Raras
Buscar doenças, sintomas, genes...
Glomerulopatia C3
ORPHA:329918CID-10 · N03.5CID-11 · MF8YDOENÇA RARA

Uma forma de glomerulonefrite membranoproliferativa primária caracterizada pela presença em amostras de biópsia renal de uma glomerulonefrite com coloração de imunofluorescência glomerular única (ou pelo menos dominante) para C3. Alterações inespecíficas ou padrões proliferativos com coloração glomerular C3-dominante também são possíveis de ocorrer. Com base nos achados da microscopia eletrónica, a glomerulopatia C3 (C3G) pode ser classificada como glomerulonefrite C3 (C3GN) ou doença de depósito denso (DDD).

Mantido por Agente Raras·Colaborar como especialista →

Introdução

O que você precisa saber de cara

📋

Uma forma de glomerulonefrita membranoproliferativa primária descrita pela presença em amostras de biópsia renal de uma glomerulonefrita com coloração de imunofluorescência glomerular única (ou pelo menos dominante) para C3. Alterações inespecíficas ou padrões proliferativos com coloração glomerular C3-dominante também são possíveis de ocorrer. Com base nos achados da microscopia eletrônica, a glomerulopatia C3 (C3G) pode ser encontrada como glomerulonefrite C3 (C3GN) ou doença de depósito denso (DDD).

Pesquisas ativas
12 ensaios
30 total registrados no ClinicalTrials.gov
Publicações científicas
642 artigos
Último publicado: 2026 Apr 10
Medicamentos
4 registrados
ANVISA / FDA

Escala de raridade

CLASSIFICAÇÃO ORPHANET · BRASIL 2024
1-9 / 1 000 000
Ultra-rara
<1/50k
Muito rara
1/20k
Rara
1/10k
Pouco freq.
1/5k
Incomum
1/2k
Prevalência
0.15
Europe
Início
All ages
🏥
SUS: Sem cobertura SUSScore: 0%
CID-10: N03.5
Você se identifica com essa condição?
O Raras está aqui pra te apoiar — com ou sem diagnóstico

Encontrou um erro ou informação desatualizada? Sugira uma correção →

Entender a doença

Do básico ao detalhe, leia no seu ritmo

Preparando trilha educativa...

Sinais e sintomas

O que aparece no corpo e com que frequência cada sintoma acontece

Partes do corpo afetadas

🫘
Rins
14 sintomas
👁️
Olhos
4 sintomas
🛡️
Imunológico
3 sintomas
💪
Músculos
1 sintomas
❤️
Coração
1 sintomas

+ 11 sintomas em outras categorias

Características mais comuns

90%prev.
Hematúria
Muito frequente (99-80%)
55%prev.
Concentração diminuída de complemento C3 circulante
Frequente (79-30%)
55%prev.
Concentração elevada de creatinina circulante
Frequente (79-30%)
55%prev.
Hipercelularidade mesangial
Frequente (79-30%)
55%prev.
Hipercelularidade extracapilar
Frequente (79-30%)
55%prev.
Doença renal crônica
Frequente (79-30%)
34sintomas
Muito frequente (1)
Frequente (11)
Ocasional (11)
Sem dados (11)

Os sintomas variam de pessoa para pessoa. Abaixo estão as 34 características clínicas mais associadas, ordenadas por frequência.

HematúriaHematuria
Muito frequente (99-80%)90%
Concentração diminuída de complemento C3 circulanteDecreased circulating complement C3 concentration
Frequente (79-30%)55%
Concentração elevada de creatinina circulanteElevated circulating creatinine concentration
Frequente (79-30%)55%
Hipercelularidade mesangialMesangial hypercellularity
Frequente (79-30%)55%
Hipercelularidade extracapilarExtracapillary hypercellularity
Frequente (79-30%)55%

Linha do tempo da pesquisa

Publicações por ano — veja quando o interesse científico cresceu
Anos de pesquisa1desde 2026
Total histórico642PubMed
Últimos 10 anos200publicações
Pico202583 papers
Linha do tempo
2026Hoje · 2026🧪 2009Primeiro ensaio clínico📈 2025Ano de pico
Publicações por ano (últimos 10 anos)

Encontrou um erro ou informação desatualizada? Sugira uma correção →

Genética e causas

O que está alterado no DNA e como passa nas famílias

Genes associados

5 genes identificados com associação a esta condição. Padrão de herança: Multigenic/multifactorial.

CFHR5Complement factor H-related protein 5Disease-causing germline mutation(s) inTolerante
FUNÇÃO

Involved in complement regulation. The dimerized forms have avidity for tissue-bound complement fragments and efficiently compete with the physiological complement inhibitor CFH

LOCALIZAÇÃO

Secreted

VIAS BIOLÓGICAS (1)
Regulation of Complement cascade
OUTRAS DOENÇAS (1)
C3 glomerulonephritis
HGNC:24668UniProt:Q9BXR6
CFHComplement factor HDisease-causing germline mutation(s) inAltamente restrito
FUNÇÃO

Glycoprotein that plays an essential role in maintaining a well-balanced immune response by modulating complement activation. Acts as a soluble inhibitor of complement, where its binding to self markers such as glycan structures prevents complement activation and amplification on cell surfaces (PubMed:21285368, PubMed:21317894, PubMed:25402769). Accelerates the decay of the complement alternative pathway (AP) C3 convertase C3bBb, thus preventing local formation of more C3b, the central player of

LOCALIZAÇÃO

Secreted

VIAS BIOLÓGICAS (1)
Regulation of Complement cascade
MECANISMO DE DOENÇA

Basal laminar drusen

Drusen are extracellular deposits that accumulate below the retinal pigment epithelium on Bruch membrane. Basal laminar drusen refers to an early adult-onset drusen phenotype that shows a pattern of uniform small, slightly raised yellow subretinal nodules randomly scattered in the macula. In later stages, these drusen often become more numerous, with clustered groups of drusen scattered throughout the retina. In time these small basal laminar drusen may expand and ultimately lead to a serous pigment epithelial detachment of the macula that may result in vision loss.

OUTRAS DOENÇAS (10)
complement factor H deficiencybasal laminar drusendense deposit diseaseDoyne honeycomb retinal dystrophy
HGNC:4883UniProt:P08603
CFHR1Complement factor H-related protein 1Candidate gene tested inTolerante
FUNÇÃO

Involved in complement regulation. The dimerized forms have avidity for tissue-bound complement fragments and efficiently compete with the physiological complement inhibitor CFH. Can associate with lipoproteins and may play a role in lipid metabolism

LOCALIZAÇÃO

Secreted

VIAS BIOLÓGICAS (1)
Regulation of Complement cascade
MECANISMO DE DOENÇA

Hemolytic uremic syndrome, atypical, 1

An atypical form of hemolytic uremic syndrome. It is a complex genetic disease characterized by microangiopathic hemolytic anemia, thrombocytopenia, renal failure and absence of episodes of enterocolitis and diarrhea. In contrast to typical hemolytic uremic syndrome, atypical forms have a poorer prognosis, with higher death rates and frequent progression to end-stage renal disease.

OUTRAS DOENÇAS (4)
dense deposit diseaseC3 glomerulonephritisage related macular degeneration 1hemolytic uremic syndrome, atypical, susceptibility to, 1
HGNC:4888UniProt:Q03591
CFHR3Complement factor H-related protein 3Candidate gene tested inTolerante
FUNÇÃO

Might be involved in complement regulation

LOCALIZAÇÃO

Secreted

VIAS BIOLÓGICAS (1)
Regulation of Complement cascade
MECANISMO DE DOENÇA

Hemolytic uremic syndrome, atypical, 1

An atypical form of hemolytic uremic syndrome. It is a complex genetic disease characterized by microangiopathic hemolytic anemia, thrombocytopenia, renal failure and absence of episodes of enterocolitis and diarrhea. In contrast to typical hemolytic uremic syndrome, atypical forms have a poorer prognosis, with higher death rates and frequent progression to end-stage renal disease.

OUTRAS DOENÇAS (3)
C3 glomerulonephritishemolytic uremic syndrome, atypical, susceptibility to, 1age related macular degeneration 1
HGNC:16980UniProt:Q02985
CFHR2Complement factor H-related protein 2Candidate gene tested inTolerante
FUNÇÃO

Involved in complement regulation. The dimerized forms have avidity for tissue-bound complement fragments and efficiently compete with the physiological complement inhibitor CFH. Can associate with lipoproteins and may play a role in lipid metabolism

LOCALIZAÇÃO

Secreted

VIAS BIOLÓGICAS (1)
Regulation of Complement cascade
INTERAÇÕES PROTEICAS (5)
OUTRAS DOENÇAS (1)
C3 glomerulonephritis
HGNC:4890UniProt:P36980

Variantes genéticas (ClinVar)

92 variantes patogênicas registradas no ClinVar.

🧬 CFHR2: GRCh37/hg19 1q25.3-32.1(chr1:180800361-203181850)x3 ()
🧬 CFHR2: GRCh37/hg19 1q21.1-44(chr1:143932350-249224684)x3 ()
🧬 CFHR2: NM_005666.4(CFHR2):c.254-6C>G ()
🧬 CFHR2: NC_000001.10:g.(?_190829412)_(216061974_?)del ()
🧬 CFHR2: NM_005666.4(CFHR2):c.59-12T>C ()
Ver todas no ClinVar

Vias biológicas (Reactome)

1 via biológica associada aos genes desta condição.

Diagnóstico

Os sinais que médicos procuram e os exames que confirmam

Carregando...

Tratamento e manejo

Remédios, cuidados de apoio e o que precisa acompanhar

Pipeline de tratamentos
Pipeline regulatório — de medicamentos já aprovados a drogas em pesquisa exploratória.
3Fase 33
2Fase 29
1Fase 11
·Pré-clínico7
Medicamentos catalogadosEnsaios clínicos· 0 medicamentos · 20 ensaios
Carregando informações de tratamento...

Onde tratar no SUS

Hospitais de referência no Brasil e o protocolo oficial do SUS (PCDT)

🇧🇷 Atendimento SUS — Glomerulopatia C3

🗺️

Selecione um estado ou use sua localização para ver resultados.

Dados de DATASUS/CNES, SBGM, ABNeuro e Ministério da Saúde. Sempre confirme a disponibilidade diretamente com o estabelecimento.

Pesquisa ativa

Ensaios clínicos abertos e novidades científicas recentes

🟢 Recrutando agora

7 pesquisas recrutando participantes. Converse com seu médico sobre a possibilidade de participar.

Outros ensaios clínicos

30 ensaios clínicos encontrados, 12 ativos.

Distribuição por fase
Ver todos no ClinicalTrials.gov
🧪 Está conduzindo uma pesquisa?
Divulgue para pacientes e familiares que acompanham esta doença.
Divulgar pesquisa →

Publicações mais relevantes

🥉Melhor nível de evidência: Relato de caso
Timeline de publicações
575 papers (10 anos)
#1

Treatment of atypical hemolytic uremic syndrome and C3 glomerulopathy in mice by hepatic expression of factor D.

Blood advances2026 Mar 24

Atypical hemolytic uremic syndrome (aHUS) and C3 glomerulopathy (C3G) are diseases driven by dysregulation of the alternative pathway (AP) complement. Current treatments of these diseases involve the use of frequent and often large doses of monoclonal antibodies, peptide inhibitors, or chemical inhibitors of complement proteins, with various limitations. In this study, we describe ectopic expression of factor D (FD) in the liver as a potential novel therapy for these indications. Unlike most plasma complement proteins, which are synthesized in the liver, FD, a serine protease in the AP, is synthesized primarily in fat tissues. Newly synthesized FD is released largely as an inactive proenzyme that requires activation by mannose-binding lectin-associated serine protease 3 (MASP3) to form the mature enzyme. We found serendipitously that ectopic expression of mature FD, but not pro-FD, in the mouse liver led to C3-dependent depletion of plasma factor B (FB) and abolished AP complement activity. Coexpression of C3, FB, and mature FD in cultured Hepa1-6 cells caused intracellular FB activation and consumption, probably within the secretory vesicles where all 3 proteins may colocalize. Hepatic FD-mediated local FB activation and depletion effectively prevented disease development in murine models of aHUS and C3G. Our results suggest that segregated tissue production of FD, FB, and C3, as well as FD regulation by MASP3, is necessary to prevent in situ FB activation and depletion. Ectopic expression of mature FD in the liver is an effective way to inhibit FB expression and AP complement activity, with potential therapeutic applications in diseases such as aHUS and C3G.

#2

Clinical Profile and Outcome of C3-Dominant Glomerulonephritis: Retrospective Study.

Kidney &amp; blood pressure research2026

Complement 3 (C3)-dominant glomerulonephritis (GN) are rare diseases resulting from alternative complement pathway dysregulation; they include C3 glomerulopathy (C3G), paraprotein-associated GN, and C3-dominant infection-related GN (IRGN). To our knowledge, long-term follow-up studies of clinical profile and outcomes of this rare disorder are sparse. We studied kidney histopathology baseline findings, outcomes, treatment, and its complications of C3-dominant GN in our setting. We studied the clinical, pathological profiles, and outcomes of patients with C3-dominant GN. This study was a single centre, retrospective, case record based observational study at a tertiary care hospital in Southern India. Consecutive patients of C3-dominant GN on kidney biopsy from 2013 to 2023 were included. Demography, laboratory and histopathological data, treatment and outcomes were studied. Of 2,175 kidney biopsies, 141 (6.48%) showed C3-dominant GN; 74 (52.5%) C3G, 67 (47.5%) IRGN. Median age was 43 years (IQR 29-59.5), males 90 (63.8%). Preceding skin/throat infections were seen in 32/141 (22.7%). At presentation, median serum creatinine was 1.7 mg/dL (IQR: 1.2-3.6), eGFR <60 mL/min/1.73 m2 in 91/141 (64.5%), 111/141 (78.7%) had low serum C3 levels. Nephrotic proteinuria was seen in 65/141 (46%), Crescents in 45 (31.9%). Remission was partial in 38/141 (27%), complete in 45/141 (31.9%) and 31/141 (22%) progressed to end-stage kidney disease (ESKD). On immunosuppression, commonest infection was pneumonia in 15/70 (21.4%) and 27/141 (19.1%) died at an average follow-up of 25.7 months. Diabetes mellitus, percentage sclerosis, and presence of crescents predicted development of CKD stage 5. Over 10 years, C3-dominant GN represented 6.48% of kidney biopsies. Nephrotic proteinuria and kidney failure are common at presentation with 58% achieving some remission, 22% going on to ESKD and mortality of 19%.

#3

Pegcetacoplan in C3 Glomerulopathy and Immune-Complex MPGN. Reply.

The New England journal of medicine2026 Mar 12
#4

Pegcetacoplan in C3 Glomerulopathy and Immune-Complex MPGN.

The New England journal of medicine2026 Mar 12
#5

Autoantibodies Targeting Complement Regulating Factors Induced C3 Glomerulopathy Resambling C4 Dense Deposit Disease: A Case Report.

Nephrology (Carlton, Vic.)2026 Apr

Dense deposit disease (DDD), a subgroup of C3 glomerulopathy, is a rare glomerular disease characterised histologically by predominant C3 staining on immunofluorescence microscopy along with intramembranous osmiophilic dense deposits. C4 DDD is a recently identified form of complement-mediated glomerulonephritis, characterised by intense C4d staining with minimal or absent staining for C3 and immunoglobulin, and dense deposits along the glomerular basement membrane. We present a 27-year-old female patient who exhibited proteinuria during pregnancy. Following delivery, the patient continued to experience persistent non-nephrotic-range proteinuria, along with microscopic hematuria and dramatically decreased serum C3 level, while maintaining preserved renal function. Renal biopsy revealed mesangial proliferative glomerulonephritis with a focal membranoproliferative glomerulonephritis pattern by light microscopy. Electron microscopy demonstrated high-density banded deposits in the glomerular basement membrane, while immunofluorescence exhibited negative C3c and immunoglobulin staining. Immunohistochemical analysis showed diffuse expression of C3d and C4d in the capillary loops, mesangial region, focal tubular basement membrane, and focal arteriolar wall. Further investigation revealed elevated circulating levels of autoantibodies against complement factor H and the C3 convertase. Mass spectrometry confirmed that C3 was the predominant component of the deposits. Ultimately, this patient was diagnosed as DDD mediated by complement factor H autoantibodies and C3 nephritic factor.

Publicações recentes

Ver todas no PubMed

📚 EuropePMC325 artigos no totalmostrando 197

2026

Autoantibodies Targeting Complement Regulating Factors Induced C3 Glomerulopathy Resambling C4 Dense Deposit Disease: A Case Report.

Nephrology (Carlton, Vic.)
2026

A pediatric case of C3 glomerulonephritis initially misclassified as IgA nephropathy with a favorable response to C3-targeted therapy.

Pediatric nephrology (Berlin, Germany)
2026

Thrombosis in paroxysmal nocturnal hemoglobinuria in the complement inhibitor era: mechanisms, risk stratification, and clinical management.

International journal of hematology
2026

Recurrent C3 glomerulopathy after prolonged remission.

Pediatric nephrology (Berlin, Germany)
2026

Pegcetacoplan in C3 Glomerulopathy and Immune-Complex MPGN. Reply.

The New England journal of medicine
2026

Pegcetacoplan in C3 Glomerulopathy and Immune-Complex MPGN.

The New England journal of medicine
2026

A novel fusion protein reduces kidney complement in experimental C3 glomerulopathy.

Clinical and experimental immunology
2026

C3 Glomerulopathy Diagnosis, Current Treatments, and Emerging Therapies.

Kidney medicine
2026

Primary membranoproliferative glomerulonephritis: natural history, pathogenesis, and treatment.

Frontiers in nephrology
2026

A young woman with membranoproliferative glomerulonephritis and persistent hypocomplementemia: a case report.

BMC nephrology
2026

Real-World Analysis of Patients With C3 Glomerulopathy in the United States.

Kidney international reports
2026

[C3 glomerulopathy: An immune-mediated kidney disease].

MMW Fortschritte der Medizin
2026

Efficacy of iptacopan in idiopathic immune complex-mediated membranoproliferative glomerulonephritis refractory to conventional treatment.

Nefrologia
2026

Monoclonal gammopathy of renal significance in western China: A large cohort study dominated by amyloidosis with distinct clinical outcomes.

Clinics (Sao Paulo, Brazil)
2026

Complement 3 Glomerulopathy Revisited: Bridging Pathogenesis and Therapy in the New Era.

Advances in kidney disease and health
2025

Case Report: Possible C3 nephritic factor-driven complement-mediated severe hemolytic anemia and acute kidney injury in a child with Bordetella parapertussis infection.

Frontiers in immunology
2026

Treatment of atypical hemolytic uremic syndrome and C3 glomerulopathy in mice by hepatic expression of factor D.

Blood advances
2026

Current and Emerging Therapies for C3 Glomerulopathy and Primary (Idiopathic) Immune Complex Membranoproliferative Glomerulonephritis.

Kidney international reports
2026

A Decade of C3 Glomerulopathy-A Nationwide Cohort Study.

Kidney international reports
2026

Clinical Profile and Outcome of C3-Dominant Glomerulonephritis: Retrospective Study.

Kidney &amp; blood pressure research
2026

Recurrence of C3 Glomerulopathy and Immune Complex-Mediated Membranoproliferative Glomerulonephritis After Kidney Transplantation: Challenges and Opportunities.

Kidney international reports
2026

Delphi Consensus on Surrogate End Points in C3 Glomerulopathy and Primary Immune Complex-Mediated Membranoproliferative Glomerulonephritis.

Kidney international reports
2026

Disentangling disease heterogeneity in C3 glomerulopathies: a slippery road.

Kidney international
2026

Probing the surrogate validity of proteinuria thresholds in C3 glomerulopathy/immune-complex membranoproliferative glomerulonephritis: unresolved biases and mechanistic gaps.

Kidney international
2026

Laboratory findings in patients treated with complement factor C3 inhibitor pegcetacoplan.

Clinical chemistry and laboratory medicine
2025

A very rare cause of oliguric acute kidney disease: crescentic C3 glomerulopathy.

Oxford medical case reports
2026

Modern challenges in infection prevention: encapsulated organisms in the era of novel complement inhibitors.

Kidney international
2026

Complement activation drives a compartmentalized innate immune response in C3 glomerulopathy contributing to the disease phenotype.

Kidney international
2025

Natural History and Clinical Associations with Long-Term Outcomes in Primary C3 Glomerulopathy and Immune Complex-Mediated Membranoproliferative GN.

Clinical journal of the American Society of Nephrology : CJASN
2025

Electron Microscopy in Renal Biopsy Interpretation: When and Why It Still Matters.

Cureus
2026

Pegcetacoplan in idiopathic and familial pediatric C3 glomerulopathy.

Pediatric nephrology (Berlin, Germany)
2025

Real-World Patient Characteristics, Burden, and Quality of Life in C3 Glomerulopathy and Primary Immune Complex Membranoproliferative Glomerulonephritis.

Kidney360
2025

Pegcetacoplan for Treatment of C3 Glomerulopathy and Immune-Complex MPGN.

The New England journal of medicine
2025

Trial of Pegcetacoplan in C3 Glomerulopathy and Immune-Complex MPGN.

The New England journal of medicine
2025

Novel treatment strategies for C3 glomerulopathy: complement blockade.

International urology and nephrology
2026

C3 glomerulopathy: advancements in diagnostics and therapeutics.

Current opinion in nephrology and hypertension
2026

Diagnosis and treatment in adult patients with C3 glomerulopathy in Japan: a real-world survey.

Clinical and experimental nephrology
2025

Complement Profiling in Glomerular Disease: Insights from Laser Microdissection and Mass Spectrometry.

Clinical journal of the American Society of Nephrology : CJASN
2025

Eculizumab in C3 Glomerulopathy: A Systematic Review of Therapeutic Efficacy and Clinical Outcomes.

Pharmaceutics
2025

From Data to Drug: The Translational Impact of RaDaR, the UK National Registry of Rare Kidney Diseases.

Nephrology, dialysis, transplantation : official publication of the European Dialysis and Transplant Association - European Renal Association
2025

Spectrum and clinical profile of glomerular diseases in a Nepalese cohort, a tertiary care center study: focus on comparing IgA nephropathy with other primary glomerulonephritis.

BMC nephrology
2026

Hierarchical clustering uncovered disease patterns and further untangled complexities in immune complex-mediated idiopathic MPGN and C3 glomerulopathy.

Kidney international
2025

In situ assessment of glomerular C3/C5 convertases indicates ongoing complement activation in IgA nephropathy.

Nephrology, dialysis, transplantation : official publication of the European Dialysis and Transplant Association - European Renal Association
2025

Iptacopan treatment for recurrent dense deposit disease after kidney transplant: A case report.

SAGE open medical case reports
2025

Oral iptacopan therapy in patients with C3 glomerulopathy: a randomised, double-blind, parallel group, multicentre, placebo-controlled, phase 3 study.

Lancet (London, England)
2025

Recurrence of Glomerular Diseases (GN) After Kidney Transplantation: A Narrative Review.

Journal of clinical medicine
2025

A rare co-existence of celiac disease and C3 glomerulopathy.

Nefrologia
2025

Iptacopan/LNP023 and rituximab as rescue therapy in a patient with systemic lupus erythematosus-associated atypical haemolytic uraemic syndrome.

Journal of nephrology
2025

A 14-year-old boy with C3 glomerulopathy and Sjögren's syndrome identified by a school urinary screening program.

Fukushima journal of medical science
2025

Corrigendum to "The Role of von Willebrand Factor in the Pathogenesis of C3 Glomerulopathy" [Kidney International Reports Volume 10, Issue 6, June 2025, Pages 1929-1938].

Kidney international reports
2026

Clinical Presentation, Treatment Patterns, Burden of Disease, and the Association of Proteinuria with Clinical Outcomes in C3 Glomerulopathy and Primary Immune Complex Membranoproliferative Glomerulonephritis: A Systematic Review.

Nephron
2025

Atypical presentation of post-streptococcal glomerulonephritis in a child with genetically confirmed susceptibility to C3-glomerulopathy: a case report and brief review of the literature.

BMC nephrology
2025

Spectrum of renal diseases caused by monoclonal immunoglobulin: experience from an Australian tertiary referral centre over a 10-year period.

Pathology
2025

Targeting the Roots of Kidney Disease: Systematic Review of the Therapies Targeting the Complement System.

Medicina (Kaunas, Lithuania)
2025

Gene-Environment Interaction: Lessons From Complement-Mediated Kidney Disease.

Seminars in nephrology
2025

The Role of von Willebrand Factor in the Pathogenesis of C3 Glomerulopathy.

Kidney international reports
2025

Quantifying association of early proteinuria and estimated glomerular filtration rate changes with long-term kidney failure in C3 glomerulopathy and immune-complex membranoproliferative glomerulonephritis using the United Kingdom RaDaR Registry.

Kidney international
2025

Advances in Complement Inhibitory Strategies for the Treatment of Glomerular Disease: A Rapidly Evolving Field.

Journal of clinical medicine
2025

Complement System Inhibitors in Nephrology: An Update-Narrative Review.

International journal of molecular sciences
2025

C3 glomerulopathy post kidney transplantation: A single center experience.

World journal of transplantation
2025

Clinical and Histologic Predictors of Kidney Outcomes in C3 Glomerulopathy and Idiopathic Membranoproliferative GN.

Clinical journal of the American Society of Nephrology : CJASN
2025

Successful Management of C3 Glomerulopathy Recurrence Post-Kidney Transplantation with Iptacopan: A Case Report.

International journal of molecular sciences
2025

C3 glomerulopathy and acute kidney injury after mRNA-1273 (Moderna) COVID-19 vaccine and genetical analysis.

Clinical nephrology
2025

Factor H-related 1 and heparan sulfate architecture contribute to complement dysregulation in C3 glomerulopathy.

Frontiers in immunology
2025

Spatially resolved transcriptomic profiling for glomerular and tubulointerstitial gene expression in C3 glomerulopathy.

Clinical kidney journal
2025

CFHR5 Nephropathy Case Report: A Novel Variant Characterized by Tubulointerstitial Kidney Disease.

Kidney &amp; blood pressure research
2025

Kidney transplant in patients with C3 glomerulopathy.

Clinical kidney journal
2025

Complement-Mediated Kidney Disease and Living Donor Transplantation: Tailoring Approaches to Improve Outcomes.

Current transplantation reports
2025

Expanding the spectrum of genetic causes of DNA-specific exonuclease TREX1 variants in thrombotic microangiopathy.

Kidney international
2025

Pregnancy outcomes in C3 glomerulopathy: a retrospective review.

BMC nephrology
2025

The 4 functional segments of Factor H: Role in physiological target recognition and contribution to disease.

Journal of immunology (Baltimore, Md. : 1950)
2025

C-model: A comprehensive enhanced pharmacokinetic/pharmacodynamic simulation environment targeting the complement system.

British journal of pharmacology
2025

Malignancies and glomerulonephritis: when to suspect and when to screen?

Clinical kidney journal
2025

Monoclonal gammopathy-associated C3 glomerulonephritis secondary to follicular lymphoma: a case report.

Frontiers in immunology
2025

Mycoplasma Infection Associated C3 Glomerulopathy.

Indian journal of pediatrics
2025

Comparative Analysis of Proteinuria and Longitudinal Outcomes in Immune Complex Membranoproliferative Glomerulonephritis and C3 Glomerulopathy.

Kidney international reports
2025

Truncated complement factor H Y402 gene therapy rescues C3 glomerulonephritis.

Molecular therapy : the journal of the American Society of Gene Therapy
2025

The Recurrence of Systemic Diseases in Kidney Transplantation.

Journal of clinical medicine
2025

Selective factor B inhibition with iptacopan: transforming C3 glomerulopathy management.

International urology and nephrology
2025

IdeZ protease does not prevent convertase stabilization by C3 nephritic factors in C3 glomerulopathy.

Nephrology, dialysis, transplantation : official publication of the European Dialysis and Transplant Association - European Renal Association
2025

Updates on Glomerular Diseases: A Summary of Inaugural GlomCon Hawaii 2024.

Glomerular diseases
2025

Factor H-related 2 levels dictate FHR dimer composition.

Scientific reports
2025

Effective long-term treatment with moss-produced factor H by overcoming the antibody response in a mouse model of C3G.

Frontiers in immunology
2025

Clinical characteristics and short term outcomes of childhood immune complex membranoproliferative glomerulonephritis and C3 glomerulopathy: a single centre retrospective study.

BMC nephrology
2025

Acquired drivers of C3 glomerulopathy.

Clinical kidney journal
2025

Assessing C3 glomerulopathy outcomes in children: how concerned should we be?

Pediatric nephrology (Berlin, Germany)
2025

Iptacopan Reduces Proteinuria and Stabilizes Kidney Function in C3 Glomerulopathy.

Kidney international reports
2025

Kidney Transplantation in Children and Adolescents With C3 Glomerulopathy or Immune Complex Membranoproliferative Glomerulonephritis: An International Survey of Current Practice.

Pediatric transplantation
2024

Clinical features and outcomes of immune complex-membranoproliferative glomerulonephritis and C3 glomerulopathy: a multicenter observational cohort study analyzing kidney biopsy cases.

Kidney research and clinical practice
2025

C3 glomerulopathy associated with mycoplasma pneumoniae infection and positive IgA staining.

BMC nephrology
2024

Novel immunochromatographic test for rapid detection of anti-factor H autoantibodies with an assessment of its clinical relevance.

Frontiers in immunology
2025

C3 glomerulonephritis associated with monoclonal gammopathy of renal significance: a diagnostic and therapeutic challenge.

Jornal brasileiro de nefrologia
2025

Why Is C5a Inflammatory Complement Inhibition Not Enough to Improve C3 Glomerulopathy?

Journal of the American Society of Nephrology : JASN
2025

Pegcetacoplan for the Treatment of Paediatric C3 Glomerulonephritis: A Case Report.

Nephrology (Carlton, Vic.)
2025

Improved therapeutic efficacy of a bifunctional anti-C5 mAb-FH SCR1-5 fusion protein over anti-C5 mAb in an accelerated mouse model of C3 glomerulopathy.

ImmunoHorizons
2024

Adverse drug events (ADEs) risk signal mining related to eculizumab based on the FARES database.

Frontiers in pharmacology
2025

Efficacy of complement inhibition with pegcetacoplan in children with C3 glomerulopathy.

Pediatric nephrology (Berlin, Germany)
2025

Anticomplement Therapies for C3 Glomerulopathy and Immune-Complex Membranoproliferative Glomerulonephritis Recurrence - A Dawn of New Hope.

Kidney international reports
2025

Efficacy and Safety of Pegcetacoplan in Kidney Transplant Recipients With Recurrent Complement 3 Glomerulopathy or Primary Immune Complex Membranoproliferative Glomerulonephritis.

Kidney international reports
2025

Outcome of Patients Transplanted for C3 Glomerulopathy and Primary Immune Complex-Mediated Membranoproliferative Glomerulonephritis.

Kidney international reports
2024

The Difficulties of Treating Complement-3-Mediated Glomerulopathy.

American journal of therapeutics
2025

Recurrence of Glomerular Diseases after Kidney Transplantation: What Do We Know New?

Nephron
2025

When a NeF Is Not Enough: Improving Assays in C3 Glomerulopathy.

Journal of the American Society of Nephrology : JASN
2025

Establishing the Future Direction of Clinical Outcomes in C3 Glomerulopathy: Perspectives From a Patient and a Physician.

Kidney medicine
2025

Monoclonal gammopathy is present in one fourth of patients undergoing renal biopsy but is pathogenic only in half of them.

Journal of nephrology
2025

Idiopathic inflammatory myopathy and C3 glomerulopathy: a rare association.

Journal of nephrology
2025

Minimal Change Disease and Focal Segmental Glomerulosclerosis Are Associated with Good Kidney Prognosis and Thrombotic Microangiopathy with Poor Kidney Survival in Patients with COVID-19-Associated Nephropathies.

American journal of nephrology
2024

Outcomes of Covid-19 Vaccine-Associated Glomerular Diseases (CVAGD) - A Case Series from India.

Indian journal of nephrology
2024

Late Recurrence of C3 Glomerulopathy After SARS-CoV-2 Infection in a Long-Term Kidney Transplant Recipient: A Case Report.

The American journal of case reports
2025

De Novo C3 Glomerulonephritis of Allograft Associated With Factor H Autoantibody in a Patient with Systemic Lupus Erythematosus: A Case Report.

Transplantation proceedings
2024

C3 Glomerulopathy: A Current Perspective in an Evolving Landscape.

Glomerular diseases
2025

Complement in Kidney Transplantation.

Transplantation reviews (Orlando, Fla.)
2025

C3 glomerulopathy in children: experience at a resource-limited center.

Clinical and experimental pediatrics
2025

C3 glomerulopathy in children: a European longitudinal study evaluating outcome.

Pediatric nephrology (Berlin, Germany)
2024

[What is proven in the treatment of complement-mediated kidney diseases?].

Innere Medizin (Heidelberg, Germany)
2024

C3 glomerulopathy is highly prevalent in French Polynesia.

Journal of translational autoimmunity
2025

Acquired and genetic drivers of C3 and C5 convertase dysregulation in C3 glomerulopathy and immunoglobulin-associated MPGN.

Nephrology, dialysis, transplantation : official publication of the European Dialysis and Transplant Association - European Renal Association
2025

Acquired and genetic determinants of disease phenotype and therapeutic strategies in C3 glomerulopathy and immunoglobulin-associated MPGN.

Nephrology, dialysis, transplantation : official publication of the European Dialysis and Transplant Association - European Renal Association
2024

C3 glomerulopathy: a kidney disease mediated by alternative pathway deregulation.

Frontiers in nephrology
2024

Childhood onset C3 glomerulopathy: recurrence after kidney transplantation-a case series.

Frontiers in pediatrics
2024

Prognostic factors and validation of the histologic chronicity score for C3 glomerulopathy: a registry analysis.

Clinical kidney journal
2025

Safety and Efficacy of Avacopan in Patients with Complement 3 Glomerulopathy: Randomized, Double-Blind Clinical Trial.

Journal of the American Society of Nephrology : JASN
2024

Truncated Complement Factor H Y402 Gene Therapy Cures C3 Glomerulonephritis.

bioRxiv : the preprint server for biology
2025

Functional Characterization of Anti-C3bBb Autoantibodies and C3 Glomerulopathy Phenotype.

Journal of the American Society of Nephrology : JASN
2024

Glomerular injury induced by vinyl carbamate in A/J inbred mice: a novel model of membranoproliferative glomerulonephritis.

Frontiers in pharmacology
2024

How Stem and Progenitor Cells Can Affect Renal Diseases.

Cells
2025

Successfully treated C3 glomerulopathy in which protein and genetic analyses were useful for diagnosis.

CEN case reports
2024

Corrigendum: Genetic investigation of Nordic patients with complement-mediated kidney diseases.

Frontiers in immunology
2024

Monoclonal gammopathy of renal significance from the perspective of nephrologists.

Blood research
2024

First Successful Treatment of a Patient with a Primary Immune Complex-Membranoproliferative Glomerulonephritis with Iptacopan: A Case Report.

Case reports in nephrology and dialysis
2024

C3 Glomerulopathy Recurs Early after Kidney Transplantation in Serial Biopsies Performed within the First 2 Years after Transplantation.

Clinical journal of the American Society of Nephrology : CJASN
2024

Kidney transplantation in children and adolescents with C3 glomerulopathy or immune complex membranoproliferative glomerulonephritis: a real-world study within the CERTAIN research network.

Pediatric nephrology (Berlin, Germany)
2024

Prognosis is still poor in patients with posttransplant C3 glomerulopathy despite eculizumab use.

Clinical kidney journal
2024

Update on C3 Glomerulopathy.

Advances in kidney disease and health
2024

Unsupervised Clustering of Membranoproliferative Glomerulonephritis and C3 Glomerulopathy Patients Discovers Distinct Patient Groups unlike the Current Classification.

Nephron
2024

Updates on C3 Glomerulopathy in Kidney Transplantation: Pathogenesis and Treatment Options.

International journal of molecular sciences
2024

Proof of concept of a new plasma complement Factor H from waste plasma fraction.

Frontiers in immunology
2024

Apolipoprotein E in dense deposits: a parting of the ways in C3 glomerulopathy.

Clinical kidney journal
2024

Urinary complement biomarkers in immune-mediated kidney diseases.

Frontiers in immunology
2024

Comprehensive functional characterization of complement factor I rare variant genotypes identified in the SCOPE geographic atrophy cohort.

The Journal of biological chemistry
2024

The role of complement in kidney disease: conclusions from a Kidney Disease: Improving Global Outcomes (KDIGO) Controversies Conference.

Kidney international
2024

Developing Therapies for C3 Glomerulopathy: Report of the Kidney Health Initiative C3 Glomerulopathy Trial Endpoints Work Group.

Clinical journal of the American Society of Nephrology : CJASN
2024

IgM autoantibodies to complement factor H in C3 glomerulopathy.

Journal of nephrology
2024

Multiple Myeloma as a Potential Cause of Low Complements in Patients With Acute Kidney Injury.

Cureus
2024

Moss-produced human complement factor H with modified glycans has an extended half-life and improved biological activity.

Frontiers in immunology
2024

Primary immunodeficiency as a cause of immune-mediated kidney diseases.

Nephrology, dialysis, transplantation : official publication of the European Dialysis and Transplant Association - European Renal Association
2024

Factor B Inhibition with Iptacopan in Recurrent C3 Glomerulopathy Following Kidney Transplant: A Report of Two Cases.

Kidney medicine
2024

Complement Terminal Pathway Activation and Intrarenal Immune Response in C3 Glomerulopathy.

Journal of the American Society of Nephrology : JASN
2024

Clinical characteristics and outcomes of immune-complex membranoproliferative glomerulonephritis and C3 glomerulopathy in Japanese children.

Pediatric nephrology (Berlin, Germany)
2024

Recurrent disease after pediatric renal transplantation.

Pediatric transplantation
2024

C3 Dominant Collapsing Focal Segmental Glomerulosclerosis - A Report of Two Rare Cases.

Indian journal of nephrology
2024

Clinical and pathological features of 52 patients with glomerulonephritis with dominant C3.

Zhong nan da xue xue bao. Yi xue ban = Journal of Central South University. Medical sciences
2024

Successful Treatment of Posttransplant Monoclonal Gammopathy-associated C3 Glomerulopathy With Plasma Cell Clone-directed Therapy.

Transplantation direct
2024

Diagnostic Challenges and Emerging Pathogeneses of Selected Glomerulopathies.

Pediatric and developmental pathology : the official journal of the Society for Pediatric Pathology and the Paediatric Pathology Society
2024

C3 concentrations can be normal in patients with C3 glomerulopathy secondary to C3 nephritic factor.

Journal of clinical pathology
2024

C3 Glomerulopathy: Novel Treatment Paradigms.

Kidney international reports
2024

Digital Ischemia as a Rare Manifestation of C3 Glomerulopathy Associated With Monoclonal Gammopathy.

Kidney international reports
2024

Apolipoprotein E is enriched in dense deposits and is a marker for dense deposit disease in C3 glomerulopathy.

Kidney international
2024

Hot Spot of Complement Factor I Rare Variant p.Ile357Met in Patients With Hemolytic Uremic Syndrome.

American journal of kidney diseases : the official journal of the National Kidney Foundation
2024

Recurrent C3 glomerulopathy after kidney transplantation.

Transplantation reviews (Orlando, Fla.)
2024

Triple-fusion protein (TriFu): A potent, targeted, enzyme-like inhibitor of all three complement activation pathways.

The Journal of biological chemistry
2024

Eculizumab dose tapering should take into account the nonlinearity of its pharmacokinetics.

British journal of clinical pharmacology
2024

Efficacy of GalNAc C3 siRNAs in factor H-deficient mice with C3 glomerulopathy.

Molecular immunology
2024

Defining Nephritic Factors as Diverse Drivers of Systemic Complement Dysregulation in C3 Glomerulopathy.

Kidney international reports
2024

Rationale and design of the Japanese Biomarkers in Nephrotic Syndrome (J-MARINE) study.

Clinical and experimental nephrology
2024

Histologic and Clinical Factors Associated with Kidney Outcomes in IgA Vasculitis Nephritis.

Clinical journal of the American Society of Nephrology : CJASN
2024

Anti-factor B antibodies in atypical hemolytic uremic syndrome.

Pediatric nephrology (Berlin, Germany)
2023

C3 Glomerulonephritis Presenting With Nephritic and Nephrotic Syndromes: Spontaneous Remission After Six Months on Dialysis.

Cureus
2023

[Comparative characteristics of the complement system in patients with C3-glomerulopathy and atypical hemolytic uremic syndrome of chronic course who suffered an acute episode of thrombotic microangiopathy].

Terapevticheskii arkhiv
2023

Efficacy and Safety of Iptacopan in Patients With C3 Glomerulopathy.

Kidney international reports
2024

The Improved Kidney Risk Score in ANCA-Associated Vasculitis for Clinical Practice and Trials.

Journal of the American Society of Nephrology : JASN
2024

[Translated article] Pharmacokinetics of eculizumab in adult and pediatric patients with atypical hemolytic uremic syndrome and C3 glomerulopathy.

Farmacia hospitalaria : organo oficial de expresion cientifica de la Sociedad Espanola de Farmacia Hospitalaria
2024

Complement gene mutations in children with C3 glomerulopathy: do they affect the response to mycophenolate mofetil?

Pediatric nephrology (Berlin, Germany)
2023

Clinical Safety and Efficacy of Pegcetacoplan in a Phase 2 Study of Patients with C3 Glomerulopathy and Other Complement-Mediated Glomerular Diseases.

Kidney international reports
2024

Low C3 in a 4-month-old baby: is it a problem?

Pediatric nephrology (Berlin, Germany)
2024

Overlapping Atypical Hemolytic Uremic Syndrome and C3 Glomerulopathy with Mutation in CFI in a Japanese Patient: A Case Report.

Internal medicine (Tokyo, Japan)
2023

Clinical research advances of CFHR5 nephropathy: a recent review.

European review for medical and pharmacological sciences
2024

C3 glomerulopathy in a patient with a history of post-infectious glomerulonephritis.

Pediatric nephrology (Berlin, Germany)
2024

Morphological and etiological analyses of C3 and non-C3 glomerulonephritis in primary membranoproliferative glomerulonephritis using periodic acid-methenamine silver stain electron microscopy: a retrospective multicentered study.

Medical molecular morphology
2023

Etiology and Outcomes of Rapidly Progressive Glomerulonephritis in Children: A Retrospective Cohort Study.

Indian pediatrics
2024

From Patterns to Proteins: Mass Spectrometry Comes of Age in Glomerular Disease.

Journal of the American Society of Nephrology : JASN
2023

Genetic investigation of Nordic patients with complement-mediated kidney diseases.

Frontiers in immunology
2024

Complement inhibitors in pediatric kidney diseases: new therapeutic opportunities.

Pediatric nephrology (Berlin, Germany)
2023

[Diagnosis and treatment of glomerular diseases with a membranoproliferative glomerulonephritis (MPGN) pattern of injury].

Wiener klinische Wochenschrift
2023

Daratumumab in the treatment of C3 glomerulopathy with monoclonal gammopathy: a case report and literature review.

Frontiers in medicine
2024

Expansion of Anticomplement Therapy Indications from Rare Genetic Disorders to Common Kidney Diseases.

Annual review of medicine
2023

Association of monoclonal gammopathy of undetermined significance and C3 glomerulopathy.

Internal medicine journal
2023

Rare Variants in Complement Gene in C3 Glomerulopathy and Immunoglobulin-Mediated Membranoproliferative GN.

Clinical journal of the American Society of Nephrology : CJASN
2024

C3G and Ig-MPGN-treatment standard.

Nephrology, dialysis, transplantation : official publication of the European Dialysis and Transplant Association - European Renal Association
2023

Recurrent C3 Glomerulonephritis along with BK-Virus-Associated Nephropathy after Kidney Transplantation: A Case Report.

Medicina (Kaunas, Lithuania)
2024

Pioglitazone, a PPAR-y agonist, as one of the new therapeutic candidates for C3 glomerulopathy.

Pediatric nephrology (Berlin, Germany)
2023

Liver factor B silencing to cure C3 glomerulopathy: Evidence from a mouse model of complement dysregulation.

Molecular immunology
2024

Targeted therapy in glomerular diseases.

Journal of the Formosan Medical Association = Taiwan yi zhi
2023

Design and Rationale of the APPELHUS Phase 3 Open-Label Study of Factor B Inhibitor Iptacopan for Atypical Hemolytic Uremic Syndrome.

Kidney international reports
2023

Targeting the Complement Pathway in Kidney Transplantation.

Journal of the American Society of Nephrology : JASN
2023

A 78-Year-Old Man with Chronic Kidney Disease and Monoclonal Gammopathy Who Developed Post-Transplant C3 Glomerulopathy - Recurrence or De Novo? A Case Report and Literature Review.

The American journal of case reports
2023

Successful treatment with avacopan (CCX168) in a pediatric patient with C3 glomerulonephritis.

Pediatric nephrology (Berlin, Germany)
Ver todos os 325 no EuropePMC

Associações

Organizações que acompanham esta doença — pra ter apoio e orientação

Ainda não temos associações cadastradas para Glomerulopatia C3.

É de uma associação que acompanha esta doença? Fale com a gente →

Comunidades

Grupos ativos de quem convive com esta doença aqui no Raras

Ainda não existe comunidade no Raras para Glomerulopatia C3

Pacientes, familiares e cuidadores se organizam em comunidades pra compartilhar experiências, fazer perguntas e se apoiar. Você pode ser o primeiro.

Tire suas dúvidas

Perguntas, dicas e experiências compartilhadas aqui na página

Participe da discussão

Faça login para postar dúvidas, compartilhar experiências e interagir com especialistas.

Fazer login

Doenças relacionadas

Doenças com sintomas parecidos — ajudam quem ainda está buscando diagnóstico

Referências e fontes

Bases de dados externas citadas neste artigo

Publicações científicas

Artigos indexados no PubMed ligados a esta doença no grafo RarasNet — título, periódico e PMID direto da fonte, sem intermediação de IA.

  1. Treatment of atypical hemolytic uremic syndrome and C3 glomerulopathy in mice by hepatic expression of factor D.
    Blood advances· 2026· PMID 41544220mais citado
  2. Clinical Profile and Outcome of C3-Dominant Glomerulonephritis: Retrospective Study.
    Kidney &amp; blood pressure research· 2026· PMID 41525388mais citado
  3. Pegcetacoplan in C3 Glomerulopathy and Immune-Complex MPGN. Reply.
    The New England journal of medicine· 2026· PMID 41812205mais citado
  4. Pegcetacoplan in C3 Glomerulopathy and Immune-Complex MPGN.
    The New England journal of medicine· 2026· PMID 41812204mais citado
  5. Autoantibodies Targeting Complement Regulating Factors Induced C3 Glomerulopathy Resambling C4 Dense Deposit Disease: A Case Report.
    Nephrology (Carlton, Vic.)· 2026· PMID 41866222mais citado
  6. New Anticomplement Drugs in Nephrology - Mechanism and Indication.
    Kidney Blood Press Res· 2026· PMID 41961736recente
  7. Clinical Images: Anti-MDA5 dermatomyositis with rapidly progressive interstitial lung disease presenting with rapidly progressive glomerulonephritis due to C3 glomerulopathy.
    ACR Open Rheumatol· 2026· PMID 41947495recente
  8. Finding the etiology of membranoproliferative glomerulonephritis.
    Kidney Int· 2026· PMID 41895686recente
  9. A Case Series of Elevated Donor-Derived Cell-Free DNA Leading to Diagnosis of Posttransplant Glomerulonephritis.
    Kidney Med· 2026· PMID 41884764recente

Bases de dados e fontes oficiais

Identificadores e referências canônicas usadas para montar este verbete.

  1. ORPHA:329918(Orphanet)
  2. MONDO:0018013(MONDO)
  3. GARD:17507(GARD (NIH))
  4. Variantes catalogadas(ClinVar)
  5. Busca completa no PubMed(PubMed)
  6. Q56014073(Wikidata)

Dados compilados pelo RarasNet a partir de fontes abertas (Orphanet, OMIM, MONDO, PubMed/EuropePMC, ClinicalTrials.gov, DATASUS, PCDT/MS). Este conteúdo é informativo e não substitui avaliação médica.

Conteúdo mantido por Agente Raras · Médicos e pesquisadores podem colaborar

Glomerulopatia C3
Compêndio · Raras BR

Glomerulopatia C3

ORPHA:329918 · MONDO:0018013
Prevalência
1-9 / 1 000 000
Herança
Multigenic/multifactorial
CID-10
N03.5 · Síndrome nefrítica crônica - glomerulonefrite mesangiocapilar difusa
CID-11
Ensaios
12 ativos
Medicamentos
4 registrados
Início
All ages
Prevalência
0.15 (Europe)
MedGen
UMLS
C4087273
EuropePMC
Wikidata
Papers 10a
Evidência
🥉 Relato de caso
DiscussaoAtiva

Nenhuma novidade ainda. O agente esta monitorando.

0membros
0novidades