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Displasia ectodérmica hipohidrótica ligada ao X
ORPHA:181CID-10 · Q82.4CID-11 · LD27.02OMIM 305100DOENÇA RARA

Forma de displasia ectodérmica ligada ao cromossomo X que resulta de mutações no gene que codifica a ectodisplasina.

Mantido por Agente Raras·Colaborar como especialista →

Introdução

O que você precisa saber de cara

📋

Forma de displasia ectodérmica ligada ao cromossomo X que resulta de mutações no gene que codifica a ectodisplasina.

Pesquisas ativas
2 ensaios
21 total registrados no ClinicalTrials.gov
Publicações científicas
232 artigos
Último publicado: 2025

Escala de raridade

CLASSIFICAÇÃO ORPHANET · BRASIL 2024
1-9 / 1 000 000
Ultra-rara
<1/50k
Muito rara
1/20k
Rara
1/10k
Pouco freq.
1/5k
Incomum
1/2k
Prevalência
0.0
Europe
Início
Childhood
+ infancy
🏥
SUS: Cobertura mínimaScore: 15%
CID-10: Q82.4
🇧🇷Dados SUS / DATASUS
PROCEDIMENTOS SIGTAP (5)
0202010503
Cariótipo — bandas G, Q ou Rgenetic_test
0202010600
Pesquisa de microdeleções/microduplicações por FISHlab_test
0202010694
Sequenciamento completo do exoma (WES)rehabilitation
0202010260
Dosagem de alfa-fetoproteína
0301070040
Atendimento em reabilitação — doenças raras
Você se identifica com essa condição?
O Raras está aqui pra te apoiar — com ou sem diagnóstico

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Entender a doença

Do básico ao detalhe, leia no seu ritmo

Preparando trilha educativa...

Sinais e sintomas

O que aparece no corpo e com que frequência cada sintoma acontece

Partes do corpo afetadas

🧬
Pele e cabelo
10 sintomas
😀
Face
9 sintomas
👁️
Olhos
5 sintomas
🦴
Ossos e articulações
2 sintomas
🦷
Dentes
2 sintomas
📏
Crescimento
2 sintomas

+ 22 sintomas em outras categorias

Características mais comuns

100%prev.
Início na infância
Frequência: 2/2
100%prev.
Cabelo esparso
Muito frequente (99-80%)
100%prev.
Hipo-hidrose
Muito frequente (99-80%)
100%prev.
Pelos corporais esparsos
Muito frequente (99-80%)
100%prev.
Hiperpigmentação periorbital
Obrigatório (100%)
100%prev.
Testa proeminente
Obrigatório (100%)
54sintomas
Muito frequente (21)
Frequente (1)
Ocasional (4)
Sem dados (28)

Os sintomas variam de pessoa para pessoa. Abaixo estão as 54 características clínicas mais associadas, ordenadas por frequência.

Início na infânciaInfantile onset
Frequência: 2/2100%
Cabelo esparsoSparse hair
Muito frequente (99-80%)100%
Hipo-hidroseHypohidrosis
Muito frequente (99-80%)100%
Pelos corporais esparsosSparse body hair
Muito frequente (99-80%)100%
Hiperpigmentação periorbitalPeriorbital hyperpigmentation
Obrigatório (100%)100%

Linha do tempo da pesquisa

Publicações por ano — veja quando o interesse científico cresceu
Anos de pesquisa1desde 2026
Total histórico232PubMed
Últimos 10 anos96publicações
Pico202115 papers
Linha do tempo
2026Hoje · 2026🧪 2009Primeiro ensaio clínico📈 2021Ano de pico
Publicações por ano (últimos 10 anos)

Encontrou um erro ou informação desatualizada? Sugira uma correção →

Genética e causas

O que está alterado no DNA e como passa nas famílias

Genes associados

2 genes identificados com associação a esta condição. Padrão de herança: X-linked recessive.

EDAEctodysplasin-ADisease-causing germline mutation(s) inAltamente restrito
FUNÇÃO

Cytokine which is involved in epithelial-mesenchymal signaling during morphogenesis of ectodermal organs. Functions as a ligand activating the DEATH-domain containing receptors EDAR and EDA2R (PubMed:11039935, PubMed:27144394, PubMed:34582123, PubMed:8696334). May also play a role in cell adhesion (By similarity) Binds only to the receptor EDAR, while isoform 3 binds exclusively to the receptor EDA2R Binds only to the receptor EDA2R

LOCALIZAÇÃO

Cell membraneSecreted

VIAS BIOLÓGICAS (1)
TNFs bind their physiological receptors
MECANISMO DE DOENÇA

Ectodermal dysplasia 1, hypohidrotic, X-linked

A form of ectodermal dysplasia, a heterogeneous group of disorders due to abnormal development of two or more ectodermal structures. Characterized by sparse hair (atrichosis or hypotrichosis), abnormal or missing teeth and the inability to sweat due to the absence of sweat glands. It is the most common form of over 150 clinically distinct ectodermal dysplasias.

EXPRESSÃO TECIDUAL(Ubíquo)
Glândula adrenal
8.1 TPM
Nervo tibial
7.0 TPM
Tireoide
6.9 TPM
Cervix Ectocervix
6.8 TPM
Ovário
6.4 TPM
OUTRAS DOENÇAS (3)
X-linked hypohidrotic ectodermal dysplasiatooth agenesis, selective, X-linked, 1tooth agenesis
HGNC:3157UniProt:Q92838
EDA2RTumor necrosis factor receptor superfamily member 27Disease-causing germline mutation(s) inTolerante
FUNÇÃO

Receptor for EDA isoform A2, but not for EDA isoform A1. Mediates the activation of the NF-kappa-B and JNK pathways. Activation seems to be mediated by binding to TRAF3 and TRAF6

LOCALIZAÇÃO

Membrane

VIAS BIOLÓGICAS (1)
TNFs bind their physiological receptors
EXPRESSÃO TECIDUAL(Ubíquo)
Fibroblastos
34.4 TPM
Linfócitos
16.9 TPM
Aorta
16.6 TPM
Útero
14.0 TPM
Cervix Endocervix
12.8 TPM
OUTRAS DOENÇAS (1)
X-linked hypohidrotic ectodermal dysplasia
HGNC:17756UniProt:Q9HAV5

Variantes genéticas (ClinVar)

598 variantes patogênicas registradas no ClinVar.

🧬 EDA: NM_001399.5(EDA):c.687del (p.Gly230fs) ()
🧬 EDA: NM_001399.5(EDA):c.913A>C (p.Ser305Arg) ()
🧬 EDA: NM_001399.5(EDA):c.583G>A (p.Gly195Arg) ()
🧬 EDA: NM_001399.5(EDA):c.1135T>C (p.Phe379Leu) ()
🧬 EDA: NM_001399.5(EDA):c.644del (p.Gly215fs) ()
Ver todas no ClinVar

Vias biológicas (Reactome)

1 via biológica associada aos genes desta condição.

Diagnóstico

Os sinais que médicos procuram e os exames que confirmam

Carregando...

Tratamento e manejo

Remédios, cuidados de apoio e o que precisa acompanhar

Pipeline de tratamentos
Pipeline regulatório — de medicamentos já aprovados a drogas em pesquisa exploratória.
2Fase 22
1Fase 11
·Pré-clínico17
Medicamentos catalogadosEnsaios clínicos· 0 medicamentos · 20 ensaios
Carregando informações de tratamento...

Onde tratar no SUS

Hospitais de referência no Brasil e o protocolo oficial do SUS (PCDT)

🇧🇷 Atendimento SUS — Displasia ectodérmica hipohidrótica ligada ao X

🗺️

Selecione um estado ou use sua localização para ver resultados.

Dados de DATASUS/CNES, SBGM, ABNeuro e Ministério da Saúde. Sempre confirme a disponibilidade diretamente com o estabelecimento.

Pesquisa ativa

Ensaios clínicos abertos e novidades científicas recentes

🟢 Recrutando agora

1 pesquisa recrutando participantes. Converse com seu médico sobre a possibilidade de participar.

Outros ensaios clínicos

21 ensaios clínicos encontrados, 2 ativos.

Distribuição por fase
NCT07096206 · Characteristics and Impacts of X-linked Hypohidrotic Ectoder…Ativo
NCT05378932 · Impact of Dysregulation of Core Body Temperature on Sleep in…Concluído
NA
NCT01135888 · Short Term Effects and Risks of Physical Exercise in Subject…Concluído
NCT04741412 · Pediatric SARS-CoV-2 Infections: Course of COVID-19, Immune …Concluído
NCT01992289 · Extension Study of XLHED-Affected Male Subjects Treated With…UNKNOWN
NCT02099552 · Natural History and Outcomes in X-Linked Hypohidrotic Ectode…Concluído
NCT01775462 · Phase 2 Study to Evaluate Safety, Pharmacokinetics, Immunoge…Concluído
PHASE2
NCT01308333 · Investigation of Chronic Inflammatory Processes in Male Indi…Concluído
NCT01871714 · Phenotypic Properties in Individuals Affected With XLHEDConcluído
NCT01564225 · A Phase 1, Open-label, Multicenter, Safety and Pharmacokinet…Concluído
PHASE1
NCT01398813 · X-Linked Hypohidrotic Ectodermal Dysplasia (XLHED) Carrier O…Concluído
NCT01629940 · Phenotypic and Genetic Properties in Males at Risk for X-lin…Concluído
NCT01108770 · Evaluation of Phenotypic and Genetic Properties in Male Subj…Concluído
NCT01342133 · Sweat Duct Imaging in Mother/Newborn DyadsConcluído
NCT01398397 · Medical Record Review of Hypohidrotic Ectodermal Dysplasia C…Concluído
NCT01629927 · Evaluation of Phenotypic and Genetic Properties in Male Subj…Concluído
NCT01293565 · Evaluation of Phenotypic and Genetic Properties in Male Subj…Concluído
NCT01386775 · Male Subjects Affected By Hypohidrotic Ectodermal Dysplasia:…Concluído
NCT01109290 · Characterization of Sweat Gland Function in Patients With Re…Concluído
Ver todos no ClinicalTrials.gov
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Publicações mais relevantes

Timeline de publicações
95 papers (10 anos)
#1

Prenatal Ultrasound Findings of X-Linked Hypohidrotic Ectodermal Dysplasia: A Case Report.

Journal of clinical ultrasound : JCU2026 Jan

X-linked hypohidrotic ectodermal dysplasia (HED) is a rare congenital hereditary disorder primarily affecting ectodermal-derived organs, including hair, sweat glands, and teeth. This case report presents a prenatal diagnosis of HED in a fetus without a familial history or parental phenotypic manifestations. The critical prenatal ultrasound finding was an abnormality in the alveolar bone. Genetic testing confirmed the fetus as a hemizygote for a mutation in the ectodysplasin A gene. This comprehensive study delineates the prenatal ultrasound observations, genetic testing outcomes, and post-mortem pathological findings associated with this syndrome. We also highlight essential considerations for early diagnosis through prenatal ultrasound examinations.

#2

Transcriptome analysis identifies EDA1 variants disrupt FOSB-mediated regulation of odontogenic epithelial cell behaviors during dental germ development.

Frontiers in cell and developmental biology2025

Here, we systematically investigated the effects of EDA1 variants on apoptosis, migration, and adhesion in ameloblast-like LS8 cells and identified downstream effectors of the EDA-NF-κB pathway through RNA sequencing (RNA-seq) combined with in vivo and in vitro validation. LS8 cells were transiently transfected with four constructs: wild-type (Wt) EDA1, nonsyndromic tooth agenesis-associated EDA1 variant (EDA1-A259E), X-linked hypohidrotic ectodermal dysplasia-associated EDA1 variant (EDA1-H252L), or empty vector control (pCMV-C-FLAG). We used flow cytometry, wound-healing assay, and cell counting kit 8 assay to assess cell apoptosis, migration, and adhesion, respectively. High-throughput RNA-seq was used to identify differentially expressed genes, which were subsequently validated through quantitative polymerase chain reaction and immunoblotting. Spatiotemporal Fosb expression patterns were comparatively analyzed in Wt and Tabby mouse tooth germs through in situ hybridization by using RNAscope. Wt EDA1 transiently enhances cellular migratory capacity, a function compromised in the pathogenic EDA1 variants. The EDA-NF-κB pathway operates through FOSB-mediated transcriptional regulation, as evidenced by coordinated suppression of Fosb expression at transcriptional and translational levels in the mutant models. Therefore, FOSB is a candidate downstream effector in EDA1-mediated odontogenesis. These results provide mechanistic insights into ectodermal dysplasia pathogenesis.

#3

Attitudes of female carriers of X-linked hypohidrotic ectodermal dysplasia towards prenatal treatment and their decisions during a pregnancy with a male fetus.

Orphanet journal of rare diseases2025 Apr 15

X-linked hypohidrotic ectodermal dysplasia (XLHED) is a severe genetic disorder that may be treatable with short-term protein replacement therapy during fetal development. This is currently being investigated in a multicenter clinical trial. Affected fetuses can be identified by the number of tooth germs during a routine ultrasound scan in mid-gestation. To understand the attitudes of female XLHED carriers towards prenatal treatment and ultrasonographic screening of the fetus, we analyzed an earlier and a very recent survey among those women and the actual decisions of potential trial participants. Initial analyses were based on a self-administered survey of 167 female XLHED carriers conducted in 2011. A similar questionnaire was completed 12 years later by 72 female XLHED carriers aged 18-45 years. Subsequently, both the path to diagnosis and further decision-making of the first 33 pregnant women screened for participation in the EDELIFE trial were investigated. Most women diagnosed with XLHED considered this disease as an obstacle to having children: About one third had decided not to have children, another third would monitor their pregnancy using invasive genetic testing. In both surveys, a small number of women stated that they would consider termination of pregnancy depending on the test result. When it came to participating in the clinical trial, 80% were likely to take part (17% moderately likely, 63% very likely). Among the first pregnant women screened for this trial, 48% underwent invasive tests, while 52% relied on non-invasive tooth germ imaging for fetal XLHED diagnosis. One pregnancy with an affected fetus was terminated, another one resulted in a miscarriage, one woman declined to participate in the trial, and 12 women (80%) decided to have the affected fetuses treated. Ultrasound-based screening and prenatal treatment of the fetus are viewed positively by the vast majority of female XLHED carriers.

#4

Prenatal Identification of an EDA Variant in Dichorionic Male Twins: CfDNA Signal with Invasive Confirmation.

Genes2025 Dec 10

X-linked hypohidrotic ectodermal dysplasia (XLHED) is a rare monogenic disorder characterized by hypohidrosis, hypotrichosis, and hypodontia, caused primarily by pathogenic variants in the EDA gene. XLHED predominantly affects males due to its X-linked recessive inheritance, while female carriers may exhibit variable phenotypes due to random X-inactivation. Early diagnosis is critical for timely counseling and emerging therapeutic interventions. We report a rare prenatal diagnosis of XLHED in dizygotic dichorionic male twins during a dichorionic diamniotic pregnancy. At 24 weeks' gestation, ultrasonographic anomalies-facial dysmorphisms, oligodontia, and hypoechogenic skin-raised suspicion for ectodermal dysplasia. Non-invasive prenatal test and targeted next-generation sequencing (NGS) of Cell-free DNA identified an hemizygous EDA deletion (c.612_629del; p.Ile205_Gly210del) with 52% variant allele frequency. This in-frame deletion affects a highly conserved region in the TNF homology domain of ectodysplasin-A1, likely compromising protein function. The variant was confirmed in both fetuses via genetic analysis on amniotic fluid and in the heterozygous state in the mother, consistent with X-linked recessive inheritance. Family history revealed a maternal uncle with XLHED. Additional heterozygous variants were also identified in CPT2, GBA1, GJB2, and SMN1 genes. Following comprehensive genetic counseling, the mother opted for abortion. This case underscores the value of applying advanced genomic technologies-cfDNA-based NGS-for prenatal diagnosis of rare genetic disorders. The identification of apathogenic EDA variant expands the mutational spectrum of XLHED and supports early diagnosis for informed reproductive decisions and potential access to emerging prenatal therapies. Broader application of such technologies may improve outcomes in future pregnancies at risk for monogenic disorders.

#5

A novel EDA variant that causes X-linked hypohidrotic ectodermal dysplasia in a Chinese family.

BMC pregnancy and childbirth2025 Aug 08

Hypohidrotic ectodermal dysplasia (HED) is a rare genetic disorder that affects the development of the skin, hair, nails, teeth, and sweat glands. Due to its rarity, there are currently few methods that can be applied to facilitate its diagnosis during the prenatal period. Although a prenatal ultrasonographic examination will detect early signs of the disease, there are few reports on specific prenatal ultrasonographic features of ectodermal dysplasia. Genetic diagnosis can confirm the disease, but the numerous gene variants that cause ectodermal dysplasia have not been fully identified. Our case was a multiparous woman carrying a single male fetus who underwent a fetal ultrasound examination at 23 weeks of gestation. The examination revealed thin alveolar bone, with no presence of hypoechoic tooth germ tissue in both the upper and lower alveolar bones. The seven-year-old male proband in this family manifested a clinical phenotype of sparse hair and underdeveloped teeth, and trio-based whole-exome sequencing (WES) performed on both parents and the proband revealed a novel and likely pathogenic variant of the EDA gene (NM_001399.4: c.806G > T, p.Gly269Val) associated with X-linked HED (XLHED; OMIM:305100). Based on the results of the fetal ultrasound examination and the results of the proband's genetic testing, the couple ultimately decided to terminate the pregnancy. The DNA of the fetal skin tissue after the induced abortion was extracted for Sanger sequencing, and it was confirmed that the fetus possessed ectodermal dysplasia generated by the afore-mentioned EDA gene mutation. Our study suggested that prenatal ultrasonography constituted an effective method for screening ectodermal dysplasia during pregnancy. In addition, our findings expanded the range of EDA variants in XLHED patients; and this discovery may now assist potential patients in receiving an accurate diagnosis, allowing them to make appropriate reproductive decisions.

Publicações recentes

Ver todas no PubMed

📚 EuropePMC160 artigos no totalmostrando 93

2025

Transcriptome analysis identifies EDA1 variants disrupt FOSB-mediated regulation of odontogenic epithelial cell behaviors during dental germ development.

Frontiers in cell and developmental biology
2025

Prenatal Identification of an EDA Variant in Dichorionic Male Twins: CfDNA Signal with Invasive Confirmation.

Genes
2026

Prenatal Ultrasound Findings of X-Linked Hypohidrotic Ectodermal Dysplasia: A Case Report.

Journal of clinical ultrasound : JCU
2025

A novel EDA variant that causes X-linked hypohidrotic ectodermal dysplasia in a Chinese family.

BMC pregnancy and childbirth
2025

X-linked hypohidrotic ectodermal dysplasia associated with gastroesophageal reflux disease.

Molecular genetics and metabolism reports
2025

Attitudes of female carriers of X-linked hypohidrotic ectodermal dysplasia towards prenatal treatment and their decisions during a pregnancy with a male fetus.

Orphanet journal of rare diseases
2024

An Interesting Case of X-linked Hypohidrotic Ectodermal Dysplasia.

Cureus
2024

EDA Missense Variant in a Cat with X-Linked Hypohidrotic Ectodermal Dysplasia.

Genes
2024

X-linked hypohidrotic ectodermal dysplasia with a deletion in exon 2 of the EDA gene: a case report and literature review.

European journal of dermatology : EJD
2024

A Novel Ectodysplasin a Gene mutation of X-Linked Hypohidrotic Ectodermal Dysplasia.

Clinical, cosmetic and investigational dermatology
2024

Craniofacial syndromes and class III phenotype: common genotype fingerprints? A scoping review and meta-analysis.

Pediatric research
2024

A missense mutation in the highly conserved TNF-like domain of Ectodysplasin A is the candidate causative variant for X-linked hypohidrotic ectodermal dysplasia in Limousin cattle: Clinical, histological, and molecular analyses.

PloS one
2024

Transcription factor FoxO1 regulates myoepithelial cell diversity and growth.

Scientific reports
2023

Rare Pediatric Genetic Case Report of X-linked Hypohidrotic Ectodermal Dysplasia Type 1.

Cureus
2024

The oligodontia phenotype in a X-linked hypohidrotic ectodermal dysplasia patient with a novel EVC2 variant.

Heliyon
2024

Identification of six novel mutations in EDA from 20 hypohidrotic ectodermal dysplasia families.

Oral diseases
2023

X-Linked Hypohidrotic Ectodermal Dysplasia (XLHED): A Case Report and Overview of the Diagnosis and Multidisciplinary Modality Treatments.

Cureus
2023

Novel EDA mutations cause X-linked hypohidrotic ectodermal dysplasia: the first study from Venezuela.

Clinical and experimental dermatology
2023

A Causal Treatment for X-Linked Hypohidrotic Ectodermal Dysplasia: Long-Term Results of Short-Term Perinatal Ectodysplasin A1 Replacement.

International journal of molecular sciences
2023

A novel deletion of exon 4 in the Ectodysplasin A gene associated with X-linked hypohidrotic ectodermal dysplasia.

Archives of oral biology
2023

A call for implementing augmented intelligence in pediatric dermatology.

Pediatric dermatology
2023

Next generation sequencing panel target genes: possible diagnostic tool for ectodermal dysplasia related diseases.

Italian journal of dermatology and venereology
2023

Ectodysplasin Signaling through XEDAR Is Required for Mammary Gland Morphogenesis.

The Journal of investigative dermatology
2023

Protocol for the Phase 2 EDELIFE Trial Investigating the Efficacy and Safety of Intra-Amniotic ER004 Administration to Male Subjects with X-Linked Hypohidrotic Ectodermal Dysplasia.

Genes
2022

Congenital Nail Disorders among Children with Suspected Ectodermal Dysplasias.

Genes
2022

Ectodysplasin A1 Deficiency Leads to Osteopetrosis-like Changes in Bones of the Skull Associated with Diminished Osteoclastic Activity.

International journal of molecular sciences
2022

Rare X-Linked Hypohidrotic Ectodermal Dysplasia in Females Associated with Ectodysplasin-A Variants and the X-Chromosome Inactivation Pattern.

Diagnostics (Basel, Switzerland)
2022

Ectodermal dysplasias: New perspectives on the treatment of so far immedicable genetic disorders.

Frontiers in genetics
2022

Functional and clinical analysis of five EDA variants associated with ectodermal dysplasia but with a hard-to-predict significance.

Frontiers in genetics
2022

Three Variants Affecting Exon 1 of Ectodysplasin A Cause X-Linked Hypohidrotic Ectodermal Dysplasia: Clinical and Molecular Characteristics.

Frontiers in genetics
2022

Reproductive decision-making by women with X-linked hypohidrotic ectodermal dysplasia.

Journal of the European Academy of Dermatology and Venereology : JEADV
2021

Prenatal Genetic Testing for X-Linked Hypohidrotic Ectodermal Dysplasia.

Advances in experimental medicine and biology
2022

Ectodysplasin pathogenic variants affecting the furin-cleavage site and unusual clinical features define X-linked hypohidrotic ectodermal dysplasia in India.

American journal of medical genetics. Part A
2022

Understanding the impact of missense mutations on the structure and function of the EDA gene in X-linked hypohidrotic ectodermal dysplasia: A bioinformatics approach.

Journal of cellular biochemistry
2021

A novel EDA variant causing X-linked hypohidrotic ectodermal dysplasia: Case report.

Molecular genetics and metabolism reports
2021

Two novel ectodysplasin A gene mutations and prenatal diagnosis of X-linked hypohidrotic ectodermal dysplasia.

Molecular genetics &amp; genomic medicine
2021

[Genetic testing and genotype-phenotype analysis for a child with X-linked hypohidrotic ectodermal dysplasia].

Zhonghua yi xue yi chuan xue za zhi = Zhonghua yixue yichuanxue zazhi = Chinese journal of medical genetics
2021

First report of X-linked hypohidrotic ectodermal dysplasia with a hemizygous c.1142G > C in the EDA gene: variant of uncertain significance or new pathogenic variant?

Italian journal of pediatrics
2021

Genetic analysis of a possible case of canine X-linked ectodermal dysplasia.

The Journal of small animal practice
2021

Prenatal sonographic diagnosis of X-linked hypohidrotic ectodermal dysplasia: An unusual case.

Journal of clinical ultrasound : JCU
2021

[Clinical and genetic analysis of a child with X-linked hypohidrotic ectodermal dysplasia].

Zhonghua yi xue yi chuan xue za zhi = Zhonghua yixue yichuanxue zazhi = Chinese journal of medical genetics
2021

X-Linked Hypohidrotic Ectodermal Dysplasia in Crossbred Beef Cattle Due to a Large Deletion in EDA.

Animals : an open access journal from MDPI
2021

No evidence for preferential X-chromosome inactivation as the main cause of divergent phenotypes in sisters with X-linked hypohidrotic ectodermal dysplasia.

Orphanet journal of rare diseases
2021

Exome sequencing enables diagnosis of X-linked hypohidrotic ectodermal dysplasia in patient with eosinophilic esophagitis and severe atopy.

Allergy, asthma, and clinical immunology : official journal of the Canadian Society of Allergy and Clinical Immunology
2021

A novel c.916C>A EDA gene pathogenic variant in a boy with X-linked hypohidrotic ectodermal dysplasia.

Clinical and experimental dermatology
2021

Methods for the Administration of EDAR Pathway Modulators in Mice.

Methods in molecular biology (Clifton, N.J.)
2020

[Prenatal diagnosis of a fetus with X-linked hypohidrotic ectodermal dysplasia].

Zhonghua yi xue yi chuan xue za zhi = Zhonghua yixue yichuanxue zazhi = Chinese journal of medical genetics
2020

X-linked hypohidrotic ectodermal dysplasia by a de novo recurrent variant in a Mexican patient.

Boletin medico del Hospital Infantil de Mexico
2020

Safety and immunogenicity of Fc-EDA, a recombinant ectodysplasin A1 replacement protein, in human subjects.

British journal of clinical pharmacology
2020

A novel EDA1 missense mutation in X-linked hypohidrotic ectodermal dysplasia.

Medicine
2020

The characterization of hypodontia, hypohidrosis, and hypotrichosis associated with X-linked hypohidrotic ectodermal dysplasia: A systematic review.

American journal of medical genetics. Part A
2020

Natural history of X-linked hypohidrotic ectodermal dysplasia: a 5-year follow-up study.

Orphanet journal of rare diseases
2019

EDA, EDAR, EDARADD and WNT10A allelic variants in patients with ectodermal derivative impairment in the Spanish population.

Orphanet journal of rare diseases
2020

An unusual manifestation of X-linked hypohidrotic ectodermal dysplasia with palmoplantar keratoderma.

Clinical and experimental dermatology
2019

A novel frameshift mutation in the EDA gene in an Iranian patient affected by X-linked hypohidrotic ectodermal dysplasia.

Cellular &amp; molecular biology letters
2019

A novel missense mutation p.S305R of EDA gene causes XLHED in a Chinese family.

Archives of oral biology
2019

Prosthetic rehabilitation of a child with X-linked hypohidrotic ectodermal dysplasia: a case report and 12-month follow-up.

General dentistry
2019

X-linked hypohidrotic ectodermal dysplasia: clinical and molecular genetic analysis of a large Russian family with a synonymous p.Ser267= (c.801A>G) splice site mutation.

Journal of the European Academy of Dermatology and Venereology : JEADV
2019

Novel mutation of EDA causes new asymmetrical X-linked hypohidrotic ectodermal dysplasia phenotypes in a female.

The Journal of dermatology
2019

Novel and Private EDA Mutations and Clinical Phenotypes of Korean Patients with X-Linked Hypohidrotic Ectodermal Dysplasia.

Cytogenetic and genome research
2019

X-Linked Hypohidrotic Ectodermal Dysplasia-General Features and Dental Abnormalities in Affected Dogs Compared With Human Dental Abnormalities.

Topics in companion animal medicine
2019

Prenatal Treatment of X-Linked Hypohidrotic Ectodermal Dysplasia using Recombinant Ectodysplasin in a Canine Model.

The Journal of pharmacology and experimental therapeutics
2019

A de Novo EDA-Variant in a Litter of Shorthaired Standard Dachshunds with X-Linked Hypohidrotic Ectodermal Dysplasia.

G3 (Bethesda, Md.)
2019

Reliability of prenatal detection of X-linked hypohidrotic ectodermal dysplasia by tooth germ sonography.

Prenatal diagnosis
2018

A frameshift variant in the EDA gene in Dachshunds with X-linked hypohidrotic ectodermal dysplasia.

Animal genetics
2018

Dental Management and Prosthetic Rehabilitation of Patients Suffering from Hypohidrotic Ectodermal Dysplasia: A Report of Two Case Histories.

The International journal of prosthodontics
2018

Upper cervical spine and craniofacial morphology in hypohidrotic ectodermal dysplasia.

European archives of paediatric dentistry : official journal of the European Academy of Paediatric Dentistry
2018

Mutation Screening of the EDA Gene in Seven Chinese Families with X-Linked Hypohidrotic Ectodermal Dysplasia.

Genetic testing and molecular biomarkers
2018

Combined Preimplantation Genetic Testing for Aneuploidy and Monogenic Disease in a Mexican Family Affected by X-linked Hypohidrotic Ectodermal Dysplasia.

Revista de investigacion clinica; organo del Hospital de Enfermedades de la Nutricion
2018

Genetic diagnosis for X-linked hypohidrotic ectodermal dysplasia family with a novel Ectodysplasin A gene mutation.

Journal of clinical laboratory analysis
2018

Defective NaCl Reabsorption in Salivary Glands of Eda-Null X-LHED Mice.

Journal of dental research
2018

Prenatal Correction of X-Linked Hypohidrotic Ectodermal Dysplasia.

The New England journal of medicine
2017

A microRNA screen reveals that elevated hepatic ectodysplasin A expression contributes to obesity-induced insulin resistance in skeletal muscle.

Nature medicine
2017

First report on an X-linked hypohidrotic ectodermal dysplasia family with X chromosome inversion: Breakpoint mapping reveals the pathogenic mechanism and preimplantation genetics diagnosis achieves an unaffected birth.

Clinica chimica acta; international journal of clinical chemistry
2017

Novel EDA or EDAR Mutations Identified in Patients with X-Linked Hypohidrotic Ectodermal Dysplasia or Non-Syndromic Tooth Agenesis.

Genes
2018

A novel 1-bp deletion mutation and extremely skewed X-chromosome inactivation causing severe X-linked hypohidrotic ectodermal dysplasia in a Chinese girl.

Clinical and experimental dermatology
2017

X-Linked Hypohidrotic Ectodermal Dysplasia: New Features and a Novel EDA Gene Mutation.

Cytogenetic and genome research
2017

Mutation detection and prenatal diagnosis of XLHED pedigree.

PeerJ
2018

Ectodysplasin A regulates epithelial barrier function through sonic hedgehog signalling pathway.

Journal of cellular and molecular medicine
2017

Automatic recognition of the XLHED phenotype from facial images.

American journal of medical genetics. Part A
2017

Ectodysplasin A protein promotes corneal epithelial cell proliferation.

The Journal of biological chemistry
2017

Hypohidrotic Ectodermal Dysplasia: Breastfeeding Complications Due to Impaired Breast Development.

Geburtshilfe und Frauenheilkunde
2018

Delayed-onset heat intolerance in a Japanese patient with X-linked hypohidrotic ectodermal dysplasia associated with a large deletion involving four genes.

The Journal of dermatology
2016

A Splice Defect in the EDA Gene in Dogs with an X-Linked Hypohidrotic Ectodermal Dysplasia (XLHED) Phenotype.

G3 (Bethesda, Md.)
2016

Anticipated stigma and blameless guilt: Mothers' evaluation of life with the sex-linked disorder, hypohidrotic ectodermal dysplasia (XHED).

Social science &amp; medicine (1982)
2016

Ectodysplasin A Pathway Contributes to Human and Murine Skin Repair.

The Journal of investigative dermatology
2015

Identification of a novel mutation of the EDA gene in X-linked hypohidrotic ectodermal dysplasia.

Genetics and molecular research : GMR
2015

[Clinical and molecular study in a child with X-linked hypohidrotic ectodermal dysplasia].

Archivos argentinos de pediatria
2016

Prenatal diagnosis of single gene disorders using amniotic fluid as the starting material for PCR.

The Analyst
2015

Novel EDA mutation in X-linked hypohidrotic ectodermal dysplasia and genotype-phenotype correlation.

Oral diseases
2015

Dental Implant Therapy for a Child with X-linked Hypohidrotic Ectodermal Dysplasia--Three Decades of Managed Care.

The International journal of prosthodontics
2015

Case of X-linked hypohidrotic ectodermal dysplasia with a novel EDA missense mutation.

The Journal of dermatology
2015

A novel missense mutation in collagenous domain of EDA gene in a Chinese family with X-linked hypohidrotic ectodermal dysplasia.

Journal of genetics
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Doenças relacionadas

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Referências e fontes

Bases de dados externas citadas neste artigo

Publicações científicas

Artigos indexados no PubMed ligados a esta doença no grafo RarasNet — título, periódico e PMID direto da fonte, sem intermediação de IA.

  1. Prenatal Ultrasound Findings of X-Linked Hypohidrotic Ectodermal Dysplasia: A Case Report.
    Journal of clinical ultrasound : JCU· 2026· PMID 40797284mais citado
  2. Transcriptome analysis identifies EDA1 variants disrupt FOSB-mediated regulation of odontogenic epithelial cell behaviors during dental germ development.
    Frontiers in cell and developmental biology· 2025· PMID 41573682mais citado
  3. Attitudes of female carriers of X-linked hypohidrotic ectodermal dysplasia towards prenatal treatment and their decisions during a pregnancy with a male fetus.
    Orphanet journal of rare diseases· 2025· PMID 40234959mais citado
  4. Prenatal Identification of an EDA Variant in Dichorionic Male Twins: CfDNA Signal with Invasive Confirmation.
    Genes· 2025· PMID 41465157mais citado
  5. A novel EDA variant that causes X-linked hypohidrotic ectodermal dysplasia in a Chinese family.
    BMC pregnancy and childbirth· 2025· PMID 40781288mais citado
  6. X-linked hypohidrotic ectodermal dysplasia associated with gastroesophageal reflux disease.
    Mol Genet Metab Rep· 2025· PMID 40469581recente

Bases de dados e fontes oficiais

Identificadores e referências canônicas usadas para montar este verbete.

  1. ORPHA:181(Orphanet)
  2. OMIM OMIM:305100(OMIM)
  3. MONDO:0010585(MONDO)
  4. GARD:10427(GARD (NIH))
  5. Variantes catalogadas(ClinVar)
  6. Busca completa no PubMed(PubMed)
  7. Artigo Wikipedia(Wikipedia)

Dados compilados pelo RarasNet a partir de fontes abertas (Orphanet, OMIM, MONDO, PubMed/EuropePMC, ClinicalTrials.gov, DATASUS, PCDT/MS). Este conteúdo é informativo e não substitui avaliação médica.

Conteúdo mantido por Agente Raras · Médicos e pesquisadores podem colaborar

Displasia ectodérmica hipohidrótica ligada ao X
Compêndio · Raras BR

Displasia ectodérmica hipohidrótica ligada ao X

ORPHA:181 · MONDO:0010585
Prevalência
1-9 / 1 000 000
Herança
X-linked recessive
CID-10
Q82.4 · Displasia ectodérmica (anidrótica)
CID-11
Ensaios
2 ativos
Início
Childhood, Infancy
Prevalência
0.0 (Europe)
MedGen
UMLS
C0162359
EuropePMC
Wikipedia
Papers 10a
DiscussaoAtiva

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