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Síndrome Proteus
ORPHA:744CID-10 · Q87.3CID-11 · LD2COMIM 176920DOENÇA RARA

A síndrome de Proteus (PS) é um distúrbio de crescimento hamartomatoso muito raro e complexo, caracterizado por crescimento excessivo progressivo do esqueleto, da pele, do sistema adiposo e do sistema nervoso central.

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Introdução

O que você precisa saber de cara

📋

A síndrome de Proteus (PS) é um distúrbio de crescimento hamartomatoso muito raro e complexo, caracterizado por crescimento excessivo progressivo do esqueleto, da pele, do sistema adiposo e do sistema nervoso central.

Pesquisas ativas
3 ensaios
7 total registrados no ClinicalTrials.gov
Publicações científicas
618 artigos
Último publicado: 2026 Jun
Medicamentos
1 registrados
MIRANSERTIB

Tem tratamento?

1 medicamento registrado
Ver detalhes, fases e interações →
MIRANSERTIB

Escala de raridade

CLASSIFICAÇÃO ORPHANET · BRASIL 2024
<1 / 1 000 000
Ultra-rara
<1/50k
Muito rara
1/20k
Rara
1/10k
Pouco freq.
1/5k
Incomum
1/2k
Prevalência
0.0
Europe
Início
Infancy
🏥
SUS: Cobertura mínimaScore: 15%
CID-10: Q87.3
🇧🇷Dados SUS / DATASUS
PROCEDIMENTOS SIGTAP (5)
0202010503
Cariótipo — bandas G, Q ou Rgenetic_test
0202010600
Pesquisa de microdeleções/microduplicações por FISHlab_test
0202010694
Sequenciamento completo do exoma (WES)rehabilitation
0202010260
Dosagem de alfa-fetoproteína
0301070040
Atendimento em reabilitação — doenças raras
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Entender a doença

Do básico ao detalhe, leia no seu ritmo

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Sinais e sintomas

O que aparece no corpo e com que frequência cada sintoma acontece

Partes do corpo afetadas

🦴
Ossos e articulações
18 sintomas
🧬
Pele e cabelo
15 sintomas
😀
Face
10 sintomas
👁️
Olhos
10 sintomas
🫁
Pulmão
6 sintomas
🧠
Neurológico
5 sintomas

+ 45 sintomas em outras categorias

Características mais comuns

100%prev.
Nevo conectivo cerebriforme
Frequente (79-30%)
90%prev.
Supercrescimento
Muito frequente (99-80%)
90%prev.
Nevo epidérmico
Muito frequente (99-80%)
90%prev.
Assimetria do tórax
Muito frequente (99-80%)
90%prev.
Escoliose
Muito frequente (99-80%)
90%prev.
Hemangioma capilar
Muito frequente (99-80%)
136sintomas
Muito frequente (28)
Frequente (24)
Ocasional (63)
Sem dados (21)

Os sintomas variam de pessoa para pessoa. Abaixo estão as 136 características clínicas mais associadas, ordenadas por frequência.

Nevo conectivo cerebriformeCerebriform connective tissue nevus
Frequente (79-30%)100%
SupercrescimentoOvergrowth
Muito frequente (99-80%)90%
Nevo epidérmicoEpidermal nevus
Muito frequente (99-80%)90%
Assimetria do tóraxAsymmetry of the thorax
Muito frequente (99-80%)90%
EscolioseScoliosis
Muito frequente (99-80%)90%

Linha do tempo da pesquisa

Publicações por ano — veja quando o interesse científico cresceu
Anos de pesquisa1desde 2025
Total histórico618PubMed
Últimos 10 anos200publicações
Pico202225 papers
Linha do tempo
2025Hoje · 2026🧪 1994Primeiro ensaio clínico📈 2022Ano de pico
Publicações por ano (últimos 10 anos)

Encontrou um erro ou informação desatualizada? Sugira uma correção →

Genética e causas

O que está alterado no DNA e como passa nas famílias

Genes associados

1 gene identificado com associação a esta condição. Padrão de herança: Not applicable.

AKT1RAC-alpha serine/threonine-protein kinaseDisease-causing somatic mutation(s) inAltamente restrito
FUNÇÃO

AKT1 is one of 3 closely related serine/threonine-protein kinases (AKT1, AKT2 and AKT3) called the AKT kinase, and which regulate many processes including metabolism, proliferation, cell survival, growth and angiogenesis (PubMed:11882383, PubMed:15526160, PubMed:15861136, PubMed:21432781, PubMed:21620960, PubMed:31204173). This is mediated through serine and/or threonine phosphorylation of a range of downstream substrates (PubMed:11882383, PubMed:15526160, PubMed:21432781, PubMed:21620960, PubMe

LOCALIZAÇÃO

CytoplasmNucleusCell membraneMitochondrion intermembrane space

VIAS BIOLÓGICAS (7)
CD28 dependent PI3K/Akt signalingVEGFR2 mediated vascular permeabilityPIP3 activates AKT signalingNegative regulation of the PI3K/AKT networkG beta:gamma signalling through PI3Kgamma
MECANISMO DE DOENÇA

Breast cancer

A common malignancy originating from breast epithelial tissue. Breast neoplasms can be distinguished by their histologic pattern. Invasive ductal carcinoma is by far the most common type. Breast cancer is etiologically and genetically heterogeneous. Important genetic factors have been indicated by familial occurrence and bilateral involvement. Mutations at more than one locus can be involved in different families or even in the same case.

OUTRAS DOENÇAS (7)
ovarian cancerProteus syndromehereditary breast carcinomacolorectal cancer
HGNC:391UniProt:P31749

Medicamentos e terapias

MIRANSERTIBPhase 2

Mecanismo: Serine/threonine-protein kinase AKT inhibitor

Ver mais no OpenTargets

Variantes genéticas (ClinVar)

93 variantes patogênicas registradas no ClinVar.

🧬 AKT1: GRCh37/hg19 14q32.2-32.33(chr14:97521552-107285437)x3 ()
🧬 AKT1: GRCh37/hg19 14q32.2-32.33(chr14:101180490-106329074)x1 ()
🧬 AKT1: NM_001382430.1(AKT1):c.16A>C (p.Ile6Leu) ()
🧬 AKT1: NM_001382430.1(AKT1):c.286_287del (p.Arg96fs) ()
🧬 AKT1: NM_001382430.1(AKT1):c.237G>C (p.Gln79His) ()
Ver todas no ClinVar

Classificação de variantes (ClinVar)

Distribuição de 18 variantes classificadas pelo ClinVar.

4
13
1
Patogênica (22.2%)
VUS (72.2%)
Benigna (5.6%)
VARIANTES MAIS SIGNIFICATIVAS
AKT1: NM_001382430.1(AKT1):c.968A>G (p.Asp323Gly) [Conflicting classifications of pathogenicity]
AKT1: NM_001382430.1(AKT1):c.49_50delinsAG (p.Glu17Arg) [Pathogenic]
AKT1: NM_001382430.1(AKT1):c.1394G>A (p.Arg465His) [Conflicting classifications of pathogenicity]
AKT1: NM_001382430.1(AKT1):c.49G>A (p.Glu17Lys) [Pathogenic]
AKT1: NM_001382430.1(AKT1):c.1418_1420del (p.Ser473del) [Uncertain significance]

Diagnóstico

Os sinais que médicos procuram e os exames que confirmam

Carregando...

Tratamento e manejo

Remédios, cuidados de apoio e o que precisa acompanhar

Pipeline de tratamentos
Pipeline regulatório — de medicamentos já aprovados a drogas em pesquisa exploratória.
2Fase 24
1Fase 11
·Pré-clínico3
Medicamentos catalogadosEnsaios clínicos· 1 medicamento · 7 ensaios
Carregando informações de tratamento...

Onde tratar no SUS

Hospitais de referência no Brasil e o protocolo oficial do SUS (PCDT)

🇧🇷 Atendimento SUS — Síndrome Proteus

🗺️

Selecione um estado ou use sua localização para ver resultados.

Dados de DATASUS/CNES, SBGM, ABNeuro e Ministério da Saúde. Sempre confirme a disponibilidade diretamente com o estabelecimento.

Pesquisa ativa

Ensaios clínicos abertos e novidades científicas recentes

🟢 Recrutando agora

2 pesquisas recrutando participantes. Converse com seu médico sobre a possibilidade de participar.

Outros ensaios clínicos

7 ensaios clínicos encontrados, 3 ativos.

Distribuição por fase
Ver todos no ClinicalTrials.gov
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Publicações mais relevantes

Timeline de publicações
195 papers (10 anos)
#1

3D CT cinematic rendering of microcardia and multiple thoracoabdominal venous dilation in Proteus syndrome.

European heart journal. Cardiovascular Imaging2026 Feb 27

The PTEN hamartoma tumor syndrome (PHTS) includes Cowden syndrome (CS), Bannayan-Riley-Ruvalcaba syndrome (BRRS), PTEN-related Proteus syndrome (PS), and PTEN-related Proteus-like syndrome. CS is a multiple hamartoma syndrome with a high risk for benign and malignant tumors of the thyroid, breast, kidney, and endometrium. Affected individuals usually have macrocephaly, trichilemmomas, and papillomatous papules, and present by the late 20s. The lifetime risk of developing breast cancer is 85%, with an average age of diagnosis between 38 and 46 years. The lifetime risk for thyroid cancer (usually follicular, rarely papillary, but never medullary thyroid cancer) is approximately 35%. The lifetime risk for renal cell cancer (predominantly of papillary histology) is 34%. The risk for endometrial cancer may approach 28%. BRRS is a congenital disorder characterized by macrocephaly, intestinal hamartomatous polyposis, lipomas, and pigmented macules of the glans penis. PS is a complex, highly variable disorder involving congenital malformations and hamartomatous overgrowth of multiple tissues, as well as connective tissue nevi, epidermal nevi, and hyperostoses. Proteus-like syndrome is undefined but refers to individuals with significant clinical features of PS who do not meet the diagnostic criteria for PS. The diagnosis of PHTS is established in a proband by identification of a heterozygous germline PTEN pathogenic variant on molecular genetic testing. Treatment of manifestations: Treatment for the benign and malignant manifestations of PHTS is the same as for their sporadic counterparts. Topical agents (e.g., 5-fluorouracil), curettage, cryosurgery, or laser ablation may alleviate the mucocutaneous manifestations of CS but are rarely utilized; cutaneous lesions should be excised only if malignancy is suspected or symptoms (e.g., pain, deformity, increased scarring) are significant. Surveillance: To detect tumors at the earliest, most treatable stages: Children (age <18 years). Yearly thyroid ultrasound from the time of diagnosis (earliest reported at age 7 years) and skin check with physical examination. Adults. Yearly thyroid ultrasound and dermatologic evaluation. Women beginning at age 30 years. Monthly breast self-examination; annual breast screening (at minimum mammogram; MRI may also be incorporated). Starting by age 35 years, consider transvaginal ultrasound or endometrial biopsy. Men and women. Colonoscopy beginning at age 35 years with frequency dependent on degree of polyposis identified or family history of early-onset colon cancer (before age 40); biennial (every 2 years) renal imaging (CT or MRI preferred) beginning at age 40 years. Those with a family history of a particular cancer type at an early age. Consider initiating screening 5 to 10 years prior to the youngest age of diagnosis in the family. Evaluation of relatives at risk: When a PTEN pathogenic variant has been identified in a proband, molecular genetic testing of asymptomatic at-risk relatives can identify those who have the family-specific pathogenic variant and warrant ongoing surveillance. PHTS is inherited in an autosomal dominant manner. Because CS is likely underdiagnosed, the actual proportion of simplex cases (defined as individuals with no obvious family history) and familial cases (defined as ≥2 related affected individuals) cannot be determined. The majority of CS cases are simplex. Perhaps 10%-50% of individuals with CS have an affected parent. Each child of an affected individual has a 50% chance of inheriting the pathogenic variant and developing PHTS. Once a PTEN pathogenic variant has been identified in an affected family member, prenatal testing for a pregnancy at increased risk is possible.

#2

Pulmonary Involvement in Proteus Syndrome: Clinical and Imaging Correlates in a Rare Case.

Case reports in radiology2026

Proteus syndrome is an uncommon, sporadic disorder characterized by progressive and heterogeneous overgrowth of tissues, resulting in distorted and asymmetric development. In most individuals, Proteus syndrome has minimal to no manifestations at birth but progresses during childhood and adolescence. Clinical manifestations of the disease include isolated asymmetric hemihyperplasia, isolated asymmetric macrodactyly, subcutaneous masses, plantar and palmar cerebriform fibrous overgrowth, exostoses, epidermal nevi, and scoliosis. Cardiothoracic structures are less commonly involved, and the manifestations include cystic lung changes, pulmonary thromboembolism and varicosities, and pulmonary nodules. Patients with Proteus syndrome have an increased risk of early death due to deep venous thrombosis and pulmonary embolism. We report a case of an adult female who was diagnosed with Proteus syndrome at the age of 5 years who had multiple pulmonary manifestations of the disease.

#3

Characterizing Paratesticular Neoplasms in Proteus Syndrome.

The American journal of surgical pathology2026 Mar 01

Proteus syndrome is a rare mosaic overgrowth disorder caused by somatic activating variants in AKT1 , most commonly the c.49G>A p.(Glu17Lys) variant. It predisposes individuals to asymmetric tissue proliferation and an elevated risk for both benign and malignant neoplasms. Among 64 males with genetically confirmed Proteus syndrome enrolled in a longitudinal natural history study, 12 (19%) underwent surgery for paratesticular masses. The average age at surgery was 9 years, most tumors were unilateral, small (median 1.6 cm), and slow growing, but 50% showed recurrence or metachronous tumor development, occasionally with progression to more atypical histology. Histologically, these tumors demonstrated a broad spectrum of differentiation. Eight reviewed cases included Müllerian-type papillary cystadenomas and low-grade papillary adenocarcinomas, a Brenner tumor, and one case of a papillary adenocarcinoma with spindle cell transformation. The epithelial components were typically arranged in papillary and glandular architectures, with variable degrees of cytologic atypia. Psammomatous calcifications were common. Immunohistochemistry showed consistent expression of PAX8(7/7), WT1(7/7), estrogen receptor (ER)(7/7), and progesterone receptor (PR)(6/7), supporting Müllerian lineage, while negative staining for germ cell and mesothelial markers excluded common paratesticular differential diagnoses. Four of the 7 tumors were positive for SF-1. All 7/7 sequenced tumors harbored the AKT1 c.49G>A variant with no additional oncogenic alterations identified by exome sequencing. This series is the largest series to date documenting the clinicopathologic features of paratesticular tumors, a poorly understood component of the Proteus syndrome phenotype.

#4

A Case Report of a Mild and Atypical Presentation of Proteus Syndrome.

Pediatric dermatology2026

Proteus syndrome (PS) is a rare genetic disorder caused by mosaic AKT1 mutations, leading to progressive and asymmetric overgrowth. We report a mildly symptomatic 12-year-old male with left lower limb overgrowth and an epidermal nevus, whose diagnosis was confirmed through molecular diagnostics. Targeted NGS identified the pathogenic AKT1 c.49G>A mutation in affected tissues, supporting the diagnosis despite the absence of hallmark features like cerebriform connective tissue nevus. This case highlights the importance of genetic testing in subtle presentations of PS, enabling early diagnosis, monitoring, and intervention to mitigate potential complications.

#5

A Case of Proteus Syndrome, Suspected as Maffucci Syndrome in a Chinese Child.

Case reports in pediatrics2025

Proteus syndrome (PS) is an exceptionally rare disorder characterized by asymmetric and disproportionate overgrowth of connective tissues. We report the case of an 8-year-old female presenting with irregular cranial protrusion, bilateral supraorbital ridge enlargement, overgrowth of the right hand and left foot, and a pelvic MRI revealing an ovarian tumor. Initially, the patient was suspected of having Maffucci syndrome (MS) upon admission. Genetic analysis of a lesion sample from the fifth toe of the left foot identified a heterozygous point mutation, 49G > A (p.Glu17Lys), in the AKT1 gene. The patient met the clinical-molecular diagnostic criteria established by Leslie G. Biesecker, scoring 15 points, thereby confirming the diagnosis of AKT1-related PS. This case report contributes to the enhanced understanding of PS diagnosis associated with AKT1 mutations.

Publicações recentes

Ver todas no PubMed

📚 EuropePMC437 artigos no totalmostrando 197

2026

Pulmonary Involvement in Proteus Syndrome: Clinical and Imaging Correlates in a Rare Case.

Case reports in radiology
2026

Characterizing Paratesticular Neoplasms in Proteus Syndrome.

The American journal of surgical pathology
2025

Analysis of the Occurrence of PIK3CA Gene Mutation in Children with Lymphatic Malformation-Single Center Study.

Children (Basel, Switzerland)
2025

Postoperative rehabilitation in a patient with Proteus syndrome following scoliosis surgery: A case report.

Medicine
2025

Targeted management of vascular anomalies.

Journal of the European Academy of Dermatology and Venereology : JEADV
2026

A Case Report of a Mild and Atypical Presentation of Proteus Syndrome.

Pediatric dermatology
2025

A Case of Proteus Syndrome, Suspected as Maffucci Syndrome in a Chinese Child.

Case reports in pediatrics
2025

Exploring Prenatal Signs of Congenital Lipomatous Overgrowth, Vascular Malformations, Epidermal Nevi, and Skeletal Anomalies (CLOVES) Syndrome: A Case Report and Literature Review.

Cureus
2026

3D CT cinematic rendering of microcardia and multiple thoracoabdominal venous dilation in Proteus syndrome.

European heart journal. Cardiovascular Imaging
2025

Safety findings from the phase 1/2 MOSAIC study of miransertib for patients with PIK3CA-related overgrowth spectrum or Proteus syndrome.

Orphanet journal of rare diseases
2025

Proteus syndrome with late diagnosis confirmation: a case report.

Frontiers in pediatrics
2025

Gross hematuria associated to bladder vascular malformation in Proteus syndrome successfully treated with holmium laser fulguration: A case report.

Urology case reports
2025

Placental transmogrification of the lung in AKT1-related Proteus syndrome.

ERJ open research
2025

Proteus Syndrome: Manifestations of Systemic Deformities.

Radiology
2025

A diagnostic challenge: A rare case of PTEN hamartoma of soft tissue of the mental region.

International journal of surgery case reports
2025

Thoracic facet overgrowth causing radiculopathy - A rare spinal manifestation of Proteus syndrome.

Clinical neurology and neurosurgery
2025

Prenatal Diagnosis of Proteus Syndrome: About a Case.

American journal of medical genetics. Part A
2025

Tumour spectrum in AKT1-related Proteus syndrome: a systematic review of clinical reports and series.

Journal of medical genetics
2024

Proteus syndrome: A rare case report.

Asian journal of surgery
2024

Management of Children with Megafoot Secondary to Proteus Syndrome: A Report of Three Cases with Long-Term Follow-Up.

Journal of the American Podiatric Medical Association
2024

Intraspinal lipomatous neurofibroma in a child with atypical Proteus syndrome.

Child's nervous system : ChNS : official journal of the International Society for Pediatric Neurosurgery
2024

Proteus syndrome with progressive paralysis of the unilateral lower limb: A rare case report and literature review.

Heliyon
2024

Alterations of the AKT Pathway in Sporadic Human Tumors, Inherited Susceptibility to Cancer, and Overgrowth Syndromes.

Current topics in microbiology and immunology
2024

Proteus Syndrome: Case Report and Updated Literature Review.

Archives of plastic surgery
2024

Proteus Syndrome: A Rare Congenital Disorder.

Cureus
2024

Dermato-Radiological Evaluation of Congenital Limb Overgrowth Vascular Syndromes.

Indian dermatology online journal
2024

Insights into Clinical Disorders in Cowden Syndrome: A Comprehensive Review.

Medicina (Kaunas, Lithuania)
2024

Proteus syndrome: a dermatologist's perspective -case report.

International journal of dermatology
2024

Case report: Association between PTEN-gene variant and an aggressive case of multiple dAVFs.

Frontiers in neurology
2024

Human vascular organoids with a mosaic AKT1 mutation recapitulate Proteus syndrome.

bioRxiv : the preprint server for biology
2024

Quantification of Proteus syndrome-associated lung disease.

Orphanet journal of rare diseases
2024

Optic nerve compression: a rare ocular manifestation of Proteus syndrome.

Journal of AAPOS : the official publication of the American Association for Pediatric Ophthalmology and Strabismus
2023

Sinonasal Neuroendocrine Carcinoma in Adult Proteus Syndrome.

Iranian journal of otorhinolaryngology
2023

Ophthalmic manifestations and treatments of proteus syndrome: a case report and systematic review.

European review for medical and pharmacological sciences
2023

Recurrent laryngeal lymphangiomatosis in a patient with Proteus syndrome: A case report.

Clinical case reports
2023

Lipomas: genetic basis of common skin lesions and their occurrence in rare diseases.

Postepy dermatologii i alergologii
2023

Cerebriform Plaques in Proteus Syndrome.

Mayo Clinic proceedings
2023

Somatic mutation spectrum of a Chinese cohort of pediatrics with vascular malformations.

Orphanet journal of rare diseases
2023

Discovering Deleterious Single Nucleotide Polymorphisms of Human AKT1 Oncogene: An In Silico Study.

Life (Basel, Switzerland)
2023

Pleckstrin Homology [PH] domain, structure, mechanism, and contribution to human disease.

Biomedicine &amp; pharmacotherapy = Biomedecine &amp; pharmacotherapie
2023

Proteus Syndrome: A Rare Disease Of Disproportionate And Asymmetric Overgrowth Of Connective Tissue.

Journal of Ayub Medical College, Abbottabad : JAMC
2023

Co-occurrence of Proteus syndrome and ventricular tachycardia cardiac arrest in a teenager.

American journal of medical genetics. Part A
2023

Epidermal nevus superimposed by psoriatic plaque in a girl with proteous syndrome.

Clinical case reports
2023

Case for diagnosis. Vascular malformations, hemihypertrophy and macrodactyly: Proteus syndrome.

Anais brasileiros de dermatologia
2023

Localized heterochrony integrates overgrowth potential of oncogenic clones.

Disease models &amp; mechanisms
2022

Proteus Syndrome, Anticipated Difficult Airway, and 2 Trusted Lieutenants!

Turkish journal of anaesthesiology and reanimation
2022

A "V"-Shaped Intraoral Lipoma on the Floor of the Mouth: A Case Report.

Cureus
2022

A Rare Case of an Asymmetric Overgrowth Syndrome in a Kenyan African Child: A Case Report and Review of Literature.

Cureus
2022

Vascular Anomaly Syndromes in the ISSVA Classification System: Imaging Findings and Role of Interventional Radiology in Management.

Radiographics : a review publication of the Radiological Society of North America, Inc
2022

Proteus syndrome with sciatic nerve fibrolipomatous hamartoma: an uncommon finding in a rare disease: report of two cases with literature review.

BJR case reports
2022

Congenital difference of the hand and foot: Pediatric macrodactyly.

Journal of plastic, reconstructive &amp; aesthetic surgery : JPRAS
2023

Verrucous epidermal nevus as a manifestation of a type 2 mosaic PTEN mutation in Cowden syndrome.

Pediatric dermatology
2022

Chemically-induced osteogenic cells for bone tissue engineering and disease modeling.

Biomaterials
2023

Multimodal ocular imaging in Proteus syndrome.

European journal of ophthalmology
2022

Sirolimus treatment of a PTEN hamartoma tumor syndrome presenting with melena.

The Turkish journal of pediatrics
2022

Assessing Cutaneous Mosaicism at the Molecular Level.

The Journal of investigative dermatology
2022

Phenotypic Features of Cystic Lung Disease in Proteus Syndrome: A Clinical Trial.

Annals of the American Thoracic Society
2022

Postmortem Diagnosis of the Proteus Syndrome by Next Generation Sequencing of Affected Brain Tissue.

Academic forensic pathology
2022

Precapillary pulmonary arterial hypertension in a patient with Proteus syndrome.

Pulmonary circulation
2022

VEGF Pathway Gene Expression Profile of Proliferating versus Involuting Infantile Hemangiomas: Preliminary Evidence and Review of the Literature.

Children (Basel, Switzerland)
2022

Progressive frontal intraosseous lipoma: Detection of the mosaic AKT1 variant discloses Proteus syndrome.

Clinical genetics
2022

The Role of Interventional Pain Management in Proteus Syndrome: A Case Report.

Cureus
2022

Proteus-Like Syndrome: A Rare Phenotype of Phosphatase and Tensin Homolog Hamartoma Tumor Syndrome.

Cureus
2022

Development of the Clinical Gestalt Assessment: a visual clinical global impression scale for Proteus syndrome.

Orphanet journal of rare diseases
2022

Late-onset Proteus syndrome with cerebriform connective tissue nevus and subsequent development of intraductal papilloma.

American journal of medical genetics. Part A
2022

Phenotypic and molecular characterization of five patients with PIK3CA-related overgrowth spectrum (PROS).

American journal of medical genetics. Part A
2022

Compartment Syndrome following Below-Knee Amputation.

Case reports in orthopedics
2022

Unusual Cause for Abdominal Pain and Chronic Constipation in a Young Female Patient.

Gastroenterology
2022

A rare gynecologic presentation of proteus syndrome: A case report.

Case reports in women's health
2021

Proteus syndrome in pregnancy: A case report.

Obstetric medicine
2021

Macrodystrophia Lipomatosa: A Rare Cause of Bilateral Lower Limb Gigantism.

Cureus
2022

Epidermal Nevi: What Is New.

Dermatologic clinics
2021

Reduction of Disease Burden With Early Sirolimus Treatment in a Child With Proteus Syndrome.

JAMA dermatology
2022

Proteus Syndrome: Case Report with Anatomopathological Correlation.

Fetal and pediatric pathology
2021

Case report: five-year experience of AKT inhibition with miransertib (MK-7075) in an individual with Proteus syndrome.

Cold Spring Harbor molecular case studies
2022

The Forgotten Phacomatoses: A Neuroimaging Review of Rare Neurocutaneous Disorders.

Current problems in diagnostic radiology
2021

Dermatologic findings in individuals with genetically confirmed Proteus syndrome.

Pediatric dermatology
2021

Immature teratoma in an adolescent with Proteus syndrome: A novel association.

Clinical case reports
2021

Clinical Phenotype and Bone Biopsy Characteristics in a Child with Proteus Syndrome.

Calcified tissue international
2021

Proteus Syndrome: A Rare Case in An Adult Ward.

European journal of case reports in internal medicine
2021

Phenotype and Surgical Treatment in a Case of Proteus Syndrome With Craniofacial and Oral Findings.

In vivo (Athens, Greece)
2021

Cardiothoracic imaging findings of Proteus syndrome.

Scientific reports
2021

Clinical experience with the AKT1 inhibitor miransertib in two children with PIK3CA-related overgrowth syndrome.

Orphanet journal of rare diseases
2020

Corrigendum: Overgrowth Syndromes-Evaluation, Diagnosis, and Management.

Frontiers in pediatrics
2021

Proteus syndrome caused by novel somatic AKT1 duplication.

Saudi medical journal
2020

Characterization and Childhood Tumor Risk Assessment of Genetic and Epigenetic Syndromes Associated With Lateralized Overgrowth.

Frontiers in pediatrics
2021

Genes and phenotypes in vascular malformations.

Clinical and experimental dermatology
2020

Giant Cell Tumor of Tendon Sheath Developed over Chimeric-Free Latissimus Dorsi and Serratus Anterior Muscle Flaps.

Journal of hand and microsurgery
2020

Overgrowth Syndromes-Evaluation, Diagnosis, and Management.

Frontiers in pediatrics
2020

Genetics of vascular anomalies.

Seminars in pediatric surgery
2020

Overgrowth syndromes and new therapies.

Seminars in pediatric surgery
2020

Phenotypic and genetic spectrum of isolated macrodactyly: somatic mosaicism of PIK3CA and AKT1 oncogenic variants.

Orphanet journal of rare diseases
2020

Ubiquitous expression of Akt1 p.(E17K) results in vascular defects and embryonic lethality in mice.

Human molecular genetics
2020

Acne following Blaschko's lines in Proteus syndrome.

JAAD case reports
2021

NAA10 p.(N101K) disrupts N-terminal acetyltransferase complex NatA and is associated with developmental delay and hemihypertrophy.

European journal of human genetics : EJHG
2020

Prenatal diagnosis of Proteus syndrome: Diagnosis of an AKT1 mutation from amniocytes.

Birth defects research
2020

Prophylactic anticoagulation of individuals with Proteus syndrome and COVID-19.

American journal of medical genetics. Part A
2021

Pathogenic postzygotic mosaicism in the tyrosine receptor kinase pathway: potential unidentified human disease hidden away in a few cells.

The FEBS journal
2020

Proteus syndrome of the foot: A case report and literature review.

Experimental and therapeutic medicine
2021

Misaligned foveal morphology and sector retinal dysfunction in AKT1-mosaic Proteus syndrome.

Documenta ophthalmologica. Advances in ophthalmology
2020

Proteus Syndrome, a rare case with an unusual presentation: Case report.

International journal of surgery case reports
2020

[Proteus syndrome in the practice of an otorhinolaryngologist: a clinical case].

Vestnik otorinolaringologii
2020

Allelic heterogeneity of Proteus syndrome.

Cold Spring Harbor molecular case studies
2020

Scoliosis Associated with Proteus Syndrome: Report of 2 Cases and Review of the Literature.

World neurosurgery
2021

Hypertrichotic patches as a mosaic manifestation of Proteus syndrome.

Journal of the American Academy of Dermatology
2020

Clinical report: one year of treatment of Proteus syndrome with miransertib (ARQ 092).

Cold Spring Harbor molecular case studies
2020

A case report of Proteus syndrome (PS).

BMC medical genetics
2019

Case Report: Occupational therapy in a patient with an overgrowth syndrome that restricts movement.

F1000Research
2020

Supraglottic Mass Management in a Pediatric Patient with Proteus Syndrome.

Anesthesiology
2021

Maxillofacial manifestations of Proteus syndrome: a systematic review with a case report.

Oral radiology
2019

Vascular malformations syndromes: an update.

Current opinion in pediatrics
2019

A dyadic genotype-phenotype approach to diagnostic criteria for Proteus syndrome.

American journal of medical genetics. Part C, Seminars in medical genetics
2019

Thrombosis risk factors in PIK3CA-related overgrowth spectrum and Proteus syndrome.

American journal of medical genetics. Part C, Seminars in medical genetics
2019

Molecular heterogeneity of the cerebriform connective tissue nevus in mosaic overgrowth syndromes.

Cold Spring Harbor molecular case studies
2019

Cloves Syndrome: A Rare Disorder of Overgrowth with Unusual Features - An Uncommon Phenotype?

Indian dermatology online journal
2019

[A clinical study of Proteus syndrome caused by a mosaic somatic mutation in AKT1 gene].

Zhonghua nei ke za zhi
2019

A mouse model of Proteus syndrome.

Human molecular genetics
2019

First evidence of a therapeutic effect of miransertib in a teenager with Proteus syndrome and ovarian carcinoma.

American journal of medical genetics. Part A
2019

What's New in Genetic Skin Diseases.

Dermatologic clinics
2019

Congenital Limb Overgrowth Syndromes Associated with Vascular Anomalies.

Radiographics : a review publication of the Radiological Society of North America, Inc
2019

Pharmacodynamic Study of Miransertib in Individuals with Proteus Syndrome.

American journal of human genetics
2019

Molecular diagnosis of somatic overgrowth conditions: A single-center experience.

Molecular genetics &amp; genomic medicine
2019

Selection of anesthesia for lower extremity surgery of patients with Proteus Syndrome.

Journal of clinical anesthesia
2018

Miransertib (ARQ 092), an orally-available, selective Akt inhibitor is effective against Leishmania.

PloS one
2018

Characterization of the hepatosplenic and portal venous findings in patients with Proteus syndrome.

American journal of medical genetics. Part A
2019

Soft-tissue vascular malformations and tumors. Part 2: low-flow lesions.

Radiologia
2019

Severe gynaecological involvement in Proteus Syndrome.

European journal of medical genetics
2018

PIK3CA c.3140A>G mutation in a patient with suspected Proteus Syndrome: a case report.

Clinical case reports
2018

Epidermal Nevi and Related Syndromes -- Part 1: Keratinocytic Nevi.

Actas dermo-sifiliograficas
2018

Case Report: "Incognito" proteus syndrome.

F1000Research
2018

Myths and Misdiagnoses of Proteus Syndrome.

Asian journal of anesthesiology
2018

Giant umbilical cord and hypoglycemia in an infant with Proteus syndrome.

American journal of medical genetics. Part A
2018

Patient with Proteus syndrome and paratesticular ovarian-type papillary serous carcinoma.

Pediatric blood &amp; cancer
2018

[New nosological and therapeutic perspectives in syndromic vascular malformations with a vein-lymphatic component].

La Revue de medecine interne
2018

Protean manifestations of Proteus syndrome.

Postgraduate medical journal
2018

Prenatal diagnosis of a fetus with Proteus syndrome.

Prenatal diagnosis
2018

In vitro efficacy of ARQ 092, an allosteric AKT inhibitor, on primary fibroblast cells derived from patients with PIK3CA-related overgrowth spectrum (PROS).

Neurogenetics
2018

Hemimegalencephaly with Bannayan-Riley-Ruvalcaba syndrome.

Epileptic disorders : international epilepsy journal with videotape
2018

Early history of the different forms of neurofibromatosis from ancient Egypt to the British Empire and beyond: First descriptions, medical curiosities, misconceptions, landmarks, and the persons behind the syndromes.

American journal of medical genetics. Part A
2018

Orthopaedic Management of Leg-length Discrepancy in Proteus Syndrome: A Case Series.

Journal of pediatric orthopedics
2018

Pathogenetic insights from quantification of the cerebriform connective tissue nevus in Proteus syndrome.

Journal of the American Academy of Dermatology
2018

The importance of prenatal 3-dimensional sonography in a case of a segmental overgrowth syndrome with unclear chromosomal microarray results.

Journal of clinical ultrasound : JCU
2017

Proteus Syndrome With a Cranial Intraosseous Lipoma.

The Journal of craniofacial surgery
2017

Proteus syndrome: Unveiling the anesthetic myths.

Asian journal of anesthesiology
2017

Clinical and sonographic features of pediatric soft-tissue vascular anomalies part 2: vascular malformations.

Pediatric radiology
2017

Nasopharyngeal angiofibroma in an adult with Proteus syndrome. First reported case.

Hippokratia
2017

Quantifying survival in patients with Proteus syndrome.

Genetics in medicine : official journal of the American College of Medical Genetics
2017

Characterization of thrombosis in patients with Proteus syndrome.

American journal of medical genetics. Part A
2017

In vivo efficacy of the AKT inhibitor ARQ 092 in Noonan Syndrome with multiple lentigines-associated hypertrophic cardiomyopathy.

PloS one
2017

Refractory sleep-disordered breathing due to unilateral lingual tonsillar hypertrophy in a child with Proteus Syndrome.

International journal of pediatric otorhinolaryngology
2017

Proteus Syndrome with Neurological Manifestations: A Rare Presentation.

Journal of pediatric neurosciences
2017

De Novo PTEN Mutation in a Young Boy with Cutaneous Vasculitis.

Case reports in pediatrics
2017

Overgrowth Syndromes Caused by Somatic Variants in the Phosphatidylinositol 3-Kinase/AKT/Mammalian Target of Rapamycin Pathway.

The Journal of molecular diagnostics : JMD
2017

Molecular Diagnosis of Mosaic Overgrowth Syndromes Using a Custom-Designed Next-Generation Sequencing Panel.

The Journal of molecular diagnostics : JMD
2017

Proteus syndrome: A case report and review of the literature.

Molecular and clinical oncology
2017

Proteus Syndrome with Arteriovenous Malformation.

Advanced biomedical research
2017

A Rare Case of Diffuse Hemangiomatosis of the Spleen with Splenic Rupture following Aortic Valve Replacement.

Case reports in radiology
2017

Anaesthesia and orphan diseases: Airway management in Proteus disease.

European journal of anaesthesiology
2016

Redundant plantar skin folds.

Romanian journal of morphology and embryology = Revue roumaine de morphologie et embryologie
2017

Mosaic Disorders of the PI3K/PTEN/AKT/TSC/mTORC1 Signaling Pathway.

Dermatologic clinics
2016

Recurrent cerebriform connective tissue nevus on the foot of a patient with Proteus syndrome.

Cutis
2016

Somatic overgrowth disorders of the PI3K/AKT/mTOR pathway & therapeutic strategies.

American journal of medical genetics. Part C, Seminars in medical genetics
2016

Bronchoscopic concerns in Proteus syndrome: a case report.

Korean journal of anesthesiology
2015

Neurocutaneous Manifestations of Genetic Mosaicism.

Journal of pediatric genetics
2016

Overgrowth syndromes with vascular malformations.

Seminars in cutaneous medicine and surgery
2016

Genetic basis for vascular anomalies.

Seminars in cutaneous medicine and surgery
2016

Somatic AKT1 mutations cause meningiomas colocalizing with a characteristic pattern of cranial hyperostosis.

American journal of medical genetics. Part A
2016

Early Recognition of Proteus Syndrome.

Pediatric dermatology
2016

Hemispherectomy Procedure in Proteus Syndrome.

Iranian journal of child neurology
2017

RHEGMATOGENOUS RETINAL DETACHMENT: A RARE OCULAR MANIFESTATION OF PROTEUS SYNDROME.

Retinal cases &amp; brief reports
2016

Lack of mutation-histopathology correlation in a patient with Proteus syndrome.

American journal of medical genetics. Part A
2016

Acquired lymphangiectasia (lymphangioma circumscriptum) of the vulva: Clinicopathologic study of 11 patients from a single institution and 67 from the literature.

International journal of dermatology
2016

Extending the spectrum of AKT1 mosaicism: not just the Proteus syndrome.

The British journal of dermatology
2016

Phosphatase and Tensin Homolog Hamartoma Tumor Syndrome: A Case Report.

Clinical advances in periodontics
2016

Proteus syndrome: evaluation of the immunological profile.

Orphanet journal of rare diseases
2015

Mosaic Neurocutaneous Disorders and Their Causes.

Seminars in pediatric neurology
2015

Repression of AKT signaling by ARQ 092 in cells and tissues from patients with Proteus syndrome.

Scientific reports
2015

Epidermal nevus syndromes.

Handbook of clinical neurology
2015

Phenotype/genotype correlations in epidermal nevus syndrome as a neurocristopathy.

Handbook of clinical neurology
2015

Endometrioid Paraovarian Borderline Cystic Tumor in an Infant with Proteus Syndrome.

Case reports in oncological medicine
2015

Unilateral hypertrophic skin lesions, hemimegalencephaly, and meningioma: The many faces of Proteus syndrome.

Indian dermatology online journal
2016

The categories of cutaneous mosaicism: A proposed classification.

American journal of medical genetics. Part A
2015

Orthopaedic manifestations of Proteus syndrome in a child with literature update.

Bone reports
2015

A Paratesticular Serous Borderline Tumor in a Pediatric Patient With Proteus Syndrome.

Urology
2015

Brentuximab vedotin in the treatment of a patient with refractory Hodgkin disease and Proteus syndrome - a case report and discussion.

Clinical case reports
2015

Island nail flap in the treatment of foot macrodactyly of the first ray in children: report of two cases.

Journal of children's orthopaedics
2015

Epithelial Tumors of the Ovary in Children and Teenagers: A Prospective Study from the Italian TREP Project.

Journal of pediatric and adolescent gynecology
2015

Operative Management of OSAS in a Complex Case of Proteus Syndrome.

Case reports in otolaryngology
2015

Huge paravertebral masses in Proteus syndrome.

The spine journal : official journal of the North American Spine Society
2015

Epidemiology of elephantiasis with special emphasis on podoconiosis in Ethiopia: A literature review.

Journal of vector borne diseases
2015

[Dermatological implications of the PI3K pathway].

Annales de dermatologie et de venereologie
2015

Advances in Skeletal Dysplasia Genetics.

Annual review of genomics and human genetics
2015

Proteus syndrome: what the anesthetist should know.

Journal of clinical anesthesia
2015

Surgical correction of kyphotic deformity in a patient with Proteus syndrome.

The spine journal : official journal of the North American Spine Society
2015

Hemilateral proteus syndrome: an unusual hamartomatous disorder with significant cerebellar tonsillar herniation.

Indian journal of dermatology
2015

Proteus syndrome: Report of a case with AKT1 mutation in a dental cyst.

European journal of medical genetics
2014

Fronto-temporal cerebriform connective tissue nevus in Proteus syndrome.

Indian journal of dental research : official publication of Indian Society for Dental Research
Ver todos os 437 no EuropePMC

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Doenças relacionadas

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Referências e fontes

Bases de dados externas citadas neste artigo

Publicações científicas

Artigos indexados no PubMed ligados a esta doença no grafo RarasNet — título, periódico e PMID direto da fonte, sem intermediação de IA.

  1. 3D CT cinematic rendering of microcardia and multiple thoracoabdominal venous dilation in Proteus syndrome.
    European heart journal. Cardiovascular Imaging· 2026· PMID 40795228mais citado
  2. Pulmonary Involvement in Proteus Syndrome: Clinical and Imaging Correlates in a Rare Case.
    Case reports in radiology· 2026· PMID 41522263mais citado
  3. Characterizing Paratesticular Neoplasms in Proteus Syndrome.
    The American journal of surgical pathology· 2026· PMID 41368924mais citado
  4. A Case Report of a Mild and Atypical Presentation of Proteus Syndrome.
    Pediatric dermatology· 2026· PMID 40903926mais citado
  5. A Case of Proteus Syndrome, Suspected as Maffucci Syndrome in a Chinese Child.
    Case reports in pediatrics· 2025· PMID 40894918mais citado
  6. Endovascular embolization of a superior gluteal artery aneurysm in Proteus syndrome.
    J Vasc Surg Cases Innov Tech· 2026· PMID 41890805recente
  7. Analysis of the Occurrence of PIK3CA Gene Mutation in Children with Lymphatic Malformation-Single Center Study.
    Children (Basel)· 2025· PMID 41300578recente
  8. Postoperative rehabilitation in a patient with Proteus syndrome following scoliosis surgery: A case report.
    Medicine (Baltimore)· 2025· PMID 41261675recente

Bases de dados e fontes oficiais

Identificadores e referências canônicas usadas para montar este verbete.

  1. ORPHA:744(Orphanet)
  2. OMIM OMIM:176920(OMIM)
  3. MONDO:0008318(MONDO)
  4. GARD:7475(GARD (NIH))
  5. Variantes catalogadas(ClinVar)
  6. Busca completa no PubMed(PubMed)
  7. Artigo Wikipedia(Wikipedia)
  8. Q281115(Wikidata)

Dados compilados pelo RarasNet a partir de fontes abertas (Orphanet, OMIM, MONDO, PubMed/EuropePMC, ClinicalTrials.gov, DATASUS, PCDT/MS). Este conteúdo é informativo e não substitui avaliação médica.

Conteúdo mantido por Agente Raras · Médicos e pesquisadores podem colaborar

Síndrome Proteus
Compêndio · Raras BR

Síndrome Proteus

ORPHA:744 · MONDO:0008318
Prevalência
<1 / 1 000 000
Herança
Not applicable
CID-10
Q87.3 · Síndromes com malformações congênitas com hipercrescimento precoce
CID-11
Ensaios
3 ativos
Medicamentos
1 registrados
Início
Infancy
Prevalência
0.0 (Europe)
MedGen
UMLS
C0085261
EuropePMC
Wikidata
Wikipedia
Papers 10a
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