressure, diaper dermatitis, aminoaciduria, decreased serum uric acid levels, and hypercalciuria. Further research is needed to fully understand the pathophysiology, molecular genetics, and clinical manifestations of renal glucosuria.

#3

Congenital Glucose-Galactose Malabsorption: A Rare Cause of Intractable Diarrhea in Infancy.

Indian pediatrics2025 Nov
#4

A Rare Case of Congenital Glucose Galactose Malabsorption Due to SLC5A1 Mutation.

Cureus2025 Dec

Protracted neonatal diarrhea is severe and potentially life-threatening if not promptly diagnosed and treated. Causes include congenital defects in sodium, chloride, glucose/galactose, bile acid transport, enterokinase deficiency, and villous atrophy. Glucose-galactose malabsorption (GGM) is a rare autosomal recessive disorder caused by mutations in the SGLT1 gene, impairing glucose and galactose absorption and leading to osmotic diarrhea. This case report highlights the rarity of GGM and emphasizes the importance of early recognition to enable prompt dietary intervention, preventing failure to thrive and reducing mortality. It further underscores the imperative need for fructose-based formulas to be readily available. We describe a five-week-old full-term male infant, born to third-cousin parents, who presented in hypovolemic shock due to persistent diarrhea that started at two days of life, accompanied by severe metabolic acidosis and acute kidney injury. Abdominal ultrasound revealed medullary nephrocalcinosis. Endoscopic evaluation showed nonspecific duodenitis. The patient initially failed to reach full feeds on multiple formula trials, including amino acid-based, extensively hydrolyzed, and rice-based formulas, necessitating parenteral nutrition, which was later discontinued due to fungemia. Extensive investigations and genetic testing (whole exome sequencing) confirmed congenital GGM (SLC5A1 mutation). Due to the unavailability of glucose and galactose-free formula, he was initially started on a ketogenic formula and subsequently transitioned to a fructose-based formula once available. Following dietary modification, the patient showed significant clinical improvement, with resolution of diarrhea, steady weight gain, and appropriate growth on follow-up. In conclusion, GGM should be considered in infants with persistent diarrhea and failure to thrive. Timely diagnosis optimizes prognosis, improves outcomes, and facilitates genetic counseling for affected families.

#5

Congenital Glucose-Galactose Malabsorption Presenting as Hypertriglyceridemia and Medullary Nephrocalcinosis.

Pediatric reports2025 Sep 05

A 4-month-old male child was admitted with failure to thrive, persistent osmotic diarrhea, and presence of multiple metabolic abnormalities, which included hypertriglyceridemia, hypercholesterolemia, hypercalcemia, and medullary nephrocalcinosis. He was diagnosed with congenital glucose-galactose malabsorption (CGGM). The exome analysis showed presence of pathogenic mutation in exon 8 of the SLC5A1 gene (c875G>A, p.Cys292Tyr). This gene codes for a sodium-glucose cotransporter called SGLT1. To date, no clinical case reports have reported hypertriglyceridemia and hypercholesterolemia with CGGM. Hypercalcemia and medullary nephrocalcinosis have also been reported only in a handful of CGGM cases worldwide. Through this case, the authors attempt to highlight the uncommon manifestation of this rare disease to facilitate timely management. Although the child died due to healthcare-associated infection (HCAI), pre-natal counseling of the family was carried out for the management of future pregnancies.

Publicações recentes

Ver todas no PubMed

📚 EuropePMC90 artigos no totalmostrando 53

2026

Congenital glucose-galactose malabsorption: An unusual cause of chronic diarrhea in infancy.

Revista de gastroenterologia de Mexico (English)
2025

A Rare Case of Congenital Glucose Galactose Malabsorption Due to SLC5A1 Mutation.

Cureus
2025

Congenital Glucose-Galactose Malabsorption Presenting as Hypertriglyceridemia and Medullary Nephrocalcinosis.

Pediatric reports
2025

Congenital Glucose-Galactose Malabsorption: A Rare Cause of Intractable Diarrhea in Infancy.

Indian pediatrics
2025

A new link between insulinoma and congenital glucose-galactose malabsorption.

Endocrine oncology (Bristol, England)
2025

Carbohydrate malabsorption mimicking immune dysregulation: A histological challenge.

JPGN reports
2025

Renal glucosuria in children.

World journal of clinical pediatrics
2024

Cracking the Codes for Congenital Diarrhea and Enteropathies (CoDEs): A Case Report and Review.

Cureus
2024

Importance of genetic sequencing studies in managing chronic neonatal diarrhea: a case report of a novel variant in the glucose-galactose transporter SLC5A1.

Frontiers in pediatrics
2023

Novel Mutation in the SLC5A1 Gene Causing Glucose-Galactose Malabsorption: First Confirmed Case From Central America.

JPGN reports
2023

Congenital Diarrhoea In A Neonate With Hypernatraemia And Dehydration.

JPMA. The Journal of the Pakistan Medical Association
2023

SLC5A1 Variants in Turkish Patients with Congenital Glucose-Galactose Malabsorption.

Genes
2023

Congenital Glucose-Galactose Malabsorption in a Neonate with Hyperbilirubinemia and Hypernatremia.

Indian journal of pediatrics
2023

Fructose Metabolism and Its Effect on Glucose-Galactose Malabsorption Patients: A Literature Review.

Diagnostics (Basel, Switzerland)
2022

Congenital Glucose-Galactose Malabsorption in a Child.

Indian pediatrics
2022

Coordinated Multi-Language Translation of A Validated Symptom Questionnaire for Carbohydrate Intolerances: A Practical Structured Procedure.

Journal of gastrointestinal and liver diseases : JGLD
2022

Importance of Early Genetic Sequencing in Neonates Admitted to NICU with Recurrent Hypernatremia: Results of a Prospective Cohort Study.

Neonatology
2021

Congenital Glucose-Galactose Malabsorption: A Case With a Novel SLC5A1 Mutation in a Saudi Infant.

Cureus
2021

The Molecular Basis of Glucose Galactose Malabsorption in a Large Swedish Pedigree.

Function (Oxford, England)
2021

Enteroendocrine Dysfunction in Two Saudi Sisters.

Case reports in gastroenterology
2021

Prokaryotic Solute/Sodium Symporters: Versatile Functions and Mechanisms of a Transporter Family.

International journal of molecular sciences
2021

NGS Gene Panel Analysis Revealed Novel Mutations in Patients with Rare Congenital Diarrheal Disorders.

Diagnostics (Basel, Switzerland)
2021

Long-Term Dietary Changes in Subjects with Glucose Galactose Malabsorption Secondary to Biallelic Mutations of SLC5A1.

Digestive diseases and sciences
2022

A Case of Congenital Glucose Galactose Malabsorption with a New Mutation in the SLC5A1 Gene.

Journal of pediatric genetics
2020

Literature review on congenital glucose-galactose malabsorption from 2001 to 2019.

Journal of paediatrics and child health
2020

Glucose transporters in the small intestine in health and disease.

Pflugers Archiv : European journal of physiology
2020

Valid Assessment of Carbohydrate Intolerance and the Need for a Distinction to Carbohydrate Malabsorption. Comment on "Roles of Lactose and Fructose Malabsorption and Dietary Outcomes in Children Presenting with Chronic Abdominal Pain.", Nutrients, 2019, 11, 3063.

Nutrients
2019

Roles of Lactose and Fructose Malabsorption and Dietary Outcomes in Children Presenting with Chronic Abdominal Pain.

Nutrients
2019

Nutrition management of congenital glucose-galactose malabsorption: Case report of a Chinese infant.

Medicine
2019

Relevance of solute carrier family 5 transporter defects to inherited and acquired human disease.

Journal of applied genetics
2019

A Rare Cause of Intractable Diarrhea of Infancy.

Journal of the College of Physicians and Surgeons--Pakistan : JCPSP
2019

What does sodium-glucose co-transporter 1 inhibition add: Prospects for dual inhibition.

Diabetes, obesity &amp; metabolism
2020

[Glucose and galactose malabsorption: A new case in Spain].

Anales de pediatria
2019

Congenital glucose-galactose malabsorption: A case report with a novel SLC5A1 mutation.

Clinical case reports
2019

Congenital glucose-galactose malabsorption: A rare and severe cause of infant diarrhea.

Medicina clinica
2018

Genetic Variants in SGLT1, Glucose Tolerance, and Cardiometabolic Risk.

Journal of the American College of Cardiology
2018

Development of SGLT1 and SGLT2 inhibitors.

Diabetologia
2018

Altered pancreatic islet morphology and function in SGLT1 knockout mice on a glucose-deficient, fat-enriched diet.

Molecular metabolism
2018

History of Acquired Monosaccharide Intolerance in Houston, Texas.

Journal of pediatric gastroenterology and nutrition
2017

Novel and Unexpected Functions of SGLTs.

Physiology (Bethesda, Md.)
2018

SLC5A1 Mutations in Saudi Arabian Patients With Congenital Glucose-Galactose Malabsorption.

Journal of pediatric gastroenterology and nutrition
2017

Causes Of Chronic Non-Infectious Diarrhoea In Infants Less Than 6 Months Of Age: Rarely Recognized Entities.

Journal of Ayub Medical College, Abbottabad : JAMC
2017

A 9-Day-Old With Weight Loss and Diarrhea.

Pediatrics
2017

Congenital Glucose-Galactose Malabsorption: A Case Report.

Journal of pediatric health care : official publication of National Association of Pediatric Nurse Associates &amp; Practitioners
2017

Two Cases of Mistaken Polyuria and Nephrocalcinosis in Infants with Glucose-Galactose Malabsorption: A Possible Role of 1,25(OH)2D3
.

Hormone research in paediatrics
2016

Congenital glucose-galactose malabsorption diagnosed from macrohematuria in an infant.

Pediatrics international : official journal of the Japan Pediatric Society
2017

[Evolution of type 2 diabetes and carbohydrate intolerance following bariatric surgery in a Mexican mestizo population].

Cirugia y cirujanos
2017

Congenital Glucose-Galactose Malabsorption in a Turkish Newborn: A Novel Mutation of Na+/Glucose Cotransporter Gene.

Digestive diseases and sciences
2016

Diagnosing and Treating Intolerance to Carbohydrates in Children.

Nutrients
2015

Breath Hydrogen as a Biomarker for Glucose Malabsorption after Roux-en-Y Gastric Bypass Surgery.

Disease markers
2015

A novel mutation within the lactase gene (LCT): the first report of congenital lactase deficiency diagnosed in Central Europe.

BMC gastroenterology
2017

Disaccharidase Deficiencies in Children With Chronic Abdominal Pain.

JPEN. Journal of parenteral and enteral nutrition
2015

Recurrent abdominal pain in children: a clinical approach.

Singapore medical journal
Ver todos os 90 no EuropePMC

Associações

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Doenças relacionadas

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Referências e fontes

Bases de dados externas citadas neste artigo

Publicações científicas

Artigos indexados no PubMed ligados a esta doença no grafo RarasNet — título, periódico e PMID direto da fonte, sem intermediação de IA.

  1. Congenital glucose-galactose malabsorption: An unusual cause of chronic diarrhea in infancy.
    Revista de gastroenterologia de Mexico (English)· 2026· PMID 41545250mais citado
  2. Renal glucosuria in children.
    World journal of clinical pediatrics· 2025· PMID 40059893mais citado
  3. Congenital Glucose-Galactose Malabsorption: A Rare Cause of Intractable Diarrhea in Infancy.
    Indian pediatrics· 2025· PMID 40920309mais citado
  4. A Rare Case of Congenital Glucose Galactose Malabsorption Due to SLC5A1 Mutation.
    Cureus· 2025· PMID 41510412mais citado
  5. Congenital Glucose-Galactose Malabsorption Presenting as Hypertriglyceridemia and Medullary Nephrocalcinosis.
    Pediatric reports· 2025· PMID 40981014mais citado
  6. A new link between insulinoma and congenital glucose-galactose malabsorption.
    Endocr Oncol· 2025· PMID 40662130recente

Bases de dados e fontes oficiais

Identificadores e referências canônicas usadas para montar este verbete.

  1. ORPHA:35710(Orphanet)
  2. OMIM OMIM:606824(OMIM)
  3. MONDO:0011731(MONDO)
  4. GARD:6521(GARD (NIH))
  5. Variantes catalogadas(ClinVar)
  6. Busca completa no PubMed(PubMed)
  7. Q5572341(Wikidata)

Dados compilados pelo RarasNet a partir de fontes abertas (Orphanet, OMIM, MONDO, PubMed/EuropePMC, ClinicalTrials.gov, DATASUS, PCDT/MS). Este conteúdo é informativo e não substitui avaliação médica.

Conteúdo mantido por Agente Raras · Médicos e pesquisadores podem colaborar

Compêndio · Raras BR

Má absorção de glicose-galactose

ORPHA:35710 · MONDO:0011731
Prevalência
Unknown
Herança
Autosomal recessive
CID-10
E74.3 · Outros distúrbios da absorção intestinal de carboidratos
CID-11
Início
Infancy, Neonatal
Prevalência
0.0 (Worldwide)
MedGen
UMLS
C0268186
EuropePMC
Wikidata
Papers 10a
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