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Síndrome Simpson-Golabi-Behmel
ORPHA:373CID-10 · Q87.3CID-11 · LD2CDOENÇA RARA

A Síndrome de Simpson-Golabi-Behmel é uma condição genética rara, ligada ao cromossomo X, caracterizada por: crescimento excessivo antes e depois do nascimento; traços distintos no rosto e na cabeça; diversas malformações presentes desde o nascimento; aumento do tamanho dos órgãos e um risco maior de desenvolver tumores.

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Introdução

O que você precisa saber de cara

📋

A Síndrome de Simpson-Golabi-Behmel é uma condição genética rara, ligada ao cromossomo X, caracterizada por: crescimento excessivo antes e depois do nascimento; traços distintos no rosto e na cabeça; diversas malformações presentes desde o nascimento; aumento do tamanho dos órgãos e um risco maior de desenvolver tumores.

Publicações científicas
342 artigos
Último publicado: 2026 Mar 22

Escala de raridade

CLASSIFICAÇÃO ORPHANET · BRASIL 2024
<1 / 1 000 000
Ultra-rara
<1/50k
Muito rara
1/20k
Rara
1/10k
Pouco freq.
1/5k
Incomum
1/2k
Prevalência
0.0
Worldwide
Casos conhecidos
250
pacientes catalogados
Início
Antenatal
+ childhood, infancy, neonatal
🏥
SUS: Cobertura mínimaScore: 15%
CID-10: Q87.3
🇧🇷Dados SUS / DATASUS
PROCEDIMENTOS SIGTAP (5)
0202010503
Cariótipo — bandas G, Q ou Rgenetic_test
0202010600
Pesquisa de microdeleções/microduplicações por FISHlab_test
0202010694
Sequenciamento completo do exoma (WES)rehabilitation
0202010260
Dosagem de alfa-fetoproteína
0301070040
Atendimento em reabilitação — doenças raras
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Entender a doença

Do básico ao detalhe, leia no seu ritmo

Preparando trilha educativa...

Sinais e sintomas

O que aparece no corpo e com que frequência cada sintoma acontece

Partes do corpo afetadas

🦴
Ossos e articulações
29 sintomas
😀
Face
15 sintomas
🧠
Neurológico
10 sintomas
🫃
Digestivo
10 sintomas
❤️
Coração
7 sintomas
🫁
Pulmão
6 sintomas

+ 49 sintomas em outras categorias

Características mais comuns

90%prev.
Displasia renal multicística
Muito frequente (99-80%)
90%prev.
Fusão vertebral
Muito frequente (99-80%)
90%prev.
Prognatismo mandibular
Muito frequente (99-80%)
90%prev.
Polidactilia pós-axial da mão
Muito frequente (99-80%)
90%prev.
Defeito do septo ventricular
Muito frequente (99-80%)
90%prev.
Traços faciais grosseiros
Muito frequente (99-80%)
145sintomas
Muito frequente (21)
Frequente (35)
Ocasional (23)
Sem dados (66)

Os sintomas variam de pessoa para pessoa. Abaixo estão as 145 características clínicas mais associadas, ordenadas por frequência.

Displasia renal multicísticaMulticystic kidney dysplasia
Muito frequente (99-80%)90%
Fusão vertebralVertebral fusion
Muito frequente (99-80%)90%
Prognatismo mandibularMandibular prognathia
Muito frequente (99-80%)90%
Polidactilia pós-axial da mãoPostaxial hand polydactyly
Muito frequente (99-80%)90%
Defeito do septo ventricularVentricular septal defect
Muito frequente (99-80%)90%

Linha do tempo da pesquisa

Publicações por ano — veja quando o interesse científico cresceu
Anos de pesquisa1desde 2026
Total histórico342PubMed
Últimos 10 anos184publicações
Pico201625 papers
Linha do tempo
2026Hoje · 2026🧪 2015Primeiro ensaio clínico📈 2016Ano de pico
Publicações por ano (últimos 10 anos)

Encontrou um erro ou informação desatualizada? Sugira uma correção →

Genética e causas

O que está alterado no DNA e como passa nas famílias

Genes associados

3 genes identificados com associação a esta condição. Padrão de herança: X-linked recessive.

GPC4Glypican-4Candidate gene tested inAltamente restrito
FUNÇÃO

Cell surface proteoglycan that bears heparan sulfate. May be involved in the development of kidney tubules and of the central nervous system (By similarity)

LOCALIZAÇÃO

Cell membraneSecreted, extracellular space

VIAS BIOLÓGICAS (1)
Glycosaminoglycan-protein linkage region biosynthesis
MECANISMO DE DOENÇA

Keipert syndrome

An X-linked recessive syndrome characterized by craniofacial and digital abnormalities. Clinical features include a prominent forehead, a flat midface, hypertelorism, a broad nose, downturned corners of mouth, and widening of all distal phalanges. Additional variable features are cognitive impairment and sensorineural deafness.

EXPRESSÃO TECIDUAL(Ubíquo)
Esôfago - Muscular
65.5 TPM
Esôfago - Junção
59.2 TPM
Aorta
57.7 TPM
Artéria tibial
52.8 TPM
Cólon sigmoide
44.6 TPM
OUTRAS DOENÇAS (2)
Keipert syndromeSimpson-Golabi-Behmel syndrome
HGNC:4452UniProt:O75487
OFD1Centriole and centriolar satellite protein OFD1Disease-causing germline mutation(s) inAltamente restrito
FUNÇÃO

Component of the centrioles controlling mother and daughter centrioles length. Recruits to the centriole IFT88 and centriole distal appendage-specific proteins including CEP164 (By similarity). Involved in the biogenesis of the cilium, a centriole-associated function. The cilium is a cell surface projection found in many vertebrate cells required to transduce signals important for development and tissue homeostasis (PubMed:33934390). Plays an important role in development by regulating Wnt signa

LOCALIZAÇÃO

Cytoplasm, cytoskeleton, microtubule organizing center, centrosome, centrioleCytoplasm, cytoskeleton, cilium basal bodyNucleusCytoplasm, cytoskeleton, microtubule organizing center, centrosome, centriolar satellite

VIAS BIOLÓGICAS (8)
Recruitment of mitotic centrosome proteins and complexesLoss of proteins required for interphase microtubule organization from the centrosomeLoss of Nlp from mitotic centrosomesRegulation of PLK1 Activity at G2/M TransitionAURKA Activation by TPX2
MECANISMO DE DOENÇA

Orofaciodigital syndrome 1

A form of orofaciodigital syndrome, a group of heterogeneous disorders characterized by abnormalities in the oral cavity, face, and digits and associated phenotypic abnormalities that lead to the delineation of various subtypes. OFD1 is X-linked dominant syndrome, lethal in males. Craniofacial findings consist of facial asymmetry, hypertelorism, median cleft, or pseudocleft of the upper lip, hypoplasia of the alae nasi, oral clefts and abnormal frenulea, tongue anomalies (clefting, cysts, hamartoma), and anomalous dentition involving missing or extra teeth. Asymmetric brachydactyly and/or syndactyly of the fingers and toes occur frequently. Approximately 50% of OFD1 females have some degree of intellectual disability. Some patients have structural central nervous system anomalies such as agenesis of the corpus callosum, cerebellar agenesis, or a Dandy-Walker malformation. Patients with OFD1 can develop fibrocystic disease of the liver and pancreas, in addition to polycystic kidneys.

EXPRESSÃO TECIDUAL(Ubíquo)
Ovário
47.1 TPM
Fallopian Tube
44.0 TPM
Tireoide
42.2 TPM
Cervix Endocervix
39.8 TPM
Útero
36.8 TPM
OUTRAS DOENÇAS (8)
Joubert syndrome 10orofaciodigital syndrome Iretinitis pigmentosa 23Simpson-Golabi-Behmel syndrome type 2
HGNC:2567UniProt:O75665
GPC3Glypican-3Disease-causing germline mutation(s) (loss of function) inAltamente restrito
FUNÇÃO

Cell surface proteoglycan (PubMed:14610063). Negatively regulates the hedgehog signaling pathway when attached via the GPI-anchor to the cell surface by competing with the hedgehog receptor PTC1 for binding to hedgehog proteins (By similarity). Binding to the hedgehog protein SHH triggers internalization of the complex by endocytosis and its subsequent lysosomal degradation (By similarity). Positively regulates the canonical Wnt signaling pathway by binding to the Wnt receptor Frizzled and stimu

LOCALIZAÇÃO

Cell membrane

VIAS BIOLÓGICAS (2)
Post-translational protein phosphorylationRegulation of Insulin-like Growth Factor (IGF) transport and uptake by Insulin-like Growth Factor Binding Proteins (IGFBPs)
MECANISMO DE DOENÇA

Simpson-Golabi-Behmel syndrome 1

A condition characterized by pre- and postnatal overgrowth (gigantism), facial dysmorphism and a variety of inconstant visceral and skeletal malformations. Characteristic dysmorphic features include macrocephaly with coarse, distinctive facies with a large protruding jaw, broad nasal bridge and cleft palate. Cardiac defects are frequent.

EXPRESSÃO TECIDUAL(Ubíquo)
Pulmão
201.3 TPM
Tecido adiposo
146.7 TPM
Nervo tibial
141.8 TPM
Mama
95.2 TPM
Rim - Medula
86.6 TPM
OUTRAS DOENÇAS (4)
Wilms tumor 1Simpson-Golabi-Behmel syndrome type 1kidney Wilms tumorSimpson-Golabi-Behmel syndrome
HGNC:4451UniProt:P51654

Variantes genéticas (ClinVar)

982 variantes patogênicas registradas no ClinVar.

🧬 GPC4: GRCh37/hg19 Xq23-28(chrX:113417246-155233731)x1 ()
🧬 GPC4: GRCh37/hg19 Xq26.2(chrX:130640808-132595361)x1 ()
🧬 GPC4: GRCh37/hg19 Xq26.1-26.3(chrX:128882432-134384406)x3 ()
🧬 GPC4: NM_001448.3(GPC4):c.1061G>A (p.Arg354His) ()
🧬 GPC4: NM_001448.3(GPC4):c.1091G>A (p.Arg364His) ()
Ver todas no ClinVar

Classificação de variantes (ClinVar)

Distribuição de 262 variantes classificadas pelo ClinVar.

26
236
Patogênica (9.9%)
VUS (90.1%)
VARIANTES MAIS SIGNIFICATIVAS
OFD1: NM_003611.3(OFD1):c.2137_2149del (p.Asp712_Val713insTer) [Likely pathogenic]
OFD1: NM_003611.3(OFD1):c.1804C>T (p.Arg602Cys) [Conflicting classifications of pathogenicity]
GPC3: NM_004484.4(GPC3):c.1198_1227del (p.Ser400_Ile409del) [Uncertain significance]
GPC3: NC_000023.11:g.133692359_133754186dup [Uncertain significance]
OFD1: NM_003611.3(OFD1):c.*20_*22del [Uncertain significance]

Diagnóstico

Os sinais que médicos procuram e os exames que confirmam

Carregando...

Tratamento e manejo

Remédios, cuidados de apoio e o que precisa acompanhar

Carregando informações de tratamento...

Onde tratar no SUS

Hospitais de referência no Brasil e o protocolo oficial do SUS (PCDT)

🇧🇷 Atendimento SUS — Síndrome Simpson-Golabi-Behmel

🗺️

Selecione um estado ou use sua localização para ver resultados.

Dados de DATASUS/CNES, SBGM, ABNeuro e Ministério da Saúde. Sempre confirme a disponibilidade diretamente com o estabelecimento.

Pesquisa ativa

Ensaios clínicos abertos e novidades científicas recentes

Pesquisa e ensaios clínicos

Nenhum ensaio clínico registrado para esta condição.

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Publicações mais relevantes

Timeline de publicações
173 papers (10 anos)
#1

Development of an integrative cross-omics approach for conceptual adverse outcome pathway network construction.

Environment international2026 Mar

The abilities of recent high throughput techniques to measure biological responses is rapidly growing, therefore methods to analyse and organise these vast amounts of data into meaningful results are needed. Adverse outcome pathways (AOPs) and AOP networks (AOPNs) are an increasingly recognised framework for translating mechanistic information into useable knowledge to support policy decisions. However, many traditional statistical approaches may be ineffective at capturing nuances of high throughput data, particularly from multiple disparate layers of biological organisation. We present a comprehensive method that combines univariate differential expression (UD) analysis and multivariate integrative modeling (MIM) approaches, using transcriptomic and metabolomic data from adipocytes exposed to a classic obesogen, to develop a conceptual AOPN (cAOPN) for metabolic syndrome (MetS). Simpson-Golabi-Behmel syndrome (SGBS) preadipocyte cells were differentiated in tributyltin (TBT) and analysed using whole genome transcriptome and untargeted metabolomics analysis. UD and MIM results were used to identify perturbed features (PFs) for over-representation analysis for pathways and diseases and followed by integrated network and cluster analyses based on Jaccard similarity to reorganise resultant complex biological phenomena into exploratory depictions of cause-and-effect relationships. The resulting cAOPN for MetS was assembled and corroborated with the literature and mechanistic pathway databases that supported the identified disruptions in lipid regulation, iron transport, growth processes, key signalling processes, adipocyte differentiation, and hormonal homeostasis. Overall, by leveraging the strengths of multiple statistical methods in combination with heterogeneous data from multiple layers of biological organisation, this method facilitated the integration and interpretation of complex data into an exploratory mechanistic schema for AOP and AOPN hypothesis generation and prioritisation.

#2

MiR-874-3p suppresses TNF-α-induced inflammation in adipocytes by targeting nucleolin.

Journal of molecular histology2026 Jan 17

Many investigations have indicated the significance of microRNAs (miRNAs) as potential biomarkers for early obesity in children. MiR-874-3p was revealed to be downregulated in overweight/obese children. However, the specific function and mechanism of miR-874-3p in the progression of childhood obesity remain unclear. Human Simpson-Golabi-Behmel syndrome (SGBS) adipocytes were stimulated with tumor necrosis factor α (TNF-α) to establish an in vitro cell model. CCK-8 assay and ELISA were used to assess cell viability and proinflammatory cytokine secretion, respectively. RT-qPCR was used for miR-874-3p expression analysis. Western blotting was utilized to evaluate protein levels of miR-874-3p downstream targets and nuclear factor kappa B (NF-κB) signaling-related markers. Luciferase reporter assay was conducted to verify the binding relation between miR-874-3p and nucleolin (NCL). MiR-874-3p overexpression attenuated TNF-α-induced inhibition of cell viability and promotion of proinflammatory cytokine production. Mechanistically, NCL served as a target of miR-874-3p, and overexpressing miR-874-3p inactivated NCL-mediated NF-κB signaling. Moreover, NCL upregulation reversed miR-874-3p overexpression-mediated effects on the viability and proinflammatory cytokines in SGBS adipocytes. MiR-874-3p alleviates TNF-α-induced inflammatory response in SGBS adipocytes by downregulating NCL and inactivating NF-κB signaling.

#3

Canagliflozin regulates adipocyte lipolysis in vitro via a SGLT2 independent signaling pathway.

International journal of obesity (2005)2026 Jan 07

Adipose lipolysis, a process involving the degradation of triglycerides and the release of fatty acids and glycerol, is an important biological event in lipid metabolism. Canagliflozin (Cana), an oral antidiabetic drug, regulates blood glucose by inhibiting sodium-glucose cotransporter 2 (SGLT2) in renal tubules and has also been shown to improve lipid metabolism in adipocytes. This study aims to determine whether Cana directly affects adipose lipolysis and to explore the underlying mechanistic pathways. Primary mature adipocytes and differentiated preadipocytes isolated from the epididymal fat pads of Sprague-Dawley rats were used as in vitro models. The effects of Cana on glycerol release and lipase activity were evaluated using ELISA and Western blot analyses. Cana treatment directly inhibited basal glycerol release and lipase activity in both primary adipocytes and topically administered adipose tissue, achieving a dose-dependent 35% to 65% suppression of lipolysis. This was associated with a 2.3-fold decrease in the level of HSL phosphorylated at the Ser660 site. Using differentiated adipocytes derived from the human Simpson-Golabi-Behmel syndrome (SGBS) pre-adipocyte cell line, we found that Cana significantly attenuated glycerol release (~32% to 53% reductions) induced by lipolysis. Moreover, Cana exerted antilipolytic effects in models of both acute (isoprenaline-induced) and chronic (tumor necrosis factor-α-induced) lipolysis. Mechanistically, the antilipolytic effect of Cana was mediated through activation of the PI3K/AKT pathway and reduction of cAMP production. In conclusion, Cana regulates adipocyte lipolysis via an SGLT2-independent signaling pathway, which enhances our understanding of its role in modulating lipid metabolism.

#4

Simpson-Golabi-Behmel Syndrome Associated With a Missense Variant at the Signal Peptide Cleavage Site of GPC3.

American journal of medical genetics. Part A2026 Apr

Translocation of newly synthesized proteins into the lumen of the endoplasmic reticulum (ER) is mediated by signal peptide recognition and cleavage. Here we report an individual with Simpson-Golabi-Behmel syndrome (SGBS) bearing a GPC3 missense variant at the signal peptide cleavage site of the glypican-3 protein. The c.71C>T; p.(Ala24Val) alteration in the key -1 position of the cleavage greatly reduces cleavage of the signal peptide, resulting in failure of the protein to efficiently exit the ER, and impaired glycosylation. Functional characterization of two other engineered variants at this position-one predicted to permit cleavage and the other to prevent it-corroborates our findings. This case highlights the potential for missense variants within the signal peptide cleavage site to underlie genetic disorders, and reinforces the idea that many of the missense variants in GPC3 that cause SGBS reside in motifs with high functional relevance to the processing and maturation of glypican-3.

#5

Functional Characterization of a Novel GPC3 Missense Variant in Simpson-Golabi-Behmel Syndrome.

American journal of medical genetics. Part A2026 Mar

Simpson-Golabi-Behmel syndrome 1 (SGBS1) is a rare X-linked recessive condition characterized by overgrowth and multiple congenital anomalies. SGBS1 is caused by damaging variants in the Glypican-3 (GPC3) gene. The GPC3 protein plays a crucial role in cellular signaling processes including cell growth, embryogenesis, and differentiation. Functional maturation of GPC3 occurs via several steps of post-translational modification (PTM) and processing to enable its transport to, and anchorage on, the plasma membrane. GPC3 positively modulates the canonical Wnt signaling pathways, while negatively regulating the Hedgehog signaling pathways. Loss-of-function is the underlying mechanism of disease for SGBS1, with a minority of reported pathogenic variants being missense substitutions. We report a family with four affected individuals in whom a novel GPC3 missense variant was identified via exome sequencing: NM_004484.3: c.695C>A; p.(Ala232Asp). The variant segregated with disease in the family, and functional studies conducted using HEK293T cells demonstrate a distinct mis-localization of the mutant GPC3 protein, thereby supporting the pathogenicity of this novel missense variant. These findings allowed for an upgraded classification of the missense variant from a variant of uncertain significance to that of likely pathogenic.

Publicações recentes

Ver todas no PubMed

📚 EuropePMC131 artigos no totalmostrando 179

2026

Development of an integrative cross-omics approach for conceptual adverse outcome pathway network construction.

Environment international
2026

MiR-874-3p suppresses TNF-α-induced inflammation in adipocytes by targeting nucleolin.

Journal of molecular histology
2026

Canagliflozin regulates adipocyte lipolysis in vitro via a SGLT2 independent signaling pathway.

International journal of obesity (2005)
2025

Palmitic acid differently modulates extracellular vesicles and cellular fatty acid composition of SGBS adipocytes without impairing their insulin signaling.

Frontiers in endocrinology
2026

Simpson-Golabi-Behmel Syndrome Associated With a Missense Variant at the Signal Peptide Cleavage Site of GPC3.

American journal of medical genetics. Part A
2025

Capsaicin camphor and caffeic acid reduce adipogenesis and promote lipolysis with TRPV1 involvement.

Scientific reports
2025

Cytochrome P450 1A1 influences obesity-induced pulmonary hypertension.

British journal of pharmacology
2026

Functional Characterization of a Novel GPC3 Missense Variant in Simpson-Golabi-Behmel Syndrome.

American journal of medical genetics. Part A
2025

Anti-Inflammatory Role of Myo-Inositol in Obesity: Suppression of TNF-α-Induced Inflammation and Monocyte Adhesion in Hypertrophic Human Adipocytes.

Food science &amp; nutrition
2025

Unraveling Glypican-3: From Structural to Pathophysiological Roles and Mechanisms-An Integrative Perspective.

Cells
2025

Radioactive Tracing of Testosterone Reveals Minimal Formation of 5α-DHT in SGBS Cells and Human Primary Adipocytes.

Journal of the Endocrine Society
2025

Vitamin D modulates the content of inflammatory microRNAs in extracellular vesicles from human adipocyte cells in inflammatory context.

BioFactors (Oxford, England)
2025

The importance of thiamine availability in the thermogenic competency of human adipocytes.

Molecular and cellular endocrinology
2025

Simpson-Golabi-Behmel syndrome type 1 in a neonate with central hepatoblastoma.

BMJ case reports
2024

Expanding the Genotypic and Phenotypic Spectrum of OFD1-Related Conditions: Three More Cases.

Genes
2025

Dysmorphic syndromes with overgrowth - systematic review.  Part 1 - monogenic syndromes.

Pediatric endocrinology, diabetes, and metabolism
2024

Implicating type 2 diabetes effector genes in relevant metabolic cellular models using promoter-focused Capture-C.

Diabetologia
2025

[Giant prostatic utricle cyst in a newborn with Simpson-Golabi-Behmel syndrome: Voiding cysturethrography essential for the diagnosis].

RoFo : Fortschritte auf dem Gebiete der Rontgenstrahlen und der Nuklearmedizin
2024

Phenotypic spectrum and tumor risk in Simpson-Golabi-Behmel syndrome: Case series and comprehensive literature review.

American journal of medical genetics. Part A
2024

Endocrine disruption of adipose physiology: Screening in SGBS cells.

Journal of applied toxicology : JAT
2024

Increased secretion of adipocyte-derived extracellular vesicles is associated with adipose tissue inflammation and the mobilization of excess lipid in human obesity.

Journal of translational medicine
2024

Human Genetics of Ventricular Septal Defect.

Advances in experimental medicine and biology
2024

A case of pancreatoblastoma in a child with Simpson-Golabi-Behmel syndrome: Highlighting the importance of alpha fetoprotein monitoring.

Pediatric blood &amp; cancer
2024

Simpson-Golabi-Behmel syndrome.

American journal of medical genetics. Part C, Seminars in medical genetics
2024

Simpson-Golabi-Behmel syndrome type 1 with normal birth parameters.

BMJ case reports
2024

SARS-CoV-2 Infection Alters the Phenotype and Gene Expression of Adipocytes.

International journal of molecular sciences
2024

Whole-exome sequencing reveals causative genetic variants for several overgrowth syndromes in molecularly negative Beckwith-Wiedemann spectrum.

Journal of medical genetics
2023

DIS3L2 Gene Mutation Causes the Perlman Syndrome of Overgrowth and Wilms Tumor Susceptibility.

Cureus
2024

Divergent effects of the antiretroviral drugs, dolutegravir, tenofovir alafenamide, and tenofovir disoproxil fumarate, on human adipocyte function.

Biochemical pharmacology
2023

Myricetin attenuates hypoxia-induced inflammation in human adipocytes.

Molecular biology reports
2023

Anti-Adipogenic Activity of Rhaponticum carthamoides and Its Secondary Metabolites.

Nutrients
2023

Circulating Levels of Cathelicidin Antimicrobial Peptide (CAMP) Are Affected by Oral Lipid Ingestion.

Nutrients
2023

Single-cell transcriptome dataset of human and mouse in vitro adipogenesis models.

Scientific data
2023

Meteorin-like levels are associated with active brown adipose tissue in early infancy.

Frontiers in endocrinology
2023

Effects of allicin on human Simpson-Golabi-Behmel syndrome cells in mediating browning phenotype.

Frontiers in endocrinology
2023

Insulin-Induced AKR1C3 Induces Fatty Acid Synthase in a Model of Human PCOS Adipocytes.

Endocrinology
2023

Prenatal diagnosis of Simpson-Golabi-Behmel syndrome type 1 with an 814 kb Xq26.2 deletion with the initial presentation of a thick nuchal fold.

Taiwanese journal of obstetrics &amp; gynecology
2022

Stages of preadipocyte differentiation: biomarkers and pathways for extracellular structural remodeling.

Hereditas
2022

Hypoxia-driven metabolic reprogramming of adipocytes fuels cancer cell proliferation.

Frontiers in endocrinology
2021

Novel GPC3 Gene Mutation in Simpson-Golabi-Behmel Syndrome with Endocrine Anomalies: A Case Report.

Balkan journal of medical genetics : BJMG
2022

Differential effects of dolutegravir, bictegravir and raltegravir in adipokines and inflammation markers on human adipocytes.

Life sciences
2022

Drug-Initiated Activity Metabolomics Identifies Myristoylglycine as a Potent Endogenous Metabolite for Human Brown Fat Differentiation.

Metabolites
2022

20 Years with SGBS cells - a versatile in vitro model of human adipocyte biology.

International journal of obesity (2005)
2022

SIMPSON-GOLABI-BEHMEL syndrome type 1: How placental immunohistochemistry can rapidly Predict the diagnosis.

Placenta
2022

Adipocyte-Breast Cancer Cell Co-Culture in Transwells.

Methods in molecular biology (Clifton, N.J.)
2022

Insulin-inducible THRSP maintains mitochondrial function and regulates sphingolipid metabolism in human adipocytes.

Molecular medicine (Cambridge, Mass.)
2022

Precocious puberty in a case of Simpson-Golabi-Behmel syndrome with a de novo 240-kb deletion including GPC3.

Human genome variation
2022

MiR-122-5p regulates the pathogenesis of childhood obesity by targeting CPEB1.

Obesity research &amp; clinical practice
2022

Transcriptomic analysis of Simpson Golabi Behmel syndrome cells during differentiation exhibit BAT-like function.

Tissue &amp; cell
2022

Type I IFN stimulates IFI16-mediated aromatase expression in adipocytes that promotes E2-dependent growth of ER-positive breast cancer.

Cellular and molecular life sciences : CMLS
2022

Conversion of Classical and 11-Oxygenated Androgens by Insulin-Induced AKR1C3 in a Model of Human PCOS Adipocytes.

Endocrinology
2022

A prenatal case of Simpson-Golabi-Behmel syndrome type 1 with a 0.26-Mb deletion fragment at Xq26.2 inherited from mother: Case report.

Medicine
2022

Hepatoblastoma in molecularly defined, congenital diseases.

American journal of medical genetics. Part A
2022

[Neuroblastoma in a boy with Simpson-Golabi-Behmel syndrome].

Zhonghua er ke za zhi = Chinese journal of pediatrics
2022

Hedgehog pathway modulation by glypican 3-conjugated heparan sulfate.

Journal of cell science
2022

Simpson-Golabi-Behmel syndrome in one of the Dichorionic-diamniotic twin: a case report and literature review.

BMC pregnancy and childbirth
2021

microRNA-27a-3p but Not -5p Is a Crucial Mediator of Human Adipogenesis.

Cells
2021

Coffee Bioactive N-Methylpyridinium Attenuates Tumor Necrosis Factor (TNF)-α-Mediated Insulin Resistance and Inflammation in Human Adipocytes.

Biomolecules
2021

A functional genomics pipeline identifies pleiotropy and cross-tissue effects within obesity-associated GWAS loci.

Nature communications
2021

Differential DNA Methylation and Expression of miRNAs in Adipose Tissue From Twin Pairs Discordant for Type 2 Diabetes.

Diabetes
2021

Prenatal case of Simpson-Golabi-Behmel syndrome with a de novo 370Kb-sized microdeletion of Xq26.2 compassing partial GPC3 gene and review.

Molecular genetics &amp; genomic medicine
2021

Simpson-Golabi-Behmel syndrome: One family, same mutation, different outcome.

American journal of medical genetics. Part A
2021

D-Chiro-Inositol Regulates Insulin Signaling in Human Adipocytes.

Frontiers in endocrinology
2021

Pro-inflammatory effects of DEHP in SGBS-derived adipocytes and THP-1 macrophages.

Scientific reports
2021

Simpson-Golabi-Behmel-Syndrome in Dichorionic-Diamniotic Twin Pregnancy.

Clinics and practice
2021

Lower plasma PCSK9 in normocholesterolemic subjects is associated with upregulated adipose tissue surface-expression of LDLR and CD36 and NLRP3 inflammasome.

Physiological reports
2021

Rosmarinic acid attenuates obesity and obesity-related inflammation in human adipocytes.

Food and chemical toxicology : an international journal published for the British Industrial Biological Research Association
2020

A Case of Simpson-Golabi-Behmel Syndrome Presenting with Cutaneous Findings.

HCA healthcare journal of medicine
2021

miR-146a regulates insulin sensitivity via NPR3.

Cellular and molecular life sciences : CMLS
2020

CD90 Is Dispensable for White and Beige/Brown Adipocyte Differentiation.

International journal of molecular sciences
2021

Growth arrest-specific 6 modulates adiponectin expression and insulin resistance in adipose tissue.

Journal of diabetes investigation
2020

Thermogenic Activation Downregulates High Mitophagy Rate in Human Masked and Mature Beige Adipocytes.

International journal of molecular sciences
2020

OFD Type I syndrome: lessons learned from a rare ciliopathy.

Biochemical Society transactions
2020

Tall stature in children and adolescents.

Minerva pediatrica
2020

In vitro characterization of the effects of chronic insulin stimulation in mouse 3T3-L1 and human SGBS adipocytes.

Adipocyte
2020

A new human adipocyte model with PTEN haploinsufficiency.

Adipocyte
2020

Browning capabilities of human primary adipose-derived stromal cells compared to SGBS cells.

Scientific reports
2020

Lipidomic Phenotyping Reveals Extensive Lipid Remodeling during Adipogenesis in Human Adipocytes.

Metabolites
2020

Results of Treatment for Patients With Multicentric or Bilaterally Predisposed Unilateral Wilms Tumor (AREN0534): A report from the Children's Oncology Group.

Cancer
2020

Rare Course of Bilateral Congenital Diaphragmatic Hernia Treated Thoracoscopically-Case Report.

Frontiers in pediatrics
2020

In Depth Quantitative Proteomic and Transcriptomic Characterization of Human Adipocyte Differentiation using the SGBS Cell Line.

Proteomics
2020

The Ability of Quercetin and Ferulic Acid to Lower Stored Fat is Dependent on the Metabolic Background of Human Adipocytes.

Molecular nutrition &amp; food research
2020

Reduced circulating levels of chemokine CXCL14 in adolescent girls with polycystic ovary syndrome: normalization after insulin sensitization.

BMJ open diabetes research &amp; care
2019

The Extra-Virgin Olive Oil Polyphenols Oleocanthal and Oleacein Counteract Inflammation-Related Gene and miRNA Expression in Adipocytes by Attenuating NF-κB Activation.

Nutrients
2020

Functional Screening of Candidate Causal Genes for Insulin Resistance in Human Preadipocytes and Adipocytes.

Circulation research
2019

Simpson-Golabi-Behmel syndrome type 1 with subclinical hypothyroidism: A case report.

Medicine
2019

Hydroxytyrosol Modulates Adipocyte Gene and miRNA Expression Under Inflammatory Condition.

Nutrients
2020

Xq26 duplications lead to undergrowth or overgrowth via competing pathways including GPC3/GPC4.

Annals of human genetics
2019

Glucose Restriction Plus Refeeding in Vitro Induce Changes of the Human Adipocyte Secretome with an Impact on Complement Factors and Cathepsins.

International journal of molecular sciences
2019

Elevated UCP1 levels are sufficient to improve glucose uptake in human white adipocytes.

Redox biology
2019

The expanding phenotype of OFD1-related disorders: Hemizygous loss-of-function variants in three patients with primary ciliary dyskinesia.

Molecular genetics &amp; genomic medicine
2019

Truncating mutations in exons 20 and 21 of OFD1 can cause primary ciliary dyskinesia without associated syndromic symptoms.

Journal of medical genetics
2020

IL-29 promoted obesity-induced inflammation and insulin resistance.

Cellular &amp; molecular immunology
2020

Ameloblastoma associated with syndromes: A systematic review.

Journal of stomatology, oral and maxillofacial surgery
2020

Whole exome sequencing aids the diagnosis of Simpson-Golabi-Behmel syndrome in two male fetuses.

The Journal of international medical research
2019

Open Chromatin Profiling in Adipose Tissue Marks Genomic Regions with Functional Roles in Cardiometabolic Traits.

G3 (Bethesda, Md.)
2019

Adipocyte abundances of CES1, CRYAB, ENO1 and GANAB are modified in-vitro by glucose restriction and are associated with cellular remodelling during weight regain.

Adipocyte
2019

Differentiating SGBS adipocytes respond to PPARγ stimulation, irisin and BMP7 by functional browning and beige characteristics.

Scientific reports
2019

Immunotherapeutic Targeting of GPC3 in Pediatric Solid Embryonal Tumors.

Frontiers in oncology
2019

Overgrowth syndromes - clinical and molecular aspects and tumour risk.

Nature reviews. Endocrinology
2019

Antioxidant and Anti-Inflammatory Properties of Nigella sativa Oil in Human Pre-Adipocytes.

Antioxidants (Basel, Switzerland)
2019

CUGC for Simpson-Golabi-Behmel syndrome (SGBS).

European journal of human genetics : EJHG
2019

Simpson-Golabi-Behmel syndrome with 46,XY disorders of sex development: A case report.

American journal of medical genetics. Part A
2018

Tetrad presentation of non-syndromic odontogenic keratocyst: An uphill diagnostic and therapeutic challenge.

Dental and medical problems
2019

Simpson-Golabi-Behmel syndrome in a 39-year-old male patient with suspected acromegaly-A case study.

American journal of medical genetics. Part A
2019

Synchronous occurrence of multiple distinct jaw lesions in Simpson-Golabi-Behmel Syndrome: A case report.

Journal of stomatology, oral and maxillofacial surgery
2019

In vitro profiling of volatile organic compounds released by Simpson-Golabi-Behmel syndrome adipocytes.

Journal of chromatography. B, Analytical technologies in the biomedical and life sciences
2018

Mutation update for the GPC3 gene involved in Simpson-Golabi-Behmel syndrome and review of the literature.

Human mutation
2019

Enhancer deletion and allelic effects define a regulatory molecular mechanism at the VLDLR cholesterol GWAS locus.

Human molecular genetics
2018

For Debate: The Significance of Etiologic Diagnosis in Neonates with Overgrowth Syndromes. Lesson Learned from the Simpson-Golabi-Behmel Syndrome.

Pediatric endocrinology reviews : PER
2018

Hydroxycarboxylic Acid Receptor Ligands Modulate Proinflammatory Cytokine Expression in Human Macrophages and Adipocytes without Affecting Adipose Differentiation.

Biological &amp; pharmaceutical bulletin
2019

miR-107 inhibits CDK6 expression, differentiation, and lipid storage in human adipocytes.

Molecular and cellular endocrinology
2018

Impact of X-ray Exposure on the Proliferation and Differentiation of Human Pre-Adipocytes.

International journal of molecular sciences
2018

Two Consecutive Pregnancies with Simpson-Golabi-Behmel Syndrome Type 1: Case Report and Review of Published Prenatal Cases.

Molecular syndromology
2018

Iron Inhibits the Secretion of Apolipoprotein E in Cultured Human Adipocytes.

Cellular and molecular gastroenterology and hepatology
2018

Adipose Tissue Transferrin and Insulin Resistance.

The Journal of clinical endocrinology and metabolism
2019

Duplications of GPC3 and GPC4 genes in symptomatic female carriers of Simpson-Golabi-Behmel syndrome type 1.

European journal of medical genetics
2018

Synthesis and biological evaluations of marine oxohexadecenoic acids: PPARα/γ dual agonism and anti-diabetic target gene effects.

European journal of medicinal chemistry
2018

Acute lymphoblastic leukemia in a male with Simpson-Golabi-Behmel syndrome.

American journal of medical genetics. Part A
2019

Detecting epistasis within chromatin regulatory circuitry reveals CAND2 as a novel susceptibility gene for obesity.

International journal of obesity (2005)
2019

Ovotesticular Disorder of Sex Development (Ovotestis) in Simpson-Golabi-Behmel Syndrome: Expansion of the Clinical Spectrum.

Pediatric and developmental pathology : the official journal of the Society for Pediatric Pathology and the Paediatric Pathology Society
2018

Simpson-Golabi-Behmel syndrome human adipocytes reveal a changing phenotype throughout differentiation.

Histochemistry and cell biology
2018

Increased Ifi202b/IFI16 expression stimulates adipogenesis in mice and humans.

Diabetologia
2018

DEHP deregulates adipokine levels and impairs fatty acid storage in human SGBS-adipocytes.

Scientific reports
2018

Are all Xq26.2 duplications overlapping GPC3 on array-CGH a cause of Simpson-Golabi-Behmel syndrome? When do we need transcript analysis?

Clinical genetics
2018

Nonisolated diaphragmatic hernia in Simpson-Golabi-Behmel syndrome.

Prenatal diagnosis
2017

[Overgrowth in children and in adults: novel clinical view, novel genes, novel phenotypes].

Casopis lekaru ceskych
2017

Interferon-gamma released from omental adipose tissue of insulin-resistant humans alters adipocyte phenotype and impairs response to insulin and adiponectin release.

International journal of obesity (2005)
2017

'The obesity paradox': a reconsideration of obesity and the risk of preterm birth.

Journal of perinatology : official journal of the California Perinatal Association
2018

Hyperechoic renal medullary pyramids in a boy with Simpson-Golabi-Behmel syndrome.

Clinical dysmorphology
2018

Extra-adrenal glucocorticoids contribute to the postprandial increase of circulating leptin in mice.

Journal of cell communication and signaling
2017

Trail (TNF-related apoptosis-inducing ligand) induces an inflammatory response in human adipocytes.

Scientific reports
2017

SGBS cells as a model of human adipocyte browning: A comprehensive comparative study with primary human white subcutaneous adipocytes.

Scientific reports
2017

Perinatal Case of Fatal Simpson-Golabi-Behmel Syndrome with Hyperplasia of Seminiferous Tubules.

The American journal of case reports
2017

First reported case of Simpson-Golabi-Behmel syndrome in a female fetus diagnosed prenatally with chromosomal microarray.

Clinical case reports
2017

Collagen beta (1-O) galactosyltransferase 1 (GLT25D1) is required for the secretion of high molecular weight adiponectin and affects lipid accumulation.

Bioscience reports
2017

Molecular analysis of a novel intragenic deletion in GPC3 in three cousins with Simpson-Golabi-Behmel syndrome.

American journal of medical genetics. Part A
2017

Teneurin-2 (TENM2) deficiency induces UCP1 expression in differentiating human fat cells.

Molecular and cellular endocrinology
2016

miR-146a-mediated suppression of the inflammatory response in human adipocytes.

Scientific reports
2016

Adipocyte-specific Hypoxia-inducible gene 2 promotes fat deposition and diet-induced insulin resistance.

Molecular metabolism
2016

Clozapine modifies the differentiation program of human adipocytes inducing browning.

Translational psychiatry
2016

Loss-of-function mutations and global rearrangements in GPC3 in patients with Simpson-Golabi-Behmel syndrome.

Human genome variation
2017

Simpson-Golabi-Behmel syndrome in a female: A case report and an unsolved issue.

American journal of medical genetics. Part A
2016

TRAIL (TNF-related apoptosis-inducing ligand) inhibits human adipocyte differentiation via caspase-mediated downregulation of adipogenic transcription factors.

Cell death &amp; disease
2016

Accumulation of CD11c+CD163+ Adipose Tissue Macrophages through Upregulation of Intracellular 11β-HSD1 in Human Obesity.

Journal of immunology (Baltimore, Md. : 1950)
2017

A role for the metalloprotease invadolysin in insulin signaling and adipogenesis.

Biological chemistry
2016

Prenatal diagnosis of Simpson-Golabi-Behmel syndrome.

American journal of medical genetics. Part A
2016

Whole exome sequencing and array-based molecular karyotyping as aids to prenatal diagnosis in fetuses with suspected Simpson-Golabi-Behmel syndrome.

Prenatal diagnosis
2016

Metformin Increases Cortisol Regeneration by 11βHSD1 in Obese Men With and Without Type 2 Diabetes Mellitus.

The Journal of clinical endocrinology and metabolism
2017

Marsupialisation of kerastocystic odontogenic tumours in a patient with Simpson-Golabi-Behmel syndrome.

The British journal of oral &amp; maxillofacial surgery
2016

Redundant roles of the phosphatidate phosphatase family in triacylglycerol synthesis in human adipocytes.

Diabetologia
2016

Quercetin Impacts Expression of Metabolism- and Obesity-Associated Genes in SGBS Adipocytes.

Nutrients
2016

Insulin/glucose induces natriuretic peptide clearance receptor in human adipocytes: a metabolic link with the cardiac natriuretic pathway.

American journal of physiology. Regulatory, integrative and comparative physiology
2016

Identification of carboxypeptidase X (CPX)-1 as a positive regulator of adipogenesis.

FASEB journal : official publication of the Federation of American Societies for Experimental Biology
2016

Therapeutic potential of the dual peroxisome proliferator activated receptor (PPAR)α/γ agonist aleglitazar in attenuating TNF-α-mediated inflammation and insulin resistance in human adipocytes.

Pharmacological research
2015

Ankyloglossia with cleft lip: A rare case report.

Journal of Indian Society of Periodontology
2016

Importance of adipocyte cyclooxygenase-2 and prostaglandin E2-prostaglandin E receptor 3 signaling in the development of obesity-induced adipose tissue inflammation and insulin resistance.

FASEB journal : official publication of the Federation of American Societies for Experimental Biology
2016

A clinical and molecular investigation of two South African families with Simpson-Golabi-Behmel syndrome.

South African medical journal = Suid-Afrikaanse tydskrif vir geneeskunde
2016

Simpson-Golabi-Behmel syndrome: a prenatal diagnosis in a foetus with GPC3 and GPC4 gene microduplications.

Clinical genetics
2016

Weight loss-induced stress in subcutaneous adipose tissue is related to weight regain.

The British journal of nutrition
2016

Rare dental manifestation in Simpson-Golabi-Behmel syndrome.

General dentistry
2016

Delayed Intervention With Pyridoxamine Improves Metabolic Function and Prevents Adipose Tissue Inflammation and Insulin Resistance in High-Fat Diet-Induced Obese Mice.

Diabetes
2016

Distinctive findings in a boy with Simpson-Golabi-Behmel syndrome.

American journal of medical genetics. Part A
2016

Functional characterization of retromer in GLUT4 storage vesicle formation and adipocyte differentiation.

FASEB journal : official publication of the Federation of American Societies for Experimental Biology
2016

Myostatin in relation to physical activity and dysglycaemia and its effect on energy metabolism in human skeletal muscle cells.

Acta physiologica (Oxford, England)
2016

A recurrent germline mutation in the PIGA gene causes Simpson-Golabi-Behmel syndrome type 2.

American journal of medical genetics. Part A
2016

Modulation of triglyceride accumulation in adipocytes by psychopharmacological agents in vitro.

Journal of psychiatric research
2015

[Fibroblast growth factor-1 inhibits Wnt/β-catenin pathway during adipogenesis].

Zhong nan da xue xue bao. Yi xue ban = Journal of Central South University. Medical sciences
2015

LipiD-QuanT: a novel method to quantify lipid accumulation in live cells.

Journal of lipid research
2015

Whole exome sequencing identifies a novel frameshift mutation in GPC3 gene in a patient with overgrowth syndrome.

Gene
2015

Angiotensin II directly impairs adipogenic differentiation of human preadipose cells.

Molecular and cellular biochemistry
2015

Fructose Alters Intermediary Metabolism of Glucose in Human Adipocytes and Diverts Glucose to Serine Oxidation in the One-Carbon Cycle Energy Producing Pathway.

Metabolites
2015

Inverse relationship between body mass index and mitochondrial oxidative phosphorylation capacity in human subcutaneous adipocytes.

American journal of physiology. Endocrinology and metabolism
2015

MFAP5 is related to obesity-associated adipose tissue and extracellular matrix remodeling and inflammation.

Obesity (Silver Spring, Md.)
2015

Additive regulation of adiponectin expression by the mediterranean diet olive oil components oleic Acid and hydroxytyrosol in human adipocytes.

PloS one
2015

Parathyroid Hormone is Related to Dysplasia and a Higher Rate of Distal Colorectal Adenoma in Women but Not Men.

Hormones &amp; cancer
2015

TNF-related apoptosis-inducing ligand promotes human preadipocyte proliferation via ERK1/2 activation.

FASEB journal : official publication of the Federation of American Societies for Experimental Biology
2015

Expression of human and mouse adenine nucleotide translocase (ANT) isoform genes in adipogenesis.

The international journal of biochemistry &amp; cell biology
2015

Intestinal epithelial cells promote secretion of leptin and adiponectin in adipocytes.

Biochemical and biophysical research communications

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Doenças relacionadas

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Referências e fontes

Bases de dados externas citadas neste artigo

Publicações científicas

Artigos indexados no PubMed ligados a esta doença no grafo RarasNet — título, periódico e PMID direto da fonte, sem intermediação de IA.

  1. Development of an integrative cross-omics approach for conceptual adverse outcome pathway network construction.
    Environment international· 2026· PMID 41797196mais citado
  2. MiR-874-3p suppresses TNF-&#x3b1;-induced inflammation in adipocytes by targeting nucleolin.
    Journal of molecular histology· 2026· PMID 41546782mais citado
  3. Canagliflozin regulates adipocyte lipolysis in vitro via a SGLT2 independent signaling pathway.
    International journal of obesity (2005)· 2026· PMID 41495449mais citado
  4. Simpson-Golabi-Behmel Syndrome Associated With a Missense Variant at the Signal Peptide Cleavage Site of GPC3.
    American journal of medical genetics. Part A· 2026· PMID 41332312mais citado
  5. Functional Characterization of a Novel GPC3 Missense Variant in Simpson-Golabi-Behmel Syndrome.
    American journal of medical genetics. Part A· 2026· PMID 41122961mais citado
  6. Active whitening of human SGBS adipocytes is associated with coordinated AMPK-HIF-autophagy signalling and mitochondrial remodelling.
    Tissue Cell· 2026· PMID 41880863recente
  7. Palmitic acid differently modulates extracellular vesicles and cellular fatty acid composition of SGBS adipocytes without impairing their insulin signaling.
    Front Endocrinol (Lausanne)· 2025· PMID 41377945recente

Bases de dados e fontes oficiais

Identificadores e referências canônicas usadas para montar este verbete.

  1. ORPHA:373(Orphanet)
  2. MONDO:0010731(MONDO)
  3. GARD:7649(GARD (NIH))
  4. Variantes catalogadas(ClinVar)
  5. Busca completa no PubMed(PubMed)
  6. Q478891(Wikidata)

Dados compilados pelo RarasNet a partir de fontes abertas (Orphanet, OMIM, MONDO, PubMed/EuropePMC, ClinicalTrials.gov, DATASUS, PCDT/MS). Este conteúdo é informativo e não substitui avaliação médica.

Conteúdo mantido por Agente Raras · Médicos e pesquisadores podem colaborar

Síndrome Simpson-Golabi-Behmel
Compêndio · Raras BR

Síndrome Simpson-Golabi-Behmel

ORPHA:373 · MONDO:0010731
Prevalência
<1 / 1 000 000
Casos
250 casos conhecidos
Herança
X-linked recessive
CID-10
Q87.3 · Síndromes com malformações congênitas com hipercrescimento precoce
CID-11
Início
Antenatal, Childhood, Infancy, Neonatal
Prevalência
0.0 (Worldwide)
MedGen
UMLS
C0796154
EuropePMC
Wikidata
Papers 10a
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