Raras
Buscar doenças, sintomas, genes...
Obesidade, genética

Obesidade é uma condição médica em que se verifica acumulação excessiva de tecido adiposo ao ponto de poder ter impacto negativo na saúde. Uma pessoa é considerada obesa quando o seu índice de massa corporal (IMC) é superior a 30 kg/m2, e com excesso de peso quando o seu IMC é superior a 25–30 kg/m2. O IMC é calculado dividindo o peso da pessoa pelo quadrado da sua altura. A obesidade aumenta a probabilidade de ocorrência de várias doenças, em particular de doenças cardiovasculares, diabetes do tipo 2, apneia do sono obstrutiva, alguns tipos de cancro, osteoartrite, e depressão.

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Introdução

O que você precisa saber de cara

📋

Obesidade genética é uma condição rara caracterizada por ganho de peso excessivo, frequentemente desde a infância, associada a alterações metabólicas (colesterol LDL alto, acantose nigricans) e de desenvolvimento (tálamo, crescimento, esqueleto). Pode ter herança autossômica dominante ou recessiva, ligada a mutações em genes como LEPR, SDC3, ENPP1, CARTPT e AGRP.

Pesquisas ativas
2 ensaios
10 total registrados no ClinicalTrials.gov
Publicações científicas
524 artigos
Último publicado: 2026 Apr 17
🏥
SUS: Sem cobertura SUSScore: 0%
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Sinais e sintomas

O que aparece no corpo e com que frequência cada sintoma acontece

Partes do corpo afetadas

📏
Crescimento
23 sintomas
🧠
Neurológico
8 sintomas
🦴
Ossos e articulações
5 sintomas
🫘
Rins
4 sintomas
🫃
Digestivo
3 sintomas
❤️
Coração
3 sintomas

+ 38 sintomas em outras categorias

Características mais comuns

Aumento da concentração de colesterol LDL
Anomalia do desenvolvimento do tálamo
Herança autossômica dominante
Herança autossômica recessiva
Hipotensão ortostática devido a disfunção autonômica
Déficit de crescimento
90sintomas
Sem dados (90)

Os sintomas variam de pessoa para pessoa. Abaixo estão as 90 características clínicas mais associadas, ordenadas por frequência.

Aumento da concentração de colesterol LDLIncreased LDL cholesterol concentration
Anomalia do desenvolvimento do tálamoHP:0010982
Herança autossômica dominanteAutosomal dominant inheritance
Herança autossômica recessivaAutosomal recessive inheritance
Hipotensão ortostática devido a disfunção autonômicaOrthostatic hypotension due to autonomic dysfunction

Linha do tempo da pesquisa

Publicações por ano — veja quando o interesse científico cresceu
Anos de pesquisa1desde 2026
Total histórico524PubMed
Últimos 10 anos200publicações
Pico202330 papers
Linha do tempo
2026Hoje · 2026🧪 1972Primeiro ensaio clínico📈 2023Ano de pico
Publicações por ano (últimos 10 anos)

Encontrou um erro ou informação desatualizada? Sugira uma correção →

Genética e causas

O que está alterado no DNA e como passa nas famílias

Genes associados

16 genes identificados com associação a esta condição.

LEPRLeptin receptorDisease-causing germline mutation(s) inTolerante
FUNÇÃO

Receptor for hormone LEP/leptin (Probable) (PubMed:22405007). On ligand binding, mediates LEP central and peripheral effects through the activation of different signaling pathways such as JAK2/STAT3 and MAPK cascade/FOS. In the hypothalamus, LEP acts as an appetite-regulating factor that induces a decrease in food intake and an increase in energy consumption by inducing anorexinogenic factors and suppressing orexigenic neuropeptides, also regulates bone mass and secretion of hypothalamo-pituitar

LOCALIZAÇÃO

Cell membraneBasolateral cell membraneSecreted

VIAS BIOLÓGICAS (1)
Signaling by Leptin
MECANISMO DE DOENÇA

Leptin receptor deficiency

A rare disease characterized by normal levels of serum leptin, hyperphagia and severe obesity from an early age. Additional features include alterations in immune function, and delayed puberty due to hypogonadotropic hypogonadism.

VIAS REACTOME (1)
EXPRESSÃO TECIDUAL(Ubíquo)
Nervo tibial
24.9 TPM
Ovário
16.1 TPM
Pulmão
13.2 TPM
Mama
12.9 TPM
Útero
11.9 TPM
OUTRAS DOENÇAS (1)
obesity due to leptin receptor gene deficiency
HGNC:6554UniProt:P48357
SDC3Syndecan-3Candidate gene tested inTolerante
FUNÇÃO

Cell surface proteoglycan that may bear heparan sulfate (By similarity). May have a role in the organization of cell shape by affecting the actin cytoskeleton, possibly by transferring signals from the cell surface in a sugar-dependent mechanism

LOCALIZAÇÃO

Cell membrane

VIAS BIOLÓGICAS (1)
Glycosaminoglycan-protein linkage region biosynthesis
EXPRESSÃO TECIDUAL(Ubíquo)
Glândula adrenal
131.2 TPM
Brain Nucleus accumbens basal ganglia
106.9 TPM
Nervo tibial
100.1 TPM
Cólon sigmoide
98.5 TPM
Baço
89.5 TPM
OUTRAS DOENÇAS (1)
inherited obesity
HGNC:HGNC:10660UniProt:O75056
ENPP1Ectonucleotide pyrophosphatase/phosphodiesterase family member 1Candidate gene tested inTolerante
FUNÇÃO

Nucleotide pyrophosphatase that generates diphosphate (PPi) and functions in bone mineralization and soft tissue calcification by regulating pyrophosphate levels (By similarity). PPi inhibits bone mineralization and soft tissue calcification by binding to nascent hydroxyapatite crystals, thereby preventing further growth of these crystals (PubMed:11004006). Preferentially hydrolyzes ATP, but can also hydrolyze other nucleoside 5' triphosphates such as GTP, CTP and UTP to their corresponding mono

LOCALIZAÇÃO

Cell membraneBasolateral cell membraneSecreted

VIAS BIOLÓGICAS (2)
Vitamin B5 (pantothenate) metabolismVitamin B2 (riboflavin) metabolism
MECANISMO DE DOENÇA

Ossification of the posterior longitudinal ligament of the spine

A calcification of the posterior longitudinal ligament of the spinal column, usually at the level of the cervical spine. Patients with OPLL frequently present with a severe myelopathy that can lead to tetraparesis.

EXPRESSÃO TECIDUAL(Ubíquo)
Útero
42.3 TPM
Tireoide
26.5 TPM
Aorta
22.2 TPM
Pituitária
22.0 TPM
Fígado
19.8 TPM
OUTRAS DOENÇAS (8)
hypophosphatemic rickets, autosomal recessive, 2hypopigmentation-punctate palmoplantar keratoderma syndromearterial calcification, generalized, of infancy, 1autosomal recessive inherited pseudoxanthoma elasticum
HGNC:3356UniProt:P22413
CARTPTCocaine- and amphetamine-regulated transcript proteinCandidate gene tested inModerado
FUNÇÃO

Satiety factor closely associated with the actions of leptin and neuropeptide Y; this anorectic peptide inhibits both normal and starvation-induced feeding and completely blocks the feeding response induced by neuropeptide Y and regulated by leptin in the hypothalamus. It promotes neuronal development and survival in vitro

LOCALIZAÇÃO

Secreted

OUTRAS DOENÇAS (1)
inherited obesity
HGNC:HGNC:24323UniProt:Q16568
AGRPAgouti-related proteinCandidate gene tested inTolerante
FUNÇÃO

Signaling protein that functions as an antagonist of melanocyte-stimulating-hormone receptors MC3R and MC4R by precluding agonist-induced signaling, thereby inhibiting cAMP production within the hypothalamus and adrenal gland (PubMed:10371151, PubMed:11145747, PubMed:9311920, PubMed:9892020). Involved in the control of feeding behavior via the central melanocortin system (PubMed:15927146, PubMed:9311920). Has very low activity towards MC5R (PubMed:9311920, PubMed:9892020). Also promotes endocyto

LOCALIZAÇÃO

SecretedGolgi apparatus lumen

VIAS BIOLÓGICAS (1)
FOXO-mediated transcription of oxidative stress, metabolic and neuronal genes
MECANISMO DE DOENÇA

Obesity

A condition characterized by an increase of body weight beyond the limitation of skeletal and physical requirements, as the result of excessive accumulation of body fat.

OUTRAS DOENÇAS (1)
inherited obesity
HGNC:HGNC:330UniProt:O00253
GHRLAppetite-regulating hormoneCandidate gene tested inTolerante
FUNÇÃO

Precursor of the appetite-regulating peptide ghrelin, including ghrelin-27 and ghrelin-28 Ghrelin is the ligand for growth hormone secretagogue receptor type 1 (GHSR) (PubMed:10604470, PubMed:35027551). Induces the release of growth hormone from the pituitary (PubMed:10604470). Has an appetite-stimulating effect, induces adiposity and stimulates gastric acid secretion. Involved in growth regulation Ghrelin is the ligand for growth hormone secretagogue receptor type 1 (GHSR) (PubMed:10604470, Pub

LOCALIZAÇÃO

Secreted

VIAS BIOLÓGICAS (1)
Synthesis, secretion, and deacylation of Ghrelin
EXPRESSÃO TECIDUAL(Tecido-específico)
Estômago
143.5 TPM
Baço
3.0 TPM
Tireoide
2.7 TPM
Nervo tibial
1.9 TPM
Sangue
1.7 TPM
OUTRAS DOENÇAS (1)
inherited obesity
HGNC:HGNC:18129UniProt:Q9UBU3
ADRB3Beta-3 adrenergic receptorCandidate gene tested inTolerante
FUNÇÃO

G protein-coupled receptor for catecholamines that couples to both G(s) and G(i) proteins, leading to either activation or inhibition of adenylate cyclase and cAMP-dependent pathway, respectively (PubMed:10188996, PubMed:2570461, PubMed:8641219). The rank order of potency for physiological agonists is norepinephrine > epinephrine (PubMed:10188996, PubMed:2570461, PubMed:8641219). Involved in the regulation of thermogenesis and lipolysis in brown and white adipose tissue, after coupling to G(s) p

LOCALIZAÇÃO

Cell membrane

VIAS BIOLÓGICAS (2)
G alpha (s) signalling eventsAdrenoceptors
OUTRAS DOENÇAS (1)
inherited obesity
HGNC:HGNC:288UniProt:P13945
UCP3Putative mitochondrial transporter UCP3Candidate gene tested inTolerante
FUNÇÃO

Putative transmembrane transporter that plays a role in mitochondrial metabolism via an as yet unclear mechanism (PubMed:21775425, PubMed:36114012). Originally, this mitochondrial protein was thought to act as a proton transmembrane transporter from the mitochondrial intermembrane space into the matrix, causing proton leaks through the inner mitochondrial membrane, thereby uncoupling mitochondrial membrane potential generation from ATP synthesis (PubMed:11171965, PubMed:12670931, PubMed:12734183

LOCALIZAÇÃO

Mitochondrion inner membrane

VIAS BIOLÓGICAS (1)
The fatty acid cycling model
MECANISMO DE DOENÇA

Obesity

A condition characterized by an increase of body weight beyond the limitation of skeletal and physical requirements, as the result of excessive accumulation of body fat.

EXPRESSÃO TECIDUAL(Ubíquo)
Músculo esquelético
145.5 TPM
Testículo
6.8 TPM
Cerebelo
6.4 TPM
Cérebro - Hemisfério cerebelar
5.6 TPM
Tireoide
3.7 TPM
OUTRAS DOENÇAS (1)
inherited obesity
HGNC:HGNC:12519UniProt:P55916
MC4RMelanocortin receptor 4Candidate gene tested inTolerante
FUNÇÃO

G protein-coupled receptor that binds melanocyte-stimulating hormones (alpha- and beta-MSH) and corticotropin/ACTH, which are peptide products of the POMC precursor (PubMed:12646665, PubMed:14764818, PubMed:25163632, PubMed:32327598, PubMed:33858992, PubMed:8392067). Functions as a central component of the leptin-melanocortin pathway, which is essential for maintaining energy homeostasis (PubMed:32327598, PubMed:33858992). Upon activation, couples to G(s) protein, stimulating adenylate cyclase a

LOCALIZAÇÃO

Cell membrane

VIAS BIOLÓGICAS (3)
G alpha (s) signalling eventsPeptide ligand-binding receptorsTranscriptional and post-translational regulation of MITF-M expression and activity
MECANISMO DE DOENÇA

Obesity

A condition characterized by an increase of body weight beyond the limitation of skeletal and physical requirements, as the result of excessive accumulation of body fat.

EXPRESSÃO TECIDUAL(Baixa expressão)
Hipotálamo
3.2 TPM
Brain Caudate basal ganglia
2.4 TPM
Brain Putamen basal ganglia
1.8 TPM
Brain Anterior cingulate cortex BA24
1.7 TPM
Brain Frontal Cortex BA9
1.5 TPM
OUTRAS DOENÇAS (1)
obesity due to melanocortin 4 receptor deficiency
HGNC:6932UniProt:P32245
SIM1Single-minded homolog 1Candidate gene tested inAltamente restrito
FUNÇÃO

Transcriptional factor that may have pleiotropic effects during embryogenesis and in the adult

LOCALIZAÇÃO

Nucleus

EXPRESSÃO TECIDUAL(Tecido-específico)
Fibroblastos
6.0 TPM
Rim - Medula
5.8 TPM
Rim - Córtex
3.4 TPM
Tecido adiposo
3.0 TPM
Pâncreas
0.9 TPM
OUTRAS DOENÇAS (3)
obesity due to SIM1 deficiencySIM1-related Prader-Willi-like syndrome6q16 deletion syndrome
HGNC:10882UniProt:P81133
POMCPro-opiomelanocortinDisease-causing germline mutation(s) inTolerante
FUNÇÃO

Precursor protein of pituitary hormones that are involved in diverse physiological processes, including the regulation of energy balance, stress response, immune function and skin pigmentation Functions as a ligand for the melanocortin receptors MC1R, MC2R, MC3R and MC5R (PubMed:8396929, PubMed:8463333, PubMed:8636348). Activation of MC1R increases melanogenesis in melanocytes found in the skin and hair (PubMed:9620771). Binding to MC2R stimulates the adrenal glands to secrete cortisol (PubMed:8

LOCALIZAÇÃO

Secreted

VIAS BIOLÓGICAS (1)
Peptide hormone biosynthesis
MECANISMO DE DOENÇA

Obesity

A condition characterized by an increase of body weight beyond the limitation of skeletal and physical requirements, as the result of excessive accumulation of body fat.

EXPRESSÃO TECIDUAL(Ubíquo)
Pituitária
29208.2 TPM
Testículo
41.1 TPM
Glândula adrenal
9.1 TPM
Linfócitos
9.0 TPM
Baço
7.9 TPM
OUTRAS DOENÇAS (2)
obesity due to pro-opiomelanocortin deficiencyinherited obesity
HGNC:9201UniProt:P01189
CEP19Centrosomal protein of 19 kDaDisease-causing germline mutation(s) inTolerante
FUNÇÃO

Required for ciliation (PubMed:28428259, PubMed:28625565, PubMed:28659385). Recruits the RABL2B GTPase to the ciliary base to initiate ciliation. After specifically capturing the activated GTP-bound RABL2B, the CEP19-RABL2B complex binds intraflagellar transport (IFT) complex B from the large pool pre-docked at the base of the cilium and thus triggers its entry into the cilia (PubMed:28428259, PubMed:28625565). Involved in the early steps in cilia formation by recruiting the ciliary vesicles (CV

LOCALIZAÇÃO

Cytoplasm, cytoskeleton, microtubule organizing center, centrosome, centrioleCytoplasm, cytoskeleton, spindle poleCytoplasm, cytoskeleton, cilium basal body

VIAS BIOLÓGICAS (7)
Recruitment of mitotic centrosome proteins and complexesLoss of proteins required for interphase microtubule organization from the centrosomeLoss of Nlp from mitotic centrosomesRegulation of PLK1 Activity at G2/M TransitionAURKA Activation by TPX2
MECANISMO DE DOENÇA

Morbid obesity and spermatogenic failure

An autosomal recessive morbid obesity syndrome characterized by hypertension, fatty liver disease, insulin resistance, and decreased sperm counts. Variable clinical manifestations are early coronary artery disease with myocardial infarction before 45 years of age, type II diabetes mellitus, and intellectual disability. Morbid obese individuals are defined as having a BMI greater than 40.

VIAS REACTOME (1)
INTERAÇÕES PROTEICAS (4)
OUTRAS DOENÇAS (2)
obesity due to CEP19 deficiencyBardet-Biedl syndrome
HGNC:28209UniProt:Q96LK0
PCSK1Neuroendocrine convertase 1Disease-causing germline mutation(s) inTolerante
FUNÇÃO

Involved in the processing of hormone and other protein precursors at sites comprised of pairs of basic amino acid residues. Substrates include POMC, renin, enkephalin, dynorphin, somatostatin, insulin and AGRP

LOCALIZAÇÃO

Cytoplasmic vesicle, secretory vesicle

VIAS BIOLÓGICAS (5)
Synthesis, secretion, and deacylation of GhrelinSynthesis, secretion, and inactivation of Glucagon-like Peptide-1 (GLP-1)Peptide hormone biosynthesisInsulin processingSynthesis, secretion, and inactivation of Glucose-dependent Insulinotropic Polypeptide (GIP)
MECANISMO DE DOENÇA

Proprotein convertase 1 deficiency

Characterized by obesity, hypogonadism, hypoadrenalism, reactive hypoglycemia as well as marked small-intestinal absorptive dysfunction It is due to impaired processing of prohormones.

EXPRESSÃO TECIDUAL(Tecido-específico)
Hipotálamo
22.3 TPM
Brain Frontal Cortex BA9
21.1 TPM
Pituitária
19.7 TPM
Córtex cerebral
11.0 TPM
Brain Anterior cingulate cortex BA24
6.4 TPM
OUTRAS DOENÇAS (1)
obesity due to prohormone convertase I deficiency
HGNC:8743UniProt:P29120
NR0B2Nuclear receptor subfamily 0 group B member 2Disease-causing germline mutation(s) inTolerante
FUNÇÃO

Transcriptional regulator that acts as a negative regulator of receptor-dependent signaling pathways (PubMed:22504882). Specifically inhibits transactivation of the nuclear receptor with which it interacts (PubMed:22504882). Inhibits transcriptional activity of NEUROD1 on E-box-containing promoter by interfering with the coactivation function of the p300/CBP-mediated transcription complex for NEUROD1 (PubMed:14752053). Essential component of the liver circadian clock which via its interaction wi

LOCALIZAÇÃO

NucleusCytoplasm

VIAS BIOLÓGICAS (1)
Nuclear Receptor transcription pathway
MECANISMO DE DOENÇA

Obesity

A condition characterized by an increase of body weight beyond the limitation of skeletal and physical requirements, as the result of excessive accumulation of body fat.

EXPRESSÃO TECIDUAL(Tecido-específico)
Fígado
74.6 TPM
Estômago
25.7 TPM
Glândula adrenal
20.0 TPM
Pâncreas
16.8 TPM
Baço
15.2 TPM
OUTRAS DOENÇAS (1)
inherited obesity
HGNC:HGNC:7961UniProt:Q15466
PPARGPeroxisome proliferator-activated receptor gammaDisease-causing germline mutation(s) inModerado
FUNÇÃO

Ligand-activated transcription factor that forms obligate heterodimers with the retinoic acid receptor and acts as a key regulator of biological processes, such as adipocyte differentiation, lipid metabolism, glucose homeostasis and beta-oxidation of fatty acids (PubMed:16150867, PubMed:20829347, PubMed:23525231, PubMed:8702406, PubMed:8706692, PubMed:9065481). Activated by lipid ligands: binds peroxisome proliferators, such as hypolipidemic drugs, and fatty acids, such as prostaglandin J2 metab

LOCALIZAÇÃO

NucleusCytoplasm

VIAS BIOLÓGICAS (7)
Regulation of PTEN gene transcriptionTranscriptional regulation of white adipocyte differentiationPPARA activates gene expressionMECP2 regulates transcription factorsNuclear Receptor transcription pathway
EXPRESSÃO TECIDUAL(Ubíquo)
Tecido adiposo
111.2 TPM
Adipose Visceral Omentum
100.8 TPM
Mama
71.3 TPM
Cólon transverso
21.6 TPM
Fibroblastos
20.4 TPM
OUTRAS DOENÇAS (6)
type 2 diabetes mellitusPPARG-related familial partial lipodystrophyinherited obesitygliosarcoma
HGNC:9236UniProt:P37231
LEPLeptinDisease-causing germline mutation(s) inTolerante
FUNÇÃO

Key player in the regulation of energy balance and body weight control. Once released into the circulation, has central and peripheral effects by binding LEPR, found in many tissues, which results in the activation of several major signaling pathways (PubMed:15899045, PubMed:17344214, PubMed:19688109). In the hypothalamus, acts as an appetite-regulating factor that induces a decrease in food intake and an increase in energy consumption by inducing anorexinogenic factors and suppressing orexigeni

LOCALIZAÇÃO

Secreted

VIAS BIOLÓGICAS (4)
Synthesis, secretion, and deacylation of GhrelinSynthesis, secretion, and inactivation of Glucagon-like Peptide-1 (GLP-1)Signaling by LeptinTranscriptional regulation of white adipocyte differentiation
MECANISMO DE DOENÇA

Leptin deficiency

A rare disease characterized by low levels of serum leptin, severe hyperphagia and intractable obesity from an early age.

EXPRESSÃO TECIDUAL(Tecido-específico)
Tecido adiposo
198.8 TPM
Adipose Visceral Omentum
55.4 TPM
Mama
38.4 TPM
Fibroblastos
5.5 TPM
Artéria coronária
3.5 TPM
OUTRAS DOENÇAS (1)
obesity due to congenital leptin deficiency
HGNC:6553UniProt:P41159

Variantes genéticas (ClinVar)

223 variantes patogênicas registradas no ClinVar.

🧬 LEPR: NM_002303.6(LEPR):c.1846del (p.Arg615_Leu616insTer) ()
🧬 LEPR: NM_002303.6(LEPR):c.2396-2A>C ()
🧬 LEPR: NM_002303.6(LEPR):c.359_360del (p.Phe120fs) ()
🧬 LEPR: GRCh37/hg19 1p31.3-22.3(chr1:61397219-85940743)x1 ()
🧬 LEPR: GRCh37/hg19 1p31.3-21.3(chr1:65412037-95735764)x1 ()
Ver todas no ClinVar

Vias biológicas (Reactome)

49 vias biológicas associadas aos genes desta condição.

Signaling by Leptin Glycosaminoglycan-protein linkage region biosynthesis HS-GAG biosynthesis HS-GAG degradation Cell surface interactions at the vascular wall Syndecan interactions Defective B4GALT7 causes EDS, progeroid type Defective B3GAT3 causes JDSSDHD Defective EXT2 causes exostoses 2 Defective EXT1 causes exostoses 1, TRPS2 and CHDS Defective B3GALT6 causes EDSP2 and SEMDJL1 Attachment and Entry Retinoid metabolism and transport Respiratory syncytial virus (RSV) attachment and entry RSV-host interactions Dengue Virus-Host Interactions Dengue Virus Attachment and Entry Vitamin B2 (riboflavin) metabolism Vitamin B5 (pantothenate) metabolism FOXO-mediated transcription of oxidative stress, metabolic and neuronal genes Peptide ligand-binding receptors G alpha (q) signalling events Synthesis, secretion, and deacylation of Ghrelin Adrenoceptors G alpha (s) signalling events The fatty acid cycling model Transcriptional and post-translational regulation of MITF-M expression and activity Transcriptional Regulation by MECP2 Opioid Signalling Androgen biosynthesis Glucocorticoid biosynthesis G-protein activation Peptide hormone biosynthesis Endogenous sterols G alpha (i) signalling events Defective ACTH causes obesity and POMCD Interleukin-4 and Interleukin-13 signaling CEP192 Insulin processing Synthesis, secretion, and inactivation of Glucagon-like Peptide-1 (GLP-1) Synthesis, secretion, and inactivation of Glucose-dependent Insulinotropic Polypeptide (GIP) Nuclear Receptor transcription pathway PPARA activates gene expression Transcriptional regulation of white adipocyte differentiation SUMOylation of intracellular receptors Regulation of PTEN gene transcription MECP2 regulates transcription factors MLL4 and MLL3 complexes regulate expression of PPARG target genes in adipogenesis and hepatic steatosis Transcriptional regulation of brown and beige adipocyte differentiation by EBF2

Diagnóstico

Os sinais que médicos procuram e os exames que confirmam

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Tratamento e manejo

Remédios, cuidados de apoio e o que precisa acompanhar

Pipeline de tratamentos
Pipeline regulatório — de medicamentos já aprovados a drogas em pesquisa exploratória.
3Fase 31
2Fase 22
·Pré-clínico3
Medicamentos catalogadosEnsaios clínicos· 0 medicamentos · 6 ensaios
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🇧🇷 Atendimento SUS — Obesidade, genética

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Pesquisa ativa

Ensaios clínicos abertos e novidades científicas recentes

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Outros ensaios clínicos

10 ensaios clínicos encontrados, 2 ativos.

Distribuição por fase
Ver todos no ClinicalTrials.gov
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Publicações mais relevantes

Timeline de publicações
219 papers (10 anos)
#1

Sleep-Disordered Breathing in Chung-Jansen Syndrome.

International journal of molecular sciences2026 Feb 11

We report a thirty-six-year-old woman with intellectual disability who was referred for evaluation of suspected obstructive sleep apnea. The initial clinical impression suggested a syndromic case, so comprehensive genetic testing was undertaken. Overnight polysomnography revealed a severe rapid eye movement-predominant obstructive sleep apnea syndrome with an apnea-hypopnea index of 31.9 events per hour, rapid eye movement apnea-hypopnea index of 113.8 events per hour, and lowest oxygen saturation of 66%. Treatment with continuous positive airway pressure improved respiratory and sleep quality indices and was well tolerated. Whole-exome sequencing identified a de novo splice site variant in the pleckstrin homology domain interacting protein gene (c.41-1G > A), confirming a molecular diagnosis of Chung-Jansen Syndrome. Chung-Jansen syndrome is a rare neurodevelopmental disorder caused by heterozygous pathogenic variants in the pleckstrin homology domain interacting protein gene, marked by developmental delay, intellectual disability, behavioral abnormalities, dysmorphism, and progressive obesity. PHIP influences central and peripheral pathways controlling satiety, pancreatic function, and body weight. Despite frequent reports of sleep problems, systematic evaluation of sleep-disordered breathing has been limited. This adult case provides the first polysomnographic confirmation in the syndrome, supporting proactive screening for obstructive sleep apnea-especially in those with obesity. Integrating genetic assessment into sleep care can reduce diagnostic delays and better guide therapy and prognosis.

#2

Targeted Next-Generation Sequencing of the Leptin-Melanocortin Pathway in Severe Obesity.

Obesity (Silver Spring, Md.)2026 Feb

Pathogenic variants in five established leptin-melanocortin pathway genes (LEP, LEPR, MC4R, PCSK1, POMC) are associated with severe early-onset obesity and are targets for emerging treatments. However, these variants are rare in these patients, suggesting the involvement of additional genes interacting with this pathway. Next-generation sequencing (NGS) analysis was performed in 395 patients with severe obesity, including 213 children (mean BMI: 56.3 kg/m2; BMI-z-score: 4.6). The analysis targeted 20 genes, including the 5 established genes. Rare genetic variants were assessed for pathogenicity using prediction algorithms, genetic databases, and literature review. Phenotypic data were retrospectively collected, focusing on obesity severity, age of onset, familial history, eating behavior disorder, neurodevelopmental and endocrine-associated diseases, and obesity complications. Pathogenic heterozygous variants were identified in 34 patients (8.6%), 18 of them harboring pathogenic variants in the 15 additional genes. In adults, early-onset obesity was more frequent in potentially pathogenic variants carriers than in non-carriers (83.3% vs. 55.0%, p = 0.04). No differences were observed in the other phenotypic characteristics. This supports the relevance of expanded genetic testing in severe obesity. Early-onset obesity remains a key clinical feature to guide genetic investigation and identify patients who may benefit from early personalized care and targeted treatments.

#3

Sex Differences in Leptin Levels in Children and Adolescents with Normal Weight and Overweight/Obesity Across Pubertal Stages: A Systematic Review and Meta-analysis.

The Journal of clinical endocrinology and metabolism2026 Jan 21

Leptin levels differ significantly between adult men and women, it is unknown whether these sex differences arise during puberty in children with normal weight (NW) or overweight (OW)/obesity (OB). To analyze sex differences in leptin levels and body mass index SD score across pubertal stages in children with NW and OW/OB. Eligible studies were obtained from Medline, Embase, Web of Science, Cochrane, and CINAHL from inception until February 2025. Twenty-four of 1713 studies assessing leptin levels in children aged 5 to 19 years were included. Two reviewers independently extracted data and assessed study quality. We performed subgroup meta-analysis stratified for pubertal stage using random effects model to estimate the weighted mean difference in R. Girls with NW had higher leptin levels than boys at all pubertal stages (pooled mean difference [MD]: 3.99; 95% CI, 2.63-5.35). In children with OW/OB, no significant differences were found in the prepubertal and pubertal stages. At the postpubertal stage, leptin levels were higher in girls compared to boys (MD: 14.60; 95% CI, 0.95-28.25), based on 1 included study. In pubertal children with OW/OB, body mass index SD score was higher in boys than girls (MD: -0.67; 95% CI, -0.74 to -0.61). The sex-specific differences in leptin levels, characteristic of normal-weight (pre-)pubertal children is lost in obesity. Therefore, leptin levels alone are unlikely to explain why obesity accelerates puberty in girls more than in boys. A combined effect with other factors, such as sex dimorphism in kisspeptin, may play a role.

#4

Case Series of Nizon-Isidor Syndrome by Heterozygous Variants in MED12L With Further Evidence of Mitotic Instability in One Case With Diploid-Triploid Mosaicism.

American journal of medical genetics. Part A2026 Jan

Nizon-Isidor syndrome is a rare disorder caused by heterozygous variants in MED12L, with only eight documented cases in the literature. Here, we present three additional cases of this syndrome. Proband 1 was a 7-year-old female who presented with developmental delay, right-leg hemihypertrophy, laryngeal cleft, esotropia, abnormal skin pigmentation, sectoral iris hypopigmentation, dysphagia, periventricular nodular heterotopia, seizures, morbid obesity, and a pelvic kidney. Genome sequencing (GS) revealed a MED12L variant, NM_053002.5:c.3559+2T>G. Both computational models and transcriptomic analysis confirmed that this variant induced splice loss of MED12L exon 25. Probands 2 and 3 presented with overlapping phenotypes of developmental delay; sequencing confirmed c.3441_3444dup; p.(G1149Nfs*13) and seq[GRCh37] del(3)(q25.1q25.1) chr3:g.?_151075120 variants affecting MED12L. Further investigation found diploid-triploid mosaicism in Proband 1, supporting the hypothesis that loss of MED12L function may increase risk for other cytogenetic abnormalities. Probands 2 and 3 did not harbor evidence of additional cytogenetic aberrations. In Proband 1, caloric restriction and semaglutide-pramlintide combination therapy were started at age eight and were effective in weight reduction. Overall, this report expands the phenotypic spectrum of Nizon-Isidor syndrome, highlights a potential link between MED12L and cytogenetic abnormalities, and demonstrates a case of weight loss through GLP-1 therapy in a child with a genetic obesity syndrome.

#5

Innovative Care for Children and Adolescents with Severe and/or Genetic Obesity.

Hormone research in paediatrics2026

Children and adolescents with severe and/or genetic obesity require continuous care and long-term treatment due to the chronic, relapsing, and progressive nature of their disease. Understanding the molecular mechanisms underlying the regulation of hunger, satiety, body weight, and the development of obesity enables a personalized treatment approach. Individualized, multimodal treatment strategies are essential for effective, long-term management of severe and/or genetic obesity in affected children and adolescents. New pharmacological treatments, such as mechanism-based medications for genetic obesity and incretin-based drugs for severe obesity, represent significant advances in chronic weight management and are valuable adjuncts to individualized lifestyle interventions. This article outlines an innovative, structured care and treatment concept for children and adolescents with severe and/or genetic obesity tailored to their specific needs and requirements. It emphasizes the importance of providing care within specialized treatment centers under the "Chronic Care Model," in close collaboration with local healthcare providers. In order to ensure long-term treatment of children and adolescents with severe and/or genetic obesity, innovative and structured care concepts consisting of individualized, multimodal treatment strategies in specialized treatment centers in collaboration with local healthcare providers are required.

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📚 EuropePMC146 artigos no totalmostrando 194

2026

Sleep-Disordered Breathing in Chung-Jansen Syndrome.

International journal of molecular sciences
2026

Targeted Next-Generation Sequencing of the Leptin-Melanocortin Pathway in Severe Obesity.

Obesity (Silver Spring, Md.)
2025

Using the stages of change model to develop an understanding of caregiver intent for family behavior change following pediatric testing for genetic obesity: A qualitative analysis.

Obesity pillars
2026

Sex Differences in Leptin Levels in Children and Adolescents with Normal Weight and Overweight/Obesity Across Pubertal Stages: A Systematic Review and Meta-analysis.

The Journal of clinical endocrinology and metabolism
2025

Early-Onset of Obesity Model: Impact of Early-Onset Obesity on Comorbidity Risk and Life Expectancy.

Obesity facts
2025

Clinical Case of Comorbid Course of Metabolically Associated Fatty Liver and Pancreas Disease in a Child with Prader-Willi Syndrome.

Journal of mother and child
2025

Protein Source Determines the Effectiveness of High-Protein Diets in Improving Adipose Tissue Function and Insulin Resistance in fa/fa Zucker Rats.

Nutrients
2025

Multidimensional Characterisation of Eating Behaviour in Genetic Obesity: A Systematic Review.

Obesity facts
2026

Case Series of Nizon-Isidor Syndrome by Heterozygous Variants in MED12L With Further Evidence of Mitotic Instability in One Case With Diploid-Triploid Mosaicism.

American journal of medical genetics. Part A
2025

Wernicke Encephalopathy in an Adolescent With Severe Genetic Obesity and Hyperphagia.

Pediatrics
2025

Assessing Metabolic Syndrome Risk in Children and Adolescents with Prader-Willi Syndrome: A Comparison of Index Performance.

Journal of clinical medicine
2025

Bariatric outcomes of high BMI patients with preoperative anti-obesity medications.

Surgical endoscopy
2025

Targeted in vivo gene integration of a secretion-enabled GLP-1 receptor agonist reverses diet-induced non-genetic obesity and pre-diabetes.

Communications medicine
2025

Improving the diagnosis of hyperphagia in melanocortin-4 receptor pathway diseases.

Obesity (Silver Spring, Md.)
2025

Missing the Target: A Scoping Review of the Use of Percent Weight Loss for Obesity Management.

Obesity reviews : an official journal of the International Association for the Study of Obesity
2025

Obesity, ovarian GLUT4 expression, and reproductive dysfunction: Insights from Zucker fatty rat.

Reproductive biology
2025

The microprotein C16orf74/MICT1 promotes thermogenesis in brown adipose tissue.

The EMBO journal
2025

Semaglutide impairs bioavailability of alectinib: a note of warning based on a cross-over pharmacokinetic drug-drug interaction study.

Cancer communications (London, England)
2025

Towards a genetic obesity risk score in a single-center study of children and adolescents with obesity.

Scientific reports
2025

Unraveling the relationship between head circumference and MC4R deficiency from infancy to adulthood: a case-control study.

Obesity (Silver Spring, Md.)
2026

Innovative Care for Children and Adolescents with Severe and/or Genetic Obesity.

Hormone research in paediatrics
2025

The effects of SGLT2 inhibitors on metabolic phenotype and FGF-21 expression from the adipose tissue and the liver are less pronounced in ob/ob mice.

BMC endocrine disorders
2025

The Interplay of Genetic Predisposition, Circadian Misalignment, and Metabolic Regulation in Obesity.

Current obesity reports
2025

Pro-Opiomelanocortin and Melanocortin Receptor 3 and 4 Mutations in Genetic Obesity.

Biomolecules
2025

Antiobesity Pharmacotherapy for Patients With Genetic Obesity Due to Defects in the Leptin-Melanocortin Pathway.

Endocrine reviews
2025

Management of Obesity-Related Genetic Disorders.

Endocrinology and metabolism clinics of North America
2024

Genomic deletions on 16p11.2 associated with severe obesity in Brazil.

Frontiers in endocrinology
2025

IGF1 enhances memory function in obese mice and stabilizes the neural structure under insulin resistance via AKT-GSK3β-BDNF signaling.

Biomedicine & pharmacotherapy = Biomedecine & pharmacotherapie
2024

Exploring the therapeutic potential of precision medicine in rare genetic obesity disorders: a scientific perspective.

Frontiers in nutrition
2025

Rare gene variants and weight loss at 10 years after sleeve gastrectomy and gastric bypass - a randomized clinical trial.

Surgery for obesity and related diseases : official journal of the American Society for Bariatric Surgery
2025

The expanding landscape of genetic causes of obesity.

Pediatric research
2024

Investigating the consequences of chronic short sleep for metabolism and survival of oxidative stress.

bioRxiv : the preprint server for biology
2025

Setmelanotide for the treatment of severe early-childhood genetic obesity.

The lancet. Diabetes & endocrinology
2024

Endurance exercise attenuates Gαq-RNAi induced hereditary obesity and skeletal muscle dysfunction via improving skeletal muscle Srl/MRCC-I pathway in Drosophila.

Scientific reports
2024

Setmelanotide: A Melanocortin-4 Receptor Agonist for the Treatment of Severe Obesity Due to Hypothalamic Dysfunction.

TouchREVIEWS in endocrinology
2025

Perspectives on obesity imaging: [18F]2FNQ1P a specific 5-HT6 brain PET radiotracer.

International journal of obesity (2005)
2024

Blind to the perils of pursuing food: Behaviors of individuals with Smith-Magenis Syndrome.

Genetics in medicine open
2024

Preventive effects of a nutraceutical mixture of berberine, citrus and apple extracts on metabolic disturbances in Zucker fatty rats.

PloS one
2024

Treatment with liraglutide or naltrexone-bupropion in patients with genetic obesity: a real-world study.

EClinicalMedicine
2024

Updates on Rare Genetic Variants, Genetic Testing, and Gene Therapy in Individuals With Obesity.

Current obesity reports
2024

Clinical phenotypes of adults with monogenic and syndromic genetic obesity.

Obesity (Silver Spring, Md.)
2024

Exploring the Complex Interplay of Obesity, Allergic Diseases, and Sleep-Disordered Breathing in Children.

Children (Basel, Switzerland)
2024

Assessment of causal associations between obesity and peripheral artery disease: a bidirectional Mendelian randomization study.

Frontiers in cardiovascular medicine
2024

Differentiating monogenic and syndromic obesities from polygenic obesity: Assessment, diagnosis, and management.

Obesity pillars
2024

The Tip of the Iceberg: Genotype of Puerto Rican Pediatric Obesity.

Genes
2025

Reduced Efficacy of Glucagon-Like Peptide-1 Receptor Agonists Therapy in People With Type 1 Diabetes and Genetic Forms of Obesity.

Journal of diabetes science and technology
2024

IMPROVE 2022 International Meeting on Pathway-Related Obesity: Vision of Excellence.

Clinical obesity
2024

GNB1 and obesity: Evidence for a correlation between haploinsufficiency and syndromic obesity.

Clinical obesity
2024

MC4R Variants Modulate α-MSH and Setmelanotide Induced Cellular Signaling at Multiple Levels.

The Journal of clinical endocrinology and metabolism
2024

Syndromic and Monogenic Obesity: New Opportunities Due to Genetic-Based Pharmacological Treatment.

Children (Basel, Switzerland)
2024

Bardet-Biedl syndrome: A clinical overview focusing on diagnosis, outcomes and best-practice management.

Diabetes, obesity & metabolism
2024

Changes of the Concentration of Short-Chain Fatty Acids in the Intestines of Mice with Different Types of Obesity.

Bulletin of experimental biology and medicine
2024

Rare genetic forms of obesity in childhood and adolescence: A narrative review of the main treatment options with a focus on innovative pharmacological therapies.

European journal of pediatrics
2024

High Prevalence of Positive Genetic Obesity Variants in Postoperative Bariatric Surgery Patients with Weight Regain Presenting for Medical Obesity Intervention.

Obesity surgery
2023

Case report of PLXNA4 variant associated with hyper-response to phentermine/topiramate pharmacotherapy: Potential genetic basis for superior weight loss response?

Obesity pillars
2023

Diagnostic challenge: A pediatric patient with severe obesity and complications of imminent death.

Obesity pillars
2024

Obesity induced disruption on diurnal rhythm of insulin sensitivity via gut microbiome-bile acid metabolism.

Biochimica et biophysica acta. Molecular and cell biology of lipids
2023

Beneficial Effects of Setmelanotide in a 5-Year-Old Boy With POMC Deficiency and on His Caregivers.

JCEM case reports
2023

A novel pathogenic variant in MRAP2 in an obese patient with successful outcome of bariatric surgery.

European journal of endocrinology
2024

GPAT1 Deficiency in Mice Modulates NASH Progression in a Model-Dependent Manner.

Cellular and molecular gastroenterology and hepatology
2023

Obesity Characteristics Are Poor Predictors of Genetic Mutations Associated with Obesity.

Journal of clinical medicine
2023

Prevalence of genetic causes of obesity in clinical practice.

Obesity science & practice
2023

Type 2 Diabetes Remission in Patients with Heterozygous Variants in the Leptin-Melanocortin Pathway after Roux-en-Y Gastric Bypass: A Matched Case-Control Study.

Obesity surgery
2024

Elucidating pathways to pediatric obesity: a study evaluating obesity polygenic risk scores related to appetitive traits in children.

International journal of obesity (2005)
2023

Rare genetic forms of obesity in childhood and adolescence, a comprehensive review of their molecular mechanisms and diagnostic approach.

European journal of pediatrics
2023

Neuroprotective Effects of a Serotonin Receptor Peptide Following Sham vs. Mild Traumatic Brain Injury in the Zucker Rat.

Endocrinology, diabetes and metabolism journal
2023

Assessing the Safety of MA-[D-Leu-4]-OB3, a Synthetic Peptide Leptin Mimetic: Two Pre-Clinical Toxicity Studies in Male and Female C57BL/6 Mice.

International journal of toxicology
2023

Genetic Obesity Disorders: Body Mass Index Trajectories and Age of Onset of Obesity Compared with Children with Obesity from the General Population.

The Journal of pediatrics
2023

The Narrative of a Patient with Leptin Receptor Deficiency: Personalized Medicine for a Rare Genetic Obesity Disorder.

Obesity facts
2023

A Personalized Approach to Determining the Caloric Needs of Children with Prader-Willi Syndrome Treated with Growth Hormone.

Journal of clinical medicine
2023

Parent-reported child appetite moderates relationships between child genetic obesity risk and parental feeding practices.

Frontiers in nutrition
2023

Genetic Contributors to Obesity.

Gastroenterology clinics of North America
2023

Autophagic Clearance of Lipid Droplets Alters Metabolic Phenotypes in a Genetic Obesity-Diabetes Mouse Model.

Phenomics (Cham, Switzerland)
2023

Current Treatments for Patients with Genetic Obesity.

Journal of clinical research in pediatric endocrinology
2023

Severe obesity and global developmental delay in preschool children: Findings from a Canadian Paediatric Surveillance Program study.

Paediatrics & child health
2023

Metabolomic Study of Aging in fa/fa Rats: Multiplatform Urine and Serum Analysis.

Metabolites
2023

Targeting senescent hepatocytes using the thrombomodulin-PAR1 inhibitor vorapaxar ameliorates NAFLD progression.

Hepatology (Baltimore, Md.)
2023

Genetic Obesity in Pregnant Ay Mice Does Not Affect Susceptibility to Obesity and Food Choice in Offspring.

International journal of molecular sciences
2023

Identifying effects of genetic obesity exposure on leukocyte telomere length using Mendelian randomization.

PeerJ
2023

Weight Loss of Over 100 lbs in a Patient of Prader-Willi Syndrome Treated With Glucagon-Like Peptide-1 (GLP-1) Agonists.

Cureus
2023

Successful naltrexone-bupropion treatment after several treatment failures in a patient with severe monogenic obesity.

iScience
2023

Genetic Obesity-Causes and Treatments.

Pediatric annals
2023

Next-generation sequencing of 12 obesity genes in a Portuguese cohort of patients with overweight and obesity.

European journal of medical genetics
2023

Setmelanotide: a promising advancement for pediatric patients with rare forms of genetic obesity.

Current opinion in endocrinology, diabetes, and obesity
2023

Multicentric Italian case-control study on 25OH vitamin D levels in children and adolescents with Prader-Willi syndrome.

Journal of endocrinological investigation
2023

Quality of life improvements following one year of setmelanotide in children and adult patients with Bardet-Biedl syndrome: phase 3 trial results.

Orphanet journal of rare diseases
2022

A Review on Drug Induced Obesity and Rodent Experimental Models of Obesity in Animals.

Maedica
2022

Nutraceuticals and the Network of Obesity Modulators.

Nutrients
2022

[A clinical challenge of evaluation and management in children with genetic obesity].

Zhonghua yu fang yi xue za zhi [Chinese journal of preventive medicine]
2022

Genetic obesity: an update with emerging therapeutic approaches.

Annals of pediatric endocrinology & metabolism
2022

Obese male Zucker rats exhibit dendritic remodeling in neurons of the hippocampal trisynaptic circuit as well as spatial memory deficits.

Hippocampus
2022

From a Cone Snail Toxin to a Competitive MC4R Antagonist.

Journal of medicinal chemistry
2022

Morphine and high-fat diet differentially alter the gut microbiota composition and metabolic function in lean versus obese mice.

ISME communications
2022

The promise of new anti-obesity therapies arising from knowledge of genetic obesity traits.

Nature reviews. Endocrinology
2022

Resting Energy Expenditure and Body Composition in Children and Adolescents With Genetic, Hypothalamic, Medication-Induced or Multifactorial Severe Obesity.

Frontiers in endocrinology
2022

Obesity and Hyperphagia With Increased Defective ACTH: A Novel POMC Variant.

The Journal of clinical endocrinology and metabolism
2022

Loss of SQSTM1/p62 Induces Obesity and Exacerbates Alcohol-induced Liver Injury in Aged Mice.

FASEB journal : official publication of the Federation of American Societies for Experimental Biology
2022

Body composition and obstructive sleep apnoea assessment in adult patients with Prader-Willi syndrome: a case control study.

Journal of endocrinological investigation
2022

Favourable Lifestyle Protects Cognitive Function in Older Adults With High Genetic Risk of Obesity: A Prospective Cohort Study.

Frontiers in molecular neuroscience
2022

Effects of Heterozygous Variants in the Leptin-Melanocortin Pathway on Roux-en-Y Gastric Bypass Outcomes: a 15-Year Case-Control Study.

Obesity surgery
2022

Mutations in melanocortin-4 receptor: From fish to men.

Progress in molecular biology and translational science
2022

Testing for rare genetic causes of obesity: findings and experiences from a pediatric weight management program.

International journal of obesity (2005)
2022

Association of Neighborhood Resources and Race and Ethnicity With Readmissions for Diabetic Ketoacidosis at US Children's Hospitals.

JAMA network open
2022

Simulated distributions from negative experiments highlight the importance of the body mass index distribution in explaining depression-body mass index genetic risk score interactions.

International journal of epidemiology
2022

Dextroamphetamine Treatment in Children With Hypothalamic Obesity.

Frontiers in endocrinology
2022

The Hyperphagia Questionnaire: Insights From a Multicentric Validation Study in Individuals With Prader Willi Syndrome.

Frontiers in pediatrics
2021

Influence of High Energy Diet and Polygenic Predisposition for Obesity on Postpartum Health in Rat Dams.

Frontiers in physiology
2022

Kidney failure in Bardet-Biedl syndrome.

Clinical genetics
2022

Do adverse childhood experiences and genetic obesity risk interact in relation to body mass index in young adulthood? Findings from the National Longitudinal Study of Adolescent to Adult Health.

Pediatric obesity
2021

Kisspeptin and the Genetic Obesity Interactome.

Advances in experimental medicine and biology
2021

PI3Kγ promotes obesity-associated hepatocellular carcinoma by regulating metabolism and inflammation.

JHEP reports : innovation in hepatology
2022

Genetic Obesity in Children: Overview of Possible Diagnoses with a Focus on SH2B1 Deletion.

Hormone research in paediatrics
2021

Intestinal, liver and lipid disorders in genetically obese rats are more efficiently reduced by dietary milk thistle seeds than their oil.

Scientific reports
2021

Effects of COVID-19 Lockdown on Weight, Body Composition, and Behavior of Children, Adolescents, and Young Adults with Prader-Willi Syndrome.

Journal of clinical medicine
2021

Hypothesizing Nutrigenomic-Based Precision Anti-Obesity Treatment and Prophylaxis: Should We Be Targeting Sarcopenia Induced Brain Dysfunction?

International journal of environmental research and public health
2021

Diet-induced- and genetic-obesity differentially alters male germline histones.

Reproduction (Cambridge, England)
2021

Genetic testing in pediatric endocrine pathology.

Medicine and pharmacy reports
2021

Evaluation and Management of Early Onset Genetic Obesity in Childhood.

Journal of pediatric genetics
2021

Nutritional phases of Prader-Willi syndrome.

Andes pediatrica : revista Chilena de pediatria
2022

Genetic Obesity Variants and Risk of Conventional Adenomas and Serrated Polyps.

Digestive diseases and sciences
2021

Dietary flaxseed reduces Myocardial Ischemic Lesions, improves cardiac function and lowers cholesterol levels despite the presence of severe obesity in JCR:LA-cp Rats.

The Journal of nutritional biochemistry
2021

Effects of glucagon-like peptide-1 analogue treatment in genetic obesity: A case series.

Clinical obesity
2021

Case Report: Liraglutide for Weight Management in Beckwith-Wiedemann Syndromic Obesity.

Frontiers in endocrinology
2021

Monogenic human obesity syndromes.

Handbook of clinical neurology
2021

Hypothalamic neuropeptides and neurocircuitries in Prader Willi syndrome.

Journal of neuroendocrinology
2021

Long-term outcomes of bariatric surgery in patients with bi-allelic mutations in the POMC, LEPR, and MC4R genes.

Surgery for obesity and related diseases : official journal of the American Society for Bariatric Surgery
2021

The Influence of Diet and Sex on the Gut Microbiota of Lean and Obese JCR:LA-cp Rats.

Microorganisms
2021

Effects of the COVID-19 pandemic and lockdown on the mental and physical health of adults with Prader-Willi syndrome.

Orphanet journal of rare diseases
2021

Exercise and Adipose Tissue Immunity: Outrunning Inflammation.

Obesity (Silver Spring, Md.)
2021

Complexity and Stigma of Pediatric Obesity.

Childhood obesity (Print)
2021

Benefits of multidisciplinary care in Prader-Willi syndrome.

Expert review of endocrinology & metabolism
2021

Independent and combined associations between fast-food outlet exposure and genetic risk for obesity: a population-based, cross-sectional study in the UK.

BMC medicine
2021

Lipocalin 13 enhances insulin secretion but is dispensable for systemic metabolic control.

Life science alliance
2021

Clinical management of patients with genetic obesity during COVID-19 pandemic: position paper of the ESE Growth & Genetic Obesity COVID-19 Study Group and Rare Endo-ERN main thematic group on Growth and Obesity.

Endocrine
2021

Experimental models of metabolic and alcoholic fatty liver disease.

World journal of gastroenterology
2020

Causal Inference for Genetic Obesity, Cardiometabolic Profile and COVID-19 Susceptibility: A Mendelian Randomization Study.

Frontiers in genetics
2020

Impact of Genetic Variations and Epigenetic Mechanisms on the Risk of Obesity.

International journal of molecular sciences
2020

MECHANISMS IN ENDOCRINOLOGY: Update on treatments for patients with genetic obesity.

European journal of endocrinology
2021

Stimulated GH levels during the transition phase in Prader-Willi syndrome.

Journal of endocrinological investigation
2021

Angiopoietin-like 8 (ANGPTL8) as a potential predictor of NAFLD in paediatric patients with Prader-Willi Syndrome.

Journal of endocrinological investigation
2021

Unilateral section of the superior ovarian nerve induces first ovulation in the Zucker fatty (fa/fa) rat.

General and comparative endocrinology
2020

Fat-Free Mass Is Better Related to Serum Uric Acid Than Metabolic Homeostasis in Prader-Willi Syndrome.

Nutrients
2020

Bariatric Surgery for Monogenic Non-syndromic and Syndromic Obesity Disorders.

Current diabetes reports
2020

Bardet-Biedl syndrome and related disorders in Japan.

Journal of human genetics
2020

Leptin-Mediated Changes in the Human Metabolome.

The Journal of clinical endocrinology and metabolism
2020

Identifying underlying medical causes of pediatric obesity: Results of a systematic diagnostic approach in a pediatric obesity center.

PloS one
2020

Dietary Hemp Seeds More Effectively Attenuate Disorders in Genetically Obese Rats than Their Lipid Fraction.

The Journal of nutrition
2020

Delivery of phosphatidylethanolamine blunts stress in hepatoma cells exposed to elevated palmitate by targeting the endoplasmic reticulum.

Cell death discovery
2021

Class A1 scavenger receptor prevents obesity-associated blood pressure elevation through suppressing overproduction of vascular endothelial growth factor B in macrophages.

Cardiovascular research
2020

Adenosine accumulation causes metabolic disorders in testes and associates with lower testosterone level in obese mice.

Molecular reproduction and development
2020

A Targeted Next Generation Sequencing Panel for Non-syndromic Early Onset Severe Obesity and Identification of Novel Likely -Pathogenic Variants in the MC4R and LEP Genes.

Indian journal of pediatrics
2020

Genetic Obesity and Bariatric Surgery Outcome in 1014 Patients with Morbid Obesity.

Obesity surgery
2019

Mendelian non-syndromic obesity.

Acta bio-medica : Atenei Parmensis
2020

Differential contribution of Nox1, Nox2 and Nox4 to kidney vascular oxidative stress and endothelial dysfunction in obesity.

Redox biology
2019

Uniparental disomy and pretreatment IGF-1 may predict elevated IGF-1 levels in Prader-Willi patients on GH treatment.

Growth hormone & IGF research : official journal of the Growth Hormone Research Society and the International IGF Research Society
2019

Adipocyte-specific deletion of IL-6 does not attenuate obesity-induced weight gain or glucose intolerance in mice.

American journal of physiology. Endocrinology and metabolism
2019

Genetics of lipedema: new perspectives on genetic research and molecular diagnoses.

European review for medical and pharmacological sciences
2019

Tracing the effect of the melanocortin-4 receptor pathway in obesity: study design and methodology of the TEMPO registry.

The application of clinical genetics
2019

Extensive Phenotyping for Potential Weight-Inducing Factors in an Outpatient Population with Obesity.

Obesity facts
2019

A comprehensive diagnostic approach to detect underlying causes of obesity in adults.

Obesity reviews : an official journal of the International Association for the Study of Obesity
2019

Genetic obesity increases pancreatic expression of mitochondrial proteins which regulate cholesterol efflux in BRIN-BD11 insulinoma cells.

Bioscience reports
2019

A toddler with a novel LEPR mutation.

Hormones (Athens, Greece)
2019

Association between genetic obesity susceptibility and mother-reported eating behaviour in children up to 5 years.

Pediatric obesity
2019

Increased brain age in adults with Prader-Willi syndrome.

NeuroImage. Clinical
2018

Obesity management in Prader-Willi syndrome: current perspectives.

Diabetes, metabolic syndrome and obesity : targets and therapy
2018

p53 Functions in Adipose Tissue Metabolism and Homeostasis.

International journal of molecular sciences
2018

Dipeptidyl-Peptidase 4 Inhibitor Sitagliptin Ameliorates Hepatic Insulin Resistance by Modulating Inflammation and Autophagy in ob/ob Mice.

International journal of endocrinology
2018

Hippocampal brain-derived neurotrophic factor determines recruitment of anatomically connected networks after stress in diabetic mice.

Hippocampus
2018

Genetically Obese Human Gut Microbiota Induces Liver Steatosis in Germ-Free Mice Fed on Normal Diet.

Frontiers in microbiology
2019

Insights into the Allosteric Mechanism of Setmelanotide (RM-493) as a Potent and First-in-Class Melanocortin-4 Receptor (MC4R) Agonist To Treat Rare Genetic Disorders of Obesity through an in Silico Approach.

ACS chemical neuroscience
2018

Genetic obesity: next-generation sequencing results of 1230 patients with obesity.

Journal of medical genetics
2018

Autoimmune pituitary involvement in Prader-Willi syndrome: new perspective for further research.

Endocrine
2018

Obesity-induced overexpression of miRNA-24 regulates cholesterol uptake and lipid metabolism by targeting SR-B1.

Gene
2018

Finding treatable genetic obesity: strategies for success.

Current opinion in pediatrics
2018

Discovery of dimethyl pent-4-ynoic acid derivatives, as potent and orally bioavailable DGAT1 inhibitors that suppress body weight in diet-induced mouse obesity model.

Bioorganic & medicinal chemistry letters
2018

A Transcriptomic Signature of the Hypothalamic Response to Fasting and BDNF Deficiency in Prader-Willi Syndrome.

Cell reports
2018

ROHHAD Syndrome, a Rare Cause of Hypothalamic Obesity: Report of Two Cases.

Journal of clinical research in pediatric endocrinology
2018

Genetic factors in sleep-disordered breathing.

Respiratory investigation
2018

Enoyl coenzyme A hydratase 1 protects against high-fat-diet-induced hepatic steatosis and insulin resistance.

Biochemical and biophysical research communications
2018

Effects of a combined intervention with a lentil protein hydrolysate and a mixed training protocol on the lipid metabolism and hepatic markers of NAFLD in Zucker rats.

Food & function
2018

Pyruvate induces torpor in obese mice.

Proceedings of the National Academy of Sciences of the United States of America
2017

Interactome of Obesity: Obesidome : Genetic Obesity, Stress Induced Obesity, Pathogenic Obesity Interaction.

Advances in experimental medicine and biology
2017

Metabolic biomarkers and gallstone disease - a population-based study.

Scandinavian journal of gastroenterology
2017

Engineering brown fat into skeletal muscle using ultrasound-targeted microbubble destruction gene delivery in obese Zucker rats: Proof of concept design.

IUBMB life
2017

Letter by Koh Regarding Article, "Genetic Obesity and the Risk of Atrial Fibrillation: Causal Estimates from Mendelian Randomization".

Circulation
2017

FTO genotype and weight status among preadolescents: Assessing the mediating effects of obesogenic appetitive traits.

Appetite
2017

Long-term effects of bariatric surgery in patients with obesity and chromosome 16 p11.2 microdeletion.

Surgery for obesity and related diseases : official journal of the American Society for Bariatric Surgery
2017

Maternal Uniparental Disomy 14 (Temple Syndrome) as a Result of a Robertsonian Translocation.

Molecular syndromology
2017

Dietary effects of Raphanus sativus cv Sango on lipid and oxysterols accumulation in rat brain: A lipidomic study on a non-genetic obesity model.

Chemistry and physics of lipids
2017

Obesity-induced discrepancy between contractile and metabolic phenotypes in slow- and fast-twitch skeletal muscles of female obese Zucker rats.

Journal of applied physiology (Bethesda, Md. : 1985)
2017

[Genetic obesity: new diagnostic options].

Nederlands tijdschrift voor geneeskunde
2017

Genetic Obesity Risk and Attenuation Effect of Physical Fitness in Mexican-Mestizo Population: a Case-Control Study.

Annals of human genetics
2016

Effects of pterostilbene in brown adipose tissue from obese rats.

Journal of physiology and biochemistry
2017

A cafeteria diet triggers intestinal inflammation and oxidative stress in obese rats.

The British journal of nutrition

Associações

Organizações que acompanham esta doença — pra ter apoio e orientação

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Comunidades

Grupos ativos de quem convive com esta doença aqui no Raras

Ainda não existe comunidade no Raras para Obesidade, genética

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Doenças relacionadas

Doenças com sintomas parecidos — ajudam quem ainda está buscando diagnóstico

Ordenadas pelo número de sintomas em comum.

Referências e fontes

Bases de dados externas citadas neste artigo

Publicações científicas

Artigos indexados no PubMed ligados a esta doença no grafo RarasNet — título, periódico e PMID direto da fonte, sem intermediação de IA.

  1. Sleep-Disordered Breathing in Chung-Jansen Syndrome.
    International journal of molecular sciences· 2026· PMID 41751879mais citado
  2. Targeted Next-Generation Sequencing of the Leptin-Melanocortin Pathway in Severe Obesity.
    Obesity (Silver Spring, Md.)· 2026· PMID 41451896mais citado
  3. Sex Differences in Leptin Levels in Children and Adolescents with Normal Weight and Overweight/Obesity Across Pubertal Stages: A Systematic Review and Meta-analysis.
    The Journal of clinical endocrinology and metabolism· 2026· PMID 41240372mais citado
  4. Case Series of Nizon-Isidor Syndrome by Heterozygous Variants in MED12L With Further Evidence of Mitotic Instability in One Case With Diploid-Triploid Mosaicism.
    American journal of medical genetics. Part A· 2026· PMID 40838347mais citado
  5. Innovative Care for Children and Adolescents with Severe and/or Genetic Obesity.
    Hormone research in paediatrics· 2026· PMID 40159376mais citado
  6. Setmelanotide in Bardet-Biedl Syndrome: A Case Report.
    Pediatr Dermatol· 2026· PMID 41994885recente
  7. A new era in childhood obesity.
    Trends Endocrinol Metab· 2026· PMID 41927456recente
  8. The Role of GLP1 Receptor Agonists and Multi-agonist Incretin Therapies for Specific Obesity-related Health Conditions: Evidence and Rationale for Prioritisation.
    Curr Obes Rep· 2026· PMID 41922811recente

Bases de dados e fontes oficiais

Identificadores e referências canônicas usadas para montar este verbete.

  1. ORPHA:77828(Orphanet)
  2. OMIM OMIM:601665(OMIM)
  3. MONDO:0019182(MONDO)
  4. GARD:18935(GARD (NIH))
  5. Variantes catalogadas(ClinVar)
  6. Busca completa no PubMed(PubMed)
  7. Q5532952(Wikidata)

Dados compilados pelo RarasNet a partir de fontes abertas (Orphanet, OMIM, MONDO, PubMed/EuropePMC, ClinicalTrials.gov, DATASUS, PCDT/MS). Este conteúdo é informativo e não substitui avaliação médica.

Conteúdo mantido por Agente Raras · Médicos e pesquisadores podem colaborar

Obesidade, genética
Compêndio · Raras BR

Obesidade, genética

ORPHA:77828 · MONDO:0019182
Ensaios
2 ativos
MedGen
UMLS
C5681294
Repurposing
2 candidatos
ephedrineadrenergic receptor agonist
ephedrine-(racemic)
EuropePMC
Wikidata
Papers 10a
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