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Síndrome Andersen-Tawil
ORPHA:37553CID-10 · G72.3CID-11 · BC65.0OMIM 170390DOENÇA RARA

A síndrome de Andersen (SA) é uma doença rara caracterizada por paralisia muscular periódica, prolongamento do intervalo QT com uma variedade de arritmias ventriculares (levando à predisposição à morte súbita cardíaca) e características físicas características: baixa estatura, escoliose, orelhas baixas, hipertelorismo, raiz nasal larga, micrognatia, clinodactilia, braquidactilia e sindactilia.

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Introdução

O que você precisa saber de cara

📋

A síndrome de Andersen (SA) é uma doença rara caracterizada por paralisia muscular periódica, prolongamento do intervalo QT com uma variedade de arritmias ventriculares (levando à predisposição à morte súbita cardíaca) e características físicas características: baixa estatura, escoliose, orelhas baixas, hipertelorismo, raiz nasal larga, micrognatia, clinodactilia, braquidactilia e sindactilia.

Pesquisas ativas
1 ensaio
4 total registrados no ClinicalTrials.gov
Publicações científicas
271 artigos
Último publicado: 2026 Mar

Escala de raridade

CLASSIFICAÇÃO ORPHANET · BRASIL 2024
Unknown
Ultra-rara
<1/50k
Muito rara
1/20k
Rara
1/10k
Pouco freq.
1/5k
Incomum
1/2k
Prevalência
0.0
Worldwide
Início
Childhood
🏥
SUS: Cobertura mínimaScore: 15%
CID-10: G72.3
🇧🇷Dados SUS / DATASUS
PROCEDIMENTOS SIGTAP (2)
0202010694
Sequenciamento completo do exoma (WES)genetic_test
0301070040
Atendimento em reabilitação — doenças rarasrehabilitation
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Entender a doença

Do básico ao detalhe, leia no seu ritmo

Preparando trilha educativa...

Sinais e sintomas

O que aparece no corpo e com que frequência cada sintoma acontece

Partes do corpo afetadas

😀
Face
14 sintomas
🦴
Ossos e articulações
12 sintomas
❤️
Coração
6 sintomas
🦷
Dentes
5 sintomas
📏
Crescimento
4 sintomas
🧠
Neurológico
4 sintomas

+ 27 sintomas em outras categorias

Características mais comuns

100%prev.
Hipertelorismo
Ocasional (29-5%)
100%prev.
Vermelhão do lábio superior fino
Ocasional (29-5%)
100%prev.
Mão pequena
Ocasional (29-5%)
100%prev.
Micrognatia
Frequente (79-30%)
100%prev.
Fraqueza muscular
100%prev.
Paralisia periódica
Frequência: 2/2
79sintomas
Muito frequente (8)
Frequente (12)
Ocasional (33)
Muito raro (3)
Sem dados (23)

Os sintomas variam de pessoa para pessoa. Abaixo estão as 79 características clínicas mais associadas, ordenadas por frequência.

HipertelorismoHypertelorism
Ocasional (29-5%)100%
Vermelhão do lábio superior finoThin upper lip vermilion
Ocasional (29-5%)100%
Mão pequenaSmall hand
Ocasional (29-5%)100%
MicrognatiaMicrognathia
Frequente (79-30%)100%
Fraqueza muscularMuscle weakness
Muito frequente100%

Linha do tempo da pesquisa

Publicações por ano — veja quando o interesse científico cresceu
Anos de pesquisa1desde 2026
Total histórico271PubMed
Últimos 10 anos161publicações
Pico202019 papers
Linha do tempo
2026Hoje · 2026🧪 2007Primeiro ensaio clínico📈 2020Ano de pico
Publicações por ano (últimos 10 anos)

Encontrou um erro ou informação desatualizada? Sugira uma correção →

Genética e causas

O que está alterado no DNA e como passa nas famílias

Genes associados

2 genes identificados com associação a esta condição. Padrão de herança: Autosomal dominant.

KCNJ5G protein-activated inward rectifier potassium channel 4Disease-causing germline mutation(s) inTolerante
FUNÇÃO

Inward rectifier potassium channels are characterized by a greater tendency to allow potassium to flow into the cell rather than out of it. Their voltage dependence is regulated by the concentration of extracellular potassium; as external potassium is raised, the voltage range of the channel opening shifts to more positive voltages. The inward rectification is mainly due to the blockage of outward current by internal magnesium. Can be blocked by external barium. This potassium channel is control

LOCALIZAÇÃO

Membrane

VIAS BIOLÓGICAS (2)
Activation of G protein gated Potassium channelsInhibition of voltage gated Ca2+ channels via Gbeta/gamma subunits
MECANISMO DE DOENÇA

Long QT syndrome 13

A heart disorder characterized by a prolonged QT interval on the ECG and polymorphic ventricular arrhythmias. They cause syncope and sudden death in response to exercise or emotional stress, and can present with a sentinel event of sudden cardiac death in infancy.

EXPRESSÃO TECIDUAL(Tecido-específico)
Glândula adrenal
62.9 TPM
Pituitária
25.4 TPM
Baço
10.2 TPM
Pâncreas
8.2 TPM
Rim - Medula
6.3 TPM
OUTRAS DOENÇAS (5)
familial hyperaldosteronism type IIIlong QT syndrome 13familial atrial fibrillationAndersen-Tawil syndrome
HGNC:6266UniProt:P48544
KCNJ2Inward rectifier potassium channel 2Disease-causing germline mutation(s) inModerado
FUNÇÃO

Inward rectifier potassium channels are characterized by a greater tendency to allow potassium to flow into the cell rather than out of it (PubMed:36149965, PubMed:7590287, PubMed:9490857). Their voltage dependence is regulated by the concentration of extracellular potassium; as external potassium is raised, the voltage range of the channel opening shifts to more positive voltages (PubMed:7590287, PubMed:7696590). The inward rectification is mainly due to the blockage of outward current by inter

LOCALIZAÇÃO

Cell membraneCell membrane, sarcolemma, T-tubule

VIAS BIOLÓGICAS (5)
Activation of G protein gated Potassium channelsInhibition of voltage gated Ca2+ channels via Gbeta/gamma subunitsClassical Kir channelsPhase 4 - resting membrane potentialSensory perception of sour taste
MECANISMO DE DOENÇA

Long QT syndrome 7

A heart disorder characterized by a prolonged QT interval on the ECG and polymorphic ventricular arrhythmias. They cause syncope and sudden death in response to exercise or emotional stress, and can present with a sentinel event of sudden cardiac death in infancy. Long QT syndrome type 7 manifests itself as a clinical triad consisting of potassium-sensitive periodic paralysis, ventricular ectopy and dysmorphic features.

EXPRESSÃO TECIDUAL(Ubíquo)
Baço
10.1 TPM
Brain Spinal cord cervical c-1
9.1 TPM
Sangue
6.5 TPM
Coração - Ventrículo esquerdo
5.5 TPM
Mama
5.1 TPM
OUTRAS DOENÇAS (5)
short QT syndrome type 3Andersen-Tawil syndromeatrial fibrillation, familial, 9short QT syndrome
HGNC:6263UniProt:P63252

Variantes genéticas (ClinVar)

302 variantes patogênicas registradas no ClinVar.

🧬 KCNJ5: NM_000890.5(KCNJ5):c.283A>G (p.Met95Val) ()
🧬 KCNJ5: GRCh38/hg38 11q24.1-25(chr11:123345328-135064169)x1 ()
🧬 KCNJ5: NM_000890.5(KCNJ5):c.637G>C (p.Glu213Gln) ()
🧬 KCNJ5: NM_000890.5(KCNJ5):c.367G>C (p.Asp123His) ()
🧬 KCNJ5: NM_000890.5(KCNJ5):c.360T>G (p.His120Gln) ()
Ver todas no ClinVar

Classificação de variantes (ClinVar)

Distribuição de 545 variantes classificadas pelo ClinVar.

27
273
245
Patogênica (5.0%)
VUS (50.1%)
Benigna (45.0%)
VARIANTES MAIS SIGNIFICATIVAS
KCNJ2: NM_000891.3(KCNJ2):c.647A>G (p.Asn216Ser) [Likely pathogenic]
KCNJ2: NM_000891.3(KCNJ2):c.748A>G (p.Ile250Val) [Uncertain significance]
KCNJ2: NM_000891.3(KCNJ2):c.847A>G (p.Ser283Gly) [Uncertain significance]
KCNJ2: NM_000891.3(KCNJ2):c.1022A>C (p.Tyr341Ser) [Uncertain significance]
KCNJ2: NM_000891.3(KCNJ2):c.801C>G (p.Ile267Met) [Uncertain significance]

Diagnóstico

Os sinais que médicos procuram e os exames que confirmam

Carregando...

Tratamento e manejo

Remédios, cuidados de apoio e o que precisa acompanhar

Pipeline de tratamentos
Pipeline regulatório — de medicamentos já aprovados a drogas em pesquisa exploratória.
2Fase 21
1Fase 11
·Pré-clínico2
Medicamentos catalogadosEnsaios clínicos· 0 medicamentos · 4 ensaios
Carregando informações de tratamento...

Onde tratar no SUS

Hospitais de referência no Brasil e o protocolo oficial do SUS (PCDT)

🇧🇷 Atendimento SUS — Síndrome Andersen-Tawil

🗺️

Selecione um estado ou use sua localização para ver resultados.

Dados de DATASUS/CNES, SBGM, ABNeuro e Ministério da Saúde. Sempre confirme a disponibilidade diretamente com o estabelecimento.

Pesquisa ativa

Ensaios clínicos abertos e novidades científicas recentes

Pesquisa e ensaios clínicos

4 ensaios clínicos encontrados, 1 ativos.

Distribuição por fase
Ver todos no ClinicalTrials.gov
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Publicações mais relevantes

Timeline de publicações
163 papers (10 anos)
#1

The importance of comprehensive diagnostic work-up and genetic testing to reveal Andersen-Tawil syndrome-a case report.

European heart journal. Case reports2026 Feb

Andersen-Tawil syndrome is characterized by a symptom triad of cardiac electrical abnormalities, periodic muscular paralysis, and distinct dysmorphic manifestations. A history of unexplained syncope has been associated with a more serious phenotype with increased risk of life-threatening arrhythmia. Due to the syndrome's rarity and highly variable clinical presentation, diagnosis remains challenging. This report highlights the importance of comprehensive diagnostic workup following a sudden cardiac arrest, particularly emphasizing the value of genetic testing. We present a 61-year-old male hypertensive patient who initially presented with a first-time syncopal episode. Initial investigations revealed ventricular ectopy exceeding 12 000 premature ventricular contractions, occasional QT prolongation of >500 ms, and mildly reduced left ventricular ejection fraction (50%). Outpatient diagnostic investigations did not yield a diagnosis. While awaiting ablation, the patient suffered from an out-of-hospital cardiac arrest and was successfully resuscitated after 17 min. Complete diagnostic work-up including guideline-adherent assessments and genetic testing eventually revealed Andersen-Tawil syndrome. The subsequent family evaluations supported the diagnosis. Diagnosis was unexpected as the patient presented with isolated cardiac manifestations and a late onset of symptoms. Cardiomyopathy and primary arrhythmic disorders were relevant differential diagnoses and investigated during admission. No clinical assessment is pathognomonic for Andersen-Tawil syndrome, making genetic testing essential for establishing a definitive diagnosis. While historically characterized as a long QT variant, research suggests Andersen-Tawil syndrome is its own disease entity. Pharmacological management follows established channelopathy principles, though the protective efficacy of beta-blockers and flecainide remains uncertain in this syndrome.

#2

Case Report of Andersen-Tawil Syndrome: Rare Presentation of a Rare Disease.

Annals of Indian Academy of Neurology2026 Jan 01

Andersen-Tawil syndrome (ATS) is a rare genetic disorder characterized by a triad of periodic paralysis, cardiac arrhythmias, and dysmorphic features, typically presenting in the first two decades of life. A 45-year-old man presented with acute lower motor neuron-type quadriparesis. He reported similar self-resolving episodes over the past 2 years, triggered by rest after exercise. There were no cardiac symptoms, dysmorphic features, or relevant family history. Biochemical evaluation revealed hypokalemia. Genetic testing confirmed a heterozygous nonsense mutation in the KCNJ2 gene (c.13C>T, p.Arg5Ter). Cardiac and dental evaluations were normal. He was treated with potassium supplementation and later acetazolamide, with no recurrence over 2 years. This case highlights a rare adult-onset presentation of ATS without cardiac or dysmorphic features and a negative family history, contributing to the limited adult ATS literature.

#3

Elective percutaneous stellate ganglion block for prediction of the clinical outcome of robotic bilateral cardiac sympathetic denervation in a patient with Andersen-Tawil syndrome: A case report.

European journal of anaesthesiology2026 Mar 20

Andersen-Tawil syndrome (ATS) is an ultra-rare channelopathy. We report the case of a 35-year-old woman with genetically confirmed ATS. She experienced sudden cardiac arrest. Her medical history was notable for multiple appropriate implantable cardioverter-defibrillator interventions due to ventricular fibrillation and ventricular tachycardia. Numerous premature ventricular contractions were revealed in 24-h Holter ECG monitoring. The arrhythmic episodes were consistently triggered by physical activity, despite multiple antiarrhythmic therapies and two endocardial ablations. A two-step strategy was planned, with the decision to proceed to bilateral cardiac sympathetic denervation (BCSD) based on the outcome of an initial percutaneous stellate ganglion block (PSGB). An elective left-sided percutaneous stellate ganglion block resulted in complete suppression of premature ventricular contractions and improved exercise tolerance. Guided by this response, the patient underwent robotic BCSD, leading to a spectacular reduction of premature beats, disappearance of symptomatic arrhythmias, and normalisation of exercise capacity. No recurrences were observed during the 5-month follow-up. This case is the first to describe elective PSGB as a predictive tool for the efficacy of BCSD in ATS. PSGB may facilitate patient selection for invasive autonomic modulation, offering a novel strategy for refractory inherited channelopathies.

#4

Identification of Kir2.1 Inhibitors from a High-Throughput Screen.

Assay and drug development technologies2026 Feb 17

The inward-rectifier potassium channel (Kir) 2.x family is an important family of ion channels in the context of human health. These potassium channels are involved in processes such as cardiac action potential, formation of skeletal muscle, bone development, vasodilation, and neuronal activity and are expressed centrally and peripherally. Given their importance, they are an attractive target for the development of tool compounds. The high homology between the members of the Kir family has made isoform selectivity challenging. In an effort to discover novel chemical matter related to this intriguing target, we performed a high-throughput screen utilizing compounds from the Vanderbilt Institute of Chemical Biology Discovery Collection. This screen of over 20,000 compounds resulted in 48 verified hits consisting of six novel chemical scaffolds. Of these hits, VU0523203 and VU0606851 were selected as promising starting points for initial medicinal chemistry optimization to improve potency and distribution, metabolism, and pharmacokinetic (DMPK) properties. These efforts resulted in the discovery of VU6073995, a compound with modest potency at Kir2.1 and improved DMPK properties compared with ML133.

#5

Perinatal Management of Andersen-Tawil Syndrome Using a Wearable Cardioverter-Defibrillator: A Case Report.

The journal of obstetrics and gynaecology research2026 Jan

Andersen-Tawil syndrome (ATS), also known as congenital long QT syndrome type 7 (LQT7), is a rare inherited channelopathy caused by KCNJ2 mutations and characterized by ventricular arrhythmias, periodic paralysis, and dysmorphic features. Pregnancy in women with ATS is extremely uncommon, and optimal perinatal management strategies are not well defined. We describe a 38-year-old primigravida with genetically confirmed ATS (p.R228X) who presented at 31 weeks of gestation without medication. During pregnancy, the burden of premature ventricular contractions and non-sustained ventricular tachycardia decreased compared with the pre-pregnancy period. At 36 weeks, atenolol and flecainide were introduced, and a wearable cardioverter-defibrillator (WCD) was applied, further reducing arrhythmias. A planned cesarean section at 37 weeks was uneventful, with favorable maternal and fetal outcomes. Postpartum, arrhythmias increased again, highlighting the importance of surveillance. This case demonstrates that combined pharmacological therapy and temporary WCD use may represent a safe and effective perinatal management strategy in high-risk pregnancies complicated by ATS.

Publicações recentes

Ver todas no PubMed

📚 EuropePMC183 artigos no totalmostrando 156

2026

Elective percutaneous stellate ganglion block for prediction of the clinical outcome of robotic bilateral cardiac sympathetic denervation in a patient with Andersen-Tawil syndrome: A case report.

European journal of anaesthesiology
2025

Phenotypic Variability in a Family with Andersen-Tawil Syndrome.

Arquivos brasileiros de cardiologia
2026

Andersen-Tawil syndrome with high-burden ventricular arrhythmias: a case report.

BMC cardiovascular disorders
2026

Identification of Kir2.1 Inhibitors from a High-Throughput Screen.

Assay and drug development technologies
2026

The importance of comprehensive diagnostic work-up and genetic testing to reveal Andersen-Tawil syndrome-a case report.

European heart journal. Case reports
2026

Case Report of Andersen-Tawil Syndrome: Rare Presentation of a Rare Disease.

Annals of Indian Academy of Neurology
2026

Gender-specific cardiac features in Andersen-Tawil syndrome: a comprehensive meta-analysis of case reports and series.

Journal of interventional cardiac electrophysiology : an international journal of arrhythmias and pacing
2026

Perinatal Management of Andersen-Tawil Syndrome Using a Wearable Cardioverter-Defibrillator: A Case Report.

The journal of obstetrics and gynaecology research
2025

Caenorhabditis elegans as an in vivo model system for human inherited primary arrhythmia syndromes.

The Journal of physiology
2026

Large-scale functional assessment of variants of the potassium channel Kir2.1: Clinical and comparative insights.

The Journal of biological chemistry
2025

Unlocking the Secrets of Andersen-Tawil Syndrome: The Role of Next-Generation Sequencing in a Family With Long QT Syndrome.

Cardiology research and practice
2025

When the U Wave Tells the Story: Andersen-Tawil Syndrome Unmasked.

Annals of noninvasive electrocardiology : the official journal of the International Society for Holter and Noninvasive Electrocardiology, Inc
2025

SUMOylation and an ATS1 variant converge to disrupt PIP2-dependent gating of Kir2.1.

The Journal of general physiology
2025

Muscle Channelopathies and Rhabdomyolysis.

Continuum (Minneapolis, Minn.)
2025

Nutritional Factors and Arrhythmic Risk in Long QT Syndrome: A Narrative Review of Mechanistic and Clinical Evidence.

Advances in nutrition (Bethesda, Md.)
2025

Broad Electrocardiogram Syndromes Spectrum: From Common Emergencies to Particular Electrical Heart Disorders-Part II.

Diagnostics (Basel, Switzerland)
2025

Extreme prolongation of QTU in a patient with Andersen-Tawil syndrome.

Kardiologia polska
2025

Flecainide for the Treatment of Andersen-Tawil Syndrome.

JACC. Clinical electrophysiology
2025

Atomic-level investigation of KCNJ2 mutations associated with ventricular arrhythmic syndrome phenotypes.

Scientific reports
2025

Potassium-sensitive loss of muscle force in the setting of reduced inward rectifier K+ current: Implications for Andersen-Tawil syndrome.

Proceedings of the National Academy of Sciences of the United States of America
2025

Mechanisms underlying the distinct K+ dependencies of periodic paralysis.

The Journal of general physiology
2024

Atypical Presentation of Andersen-Tawil Syndrome: Heart Failure with Reduced Ejection without Periodic Paralysis or Dysmorphic Features.

European journal of case reports in internal medicine
2024

Kir2.1 mutations differentially increase the risk of flecainide proarrhythmia in Andersen Tawil Syndrome.

medRxiv : the preprint server for health sciences
2024

A pediatric case of Andersen-Tawil syndrome with slowly progressive myopathy.

Pediatrics international : official journal of the Japan Pediatric Society
2024

Biochemical, biophysical, and structural investigations of two mutants (C154Y and R312H) of the human Kir2.1 channel involved in the Andersen-Tawil syndrome.

FASEB journal : official publication of the Federation of American Societies for Experimental Biology
2025

Development of new Kir2.1 channel openers from propafenone analogues.

British journal of pharmacology
2024

[Andersen-Tawil Syndrome, a differential of bidirectional ventricular tachycardia: a case report].

Archivos peruanos de cardiologia y cirugia cardiovascular
2024

Clinical, myopathological, and genetic features of two Chinese families with Andersen-Tawil syndrome.

Frontiers in neurology
2024

Rare electrocardiographic findings in a young woman with acute barium poisoning: A case report.

Heliyon
2024

A Late Diagnosis of Andersen-Tawil Syndrome in Teenage Siblings.

Pediatric neurology
2024

Pediatric neuromuscular channelopathies.

Handbook of clinical neurology
2024

Rare Presentation of Wide QRS Tachycardia in a Patient in Their 40s.

Annals of noninvasive electrocardiology : the official journal of the International Society for Holter and Noninvasive Electrocardiology, Inc
2024

Relevant obstetrics outcomes and gynecology-related clinical data on Andersen-Tawil syndrome.

Taiwanese journal of obstetrics &amp; gynecology
2024

Pediatric and Familial Genetic Arrhythmia Syndromes-Evaluation of Prolonged QTc-Differential Diagnosis and what You Need to Know.

Cardiac electrophysiology clinics
2024

Phenotypic Variability of Andersen-Tawil Syndrome Due to Allelic Mutation c.652C>T in the KCNJ2 Gene-A New Family Case Report.

Biomolecules
2024

Transcriptome and open chromatin analysis reveals the process of myocardial cell development and key pathogenic target proteins in Long QT syndrome type 7.

Journal of translational medicine
2024

Extracellular Kir2.1C122Y Mutant Upsets Kir2.1-PIP2 Bonds and Is Arrhythmogenic in Andersen-Tawil Syndrome.

Circulation research
2024

Kir2.1-NaV1.5 channelosome and its role in arrhythmias in inheritable cardiac diseases.

Heart rhythm
2024

Andersen-Tawil syndrome: A long QT syndrome with variable expression.

Medicina clinica
2023

Bidirectional Ventricular Tachycardia and Prominent U Waves: Look at Fingers and Muscles and Use Flecainide.

The journal of pediatric pharmacology and therapeutics : JPPT : the official journal of PPAG
2023

Muscle MRI in periodic paralysis shows myopathy is common and correlates with intramuscular fat accumulation.

Muscle &amp; nerve
2023

A case report of Andersen-Tawil syndrome misdiagnosed with myodystrophy.

Frontiers in neurology
2023

Extracellular cysteine disulfide bond break at Cys122 disrupts PIP2-dependent Kir2.1 channel function and leads to arrhythmias in Andersen-Tawil Syndrome.

bioRxiv : the preprint server for biology
2023

Chronic Propafenone Application Increases Functional KIR2.1 Expression In Vitro.

Pharmaceuticals (Basel, Switzerland)
2023

Successful cardiac sympathetic denervation for Andersen-Tawil syndrome.

Europace : European pacing, arrhythmias, and cardiac electrophysiology : journal of the working groups on cardiac pacing, arrhythmias, and cardiac cellular electrophysiology of the European Society of Cardiology
2023

General anesthesia using propofol infusion for implantation of an implantable cardioverter defibrillator in a pediatric patient with Andersen-Tawil syndrome: a case report.

Journal of dental anesthesia and pain medicine
2023

Prevalence of genetically confirmed skeletal muscle channelopathies in the era of next generation sequencing.

Neuromuscular disorders : NMD
2022

Case report: SCN4A p.R1135H gene variant in combination with thyrotoxicosis causing hypokalemic periodic paralysis.

Frontiers in neurology
2023

Ventricular bigeminy characterization in 24-h Holter monitoring from Andersen-Tawil patients: An initial proof of concept versus patients with ischemic heart disease.

Journal of electrocardiology
2022

Kir2.1 dysfunction at the sarcolemma and the sarcoplasmic reticulum causes arrhythmias in a mouse model of Andersen-Tawil syndrome type 1.

Nature cardiovascular research
2022

[A case report of Andersen-Tawil Syndrome with ventricular tachycardia and syncope].

Zhonghua xin xue guan bing za zhi
2022

Case report: Mexiletine suppresses ventricular arrhythmias in Andersen-Tawil syndrome.

Frontiers in cardiovascular medicine
2023

Molecular stratification of arrhythmogenic mechanisms in the Andersen Tawil syndrome.

Cardiovascular research
2022

A dangerous food binge: a case report of hypokalemic periodic paralysis and review of current literature.

Italian journal of pediatrics
2022

Bidirectional Ventricular Tachycardia: Challenges and Solutions.

Vascular health and risk management
2023

Congenital Long QT Syndrome: A Review of Genetic and Pathophysiologic Etiologies, Phenotypic Subtypes, and Clinical Management.

Cardiology in review
2022

Phenotypical variability and atypical presentations in a French cohort of Andersen-Tawil syndrome.

European journal of neurology
2022

Variable Clinical Appearance of the Kir2.1 Rare Variants in Russian Patients with Long QT Syndrome.

Genes
2022

Efficacy of flecainide in bidirectional ventricular tachycardia and tachycardia-induced cardiomyopathy with Andersen-Tawil syndrome.

European journal of medical genetics
2022

A peculiar case of palpitations and syncope.

Heart rhythm
2021

Inwardly Rectifying Potassium Channel Kir2.1 and its "Kir-ious" Regulation by Protein Trafficking and Roles in Development and Disease.

Frontiers in cell and developmental biology
2021

Andersen-Tawil Syndrome With Novel Mutation in KCNJ2: Case Report.

Frontiers in pediatrics
2022

Andersen-Tawil syndrome: deep phenotyping reveals significant cardiac and neuromuscular morbidity.

Brain : a journal of neurology
2021

Characterization of Loss-Of-Function KCNJ2 Mutations in Atypical Andersen Tawil Syndrome.

Frontiers in genetics
2022

Andersen-Tawil syndrome: Overlapping clinical features with Noonan syndrome?

European journal of medical genetics
2021

Mind the Gap: Acetazolamide Prolonged Periods without Paralysis in a Girl with Andersen-Tawil Syndrome.

Case reports in neurology
2023

Catheter ablation of frequent monomorphic ventricular arrhythmias in Andersen-Tawil syndrome: case report and focused literature review.

Journal of interventional cardiac electrophysiology : an international journal of arrhythmias and pacing
2021

[17-year-old patient with polymorphic premature ventricular contractions].

Herzschrittmachertherapie &amp; Elektrophysiologie
2021

Failure of radiofrequency catheter ablation and success of flecainide to suppress premature ventricular contractions in Andersen-Tawil syndrome: A case report.

Journal of electrocardiology
2021

A Visual Resolution of Cardiotoxicity: A Case Report of Digoxin-Induced Bidirectional Ventricular Tachycardia.

Cureus
2021

Marked reduction in paralytic attacks in a patient with Andersen-Tawil syndrome switched from acetazolamide to dichlorphenamide.

Neuromuscular disorders : NMD
2021

The Role of Nutrition and Physical Activity as Trigger Factors of Paralytic Attacks in Primary Periodic Paralysis.

Journal of neuromuscular diseases
2021

Neurologic complications of genetic channelopathies.

Handbook of clinical neurology
2023

Bidirectional Ventricular Tachycardia in a Young Female: A Case of Andersen-Tawil Syndrome.

Military medicine
2021

Distinctive facial features in Andersen-Tawil syndrome: A three-dimensional stereophotogrammetric analysis.

American journal of medical genetics. Part A
2021

The clinical and genetic heterogeneity analysis of five families with primary periodic paralysis.

Channels (Austin, Tex.)
2021

Obstetric management of a patient with Andersen-Tawil syndrome: A case report.

The journal of obstetrics and gynaecology research
2021

Familial periodic paralysis associated with a rare KCNJ5 variant that supposed to have incomplete penetrance.

Brain &amp; development
2021

Andersen-Tawil syndrome presenting as premenstrual periodic paralysis.

Muscle &amp; nerve
2021

Andersen-Tawil Syndrome Presenting with Complete Heart Block.

Journal of neuromuscular diseases
2020

Andersen-Tawil Syndrome with High Risk of Sudden Cardiac Death in Four Mexican Patients. Cardiac and Extra-Cardiac Phenotypes.

Revista de investigacion clinica; organo del Hospital de Enfermedades de la Nutricion
2020

Andersen-Tawil syndrome associated with myopathy.

World journal of emergency medicine
2021

Successful treatment of arrhythmia with β-blocker and flecainide combination in pregnant patients with Andersen-Tawil syndrome: A case report and literature review.

Annals of noninvasive electrocardiology : the official journal of the International Society for Holter and Noninvasive Electrocardiology, Inc
2021

Andersen-Tawil Syndrome: A Comprehensive Review.

Cardiology in review
2020

Treatment Updates for Neuromuscular Channelopathies.

Current treatment options in neurology
2020

Compound heterozygous mutations in KCNJ2 and KCNH2 in a patient with severe Andersen-Tawil syndrome.

BMJ case reports
2021

Impaired cytoplasmic domain interactions cause co-assembly defect and loss of function in the p.Glu293Lys KNCJ2 variant isolated from an Andersen-Tawil syndrome patient.

Cardiovascular research
2020

An unusual case of recurrent episodes of muscle weakness: Co-occurrence of Andersen-Tawil syndrome and glycogen storage disease type IXd.

Neuromuscular disorders : NMD
2020

Managing pregnancy and anaesthetics in patients with skeletal muscle channelopathies.

Neuromuscular disorders : NMD
2020

Every face tells a story-unravelling a case of bidirectional ventricular tachycardia.

Indian pacing and electrophysiology journal
2020

"Electrifying dysmorphology": Potassium channelopathies causing dysmorphic syndromes.

Advances in genetics
2020

Kir2.1 Interactome Mapping Uncovers PKP4 as a Modulator of the Kir2.1-Regulated Inward Rectifier Potassium Currents.

Molecular &amp; cellular proteomics : MCP
2020

Andersen-Tawil Syndrome Is Associated With Impaired PIP2 Regulation of the Potassium Channel Kir2.1.

Frontiers in pharmacology
2020

Thyrotoxic Periodic Paralysis With Features of Andersen-Tawil Syndrome: A Case Report and Literature Review.

Cureus
2020

Time to Redefine the Natural History and Clinical Management of Type 1 Andersen-Tawil Syndrome?

Journal of the American College of Cardiology
2020

Natural History and Risk Stratification in Andersen-Tawil Syndrome Type 1.

Journal of the American College of Cardiology
2020

Mitochondrial DNA polymorphisms in Andersen-Tawil syndrome.

Kardiologia polska
2020

Periodic Paralysis Syndromes: A T3 Thyrotoxicosis Case and Review of Literature.

HCA healthcare journal of medicine
2020

Andersen-Tawil syndrome with sex-specific phenotype: Usefulness of the long exercise test.

Neurologia
2019

Phenotypic variability in a series of four pediatric patients with Andersen-Tawil syndrome: A Saudi experience.

International journal of pediatrics &amp; adolescent medicine
2020

Child Neurology: Andersen-Tawil syndrome.

Neurology
2019

Episodic Muscle Disorders.

Continuum (Minneapolis, Minn.)
2020

Multivariate analysis of TU wave complex on electrocardiogram in Andersen-Tawil syndrome with KCNJ2 mutations.

Annals of noninvasive electrocardiology : the official journal of the International Society for Holter and Noninvasive Electrocardiology, Inc
2020

Therapeutic management of ventricular arrhythmias in Andersen-Tawil syndrome.

Journal of electrocardiology
2019

Functional analysis of a double-point mutation in the KCNJ2 gene identified in a family with Andersen-Tawil syndrome.

Journal of the neurological sciences
2019

Clinical and neurophysiological variability in Andersen-Tawil syndrome.

Muscle &amp; nerve
2019

Andersen-Tawil Syndrome and Hypothyroidism: A Case Report with an Unusual Association.

International journal of applied &amp; basic medical research
2019

Identification of a PEST Sequence in Vertebrate KIR2.1 That Modifies Rectification.

Frontiers in physiology
2019

Usefulness of the intravenous flecainide challenge test before oral flecainide treatment in a patient with Andersen-Tawil syndrome.

BMJ case reports
2019

Delayed diagnosed atypical case of Andersen-Tawil syndrome.

Neurology international
2019

Bioinformatics characterisation of the (mutated) proteins related to Andersen-Tawil syndrome.

Mathematical biosciences and engineering : MBE
2018

Asymptomatic ventricular tachycardia: diagnostic pitfalls of Andersen-Tawil syndrome-a case report.

European heart journal. Case reports
2019

Role of the Purkinje system in heritable arrhythmias.

Heart rhythm
2019

A study supporting possible expression of inward-rectifying potassium channel 2.1 channels in peripheral nerve in a patient with Andersen-Tawil syndrome.

Muscle &amp; nerve
2019

Coincidence of Andersen-Tawil syndrome and Marfan syndrome: A case report.

Annals of noninvasive electrocardiology : the official journal of the International Society for Holter and Noninvasive Electrocardiology, Inc
2018

Variable penetrance of Andersen-Tawil syndrome in a family with a rare missense KCNJ2 mutation.

Neurology. Genetics
2019

Short-term response to phenytoin sodium in Andersen-Tawil syndrome-1 with a cardiac-dominant phenotype.

Pacing and clinical electrophysiology : PACE
2018

Can flecainide totally eliminate bidirectional ventricular tachycardia in pediatric patients with Andersen-Tawil syndrome?

Turk Kardiyoloji Dernegi arsivi : Turk Kardiyoloji Derneginin yayin organidir
2018

[Analysis of clinical phenotypes and KCNJ2 gene mutations in a Chinese pedigree affected with Andersen-Tawil syndrome].

Zhonghua yi xue yi chuan xue za zhi = Zhonghua yixue yichuanxue zazhi = Chinese journal of medical genetics
2018

A Novel KCNJ2 Mutation Identified in an Autistic Proband Affects the Single Channel Properties of Kir2.1.

Frontiers in cellular neuroscience
2018

Prevalence and mutation spectrum of skeletal muscle channelopathies in the Netherlands.

Neuromuscular disorders : NMD
2018

Kir2.1 is important for efficient BMP signaling in mammalian face development.

Developmental biology
2018

Accelerated idioventricular rhythm degenerating into bidirectional ventricular tachycardia following acute myocardial infarction.

The American journal of emergency medicine
2018

Propafenone is not effective for severe ventricular arrhythmias in Andersen-Tawil syndrome.

Archives of medical science : AMS
2018

Neurophysiologic characterization of periodic paralysis episode in a patient with Andersen-Tawil syndrome.

Clinical neurophysiology : official journal of the International Federation of Clinical Neurophysiology
2018

Different responses to exercise between Andersen-Tawil syndrome and catecholaminergic polymorphic ventricular tachycardia.

Europace : European pacing, arrhythmias, and cardiac electrophysiology : journal of the working groups on cardiac pacing, arrhythmias, and cardiac cellular electrophysiology of the European Society of Cardiology
2018

Review of the Diagnosis and Treatment of Periodic Paralysis.

Muscle &amp; nerve
2017

Sanger sequencing as a first-line approach for molecular diagnosis of Andersen-Tawil syndrome.

F1000Research
2017

Clinical heterogeneity in Andersen-Tawil syndrome.

Neuromuscular disorders : NMD
2017

Characterization of a novel KCNJ2 sequence variant detected in Andersen-Tawil syndrome patients.

BMC medical genetics
2017

Flecainide ameliorates arrhythmogenicity through NCX flux in Andersen-Tawil syndrome-iPS cell-derived cardiomyocytes.

Biochemistry and biophysics reports
2017

Flecainide treats a novel KCNJ2 mutation associated with Andersen-Tawil syndrome.

HeartRhythm case reports
2017

Andersen-Tawil syndrome: Clinical presentation and predictors of symptomatic arrhythmias - Possible role of polymorphisms K897T in KCNH2 and H558R in SCN5A gene.

Journal of cardiology
2017

Spectrum of Nondystrophic Skeletal Muscle Channelopathies in Children.

Pediatric neurology
2017

Andersen-Tawil Syndrome with Early Onset Myopathy: 2 Cases.

Journal of neuromuscular diseases
2017

Intrafamilial phenotypic variability in Andersen-Tawil syndrome: A diagnostic challenge in a potentially treatable condition.

Neuromuscular disorders : NMD
2016

Reversible Dilated Cardiomyopathy Caused by a High Burden of Ventricular Arrhythmias in Andersen-Tawil Syndrome.

The Canadian journal of cardiology
2016

Concomitant presentation of Anderson-Tawil syndrome and myasthenia gravis in an adult patient: A case report.

Experimental and therapeutic medicine
2016

Clinical features and long exercise test in Chinese patients with Andersen-Tawil syndrome.

Muscle &amp; nerve
2016

7-T (35)Cl and (23)Na MR Imaging for Detection of Mutation-dependent Alterations in Muscular Edema and Fat Fraction with Sodium and Chloride Concentrations in Muscular Periodic Paralyses.

Radiology
2015

Recurrent syncope in the Andersen Tawil syndrome - Cardiac or neurological?

Indian pacing and electrophysiology journal
2016

Identification of the KCNJ2 Mutation in a Korean Family with Andersen-Tawil Syndrome and Developmental Delay.

Annals of clinical and laboratory science
2016

Bioelectric signalling via potassium channels: a mechanism for craniofacial dysmorphogenesis in KCNJ2-associated Andersen-Tawil Syndrome.

The Journal of physiology
2016

Andersen-Tawil syndrome. A diagnostic challenge.

International journal of cardiology
2016

An 88-year-old man with syncope and an alternating axis.

Heart (British Cardiac Society)
2015

Andersen-Tawil syndrome: A review of literature.

Neurology India
2015

[Molecular genetic diagnostics of the cause of ventricular arrhythmias in children].

Ugeskrift for laeger
2015

Rarity and phenotypic heterogeneity provide challenges in the diagnosis of Andersen-Tawil syndrome: Two cases presenting with ECGs mimicking catecholaminergic polymorphic ventricular tachycardia (CPVT).

International journal of cardiology
2015

Atrial pacing for the management of ventricular arrhythmias in Andersen-Tawil syndrome.

HeartRhythm case reports
2016

Coexistence of Andersen-Tawil Syndrome with Polymorphisms in hERG1 Gene (K897T) and SCN5A Gene (H558R) in One Family.

Annals of noninvasive electrocardiology : the official journal of the International Society for Holter and Noninvasive Electrocardiology, Inc
2015

Identification and functional characterisation of a novel KCNJ2 mutation, Val302del, causing Andersen-Tawil syndrome.

Canadian journal of physiology and pharmacology
2015

Pharmacotherapy for inherited arrhythmia syndromes: mechanistic basis, clinical trial evidence and practical application.

Expert review of cardiovascular therapy
2015

Case report: A Chinese child with Andersen-Tawil syndrome due to a de novo KCNJ2 mutation.

Journal of the neurological sciences
2015

Imipramine for incessant ventricular arrhythmias in 2 unrelated patients with Andersen-Tawil syndrome.

Heart rhythm
2015

Ion channelopathies in human induced pluripotent stem cell derived cardiomyocytes: a dynamic clamp study with virtual IK1.

Frontiers in physiology
2015

Vanishing Weakness and Persistent Cardiac Dysrhythmia: Are We Dealing with Andersen Tawil Syndrome?

Indian journal of pediatrics
Ver todos os 183 no EuropePMC

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Doenças relacionadas

Doenças com sintomas parecidos — ajudam quem ainda está buscando diagnóstico

Referências e fontes

Bases de dados externas citadas neste artigo

Publicações científicas

Artigos indexados no PubMed ligados a esta doença no grafo RarasNet — título, periódico e PMID direto da fonte, sem intermediação de IA.

  1. The importance of comprehensive diagnostic work-up and genetic testing to reveal Andersen-Tawil syndrome-a case report.
    European heart journal. Case reports· 2026· PMID 41696039mais citado
  2. Case Report of Andersen-Tawil Syndrome: Rare Presentation of a Rare Disease.
    Annals of Indian Academy of Neurology· 2026· PMID 41643185mais citado
  3. Elective percutaneous stellate ganglion block for prediction of the clinical outcome of robotic bilateral cardiac sympathetic denervation in a patient with Andersen-Tawil syndrome: A case report.
    European journal of anaesthesiology· 2026· PMID 41858297mais citado
  4. Identification of Kir2.1 Inhibitors from a High-Throughput Screen.
    Assay and drug development technologies· 2026· PMID 41701551mais citado
  5. Perinatal Management of Andersen-Tawil Syndrome Using a Wearable Cardioverter-Defibrillator: A Case Report.
    The journal of obstetrics and gynaecology research· 2026· PMID 41482511mais citado
  6. Lifestyle and dietary measures in Periodic Paralyses.
    Acta Myol· 2026· PMID 41954145recente
  7. Phenotypic Variability in a Family with Andersen-Tawil Syndrome.
    Arq Bras Cardiol· 2025· PMID 41779514recente
  8. Andersen-Tawil syndrome with high-burden ventricular arrhythmias: a case report.
    BMC Cardiovasc Disord· 2026· PMID 41742041recente

Bases de dados e fontes oficiais

Identificadores e referências canônicas usadas para montar este verbete.

  1. ORPHA:37553(Orphanet)
  2. OMIM OMIM:170390(OMIM)
  3. MONDO:0008222(MONDO)
  4. GARD:9453(GARD (NIH))
  5. Variantes catalogadas(ClinVar)
  6. Busca completa no PubMed(PubMed)
  7. Q773118(Wikidata)

Dados compilados pelo RarasNet a partir de fontes abertas (Orphanet, OMIM, MONDO, PubMed/EuropePMC, ClinicalTrials.gov, DATASUS, PCDT/MS). Este conteúdo é informativo e não substitui avaliação médica.

Conteúdo mantido por Agente Raras · Médicos e pesquisadores podem colaborar

Síndrome Andersen-Tawil
Compêndio · Raras BR

Síndrome Andersen-Tawil

ORPHA:37553 · MONDO:0008222
Prevalência
Unknown
Herança
Autosomal dominant
CID-10
G72.3 · Paralisia periódica
CID-11
Ensaios
1 ativos
Início
Childhood
Prevalência
0.0 (Worldwide)
MedGen
UMLS
C1563715
EuropePMC
Wikidata
Papers 10a
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